NCT01001377

Brief Summary

The primary objective of this study is to compare the effect of panitumumab versus cetuximab on overall survival (OS) for chemorefractory metastatic colorectal cancer (mCRC) among patients with wild-type Kirsten rat Sarcoma-2 virus (KRAS) tumors.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,010

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Feb 2010

Longer than P75 for phase_3

Geographic Reach
28 countries

146 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 22, 2009

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 26, 2009

Completed
3 months until next milestone

Study Start

First participant enrolled

February 2, 2010

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 5, 2013

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

March 24, 2014

Completed
3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 7, 2017

Completed
Last Updated

September 21, 2022

Status Verified

September 1, 2022

Enrollment Period

3 years

First QC Date

October 22, 2009

Results QC Date

February 3, 2014

Last Update Submit

September 8, 2022

Conditions

Keywords

PanitumumabVectibixColon CancerColorectal CancerRectal CancerCetuximabErbituxMetastatic

Outcome Measures

Primary Outcomes (1)

  • Overall Survival

    Overall survival is the time from the date of randomization until the date of death. Participants who had not died by the analysis data cut-off date were censored at their last contact date.

    From randomization until the data cut-off date of 5 February 2013. Maximum time on study was 155 weeks.

Secondary Outcomes (11)

  • Progression-free Survival

    From randomization until the data cut-off date of 5 February 2013. Maximum time on study was 155 weeks.

  • Objective Response

    From randomization until the data cut-off date of 5 February 2013. Maximum time on study was 155 weeks.

  • Duration of Response

    From randomization until the data cut-off date of 5 February 2013. Maximum time on study was 155 weeks.

  • Time to Response

    From randomization until the data cut-off date of 5 February 2013. Maximum time on study was 155 weeks.

  • Time to Treatment Failure

    From randomization until the data cut-off date of 5 February 2013. Maximum time on study was 155 weeks.

  • +6 more secondary outcomes

Study Arms (2)

Cetuximab

ACTIVE COMPARATOR

Cetuximab 400 mg/m\^2 as an initial dose, followed by 250 mg/m\^2 intravenously (IV) every 7 days. Participants were treated until disease progression, intolerability, withdrawal of consent, or death.

Drug: Cetuximab

Panitumumab

EXPERIMENTAL

Panitumumab 6 mg/kg IV every 14 days. Participants were treated until disease progression, intolerability, withdrawal of consent, or death.

Drug: Panitumumab

Interventions

Administered by intravenous infusion

Also known as: Erbitux
Cetuximab

Administered by intravenous infusion

Also known as: Vectibix
Panitumumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed diagnosis of adenocarcinoma of the colon or rectum, metastatic disease
  • Wild-type KRAS tumor status
  • Eastern Cooperative Oncology Group (ECOG) score of 0, 1 or 2
  • Must have failed a prior regimen containing irinotecan for metastatic disease and a prior regimen containing oxaliplatin for metastatic disease
  • Must have previously received a thymidylate synthase inhibitor (eg, fluorouracil, capecitabine, raltitrexed, or fluorouracil-uracil) at any point for treatment of colorectal cancer (CRC)
  • Adequate hematologic, renal, hepatic and metabolic function

You may not qualify if:

  • Symptomatic brain metastases requiring treatment
  • Prior anti-epidermal growth factor receptor (EGFr) antibody therapy (eg, panitumumab or cetuximab) or treatment with small molecule EGFr inhibitors (eg, gefitinib, erlotinib, lapatinib)
  • Antitumor therapy (eg, chemotherapy, hormonal therapy, immunotherapy, antibody therapy, radiotherapy), or investigational agent or therapy ≤ 30 days before randomization.
  • Clinically significant cardiovascular disease
  • Active infection requiring systemic treatment or any uncontrolled infection ≤14 days prior to randomization

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (152)

Research Site

Stockton, California, 95204, United States

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Boynton Beach, Florida, 33426, United States

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Wichita, Kansas, 67214, United States

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Temple, Texas, 76508, United States

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Ogden, Utah, 84403, United States

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Liverpool, New South Wales, 2170, Australia

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St Leonards, New South Wales, 2065, Australia

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Wahroonga, New South Wales, 2076, Australia

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Wollongong, New South Wales, 2500, Australia

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Woodville South, South Australia, 5011, Australia

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Ballarat, Victoria, 3350, Australia

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Box Hill, Victoria, 3128, Australia

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Epping, Victoria, 3076, Australia

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Footscray, Victoria, 3011, Australia

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Heidelberg, Victoria, 3084, Australia

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Parkville, Victoria, 3050, Australia

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Edegem, 2650, Belgium

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Sofia, 1527, Bulgaria

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Sofia, 1784, Bulgaria

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Edmonton, Alberta, T6G 1Z2, Canada

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Halifax, Nova Scotia, B3H 2Y9, Canada

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Guangzhou, Guangdong, 510060, China

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Guangzhou, Guangdong, 510180, China

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Guangzhou, Guangdong, 510280, China

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Guangzhou, Guangdong, 515515, China

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Harbin, Heilongjiang, 150040, China

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Changsha, Hunan, 410013, China

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Nanjing, Jiangsu, 210002, China

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Changchun, Jilin, 130012, China

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Xi'an, Shaanxi, 710061, China

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Shanghai, Shanghai Municipality, 200092, China

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Chengdu, Sichuan, 610041, China

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Chongqing, Sichuan, 400038, China

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Hangzhou, Zhejiang, 310009, China

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Hangzhou, Zhejiang, 310016, China

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Beijing, 100021, China

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Beijing, 100071, China

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Beijing, 100142, China

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Shanghai, 200003, China

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Shanghai, 200032, China

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Shanghai, 200080, China

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Tianjin, 300060, China

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Hořovice, 268 31, Czechia

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Nová Ves pod Pleší, 262 04, Czechia

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Olomouc, 775 20, Czechia

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Prague, 100 34, Czechia

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Příbram, 261 01, Czechia

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Znojmo, 669 02, Czechia

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Besançon, 25030, France

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Montbéliard, 25200, France

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Saint-Brieuc, 22015, France

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Saint-Herblain, 44800, France

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Villejuif, 94805, France

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Kowloon, Hong Kong

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New Territories, Hong Kong

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Hyderabad, Andhra Pradesh, 500 024, India

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Hyderabad, Andhra Pradesh, 500 034, India

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Kochi, Kerala, 682 304, India

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Ahilyanagar, Maharashtra, 413 736, India

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Nagpur, Maharashtra, 440 012, India

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Nashik, Maharashtra, 422 004, India

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Nashik, Maharashtra, 422 005, India

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Pune, Maharashtra, 411 004, India

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Jaipur, Rajasthan, 302 013, India

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Chennai, Tamil Nadu, 600 018, India

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Kolkata, West Bengal, 700 016, India

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Beersheba, 64239, Israel

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Jerusalem, 91031, Israel

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Kfar Saba, 44281, Israel

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Ramat Gan, 52621, Israel

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Rehovot, 76100, Israel

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Ancona, 60131, Italy

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Cesena, 47023, Italy

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Cremona, 26100, Italy

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Faenza RA, 48018, Italy

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Genova, 16132, Italy

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Lugo, 48022, Italy

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Meldola FC, 47014, Italy

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Ravenna, 48100, Italy

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Rimini, 47900, Italy

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Torino, 10126, Italy

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Daugavpils, 5417, Latvia

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Riga, 1002, Latvia

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Riga, 1079, Latvia

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Kaunas, 50009, Lithuania

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Vilnius, 08660, Lithuania

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Kota Bharu, Kelantan, 16150, Malaysia

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Kuala Lumpur, Kuala Lumpur, 56000, Malaysia

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Kuala Lumpur, Kuala Lumpur, 59100, Malaysia

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Kota Kinabalu, Sabah, 88996, Malaysia

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Rotterdam, 3000 CA, Netherlands

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Lima, 13, Peru

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Lima, 34, Peru

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Lima, Lima 27, Peru

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Cebu City, 6000, Philippines

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Manila, 1000, Philippines

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Quezon City, 1102, Philippines

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Elblag, 82-300, Poland

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Gdansk, 80-219, Poland

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Jelenia Góra, 58-506, Poland

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Poznan, 61-485, Poland

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Szczecin, 71-730, Poland

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Warsaw, 02-097, Poland

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Warsaw, 02-507, Poland

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Warsaw, 02-781, Poland

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Bucharest, 022328, Romania

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Sibiu, 550245, Romania

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Moscow, 115478, Russia

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Moscow, 117997, Russia

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Saint Petersburg, 197022, Russia

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Saint Petersburg, 197758, Russia

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Saint Petersburg, 198255, Russia

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Kamenitz, 21204, Serbia

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Niš, 18000, Serbia

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Singapore, 119228, Singapore

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Singapore, 308433, Singapore

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Bardejov, 085 01, Slovakia

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Bratislava, 831 01, Slovakia

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Nitra, 950 01, Slovakia

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Groenkloof, Gauteng, 0181, South Africa

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Johannesburg, Gauteng, 2199, South Africa

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Kraaifontein, Western Cape, 7570, South Africa

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Johannesburg, 2193, South Africa

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Port Elizabeth, 6045, South Africa

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Goyang-si, Gyeonggi-do, 410-769, South Korea

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Seoul, 110-744, South Korea

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Seoul, 120-752, South Korea

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Seoul, 135-710, South Korea

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Seoul, 136-705, South Korea

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Seoul, 138-736, South Korea

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Gothenburg, 416 85, Sweden

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Linköping, 581 85, Sweden

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Lund, 221 85, Sweden

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Uppsala, 751 85, Sweden

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Vaxjo, 351 85, Sweden

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Västerås, 721 89, Sweden

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Putzu City, Chiayi, 61363, Taiwan

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Keelung, 20401, Taiwan

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Tainan, 70403, Taiwan

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Taipei, 11031, Taiwan

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Taoyuan District, 33305, Taiwan

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Belfast, BT9 7AB, United Kingdom

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Bristol, BS2 8ED, United Kingdom

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Cardiff, CF14 2TL, United Kingdom

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Guildford, GU2 7XX, United Kingdom

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Leicester, LE1 5WW, United Kingdom

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London, SW17 0QT, United Kingdom

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Maidstone, ME16 9QQ, United Kingdom

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Manchester, M20 4BX, United Kingdom

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Oxford, OX3 7LJ, United Kingdom

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Sutton, SM2 5PT, United Kingdom

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Wolverhampton, WV10 0QP, United Kingdom

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Related Publications (7)

  • Price T, Kim TW, Li J, Cascinu S, Ruff P, Suresh AS, Thomas A, Tjulandin S, Guan X, Peeters M. Final results and outcomes by prior bevacizumab exposure, skin toxicity, and hypomagnesaemia from ASPECCT: randomized phase 3 non-inferiority study of panitumumab versus cetuximab in chemorefractory wild-type KRAS exon 2 metastatic colorectal cancer. Eur J Cancer. 2016 Nov;68:51-59. doi: 10.1016/j.ejca.2016.08.010. Epub 2016 Oct 5.

    PMID: 27716478BACKGROUND
  • Price TJ, Peeters M, Kim TW, Li J, Cascinu S, Ruff P, Suresh AS, Thomas A, Tjulandin S, Zhang K, Murugappan S, Sidhu R. Panitumumab versus cetuximab in patients with chemotherapy-refractory wild-type KRAS exon 2 metastatic colorectal cancer (ASPECCT): a randomised, multicentre, open-label, non-inferiority phase 3 study. Lancet Oncol. 2014 May;15(6):569-79. doi: 10.1016/S1470-2045(14)70118-4. Epub 2014 Apr 14.

    PMID: 24739896BACKGROUND
  • Kim TW, Peeters M, Thomas A, Gibbs P, Hool K, Zhang J, Ang AL, Bach BA, Price T. Impact of Emergent Circulating Tumor DNA RAS Mutation in Panitumumab-Treated Chemoresistant Metastatic Colorectal Cancer. Clin Cancer Res. 2018 Nov 15;24(22):5602-5609. doi: 10.1158/1078-0432.CCR-17-3377. Epub 2018 Jun 13.

    PMID: 29898991BACKGROUND
  • Peeters M, Price T, Boedigheimer M, Kim TW, Ruff P, Gibbs P, Thomas A, Demonty G, Hool K, Ang A. Evaluation of Emergent Mutations in Circulating Cell-Free DNA and Clinical Outcomes in Patients with Metastatic Colorectal Cancer Treated with Panitumumab in the ASPECCT Study. Clin Cancer Res. 2019 Feb 15;25(4):1216-1225. doi: 10.1158/1078-0432.CCR-18-2072. Epub 2018 Nov 28.

    PMID: 30487126BACKGROUND
  • Price T, Ang A, Boedigheimer M, Kim TW, Li J, Cascinu S, Ruff P, Satya Suresh A, Thomas A, Tjulandin S, Peeters M. Frequency of S492R mutations in the epidermal growth factor receptor: analysis of plasma DNA from patients with metastatic colorectal cancer treated with panitumumab or cetuximab monotherapy. Cancer Biol Ther. 2020 Oct 2;21(10):891-898. doi: 10.1080/15384047.2020.1798695. Epub 2020 Oct 7.

    PMID: 33026965BACKGROUND
  • Taniguchi H, Yamanaka T, Sakai D, Muro K, Yamazaki K, Nakata S, Kimura H, Ruff P, Kim TW, Peeters M, Price T. Efficacy of Panitumumab and Cetuximab in Patients with Colorectal Cancer Previously Treated with Bevacizumab; a Combined Analysis of Individual Patient Data from ASPECCT and WJOG6510G. Cancers (Basel). 2020 Jun 28;12(7):1715. doi: 10.3390/cancers12071715.

  • Graham CN, Maglinte GA, Schwartzberg LS, Price TJ, Knox HN, Hechmati G, Hjelmgren J, Barber B, Fakih MG. Economic Analysis of Panitumumab Compared With Cetuximab in Patients With Wild-type KRAS Metastatic Colorectal Cancer That Progressed After Standard Chemotherapy. Clin Ther. 2016 Jun;38(6):1376-1391. doi: 10.1016/j.clinthera.2016.03.023. Epub 2016 Apr 13.

Related Links

MeSH Terms

Conditions

Colorectal NeoplasmsColonic NeoplasmsRectal NeoplasmsNeoplasm Metastasis

Interventions

CetuximabPanitumumab

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Study Director
Organization
Amgen Inc.

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 22, 2009

First Posted

October 26, 2009

Study Start

February 2, 2010

Primary Completion

February 5, 2013

Study Completion

March 7, 2017

Last Updated

September 21, 2022

Results First Posted

March 24, 2014

Record last verified: 2022-09

Locations