NCT00303667

Brief Summary

RATIONALE: Giving chemotherapy, such as fludarabine phosphate and cyclophosphamide, and total body irradiation, before peripheral blood stem cell transplant helps stop the growth of cancer cells. It may also stop the patient's immune system from rejecting the donor's stem cells. When the healthy stem cells and natural killer (NK) cells from a donor are infused into the patient they may help the patient's bone marrow make stem cells, red blood cells, white blood cells, and platelets. Giving IL-2 (aldesleukin) after NK cell infusion may stimulate them to kill any remaining cancer cells. PURPOSE: This phase I/II (currently enrolling in phase II) trial is studying how well a donor natural killer cell infusion works in treating patients who are undergoing donor stem cell transplant for acute myeloid leukemia.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jan 2005

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2005

Completed
1.2 years until next milestone

First Submitted

Initial submission to the registry

March 15, 2006

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 17, 2006

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2011

Completed
4.3 years until next milestone

Results Posted

Study results publicly available

July 3, 2015

Completed
Last Updated

December 28, 2017

Status Verified

December 1, 2017

Enrollment Period

6.2 years

First QC Date

March 15, 2006

Results QC Date

June 11, 2015

Last Update Submit

December 3, 2017

Conditions

Keywords

NK cellsnatural killer cellsimmunotherapyhematopoietic cell transplantacute myelogenous leukemia

Outcome Measures

Primary Outcomes (2)

  • Disease-free Survival at 6 Months

    Number of patients alive without evidence of disease at 6 months after transplant

    Month 6

  • Disease-free Survival at 1 Year

    Number of patients alive without evidence of disease at 1 year after transplant

    1 Year

Secondary Outcomes (7)

  • In Vivo Expansion of a Donor NK Cells NK Cell Product

    12 - 14 days after NK cell infusion

  • Number of Patients With Graft Failure

    Day 28

  • Incidence of Grade III-IV Acute Graft Versus Host Disease

    Month 6

  • Number of Patients With Treatment-Related Mortality

    Day 100

  • Incidence of Chronic Graft Versus Host Disease

    1 Year

  • +2 more secondary outcomes

Study Arms (2)

SCT w/Donor Natural Killer Cells - short schema

EXPERIMENTAL

Patients with high risk myeloid malignancies undergoing allogeneic hematopoietic stem cell transplantation, receiving fludarabine phosphate (daily dose of 40mg/m\^2), cyclophosphamide (administered on Day -15 only), cyclosporin A, total body irradiation, natural killer cells, aldesleukin, and thymoglobulin.

Biological: aldesleukinBiological: natural killer cellsDrug: cyclophosphamideDrug: fludarabine phosphateProcedure: allogeneic hematopoietic stem cell transplantationRadiation: total body irradiationBiological: ThymoglobulinDrug: Cyclosporin A

SCT w/Donor Natural Killer Cells - extended schema

EXPERIMENTAL

Patients with high risk myeloid malignancies undergoing allogeneic hematopoietic stem cell transplantation, receiving fludarabine phosphate (daily dose of 35mg/m\^2), cyclophosphamide (administered on Days -15 and -16), cyclosporin A, total body irradiation, natural killer cells, aldesleukin, and thymoglobulin.

Biological: aldesleukinBiological: natural killer cellsProcedure: allogeneic hematopoietic stem cell transplantationRadiation: total body irradiationBiological: ThymoglobulinDrug: Cyclosporin ADrug: cyclophosphamideDrug: fludarabine phosphate

Interventions

aldesleukinBIOLOGICAL

Administered subcutaneously (SQ) 9 million units every other day beginning Day -12 through -2 (evening of natural killer cell infusion) for a total of 6 doses.

Also known as: Interleukin-2, IL-2
SCT w/Donor Natural Killer Cells - extended schemaSCT w/Donor Natural Killer Cells - short schema

Infusion given on Day -12; The targeted infused cell dose of CD3- CD19- selected NK product is within the range of 2-3 x 10\^7 cells/kg.

Also known as: therapeutic allogeneic lymphocytes
SCT w/Donor Natural Killer Cells - extended schemaSCT w/Donor Natural Killer Cells - short schema

Administered intravenously (IV) 50 mg/kg on Day -15

Also known as: Cytoxan
SCT w/Donor Natural Killer Cells - short schema

Administered intravenously (IV) 40 mg/m\^2 on Days -18 through -14

Also known as: Fludara
SCT w/Donor Natural Killer Cells - short schema

On day 0, patients will receive an allogeneic transplant using pool cells from the day -1 and day 0 PBSC which will be CD34+ selected as the donor graft. The graft will be infused over 15-60 minutes.

Also known as: PBSC
SCT w/Donor Natural Killer Cells - extended schemaSCT w/Donor Natural Killer Cells - short schema

Administered on Day -13, 200 cGy two times.

SCT w/Donor Natural Killer Cells - extended schemaSCT w/Donor Natural Killer Cells - short schema
ThymoglobulinBIOLOGICAL

intravenous (IV) 3 mg/kg on Day 0 (day of donor CD34 cell infusion)

Also known as: rabbit ATG
SCT w/Donor Natural Killer Cells - extended schemaSCT w/Donor Natural Killer Cells - short schema

1.5 mg/kg by mouth or intravenously for target dose range of 150-250; day -15 through day -8.

Also known as: CSA
SCT w/Donor Natural Killer Cells - extended schemaSCT w/Donor Natural Killer Cells - short schema

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • High risk acute myeloid leukemia (AML) fitting within one of the following disease groups:
  • Primary induction failure defined as no complete remission (CR) after two or more induction cycles. For primary induction failure (PIF) or refractory AML, the patient must have \<5% circulating blasts (and \<1000 absolute circulating blasts) beyond Day 28 after last chemo. During work-up period if circulating blasts rise above these levels, the patient is ineligible. The use of hydrea or other non-induction cytotoxic agents is not allowed to reduce blasts and achieve this eligibility. If the blasts are higher than these limits, the patient should be treated on an alternative therapeutic protocol or receive another reinduction attempt. (See section 7 regarding final check of blast status within 7 days of preparative regimen start).
  • Relapsed AML with low disease burden must have less than 5% marrow blasts at time of enrollment for patients who did not receive re-induction or measured at least 28 days from the start of reinduction therapy for patients who did receive re-induction (maximum of 2 re-induction attempts). Patients who have relapsed more than 12 months following a prior HCT and did not reach CR following one re-induction cycle but have less than 10% marrow blasts are eligible.
  • CR3 or greater. This will include CRp defined as CR without platelet recovery to 100,000/mcL.
  • CR1 or CR2 with high risk features (therapy induced, prior myelodysplastic syndrome \[MDS\] or myeloproliferative disease \[MPD\], high risk cytogenetic or molecular phenotype) with no available alternate (sibling, unrelated donor \[URD\] or umbilical cord blood \[UCB\]) donors.
  • Patients with prior central nervous system (CNS) involvement are eligible provided that it has been treated and CFS must be clear for at least 2 weeks prior to enrollment.
  • Available related HLA-haploidentical donor (3-5 of 6 HLA, A, B and DRB1 matched)
  • Karnofsky performance status \> 50
  • Pulmonary Function: oxygen saturation ≥ on room air and diffusion lung capacity for carbon monoxide (DLCOcor) ≥ 40%
  • Cardiac Function: Ejection fraction (EF) ≥ 30%, no uncontrolled angina, severe uncontrolled ventricular arrhythmias, or electrocardiographic evidence of acute ischemia or active conduction system abnormalities.
  • Able to be off prednisone or other immunosuppressive medications for at least 3 days prior to Day 0
  • Women of child bearing potential must have a negative pregnancy test within 14 days prior to study registration and agree to use adequate birth control during study treatment
  • Human anti-mouse antibody (HAMA) monitoring: All subjects will be questioned about prior exposure to antibody therapy (including OKT3, rituximab, trastuzumab, etc).
  • For subjects with no prior antibody therapy exposure, no further action will be taken
  • For subjects who have received previous antibody therapies 10 ml of serum will be drawn before starting therapy. The presence of HAMA will not preclude proceeding with treatment.
  • +1 more criteria

You may not qualify if:

  • Biphenotypic leukemia
  • New or progressive pulmonary infiltrates on screening chest x-ray or chest computed tomography (CT) scan that has not been evaluated with bronchoscopy, if feasible. Infiltrates attributed to infection must be stable/improving (with associated clinical improvement) after 1 week of appropriate therapy (2 weeks for presumed or documented fungal infections). Surgical resection waives any waiting requirements.
  • Uncontrolled bacterial or viral infections. Chronic asymptomatic viral hepatitis is allowed.
  • Known hypersensitivity to any of the study agents used
  • Received other investigational drugs within the 14 days before enrollment
  • Donor Selection:
  • years of age
  • \> 40 kilogram body weight
  • In general good health as determined by the evaluating physician
  • Donors must be HLA-A, B, DRB1 haploidentical (3-5/6 antigens HLA, A, B, DRB1) match to recipient. Patients and donors will be typed for HLA-A, B and C using at least intermediate resolution DNA techniques for DRB1 at high (allele) resolution. KIR B genotyping will be done on all haploidentical donors, and when feasible, the donor with the most favorable KIR gene profile will be used.
  • Able and willing to have up to 4 separate apheresis collections per formed
  • Not pregnant
  • Human immunodeficiency virus (HIV): HIV-1, HIV-2 negative; HTLV-1, HTLV-2 negative, Hepatitis B and C negative
  • Voluntary written consent

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Masonic Cancer Center, University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

aldesleukinInterleukin-2IL32 protein, humanCyclophosphamidefludarabine phosphateWhole-Body IrradiationthymoglobulinCyclosporine

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

InterleukinsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsLymphokinesProteinsBiological FactorsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsRadiotherapyTherapeuticsInvestigative TechniquesCyclosporinsPeptides, CyclicMacrocyclic CompoundsPolycyclic Compounds

Results Point of Contact

Title
Sarah Cooley, M.D.
Organization
Masonic Cancer Center

Study Officials

  • Sarah Cooley, MD

    Masonic Cancer Center, University of Minnesota

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 15, 2006

First Posted

March 17, 2006

Study Start

January 1, 2005

Primary Completion

March 1, 2011

Study Completion

March 1, 2011

Last Updated

December 28, 2017

Results First Posted

July 3, 2015

Record last verified: 2017-12

Locations