NCT00045968

Brief Summary

The primary purpose of the study is to determine the efficacy of an investigational therapy called DCVax(R)-L in patients with newly diagnosed GBM for whom surgery is indicated. Patients must enter screening at a participating site prior to surgical resection of the tumor. Patients will receive the standard of care, including radiation and Temodar therapy and two out of three will additionally receive DCVax-L, with the remaining one third receiving a placebo. All patients will have the option to receive DCVax-L in a crossover arm upon documented disease progression. (note: DCVax-L when used for patients with brain cancer is sometimes also referred to as DCVax-Brain)

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
348

participants targeted

Target at P50-P75 for phase_3

Geographic Reach
4 countries

86 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 17, 2002

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 19, 2002

Completed
4.2 years until next milestone

Study Start

First participant enrolled

December 1, 2006

Completed
15.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2022

Completed
Last Updated

May 18, 2022

Status Verified

May 1, 2022

Enrollment Period

15.9 years

First QC Date

September 17, 2002

Last Update Submit

May 12, 2022

Conditions

Keywords

oncologyneurologygliomabrain tumorbrain cancerglioblastoma multiformeglioblastomanewly diagnosed glioblastomaimmunotherapydendritic cellsimmune therapyGBMBrain cancer, primarytumor vaccinegrade IV astrocytomaDCVaxGrade IV brain cancer

Outcome Measures

Primary Outcomes (1)

  • The primary objective of this study is to compare overall survival (OS) between patients randomized to DCVax-L and control patients from comparable, contemporaneous trials who received standard of care therapy only, in newly diagnosed glioblastoma.

    Until death

Secondary Outcomes (1)

  • The first secondary objective is to compare overall survival (OS) between patients randomized to placebo who received DCVax-L treatment following disease recurrence, and control patients from comparable, contemporaneous clinical trials, in recurrent GBM.

    Until death

Study Arms (2)

treatment cohort

ACTIVE COMPARATOR
Drug: Dendritic cell immunotherapy

Placebo Chohort

PLACEBO COMPARATOR

Autologous PBMC

Drug: Dendritic cell immunotherapy

Interventions

Two intradermal (i.d.) injections of DCVax-L(treatment cohort) or autologous PBMC (placebo cohort) per treatment. Treatments will be given at days 0, 10, 20, and at weeks 8, 16, 32, 48, 72, 96 and 120.

Also known as: DCVax-L, DCVax, DCVax-Brain
Placebo Chohorttreatment cohort

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have sufficient tumor lysate protein that was generated from the surgically obtained tumor material. Patients must also have sufficient DCVax-L product available after manufacturing. These determinations will be made by Cognate BioServices, Inc. (Cognate) and communicated to the clinical site through the Sponsor, or its designee.
  • Patients with newly diagnosed, unilateral GBM (Grade IV) are eligible for this protocol. An independent neuropathologist will review this diagnosis during the enrollment process.
  • Subjects ≥18 and ≤70 years of age at surgery who are capable of informed consent. Patients must be able to understand and sign the informed consent documents indicating that they are aware of the investigational nature of this study.
  • Patients must have a life expectancy of \>8 weeks.
  • Patients must have a KPS rating of ≥70 at the baseline visit (Visit 3).
  • Primary therapy must consist of surgical resection with the intent for a gross or near total resection of the contrast-enhancing tumor mass, followed by conventional external beam radiation therapy and concurrent Temodar chemotherapy. Patients having a biopsy only will be excluded. These primary treatments must be completed at least two weeks prior to first immunization.
  • Patients may have received steroid therapy as part of their primary treatment. Steroid treatment must be stopped at least 10 days prior to leukapheresis.
  • Patients must not have progressive disease at completion of radiation therapy. Patients with suspected pseudoprogression will be enrolled and analyzed separately.
  • Patients must be willing to forego cytotoxic anti-tumor therapies except temozolomide essentially according to the schedule of the Stupp Protocol (Stupp et al. N Engl J Med 352: 987-96, 2005) while being treated with DCVax-L. DCVax-L treatment must be given as described and temozolomide/Temodar treatment schedules must be given essentially according to the Stupp Protocol.
  • Patients must have adequate bone marrow function (e.g., hemoglobin \>10 g/dl, white blood count 3600-11,000mm3, absolute granulocyte count ≥1,500/mm3, absolute lymphocyte count ≥1,000/mm3, and platelet count ≥100K/mm3. Eligibility level of hemoglobin can be reached by transfusion.
  • Adequate liver function (SGPT, SGOT, and alkaline phosphatase ≤1.5 times upper limits of normals (ULN) and total bilirubin ≤1.5mg/dl), and adequate renal function (BUN or creatinine ≤1.5 times ULN) prior to starting therapy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (86)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

Sutter East Bay Neuroscience Institute-Eden Medical Center

Castro Valley, California, 94546, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

UCSD Moores Cancer Center

La Jolla, California, 93093, United States

Location

Kaiser Permanente - Los Angeles

Los Angeles, California, 90027, United States

Location

UCLA Medical Center

Los Angeles, California, 90095, United States

Location

Hoag Memorial Hospital Presbyterian

Newport Beach, California, 92663, United States

Location

St. Joseph Hospital of Orange

Orange, California, 92868, United States

Location

University of California, Irvine Medical Center

Orange, California, 92868, United States

Location

Kaiser Permanente - Redwood City

Redwood City, California, 94063, United States

Location

Sutter Institute for Medical Research

Sacramento, California, 95816, United States

Location

University of Colorado Cancer Center

Aurora, Colorado, 80045, United States

Location

Colorado Neurological Institute

Englewood, Colorado, 80113, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20057, United States

Location

University of Florida

Gainesville, Florida, 32611, United States

Location

Memorial Cancer Institute

Hollywood, Florida, 33021, United States

Location

Mount Sinai Community Clinical Oncology Program

Miami Beach, Florida, 33140, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Piedmont Atlanta Hospital

Atlanta, Georgia, 30309, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Illinois Cancer Care

Peoria, Illinois, 61615, United States

Location

Cadence Cancer Center

Warrenville, Illinois, 60555, United States

Location

IU Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

University of Kansas Cancer Center

Westwood, Kansas, 66205, United States

Location

Markey Cancer Center/University of Kentucky

Lexington, Kentucky, 40536, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

University of Michigan Cancer Center

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Spectrum Health

Grand Rapids, Michigan, 49503, United States

Location

John Nasseff Neuroscience Institute at Abbott Northwestern Hospital

Minneapolis, Minnesota, 55407, United States

Location

St. Luke's Hospital

Kansas City, Missouri, 64111, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

The Brain Tumor Center at JFK Medical Center

Edison, New Jersey, 08818, United States

Location

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

The Valley Hospital

Ridgewood, New Jersey, 07450, United States

Location

Overlook Hospital

Summit, New Jersey, 07902, United States

Location

Capital Health Regional Medical Center

Trenton, New Jersey, 08638, United States

Location

Long Island Brain Tumor Center at Neurological Surgery, P.C.

Lake Success, New York, 11042, United States

Location

North Shore University Hospital

Manhasset, New York, 11030, United States

Location

New York University Clinical Cancer Center

New York, New York, 10016, United States

Location

Mount Sinai Medical Center

New York, New York, 10029-6574, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

Stony Brook Medicine

Stony Brook, New York, 11794, United States

Location

Brain and Spine Surgeons of New York and Northern Westchester Hospital

White Plains, New York, 10604, United States

Location

University of North Carolina, Chapel Hill

Chapel Hill, North Carolina, 27514, United States

Location

Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, 27157, United States

Location

University of Cincinnati Cancer Institute

Cincinnati, Ohio, 45267, United States

Location

University Hospitals Seidman Cancer Center

Cleveland, Ohio, 44106, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

OhioHealth

Columbus, Ohio, 43214, United States

Location

Oklahoma University Health Science Center

Oklahoma City, Oklahoma, 73104, United States

Location

Geisinger Medical Center

Danville, Pennsylvania, 17822, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Jefferson Hospital for Neuroscience

Philadelphia, Pennsylvania, 19107, United States

Location

Temple University School of Medicine

Philadelphia, Pennsylvania, 19140, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Medical University of South Carolina Hospitals and Clinics

Charleston, South Carolina, 29425, United States

Location

Saint Thomas Research Institute

Nashville, Tennessee, 37205, United States

Location

Vanderbilt Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Baylor Research Institute

Dallas, Texas, 75246, United States

Location

The Methodist Hospital

Houston, Texas, 77030, United States

Location

University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

Cancer Therapy & Research at University of Texas Health Science Center San Antonio

San Antonio, Texas, 78229, United States

Location

Benaroya Research Institute at Virginia Mason

Seattle, Washington, 98101, United States

Location

Swedish Hospital Neuroscience Research

Seattle, Washington, 98122, United States

Location

Aurora Saint Luke's Medical Center

Milwaukee, Wisconsin, 23215, United States

Location

Montreal Neurological Institute, McGill University

Montreal, Quebec, H3A 2B4, Canada

Location

CHUS - Hôpital Fleurimont

Sherbrooke, Quebec, J1H 5N4, Canada

Location

Universitätsklinikum Heidelberg Neurochirurgische Klinik

Heidelberg, Baden-Wurttemberg, 69120, Germany

Location

Katharinenhospital

Stuttgart, Baden-Wurttemberg, 70174, Germany

Location

Universitätsklinikum FrankfurtKlinik und Poliklinik für Neurochirurgie

Frankfurt am Main, Hesse, 60528, Germany

Location

Universitätsklinikum Bonn Nervenklinik (Zentrum), Klinik und Poliklinik für Neurochirurgie

Bonn, North Rhine-Westphalia, 53105, Germany

Location

Universitätsklinikum Klinik für allgemeine Neurochirurgie

Cologne, North Rhine-Westphalia, 50924, Germany

Location

Klinik für Neurochirurgie, Klinikum Chemnitz gGmbH

Chemnitz, Saxony, 09116, Germany

Location

Universitätsklinikum Carl Gustav Carus an der Technischen Universität Dresden

Dresden, Saxony, 01307, Germany

Location

BG-Kliniken Bergmannstrost, Klinik für Neurochirurgie

Halle, Saxony-Anhalt, 06112, Germany

Location

Neurochirurgische Klinik

Hamburg, 20246, Germany

Location

Addenbrookes NHS Trust

Cambridge, Cambridgeshire, East Anglia, CB2 2QQ, United Kingdom

Location

Kings College Hosital NHS Foundation Trust

London, Greater London, SE5 9RS, United Kingdom

Location

University College Hospital London

London, Greater London, WC1E 6BT, United Kingdom

Location

University Hospital of Birmingham NHS Foundation Trust

Birmingham, West Midlands, N15 2WB, United Kingdom

Location

Related Publications (3)

  • Liau LM, Ashkan K, Brem S, Campian JL, Trusheim JE, Iwamoto FM, Tran DD, Ansstas G, Cobbs CS, Heth JA, Salacz ME, D'Andre S, Aiken RD, Moshel YA, Nam JY, Pillainayagam CP, Wagner SA, Walter KA, Chaudhary R, Goldlust SA, Lee IY, Bota DA, Elinzano H, Grewal J, Lillehei K, Mikkelsen T, Walbert T, Abram S, Brenner AJ, Ewend MG, Khagi S, Lovick DS, Portnow J, Kim L, Loudon WG, Martinez NL, Thompson RC, Avigan DE, Fink KL, Geoffroy FJ, Giglio P, Gligich O, Krex D, Lindhorst SM, Lutzky J, Meisel HJ, Nadji-Ohl M, Sanchin L, Sloan A, Taylor LP, Wu JK, Dunbar EM, Etame AB, Kesari S, Mathieu D, Piccioni DE, Baskin DS, Lacroix M, May SA, New PZ, Pluard TJ, Toms SA, Tse V, Peak S, Villano JL, Battiste JD, Mulholland PJ, Pearlman ML, Petrecca K, Schulder M, Prins RM, Boynton AL, Bosch ML. Association of Autologous Tumor Lysate-Loaded Dendritic Cell Vaccination With Extension of Survival Among Patients With Newly Diagnosed and Recurrent Glioblastoma: A Phase 3 Prospective Externally Controlled Cohort Trial. JAMA Oncol. 2023 Jan 1;9(1):112-121. doi: 10.1001/jamaoncol.2022.5370.

  • Liau LM, Ashkan K, Tran DD, Campian JL, Trusheim JE, Cobbs CS, Heth JA, Salacz M, Taylor S, D'Andre SD, Iwamoto FM, Dropcho EJ, Moshel YA, Walter KA, Pillainayagam CP, Aiken R, Chaudhary R, Goldlust SA, Bota DA, Duic P, Grewal J, Elinzano H, Toms SA, Lillehei KO, Mikkelsen T, Walbert T, Abram SR, Brenner AJ, Brem S, Ewend MG, Khagi S, Portnow J, Kim LJ, Loudon WG, Thompson RC, Avigan DE, Fink KL, Geoffroy FJ, Lindhorst S, Lutzky J, Sloan AE, Schackert G, Krex D, Meisel HJ, Wu J, Davis RP, Duma C, Etame AB, Mathieu D, Kesari S, Piccioni D, Westphal M, Baskin DS, New PZ, Lacroix M, May SA, Pluard TJ, Tse V, Green RM, Villano JL, Pearlman M, Petrecca K, Schulder M, Taylor LP, Maida AE, Prins RM, Cloughesy TF, Mulholland P, Bosch ML. First results on survival from a large Phase 3 clinical trial of an autologous dendritic cell vaccine in newly diagnosed glioblastoma. J Transl Med. 2018 May 29;16(1):142. doi: 10.1186/s12967-018-1507-6.

  • Badhiwala J, Decker WK, Berens ME, Bhardwaj RD. Clinical trials in cellular immunotherapy for brain/CNS tumors. Expert Rev Neurother. 2013 Apr;13(4):405-24. doi: 10.1586/ern.13.23.

Related Links

MeSH Terms

Conditions

GlioblastomaGliomaBrain NeoplasmsNeoplasms

Condition Hierarchy (Ancestors)

AstrocytomaNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueCentral Nervous System NeoplasmsNervous System NeoplasmsNeoplasms by SiteBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Study Officials

  • Linda Liau, M.D.

    University of California, Los Angeles

    PRINCIPAL INVESTIGATOR
  • Marnix L. Bosch, MBA, PhD

    Northwest Biotherapeutics

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 17, 2002

First Posted

September 19, 2002

Study Start

December 1, 2006

Primary Completion

November 1, 2022

Last Updated

May 18, 2022

Record last verified: 2022-05

Locations