NCT06382948

Brief Summary

This trial will study a type of advanced breast cancer (ABC) defined as endocrine receptor (ER)-positive/human epidermal growth factor receptor 2(HER2)-negative and estrogen receptor 1 (ESR1)-mutated. Patients will be treated with elacestrant, a compound that acts as a selective estrogen receptor degrader, and everolimus (or placebo), a kinase inhibitor indicated for the treatment of postmenopausal women with advanced hormone receptor-positive, HER2-negative breast cancer. The main purpose of the study is to analyze the efficacy (to find out how effective a treatment is) of elacestrant plus everolimus therapy in patients who have ER-positive/HER2-negative, ESR1-mutated, ABC progressing to endocrine therapy and cyclin-dependent kinase 4/6 (CDK4/6) inhibitor. The efficacy of elacestrant plus everolimus combination will be determined by assessing the period from elacestrant plus everolimus (or placebo) treatment initiation until to the first occurrence of disease progression, unacceptable toxicity, death, or discontinuation from the study treatment for any other reason, whichever occurs first, defined as progression free survival. Rigorous eligibility criteria based on specific co-morbidities and clinicopathologic features of their disease have been designed to minimize the risk of patients participating in this study. The anticipated favorable clinical benefits of elacestrant combined with everolimus are projected to outweigh the risks of this treatment. This study will be performed in full compliance with International Council for Harmonisation of Technical Requirements for Pharmaceuticals for Human Use (ICH) and all applicable local Good Clinical Practice (GCP) and regulations.

Trial Health

83
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
240

participants targeted

Target at P50-P75 for phase_3

Timeline
23mo left

Started Dec 2024

Typical duration for phase_3

Geographic Reach
8 countries

69 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress43%
Dec 2024Apr 2028

First Submitted

Initial submission to the registry

April 5, 2024

Completed
19 days until next milestone

First Posted

Study publicly available on registry

April 24, 2024

Completed
8 months until next milestone

Study Start

First participant enrolled

December 5, 2024

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2027

Expected
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2028

Last Updated

March 12, 2026

Status Verified

December 1, 2025

Enrollment Period

2.7 years

First QC Date

April 5, 2024

Last Update Submit

March 11, 2026

Conditions

Keywords

ER-positiveHER22-negativeESR1-mutationCDK4/6-inhibitorSelective endocrine receptor degrader (SERD)

Outcome Measures

Primary Outcomes (1)

  • To demonstrate superiority of elacestrant+everolimus vs. elacestrant+placebo in prolonging PFS based on a BIRC in patients with ER[+]/HER2[-], ESR1-mutated, ABC that have previously received ET+CDK4/6i (all patients).

    Progression Free Survival (PFS), defined as the period from randomization to the first occurrence of disease progression or death from any cause, whichever occurs first, as assessed by a Blinded Imaging Review Committee (BIRC) through the use of RECIST v.1.1.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

Secondary Outcomes (17)

  • To compare overall survival (OS) between treatment groups, in all patients.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • To compare investigator-assessed PFS based on local assessment between treatment groups, in all patients.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • To compare objective response rate (ORR) between treatment groups, in all patients.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • To compare clinical benefit rate (CBR) between treatment groups, in all patients.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • To compare overall time to response (TTR) between treatment groups, in all patients.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • +12 more secondary outcomes

Other Outcomes (6)

  • Exploratory endpoint: protein expression studies using blood samples to investigate the potential association with clinical outcomes.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • Exploratory endpoint: analysis of allele mutation frequencies in circulating tumor DNA (ctDNA) in blood samples to investigate the potential association with clinical outcomes.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • Exploratory endpoint: Genetic studies using blood samples to investigate the potential association with clinical outcomes.

    Until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first, assessed through study completion, an average of 12 months.

  • +3 more other outcomes

Study Arms (2)

Interventional Arm 1

EXPERIMENTAL

Patients will receive 345 mg of elacestrant and 7.5 mg of everolimus orally once daily. Patients will remain in treatment until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first.

Drug: EverolimusDrug: ElacestrantDrug: Auxiliary Medicinal Product - DexamethasoneDrug: Auxiliary Medicinal Product - Luteinizing hormone-releasing hormone (LHRH) analogues

Control Arm 2

ACTIVE COMPARATOR

Patients will receive elacestrant at (345 mg orally once daily) plus matched everolimus placebo. Patients will remain in treatment until disease progression, treatment discontinuation, the start of new anti-cancer treatment, withdrawal of consent, death, or EoS, whichever occurs first.

Drug: ElacestrantDrug: PlaceboDrug: Auxiliary Medicinal Product - DexamethasoneDrug: Auxiliary Medicinal Product - Luteinizing hormone-releasing hormone (LHRH) analogues

Interventions

According to clinical practice (for premenopausal/perimenopausal patients and male patients in both treatment arms). Used to suppress estrogen production.

Control Arm 2Interventional Arm 1

Patients will receive 7.5 mg of everolimus orally once daily.

Also known as: Zortress, Votubia, RAD001, Certican, Afinitor
Interventional Arm 1

Patients will receive elacestrant 345 mg orally once daily

Also known as: ER-306323, RAD1901, Selective estrogen receptor degrader/selective estrogen receptor modulator (SERD/SERM) RAD1901
Control Arm 2Interventional Arm 1

Patients will receive placebo orally once daily

Control Arm 2

10 mL of alcohol-free dexamethasone 0.5 mg per 5 mL mouthwashes (swish for 2 min and spit, four times daily for 8 weeks). After 8 weeks, dexamethasone mouthwash could be continued for up to eight additional weeks at the discretion of the clinician and patient. Used for prevention of treatment-induced stomatitis.

Control Arm 2Interventional Arm 1

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients will be included in the study only if they meet ALL of the following criteria:
  • Patient must be capable to understand the purpose of the study and have signed written informed consent form (ICF) prior to beginning specific protocol procedures.
  • Female or male patients ≥ 18 years of age at the time of signing ICF.
  • Pre- or perimenopausal women, who do not meet the criteria for post-menopausal status (defined in continuation) and men must be concurrently receiving a LHRH analogue for at least 28 days (if shorter, post-menopausal levels of serum estradiol/follicle-stimulating hormone \[FSH\] must be confirmed analytically) prior to study randomization and are planning to continue LHRH agonist treatment during the study.
  • Post-menopausal women as defined by any of the following criteria:
  • Age ≥ 60 years;
  • Age \< 60 years and cessation of regular menses for at least 12 consecutive months with no alternative pathological or physiological cause; and serum estradiol and/or FSH levels within the laboratory's reference range for post-menopausal females;
  • Documented bilateral surgical oophorectomy.
  • Histologically- or cytologically proven diagnosis of adenocarcinoma of the breast with evidence of either unresectable locally recurrent or metastatic disease confirmed by computerized tomography (CT) scan or magnetic resonance imaging (MRI) that is not amenable to resection with curative intent.
  • Documentation of ER\[+\] (≥10% positive stained cells) and HER2\[-\] (0-1+ by immunohistochemistry \[IHC\] or 2+ and negative by in situ hybridization \[ISH\] test) tumor according to the most recent American Society of Clinical Oncology (ASCO)/College of American Pathologists (CAP) guidelines as per local assessment. ER\[+\]/HER2\[-\] status should be confirmed in metastatic setting, with exception of patients with bone and lung only disease.
  • Patients with ESR1 mutational status will be determined before patient randomization using Guardant360 CDx (Guardant Health) test.
  • Radiological or objective evidence of disease progression on prior treatment with a CDK4/6 inhibitor in combination with endocrine therapy for advanced disease after at least 6 months of treatment. Patients receiving CDK4/6 inhibitor-based therapy in the adjuvant setting are also eligible provided that disease progression is confirmed after at least 12 months of treatment but no more than 12 months following CDK4/6 inhibitor treatment completion in this scenario.
  • Patients must have previously received at least one and no more than two lines of endocrine therapy for ABC. Progression during or within 12 months of adjuvant endocrine therapy is considered as a line of endocrine therapy for advanced disease.
  • No prior elacestrant or other investigational SERDs, proteolysis targeting chimera (PROTAC), complete estrogen receptor antagonist (CERAN), or novel SERM, and/or PI3K/AKT/mTOR inhibitors, including everolimus, for advanced disease are permitted.
  • Note: Fulvestrant is permitted if treatment was completed administered at least 28 days before randomization.
  • +8 more criteria

You may not qualify if:

  • Resolution of all acute toxic effects of prior anti-cancer therapy to grade ≤ 1 as determined by the National Cancer Institute (NCI)-Common Terminology Criteria for Adverse Events (CTCAE) v.5.0 (except for toxicities not considered a safety risk for the patient at Investigator's discretion).
  • Note: Patients with grade 2 alopecia are allowed.
  • Women of childbearing potential who are sexually active with a non-sterilized male partner must have a negative serum pregnancy test within 7 days before randomization. In addition, they agree to use one highly effective method of birth control 28 days prior to start of treatment until 120 days after the last dose of study treatments. Female patients must refrain from egg cell donation and breastfeeding during this same time period.
  • Male participants with a female partner of childbearing potential must be surgically sterile or using a highly effective method of contraception 28 days prior to treatment until 120 days after the last dose of study treatments to prevent pregnancy in a partner. Male participants must not donate or bank sperm during this same time period. Not engaging in heterosexual activity (sexual abstinence) for the duration of the study and 120 days after the last dose of study treatments is an acceptable practice if this is the preferred usual lifestyle of the participant.
  • ECOG performance status of 0-1.
  • Minimum life expectancy of ≥ 12 weeks at screening.
  • Any patient meeting ANY of the following criteria will be excluded from the study:
  • Inability to comply with study and follow-up procedures.
  • Formal contraindication to endocrine therapy defined as visceral crisis and/or rapidly or symptomatic progressive visceral disease.
  • Current participation in another therapeutic clinical trial.
  • Treatment with approved or investigational cancer therapy within 14 days prior to randomization except for fulvestrant that must be administered completed at least 28 days before randomization.
  • Known active uncontrolled or symptomatic central nervous system (CNS) metastases and/or leptomeningeal disease as indicated by clinical symptoms, cerebral edema, and/or progressive growth. Patients with a history of CNS metastases are eligible if they have been previously treated with local therapy, are clinically stable, and off anticonvulsants and steroids for at least 14 days before randomization.
  • Intact uterus with a history of endometrial intraepithelial neoplasia (atypical endometrial hyperplasia or higher-grade lesion).
  • Concurrent malignancy or malignancy within three years before randomization with the exception of carcinoma in situ of the cervix, non-melanoma skin carcinoma, or stage I uterine cancer. For other cancers considered to have a low risk of recurrence, discussion with the Medical Monitor is required.
  • Known allergy or hypersensitivity reaction to any investigational medicinal products (IMPs) or their incorporated substances.
  • +20 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (69)

Medizinische Universität Innsbruck

Innsbruck, Austria

RECRUITING

Ordensklinikum Linz Barmherzige Schwestern

Linz, Austria

RECRUITING

Ordination Priv.-Doz. Dr. Michael Hubalek

Schwaz, Austria

RECRUITING

Masaryk Memorial Cancer Institute

Brno, Czechia

RECRUITING

Multiscan Nemocnice Horovice

Hořovice, Czechia

RECRUITING

Tomas Bata Regional Hospital in Zlin

Zlín, Czechia

RECRUITING

Polyclinique Bordeaux Nord Aquitaine

Bordeau, France

RECRUITING

Centre Georges François Leclerc

Dijon, France

RECRUITING

CHU Lyon Sud

Lyon, France

RECRUITING

Hospital prive des Cotes d'Amor

Plérin, France

RECRUITING

CHU Saint Etienne

Saint-Priest-en-Jarez, France

RECRUITING

IUCT Oncopole

Toulouse, France

RECRUITING

Institute de Cancerologie de Lorraine - Nancy

Vandœuvre-lès-Nancy, France

RECRUITING

MVZ II der Niels Stensen Kliniken

Georgsmarienhütte, Germany

RECRUITING

Klinikum Worms - Frauenklinik

Worms, Germany

RECRUITING

University General Hospital Alexandroupoli

Alexandroupoli, Greece

RECRUITING

251 Air Force General Hospital

Athens, Greece

RECRUITING

Aretaeio Hospital

Athens, Greece

RECRUITING

Attikon University Hospital

Athens, Greece

RECRUITING

Metropolitan General Hospital 4th department

Athens, Greece

RECRUITING

University General Hospital of Heraklion

Heraklion, Greece

RECRUITING

University General Hospital of Larissa

Larissa, Greece

RECRUITING

Metropolitan Hospital Greece 1st department

Piraeus, Greece

RECRUITING

EU Interbalkan Medical Center

Thessaloniki, Greece

RECRUITING

Ospedali Riuniti Livorno

Livorno, Italy

RECRUITING

Instituto Europeo di Oncologia

Milan, Italy

RECRUITING

Azienda Ospedaliero- Universitaria Maggiore Della Carita

Novara, Italy

RECRUITING

Hospital Universitari Dexeus

Barcelona, Barcelona, Spain

RECRUITING

Centro Oncológico de Galicia

A Coruña, Spain

RECRUITING

Complejo Hospitalario Universitario de Santiago (CHUS)

A Coruña, Spain

RECRUITING

Hospital General Universitario Dr. Balmis (Alicante)

Alicante, Spain

RECRUITING

Hospital Universitario San Juan de Alicante

Alicante, Spain

RECRUITING

Institut Català d' Oncologia Badalona (ICO)

Badalona, Spain

RECRUITING

Hospital Clínic i Provincial de Barcelona

Barcelona, Spain

RECRUITING

Hospital del Mar

Barcelona, Spain

RECRUITING

Hospital Universitari Vall D'Hebron

Barcelona, Spain

RECRUITING

Hospital Universitario de Basurto

Bilbao, Spain

RECRUITING

Hospital Universitario de Burgos

Burgos, Spain

RECRUITING

Hospital Provincial de Castellón

Castellon, Spain

RECRUITING

Hospital San Pedro de Alcántara

Cáceres, Spain

RECRUITING

Hospital Universitario Clínico San Cecilio de Granada

Granada, Spain

RECRUITING

Complejo Hospitalario de Jaén

Jaén, Spain

RECRUITING

Hospital Universitario Insular de Gran Canaria

Las Palmas de Gran Canaria, Spain

RECRUITING

Hospital Universitario de León

León, Spain

RECRUITING

Hospital Universitario Arnau de Vilanova de Lleida

Lleida, Spain

RECRUITING

Hospital Beata María Ana

Madrid, Spain

RECRUITING

Hospital Universitario Doce de Octubre

Madrid, Spain

RECRUITING

Hospital Universitario La Paz

Madrid, Spain

RECRUITING

Hospital Universitario Puerta de Hierro Majadahonda

Madrid, Spain

RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, Spain

RECRUITING

Hospital Universitario Sanchinarro-START-CIOCC

Madrid, Spain

RECRUITING

MD Anderson Cancer Center Madrid

Madrid, Spain

RECRUITING

Hospital Clínico Universitario Virgen de la Arrixaca

Murcia, Spain

RECRUITING

Hospital Universitari Son Espases

Palma de Mallorca, Spain

RECRUITING

Hospitalario Universitario de Navarra

Pamplona, Spain

RECRUITING

Hospital Universitario de Canarias

Santa Cruz de Tenerife, Spain

RECRUITING

Hospital Quirónsalud Sagrado Corazón

Seville, Spain

RECRUITING

Hospital Universitario Virgen del Rocío

Seville, Spain

RECRUITING

Hospital Universitario Virgen Macarena

Seville, Spain

RECRUITING

Hospital Universitari Sant Joan de Reus

Tarragona, Spain

RECRUITING

Hospital Universitario Marqués de Valdecilla

Valdecilla, Spain

RECRUITING

Consorci Hospital General Universitari de València

Valencia, Spain

RECRUITING

Hospital Arnau de Vilanova de Valencia

Valencia, Spain

RECRUITING

Hospital Clínico Universitario de Valencia

Valencia, Spain

RECRUITING

Hospital Universitario La Ribera - Alzira

Valencia, Spain

RECRUITING

Hospital Clínico Universitario Lozano Blesa

Zaragoza, Spain

RECRUITING

Barts Health NHS Trust

London, United Kingdom

RECRUITING

Royal Cornwall Hospital NHS Trust

Truro, United Kingdom

RECRUITING

Genesis Cancer Care UK

Waterlooville, United Kingdom

RECRUITING

MeSH Terms

Interventions

EverolimuselacestrantRAD1901Selective Estrogen Receptor ModulatorsGonadotropin-Releasing Hormone

Intervention Hierarchy (Ancestors)

SirolimusMacrolidesLactonesOrganic ChemicalsEstrogen Receptor ModulatorsHormone AntagonistsHormones, Hormone Substitutes, and Hormone AntagonistsPhysiological Effects of DrugsPharmacologic ActionsChemical Actions and UsesPituitary Hormone-Releasing HormonesHypothalamic HormonesPeptide HormonesHormonesNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteins

Study Officials

  • Javier Cortés, M.D., Ph.D.

    IOB Institute of Oncology, Quironsalud Group, Madrid & Barcelona, Spain

    PRINCIPAL INVESTIGATOR
  • Antonio Llombart-Cussac, M.D., Ph.D.

    Arnau de Vilanova Hospital, Valencia, Spain

    PRINCIPAL INVESTIGATOR
  • José Pérez-García, M.D., Ph.D.

    International Breast Cancer Center, Barcelona, Spain

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
A blinded, independent IRC will perform a review of radiographic images and clinical information collected on study to determine the protocol-defined endpoints of disease response and progression. Further information on the independent review process will be provided in the BIRC Charter.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Double-blind, parallel group (two arms: elacestrant plus everolimus, and elacestrant plus placebo).
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 5, 2024

First Posted

April 24, 2024

Study Start

December 5, 2024

Primary Completion (Estimated)

September 1, 2027

Study Completion (Estimated)

April 1, 2028

Last Updated

March 12, 2026

Record last verified: 2025-12

Locations