NCT06302426

Brief Summary

Phase 1 open-label, dose-escalation and dose-expansion study of INI-4001 as a single agent and in combination with approved checkpoint inhibitors in subjects with advanced solid tumors.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P50-P75 for phase_1

Timeline
10mo left

Started Jul 2024

Typical duration for phase_1

Geographic Reach
1 country

3 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress67%
Jul 2024Mar 2027

First Submitted

Initial submission to the registry

January 16, 2024

Completed
2 months until next milestone

First Posted

Study publicly available on registry

March 8, 2024

Completed
4 months until next milestone

Study Start

First participant enrolled

July 1, 2024

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 30, 2026

Expected
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 30, 2027

Last Updated

January 16, 2026

Status Verified

May 1, 2025

Enrollment Period

2.3 years

First QC Date

January 16, 2024

Last Update Submit

January 15, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence of dose-limiting toxicities (DLTs) during Cycle 1 to determine the maximum tolerated dose of INI-4001 Monotherapy

    Graded using a 5 point scale

    Assessed from Cycle 1 Day 1 through to Cycle 1 Day 21

Secondary Outcomes (31)

  • Incidence, type, and severity of treatment-emergent adverse events (TEAEs) leading to discontinuation of study treatment after multiple ascending doses

    Assessed at Screening, then daily from Cycle 1 Day 1 through to 30 days post last dose of INI-4001

  • Incidence and nature of dose-limiting toxicities (DLTs) and regimen-limiting toxicities (RLTs) leading to discontinuation of study treatment after multiple ascending doses

    Assessed from Cycle 1 Day 1 through to Cycle 1 Day 21

  • Number of Participants with a Change from baseline in Vital signs measurements after multiple ascending doses

    Assessed at Screening, then Cycle 1 Day 1 through to 30 days post last dose of INI-4001

  • Number of Participants with a Change from baseline in body weight after multiple ascending doses

    Assessed at Screening then pre-dose on Day 1 of each 21 day cycle, assessed for up to 36 months or until disease progression, which occurs first

  • Number of Participants with a Change from baseline in clinical laboratory parameters (haematology) after multiple ascending doses

    Assessed at Screening, then Day 1 and Day 15 of each 21 day cycle, assessed for up to 36 months or until disease progression, which occurs first

  • +26 more secondary outcomes

Study Arms (6)

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1

EXPERIMENTAL

For dose-level 1, INI-4001 will be administered intravenously once per week on Days 1, 8 and 15 of a 21-day cycle. A complementary therapy may be introduced in combination with INI-4001.

Drug: INI-4001Combination Product: NivolumabCombination Product: PembrolizumabCombination Product: CemiplimabCombination Product: AvelumabCombination Product: AtezolizumabCombination Product: Durvalumab

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2

EXPERIMENTAL

For dose-level 2, INI-4001 will be administered intravenously once per week on Days 1, 8 and 15 of a 21-day cycle. A complementary therapy may be introduced in combination with INI-4001.

Drug: INI-4001Combination Product: NivolumabCombination Product: PembrolizumabCombination Product: CemiplimabCombination Product: AvelumabCombination Product: AtezolizumabCombination Product: Durvalumab

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3

EXPERIMENTAL

For dose-level 3, INI-4001 will be administered intravenously once per week on Days 1, 8 and 15 of a 21-day cycle. A complementary therapy may be introduced in combination with INI-4001.

Drug: INI-4001Combination Product: NivolumabCombination Product: PembrolizumabCombination Product: CemiplimabCombination Product: AvelumabCombination Product: AtezolizumabCombination Product: Durvalumab

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4

EXPERIMENTAL

For dose-level 4, INI-4001 will be administered intravenously once per week on Days 1, 8 and 15 of a 21-day cycle. A complementary therapy may be introduced in combination with INI-4001.

Drug: INI-4001Combination Product: NivolumabCombination Product: PembrolizumabCombination Product: CemiplimabCombination Product: AvelumabCombination Product: AtezolizumabCombination Product: Durvalumab

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5

EXPERIMENTAL

For dose-level 5, INI-4001 will be administered intravenously once per week on Days 1, 8 and 15 of a 21-day cycle. A complementary therapy may be introduced in combination with INI-4001.

Drug: INI-4001Combination Product: NivolumabCombination Product: PembrolizumabCombination Product: CemiplimabCombination Product: AvelumabCombination Product: AtezolizumabCombination Product: Durvalumab

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6

EXPERIMENTAL

For dose-level 6, INI-4001 will be administered intravenously once per week on Days 1, 8 and 15 of a 21-day cycle. A complementary therapy may be introduced in combination with INI-4001.

Drug: INI-4001Combination Product: NivolumabCombination Product: PembrolizumabCombination Product: CemiplimabCombination Product: AvelumabCombination Product: AtezolizumabCombination Product: Durvalumab

Interventions

INI-4001 is a small molecule TLR7/8 agonist being developed as a standalone treatment for the induction of anti-tumour immune responses and sensitization to immune checkpoint inhibitor (ICI) therapy.

INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6
NivolumabCOMBINATION_PRODUCT

During both Phase Ia and Phase Ib, patients may meeting required criteria (at the discretion of the PI in consultation with the study Sponsor) may transition to combination therapy.

Also known as: Opdivo
INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6
PembrolizumabCOMBINATION_PRODUCT

During both Phase Ia and Phase Ib, patients meeting required criteria (at the discretion of the PI in consultation with the study Sponsor) transition to combination therapy.

Also known as: Keytruda
INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6
CemiplimabCOMBINATION_PRODUCT

During both Phase Ia and Phase Ib, patients meeting required criteria (at the discretion of the PI in consultation with the study Sponsor) transition to combination therapy.

Also known as: Libtayo
INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6
AvelumabCOMBINATION_PRODUCT

During both Phase Ia and Phase Ib, patients meeting required criteria (at the discretion of the PI in consultation with the study Sponsor) transition to combination therapy.

Also known as: Bavencio
INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6
AtezolizumabCOMBINATION_PRODUCT

During both Phase Ia and Phase Ib, patients meeting required criteria (at the discretion of the PI in consultation with the study Sponsor) transition to combination therapy.

Also known as: Tecentriq
INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6
DurvalumabCOMBINATION_PRODUCT

During both Phase Ia and Phase Ib, patients meeting required criteria (at the discretion of the PI in consultation with the study Sponsor) transition to combination therapy.

Also known as: Imfinzi
INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 1INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 2INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 3INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 4INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 5INI-4001 Monotherapy Dose Escalation - INI-4001 Dose Level 6

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient has locally advanced or metastatic cancer (all solid tumours allowed except primary brain/CNS tumour or untreated spinal cord compression)
  • Patient has at least one extracranial measurable disease lesion per RECIST 1.1/ iRECIST criteria.
  • Patients with known brain metastases are eligible if they meet all the following criteria:
  • Patient has received definitive treatment of brain metastases with stereotactic body radiation therapy (SBRT) or surgery provided that the brain lesions are stable (without evidence of progression by imaging for at least 4 weeks before the first dose of study treatment)
  • Patient is neurologically stable and has had no persistent side effects / complications from prior treatment.
  • Patient has no evidence of new or enlarging brain metastases (confirmed by repeat imaging) and has not required steroids for at least 14 days prior to first dose administration on Day 1.
  • Female patients must be of non-child-bearing potential i.e., surgically sterilised at least 6 weeks before the screening visit or postmenopausal

You may not qualify if:

  • Prior therapy with a TLR7 and/or TLR8 agonist, unless first approved by the medical monitor.
  • Has primary brain/CNS tumour or untreated spinal cord compression.
  • Has known active, uncontrolled brain or CNS metastases and/or carcinomatous meningitis.
  • Evidence of abnormal cardiac function
  • Clinically significant active infection within 2 weeks prior to commencement of treatment, or unexplained fever (temperature \> 38.1°C) within 7 days prior to first dose administration on Cycle 1 Day 1.
  • Known active human immunodeficiency virus (HIV-1 or HIV-2), hepatitis B surface antigen (HBsAg) or hepatitis C virus (HCV) antibodies at the screening visit.
  • Major surgery within 28 days of Cycle 1, Day 1, or minor surgical procedures within 7 days of Cycle 1, Day 1.
  • Received cancer-directed therapy
  • A history of autoimmune diseases that has caused terminal organ damage or required systemic immunosuppression / systemic disease modulating drugs within the past 2 years.
  • Chronic use of immune-suppressive drugs (i.e., systemic corticosteroids used in the management of cancer or non-cancer related illnesses, (e.g., COPD) in dosing exceeding 10 mg daily of prednisone equivalent). Inhaled steroids are allowed.
  • History of prior organ allograft.
  • Known hypersensitivity to the study drug or its inactive ingredients.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

The Border Cancer Hospital

Albury, New South Wales, 2640, Australia

RECRUITING

Southern Oncology Clinical Research Unit

Bedford Park, South Australia, 5042, Australia

RECRUITING

Cabrini Hospital

Malvern, Victoria, 3144, Australia

RECRUITING

MeSH Terms

Interventions

Nivolumabpembrolizumabcemiplimabavelumabatezolizumabdurvalumab

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Jon L Ruckle

    Inimmune Corp

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Model Details: This is a Phase Ia/Ib, open-label, dose-escalation and dose expansion study. This study will be conducted in two parts: Phase Ia (dose escalation) and Phase Ib (dose expansion).
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 16, 2024

First Posted

March 8, 2024

Study Start

July 1, 2024

Primary Completion (Estimated)

October 30, 2026

Study Completion (Estimated)

March 30, 2027

Last Updated

January 16, 2026

Record last verified: 2025-05

Data Sharing

IPD Sharing
Will not share

Locations