NCT04916002

Brief Summary

The goal of this study is to learn if giving cemiplimab and vidutolimod together could be effective in treating advanced cancer. The main questions it aims to answer are:

  • How many participants' cancers respond to vidutolimod together with cemiplimab?
  • Is vidutolimod together with cemiplimab safe and well-tolerated?
  • How well does vidutolimod together with cemiplimab treat participants' cancer? Participants will receive trial treatment for up to 2 years. 30 days after stopping treatment, participants will have a follow-up visit. After that visit, the trial staff will continue to follow up with participants about every 3 months, until the trial ends.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
77

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Nov 2021

Typical duration for phase_2

Geographic Reach
2 countries

24 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 1, 2021

Completed
6 days until next milestone

First Posted

Study publicly available on registry

June 7, 2021

Completed
6 months until next milestone

Study Start

First participant enrolled

November 30, 2021

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 31, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 31, 2024

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

December 5, 2025

Completed
Last Updated

December 5, 2025

Status Verified

November 1, 2025

Enrollment Period

2.9 years

First QC Date

June 1, 2021

Results QC Date

October 30, 2025

Last Update Submit

November 20, 2025

Conditions

Keywords

vidutolimodMetastatic CancerAdvanced CancerMCCCSCCBCCTNBCNSCLCOPSCC

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR)

    ORR is defined as the Percent of participants with a confirmed objective response of complete response (CR) or partial response (PR) based on Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST v1.1) by investigator assessment

    Up to 31.5 Months

Secondary Outcomes (5)

  • Number of Participants With Any Treatment-emergent Adverse Event (TEAE), Any Serious TEAE, and Any TEAE Leading to Discontinuation or Death

    Up to 31.5 months

  • Severity of TEAEs as Assessed by the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE)

    Up to 31.5 months

  • Duration of Response (DOR)

    Up to 31.5 months

  • Progression Free Survival (PFS)

    Up to 31.5 months

  • Overall Survival (OS)

    Up to 31.5 months

Study Arms (9)

Vidutolimod and cemiplimab for cutaneous squamous cell carcinoma (CSCC) (A1)

EXPERIMENTAL

Participants who have not received prior systemic therapy for metastatic or locally and/or regionally advanced unresectable CSCC and who are not eligible for curative radiation will receive vidutolimod intratumoral(ly) (IT) and cemiplimab intravenous (IV) according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for CSCC (A2)

EXPERIMENTAL

Participants who have progressed while receiving a programmed cell death protein 1 (PD-1)-blocking antibody or within 12 weeks of discontinuation of PD-1 blocking antibody for metastatic or locally and/or regionally advanced unresectable CSCC, will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for Merkel cell carcinoma (MCC) (B1)

EXPERIMENTAL

Participants who have not received prior systemic therapy for metastatic or locally and/or regionally advanced unresectable MCC will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for MCC (B2)

EXPERIMENTAL

Participants who have progressed while receiving a PD-1-blocking antibody or within 12 weeks of discontinuation of the PD-1 blocking antibody, will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for triple negative breast cancer (TNBC) (C1)

EXPERIMENTAL

Participants who have not received prior therapy with immune checkpoint inhibitors (iCPIs) and who must have previously received treatment with sacituzumab govitecan (all advanced or metastatic TNBC participants), with trastuzumab deruxtecan \[human epidermal growth factor receptor 2 (HER2)-low participants\] and with adenosine diphosphate ribose polymerase (PARP) inhibitor \[for BReast CAncer gene (BRCA)\] for TNBC will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for TNBC (C2)

EXPERIMENTAL

Participants who have previously received treatment with sacituzumab govitecan (all advanced or metastatic TNBC participants), with trastuzumab deruxtecan (HER2-low participants) and with PARP inhibitor (for BRCA) and who have progressed while receiving a PD-1-blocking antibody or within 12 weeks of discontinuation of a PD-1 blocking antibody for advanced or metastatic TNBC, will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for basal cell carcinoma (BCC) (D)

EXPERIMENTAL

Participants who have not received prior hedgehog pathway inhibitor therapy, or prior anti-PD-1/programmed cell death ligand 1 (PD-L1) therapy and who do not wish to receive or who are not candidates for a hedgehog inhibitor, for metastatic or locally and/or regionally advanced unresectable BCC and will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for non-small cell lung cancer (NSCLC) (E)

EXPERIMENTAL

Participants with advanced NSCLC (locally advanced who are not candidates for surgical resection or definitive chemoradiation or metastatic) whose tumors have high PD-L1 expression \[tumor proportion score (TPS) ≥50%\] based on a prior PD-L1 result as determined by College of American Pathologists (CAP)/Clinical Laboratory Improvement Amendments (CLIA) (or equivalently licensed) lab, with no epidermal growth factor receptor (EGFR), anaplastic lymphoma kinase (ALK) or ros oncogene 1 (ROS1) aberrations, and who have not received prior anti-PD-1/PD-L1 therapy and are amenable to IT therapy and do not wish to receive chemotherapy. Note: this cohort is not conducted in Europe

Drug: vidutolimodDrug: cemiplimab

Vidutolimod and cemiplimab for recurrent/metastatic Oropharynx Squamous Cell Carcinoma (OPSCC) (F)

EXPERIMENTAL

Participants with PD-L1 combined positive score (CPS) ≥ 1, based on a prior PD-L1 result and human papillomavirus (HPV)-positive disease based on a prior result, who have not received prior systemic therapy for recurrent/metastatic disease. Participants will receive vidutolimod IT and cemiplimab IV according to the treatment schedule until a reason for treatment discontinuation is reached.

Drug: vidutolimodDrug: cemiplimab

Interventions

Participants will receive cemiplimab for up to 2 years as follows: 350 mg IV infusion over 30 minutes at week 1 dose 1 (W1D1) and Q3W thereafter.

Also known as: Libtayo, REGN2810
Vidutolimod and cemiplimab for CSCC (A2)Vidutolimod and cemiplimab for MCC (B2)Vidutolimod and cemiplimab for Merkel cell carcinoma (MCC) (B1)Vidutolimod and cemiplimab for TNBC (C2)Vidutolimod and cemiplimab for basal cell carcinoma (BCC) (D)Vidutolimod and cemiplimab for cutaneous squamous cell carcinoma (CSCC) (A1)Vidutolimod and cemiplimab for non-small cell lung cancer (NSCLC) (E)Vidutolimod and cemiplimab for recurrent/metastatic Oropharynx Squamous Cell Carcinoma (OPSCC) (F)Vidutolimod and cemiplimab for triple negative breast cancer (TNBC) (C1)

Participants will receive vidutolimod for up to 2 years as follows: 10 mg IT weekly for 7 doses after which vidutolimod will be administered every 3 weeks (Q3W). The first dose of vidutolimod may be administered subcutaneously (SC) or IT at the discretion of Investigator. All subsequent doses will be IT. The initial 7 doses of vidutolimod, delivered on a weekly dosing schedule, must be completed before starting the Q3W vidutolimod dosing schedule.

Also known as: CMP-001
Vidutolimod and cemiplimab for CSCC (A2)Vidutolimod and cemiplimab for MCC (B2)Vidutolimod and cemiplimab for Merkel cell carcinoma (MCC) (B1)Vidutolimod and cemiplimab for TNBC (C2)Vidutolimod and cemiplimab for basal cell carcinoma (BCC) (D)Vidutolimod and cemiplimab for cutaneous squamous cell carcinoma (CSCC) (A1)Vidutolimod and cemiplimab for non-small cell lung cancer (NSCLC) (E)Vidutolimod and cemiplimab for recurrent/metastatic Oropharynx Squamous Cell Carcinoma (OPSCC) (F)Vidutolimod and cemiplimab for triple negative breast cancer (TNBC) (C1)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histopathologically-confirmed diagnosis of cancer, as defined by the protocol.
  • Measurable disease, as defined by RECIST v1.1 and as defined in the protocol. Note: CSCC, MCC and BCC subjects without radiographically measurable disease are not excluded if there is at least 1 lesion ≥ 10 mm in at east 1 dimension documented by color photography.
  • Adequate organ function based on most recent laboratory values within 3 weeks before first dose of study treatment on Week 1 Day 1 (W1D1), as defined in the protocol.
  • Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 to 1 at Screening.

You may not qualify if:

  • Participants presenting with any of the following will not qualify for entry into the study:
  • Received radiation therapy (or other non-systemic therapy) within 2 weeks before first dose of study treatment on W1D1. Participants should have recovered (i.e. Grade ≤ 1 or at baseline) from radiation-related toxicities.
  • Had major surgeries (including complete oncologic resection) within last 4 weeks prior to enrollment, and/or have not recovered adequately from the toxicities and/or complications from the intervention. Minor surgeries (including routine resections of early stage CSCCs and BCCs that may be due to field cancerization) require a 7-day washout.
  • Received systemic pharmacologic doses of corticosteroids \> 10 mg/day prednisone within 15 days before first dose of study treatment on W1D1, as defined in the protocol.
  • History of immune-mediated AE leading to permanent discontinuation due to prior PD-1-blocking antibody.
  • Not fully recovered from AEs due to prior treatment (to Grade 1 or less, per Common Terminology Criteria for Adverse Events (CTCAE), with the exception of persistent vitiligo, alopecia, hypothyroidism, diabetes mellitus, and adrenal and/or pituitary insufficiency.
  • Active pneumonitis or history of noninfectious pneumonitis that required steroids.
  • Severe uncontrolled medical disease within 12 months of screening, including but not limited to poorly controlled hypertension, unstable angina, myocardial infarction, congestive heart failure (New York Heart Association Class II or greater), pericarditis, cerebrovascular accident, or implanted or continuous use of a pacemaker or defibrillator, or emphysema with FEV1 ≤ 50% predicted.
  • Known history of immunodeficiency.
  • Known additional malignancy that is progressing or required active treatment within the past 3 years, as defined in the protocol.
  • Active autoimmune disease that required systemic treatment in past 2 years; replacement therapy is not considered a form of systemic treatment.
  • Untreated, symptomatic, or enlarging central nervous system metastases or carcinomatous meningitis (including leptomeningeal metastases from solid tumors).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

University of Alabama

Birmingham, Alabama, 35294, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

UC San Diego Moores Cancer Center

La Jolla, California, 92037-0845, United States

Location

University of California

Los Angeles, California, 90095, United States

Location

GenesisCare USA

Jacksonville, Florida, 32204, United States

Location

Orlando Health Cancer Institute

Orlando, Florida, 32806, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

VA Maryland Health Care System

Baltimore, Maryland, 20814, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Dartmouth Clinical Trial Office

Lebanon, New Hampshire, 03756, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

East Carolina University

Greenville, North Carolina, 27858, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

OU Health Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15232, United States

Location

Oncology Consultants

Houston, Texas, 77030, United States

Location

University of Utah Huntsman Cancer Center

Salt Lake City, Utah, 84112, United States

Location

University of Washington

Seattle, Washington, 98109, United States

Location

St. Vincent's Hospital

Darlinghurst, New South Wales, 2010, Australia

Location

Princess Alexandra Hospital

Woolloongabba, Queensland, 4102, Australia

Location

Peter MacCallum Cancer Centre (PMCC) and The Royal Melbourne Hospital

Melbourne, Victoria, 3050, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

MeSH Terms

Conditions

Carcinoma, Merkel CellCarcinoma, Basal CellTriple Negative Breast NeoplasmsCarcinoma, Non-Small-Cell LungSquamous Cell Carcinoma of Head and NeckNeoplasm Metastasis

Interventions

cemiplimab

Condition Hierarchy (Ancestors)

Polyomavirus InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsCarcinoma, NeuroendocrineNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueNeoplasms, Basal CellBreast NeoplasmsNeoplasms by SiteBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesCarcinoma, Squamous CellHead and Neck NeoplasmsNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Limitations and Caveats

Terminated early due to study drug supply. Enrolled 77 of 225 planned participants. Participants only enrolled in CSCC, MCC, \& BCC cohorts at time of diagnosis. Results descriptive in nature. No conclusions can be inferred from cohorts analyzed.

Results Point of Contact

Title
Clinical Trials Administrator
Organization
Regeneron Pharmaceuticals, Inc.

Study Officials

  • Clinical Trial Management

    Regeneron Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 1, 2021

First Posted

June 7, 2021

Study Start

November 30, 2021

Primary Completion

October 31, 2024

Study Completion

October 31, 2024

Last Updated

December 5, 2025

Results First Posted

December 5, 2025

Record last verified: 2025-11

Data Sharing

IPD Sharing
Will share

All Individual Patient Data (IPD) that underlie publicly available results will be considered for sharing

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR, ANALYTIC CODE
Time Frame
When Regeneron has received marketing authorization from major health authorities (e.g., FDA, European Medicines Agency (EMA), Pharmaceuticals and Medical Devices Agency (PMDA), etc.) for the product and indication, has made the study results publicly available (e.g., scientific publication, scientific conference, clinical trial registry), has the legal authority to share the data, and has ensured the ability to protect participant privacy.
Access Criteria
Qualified researchers can submit a proposal for access to individual patient or aggregate level data from a Regeneron-sponsored clinical trial through Vivli. Regeneron's Independent Research Request Evaluation Criteria can be found at: https://www.regeneron.com/sites/default/files/Regeneron-External-Data-Sharing-Policy-and-Independent-Research-Request-Evaluation-Criteria.pdf
More information

Locations