NCT04834349

Brief Summary

This phase II trial studies the effect of re-irradiation with NBTXR3 in combination with pembrolizumab in treating patients with head and neck squamous cell cancer that cannot be removed by surgery (inoperable) and has come back (recurrent). NBTXR3 is a drug that is designed to improve the effectiveness (how well something works) of radiation therapy. The drug is injected into a tumor and activated (turned on) by radiation. Stereotactic body radiation therapy uses special equipment to position a patient and deliver radiation to tumors with high precision. This method may kill tumor cells with fewer doses over a shorter period and cause less damage to normal tissue. Radiation therapy, such as intensity modulated radiation therapy or intensity modulated proton therapy, uses high energy to kill tumor cells and shrink tumors. Immunotherapy with monoclonal antibodies, such as pembrolizumab, may help the body's immune system attack the cancer, and may interfere with the ability of tumor cells to grow and spread. Giving NBTXR3 activated by radiation together with pembrolizumab may help to control head and neck squamous cell cancer.

Trial Health

15
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Mar 2021

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 5, 2021

Completed
4 days until next milestone

Study Start

First participant enrolled

March 9, 2021

Completed
1 month until next milestone

First Posted

Study publicly available on registry

April 8, 2021

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 21, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 21, 2022

Completed
Last Updated

September 13, 2023

Status Verified

September 1, 2023

Enrollment Period

1.7 years

First QC Date

March 5, 2021

Last Update Submit

September 11, 2023

Conditions

Outcome Measures

Primary Outcomes (5)

  • Progression free survival (PFS)

    Will be estimated using the method of Kaplan-Meier. Median times and 95% confidence intervals will also be estimated.

    From NBTXR3 injection to local or regional recurrence, local or regional progression, distant (outside the head and neck region) progression, or death from any cause, whichever occurs first, assessed up to 5 years

  • Early clinical benefit activated by SBRT reirradiation

    Defined as radiographic evidence of complete response (CR), partial response (PR) or stable disease (SD)

    At 6-months post radiation therapy (RT)

  • Incidence of acute adverse events activated by dose reduction IMRT or IMPT reirradiation

    Will assess treatment related acute and late onset toxicities defined as any grade \>= 3 adverse event (AE), excluding dermatitis and mucositis as per National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) version (v) 5.0.

    Up to 90 days post RT

  • Incidence of late adverse events activated by dose reduction IMRT or IMPT reirradiation

    Will assess treatment related acute and late onset toxicities defined as any grade \>= 3 AE, excluding dermatitis and mucositis as per NCI CTCAE v 5.0.

    From 90 days post RT to end of study (up to 5 years) From 90 days post RT to end of study (up to 5 years)

  • Incidence of late adverse events activated by SBRT reirradiation

    Will assess treatment related acute and late onset toxicities defined as any grade \>= 3 AE, excluding dermatitis and mucositis as per NCI CTCAE v 5.0.

    From 90 days post RT to end of study (up to 5 years)

Secondary Outcomes (7)

  • Objective response rate

    Up to 5 years post treatment

  • Overall response

    Up to 5 years post treatment

  • Incidence of acute adverse events activated by SBRT reirradiation

    Up to 90 days post RT

  • Local PFS

    From NBTXR3 injection to the radiographic and/or histological confirmation of local (within 2 cm of the high-dose reirradiation treatment volume [PTV]) disease recurrence, local progression, or death from any cause, assessed up to 5 years

  • Regional PFS

    From NBTXR3 injection to the radiographic and/or histological confirmation of regional disease recurrence, regional progression, or death from any cause, whichever occurs first, assessed up to 5 years

  • +2 more secondary outcomes

Other Outcomes (5)

  • Evaluation of the clinical-grading of lymphedema/fibrosis

    Up to 5 years post treatment

  • Evaluation of the clinical-grading of lymphedema/fibrosis

    Up to 5 years post treatment

  • Evaluation of the clinical-grading of lymphedema/fibrosis

    Up to 5 years post treatment

  • +2 more other outcomes

Study Arms (2)

Cohort I (NBTXR3, SBRT, pembrolizumab)

EXPERIMENTAL

Patients receive NBTXR3 IT on day 1. Patients then undergo SBRT QOD on days 15-29. Beginning the first day of radiation therapy, patients also receive pembrolizumab IV over 30 minutes on day 1. Cycles repeat every 3 weeks for up to 2 years in the absence of disease progression or unacceptable toxicity.

Other: Hafnium Oxide-containing Nanoparticles NBTXR3Biological: PembrolizumabOther: Quality-of-Life AssessmentOther: Questionnaire AdministrationRadiation: Stereotactic Body Radiation Therapy

Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)

EXPERIMENTAL

Patients receive NBTXR3 IT on day 1. Patients then undergo IMRT/IMPT QD on days 15-50. Beginning the first day of radiation therapy, patients also receive pembrolizumab IV over 30 minutes on day 1. Cycles repeat every 3 weeks for up to 2 years in the absence of disease progression or unacceptable toxicity.

Other: Hafnium Oxide-containing Nanoparticles NBTXR3Procedure: Intensity-Modulated Proton TherapyRadiation: Intensity-Modulated Radiation TherapyBiological: PembrolizumabOther: Quality-of-Life AssessmentOther: Questionnaire Administration

Interventions

Given IT

Also known as: NBTXR3
Cohort I (NBTXR3, SBRT, pembrolizumab)Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)

Undergo IMPT

Also known as: IMPT
Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)

Undergo IMRT

Also known as: IMRT, Intensity Modulated RT, Intensity-Modulated Radiotherapy, Radiation, Intensity-Modulated Radiotherapy
Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)
PembrolizumabBIOLOGICAL

Given IV

Also known as: Keytruda, Lambrolizumab, MK-3475, SCH 900475
Cohort I (NBTXR3, SBRT, pembrolizumab)Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)

Ancillary studies

Also known as: Quality of Life Assessment
Cohort I (NBTXR3, SBRT, pembrolizumab)Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)

Ancillary studies

Cohort I (NBTXR3, SBRT, pembrolizumab)Cohort II (NBTXR3, IMRT/IMPT, pembrolizumab)

Undergo SBRT

Also known as: SABR, SBRT, Stereotactic Ablative Body Radiation Therapy
Cohort I (NBTXR3, SBRT, pembrolizumab)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with biopsy proven locoregional recurrent squamous cell carcinoma of the head and neck, or second primary HNSCC
  • Previous documented receipt of at least 30 Gy and up to 70 Gy of radiation for HNSCC with overlapping fields based on actual dose, prescription percentage
  • Gy for conventional fractionation
  • Gy for hypofractionation
  • Gy for single fraction
  • Time interval from prior radiotherapy to NBTXR3 injection (day 1) of at least 6 months
  • Not eligible (unresectable) or poor candidate or patient refusal of surgery for HNSCC recurrence
  • Amenable to undergo the image guided intratumoral/intranodal injection of NBTXR3 by Interventional Radiologist or ear, nose, and throat (ENT) surgeon, as per investigator or treating physician
  • The target lesion(s) in the head and neck should be measurable as per Response Evaluation Criteria in Solid Tumors (RECIST) version (v)1.1 on cross sectional imaging and repeated measurements at the same anatomical location should be achievable
  • Up to 3 target lesions may be injected with NBTXR3 and radiated, including the primary tumor and involved lymph node(s)
  • SBRT cohort: =\< 60 cm\^3 per site, total volume =\< 120 cm\^3
  • IMRT/IMPT cohort: =\< 120 cm\^3 per site, total volume =\< 200 cm\^3
  • Nodal target lesions must be \>= 15mm (short axis) based on computed tomography (CT) (slice thickness of 5 mm or less) or magnetic resonance imaging (MRI)
  • Age \>= 18 years
  • Eastern Cooperative Oncology Group (ECOG) performance status 0-2
  • +11 more criteria

You may not qualify if:

  • Locoregional relapse with skin ulceration
  • Head and neck carcinoma with radiographic evidence of metastasis at screening
  • Surgery to the head and neck
  • Excluding diagnostic biopsy
  • History of severe immune-related adverse events observed with previous immunotherapy (anti-PD-1/L1) or known sensitivity (grade \>= 3) to any excipients
  • Has received any approved or investigational anti-neoplastic agent within 4 weeks prior to NBTXR3 injection
  • Except anti-PD-1 therapy, which will not require a washout window
  • Note: a reduced washout window may be considered for therapies with short half-lives (i.e., kinase inhibitors) after discussion with Nanobiotix and investigator
  • Active autoimmune disease that has required systemic treatment in the past 2 years (i.e., with use of disease-modifying agents, corticosteroids, or immunosuppressive drugs)
  • Replacement therapy (i.e., thyroxine, insulin, or physiologic corticosteroid replacement \[=\< 10 mg prednisone\] therapy for adrenal or pituitary insufficiency, etc.) is not considered a form of systemic treatment
  • Has not recovered from adverse events (AEs) due to previous anti-neoplastic or immune-oncology therapy and/or interventions (including radiation) to =\< grade 1
  • Participants with alopecia and =\< grade 2 neuropathy may be eligible
  • Any live-virus vaccine therapy used for prevention of infectious diseases administered within 4 weeks prior to NBTXR3 injection
  • Except killed-virus Influenza vaccine
  • Exception of other vaccines (e.g. pneumonia) is at the discretion of the treating physician after conducting a personalized risk assessment on a case by case basis
  • +9 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Related Links

MeSH Terms

Conditions

Squamous Cell Carcinoma of Head and Neck

Interventions

Radiotherapy, Intensity-ModulatedpembrolizumabRadiosurgery

Condition Hierarchy (Ancestors)

Carcinoma, Squamous CellCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsHead and Neck NeoplasmsNeoplasms by Site

Intervention Hierarchy (Ancestors)

Radiotherapy, ConformalRadiotherapy, Computer-AssistedRadiotherapyTherapeuticsStereotaxic TechniquesNeurosurgical ProceduresSurgical Procedures, OperativeInvestigative Techniques

Study Officials

  • Jack Phan, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 5, 2021

First Posted

April 8, 2021

Study Start

March 9, 2021

Primary Completion

November 21, 2022

Study Completion

November 21, 2022

Last Updated

September 13, 2023

Record last verified: 2023-09