NCT04579380

Brief Summary

This trial studies how well tucatinib works for solid tumors that make either more HER2 or a different type of HER2 than usual (HER2 alterations) The solid tumors studied in this trial have either spread to other parts of the body (metastatic) or cannot be removed completely with surgery (unresectable). All participants will get both tucatinib and trastuzumab. People with hormone-receptor positive breast cancer will also get a drug called fulvestrant. The trial will also look at what side effects happen. A side effect is anything a drug does besides treating cancer.

Trial Health

62
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
217

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2021

Longer than P75 for phase_2

Geographic Reach
8 countries

106 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 1, 2020

Completed
7 days until next milestone

First Posted

Study publicly available on registry

October 8, 2020

Completed
3 months until next milestone

Study Start

First participant enrolled

January 11, 2021

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2023

Completed
1 year until next milestone

Results Posted

Study results publicly available

November 13, 2024

Completed
1.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2026

Completed
Last Updated

December 19, 2025

Status Verified

December 1, 2025

Enrollment Period

2.8 years

First QC Date

October 1, 2020

Results QC Date

October 16, 2024

Last Update Submit

December 3, 2025

Conditions

Keywords

Cervical cancerUterine cancerBiliary tract cancerUrothelial cancerNon-squamous non-small cell lung cancerNon-squamous NSCLCBreast cancerColorectal cancerAmpullary cancerSolid tumorsSolid tumors harboring somatic HER2 mutationsSeattle Genetics

Outcome Measures

Primary Outcomes (1)

  • Confirmed Objective Response Rate (cORR) as Assessed by Investigator

    Confirmed ORR was defined as the percentage of participants with best overall response of complete response (CR) or partial response (PR) according to Response Evaluation Criteria in Solid Tumors (RECIST) criteria version (v)1.1 as assessed by investigator and was considered as confirmed when subsequent response was at least 4 weeks after initial response. As per RECIST v1.1, CR: disappearance of all target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to less than (\<)10 millimeter (mm). PR: at least a greater than or equal to (\>=)30 % decrease in the sum of diameters (SOD) of target lesions (longest for non-nodal target lesions and the short axes for nodal target lesions), taking as reference the baseline sum diameters. Disease progression (PD): at least \>=20% relative increase in SOD of target lesion taking as reference the smallest sum on study (including baseline sum if that is the smallest on study).

    From the first dose of study treatment until the first documented CR or PR on or before the first documented PD or new anti-cancer therapies or death, whichever occurred first (up to 28.3 months)

Secondary Outcomes (10)

  • Confirmed Disease Control Rate (DCR) as Assessed by Investigator

    From the first dose study treatment until PD or death, whichever occurred first (approximately 52.7 months)

  • Duration of Response (DOR) as Assessed by Investigator

    From the first documented CR or PR until the first documentation of PD or death or censoring date, whichever occurred first (approximately 52.7 months)

  • Progression-Free Survival (PFS) as Assessed by Investigator

    From the first documented CR or PR until the first documentation of PD or death or censoring date, whichever occurred first (approximately 52.7 months)

  • Overall Survival (OS)

    From date of start of study treatment until date of death or censoring date (approximately 52.7 months)

  • Number of Participants With Treatment Emergent Adverse Events (TEAEs)

    From first dose of the study treatment (Day 1) up to 30 days after the last dose of study treatment (approximately 52.7 months)

  • +5 more secondary outcomes

Study Arms (1)

Tucatinib + Trastuzumab (+ Fulvestrant)

EXPERIMENTAL

Tucatinib + trastuzumab (+ fulvestrant in hormone-receptor positive HER2-mutant breast cancer only)

Drug: tucatinibDrug: trastuzumabDrug: fulvestrant

Interventions

300 mg orally twice daily

Also known as: TUKYSA, ARRY-380, ONT-380
Tucatinib + Trastuzumab (+ Fulvestrant)

Given into the vein (intravenously; IV). 8mg/kg IV on Cycle 1 Day 1, and 6mg/kg every 21 days starting on Cycle 2 Day 1

Also known as: Herceptin
Tucatinib + Trastuzumab (+ Fulvestrant)

Given into the muscle (intramuscular; IM) once every 4 weeks starting from Cycle 1 Day 1, plus one dose on Cycle 1 Day 15. Only administered to participants with hormone-receptor positive breast cancer.

Also known as: Faslodex
Tucatinib + Trastuzumab (+ Fulvestrant)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed diagnosis of locally-advanced unresectable or metastatic solid tumor, including primary brain tumors
  • Participants with non-squamous NSCLC must have progressed during or after standard treatment or for which no standard treatment is available
  • Participants with other disease types must have progressed during or after ≥1 prior line of systemic therapy for locally-advanced unresectable or metastatic disease
  • Disease progression during or after, or intolerance of, the most recent line of systemic therapy
  • Disease demonstrating HER2 alterations (overexpression/amplification or HER2 activating mutations), as determined by local or central testing processed in a Clinical Laboratory Improvement Amendments (CLIA)- or International Organization for Standardization (ISO) accredited laboratory, according to one of the following:
  • HER2 overexpression/amplification from fresh or archival tumor tissue or blood
  • Known activating HER2 mutations detected in fresh or archival tumor tissue or blood
  • Have measurable disease per RECIST v1.1 criteria according to investigator assessment
  • Have Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1

You may not qualify if:

  • Participants with breast cancer, gastric or gastroesophageal junction adenocarcinoma, or CRC whose disease shows HER2 amplification/overexpression.
  • Previous treatment with HER2-directed therapy; participants with uterine serous carcinoma or HER2-mutated gastric or gastroesophageal junction adenocarcinoma without HER2-overexpression/amplification may have received prior trastuzumab
  • Known hypersensitivity to any component of the drug formulation of tucatinib or trastuzumab (drug substance, excipients, murine proteins), or any component of the drug formulation of fulvestrant in participants with HR+ HER2-mutated breast cancer
  • History of exposure to a 360 mg/m² doxorubicin-equivalent or \>720 mg/m\^2 epirubicin-equivalent cumulative dose of anthracyclines
  • Treatment with any systemic anti-cancer therapy, radiation therapy, major surgery, or experimental agent within ≤3 weeks of first dose of study treatment or are currently participating in another interventional clinical trial.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (106)

HonorHealth

Phoenix, Arizona, 85016, United States

Location

HonorHealth

Tempe, Arizona, 85284, United States

Location

The University of Arizona Cancer Center-North Campus

Tucson, Arizona, 85719, United States

Location

City of Hope at Huntington Beach

Huntington Beach, California, 92648, United States

Location

City of Hope at Irvine Sand Canyon

Irvine, California, 92618, United States

Location

Koman Family Outpatient Pavilion

La Jolla, California, 92037, United States

Location

UC San Diego Medical Center - La Jolla (Jacobs Medical Center / Thornton Pavilion)

La Jolla, California, 92037, United States

Location

UC San Diego Moores Cancer Center- Investigational Drug Services

La Jolla, California, 92037, United States

Location

UC San Diego Moores Cancer Center

La Jolla, California, 92037, United States

Location

City of Hope at Long Beach Worsham

Long Beach, California, 90808, United States

Location

City of Hope at Long Beach Elm

Long Beach, California, 90813, United States

Location

City of Hope at Newport Beach Lido

Newport Beach, California, 92663, United States

Location

City of Hope Torrance

Torrance, California, 90505, United States

Location

Rocky Mountain Cancer Centers

Aurora, Colorado, 80012, United States

Location

Rocky Mountain Cancer Centers

Boulder, Colorado, 80303, United States

Location

Rocky Mountain Cancer Centers

Thornton, Colorado, 80260, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Minnesota Oncology Hematology, PA

Coon Rapids, Minnesota, 55433, United States

Location

Metro Minnesota Community Oncology Research Consortium (MMCORC)

Saint Louis Park, Minnesota, 55426, United States

Location

Washington University School of Medicine - Obstetrics & Gynecology [Academic Offices)

St Louis, Missouri, 63108, United States

Location

Barnes-Jewish Hospital Investigational Drug Pharmacy (IDS)

St Louis, Missouri, 63110, United States

Location

Washington University School of Medicine - Obstetrics & Gynecology

St Louis, Missouri, 63110, United States

Location

Washington University School of Medicine [Patient Clinics]

St Louis, Missouri, 63110, United States

Location

Oncology Hematology West P.C. dba Nebraska Cancer Specialists

Omaha, Nebraska, 68114, United States

Location

Oncology Hematology West P.C. dba Nebraska Cancer Specialists

Omaha, Nebraska, 68130, United States

Location

NYU Langone Health - Long Island (Winthrop Hospital)

Mineola, New York, 11501, United States

Location

Perlmutter Cancer Center at NYU Langone GYN Oncology Associates

Mineola, New York, 11501, United States

Location

Perlmutter Cancer Center at NYU Langone Hospital - Long Island

Mineola, New York, 11501, United States

Location

Laura and Isaac Perlmutter Cancer Center at NYU Langone

New York, New York, 10016, United States

Location

NYU Langone Medical Center

New York, New York, 10016, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Duke University Medical Center/Duke Cancer Center

Durham, North Carolina, 27710, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

OSU Wexner Medical Center, CarePoint East

Columbus, Ohio, 43203, United States

Location

OSU Wexner Medical Center, Ohio State University Hospital East

Columbus, Ohio, 43203, United States

Location

OSU Wexner Medical Center, Arther G. James Cancer Hospital, and Solove Research Institute

Columbus, Ohio, 43210, United States

Location

OSU Wexner Medical Center, Investigational Drug Services(IP Ship to)

Columbus, Ohio, 43210, United States

Location

Osu Wexner Medical Center, The Ohio State University Hospital

Columbus, Ohio, 43210, United States

Location

OSU Wexner Medical Center, Stephanie Spielman Comprehensive Breast Center

Columbus, Ohio, 43212, United States

Location

OSU Wexner Medical Center, Martha Morehouse Medical Plaza

Columbus, Ohio, 43221, United States

Location

OSU Wexner Medical Center, OutPatient Care Upper Arlington

Columbus, Ohio, 43221, United States

Location

OSU Wexner Medical Center, CarePoint Gahanna

Gahanna, Ohio, 43230, United States

Location

OSU Wexner Medical Center, Gynecologic Oncology at Mill Run

Hilliard, Ohio, 43026, United States

Location

OSU Wexner Medical Center, Outpatient Care Lewis Center

Lewis Center, Ohio, 43035, United States

Location

UH Minoff Health Center at Chagrin Highlands

Orange, Ohio, 44122, United States

Location

OSU Wexner Medical Center, Outpatient Care New Albany

Westerville, Ohio, 43081, United States

Location

Northwest Cancer Specialists, P.C.

Portland, Oregon, 97213, United States

Location

Northwest Cancer Specialists, P.C.

Portland, Oregon, 97227, United States

Location

Northwest Cancer Specialists, P.C.

Tigard, Oregon, 97223, United States

Location

UPMC Hillman Cancer Center - Washington

Washington, Pennsylvania, 15301, United States

Location

Prisma Health Cancer Institute

Boiling Springs, South Carolina, 29316, United States

Location

Prisma Health Cancer Institute

Easley, South Carolina, 29640, United States

Location

Prisma Health Cancer Institute

Greenville, South Carolina, 29605, United States

Location

Prisma Health Cancer Institute

Greenville, South Carolina, 29615, United States

Location

Prisma Health Cancer Institute

Greer, South Carolina, 29650, United States

Location

Prisma Health Cancer Institute

Seneca, South Carolina, 29672, United States

Location

Tennessee Oncology, PLLC

Gallatin, Tennessee, 37066, United States

Location

Tennessee Oncology, PLLC

Hendersonville, Tennessee, 37075, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology, PLLC

Shelbyville, Tennessee, 37160, United States

Location

Texas oncology-West Texas

Abilene, Texas, 79606, United States

Location

US Oncology Investigational Product Center (IPC)

Irving, Texas, 75063, United States

Location

US Oncology Investigational Products Center (IPC)

Irving, Texas, 75063, United States

Location

US Oncology lnvestigational Products Center (IPC)

Irving, Texas, 75063, United States

Location

Texas Oncology - Central South

Waco, Texas, 76712, United States

Location

Huntsman Cancer Institute, University of Utah

Salt Lake City, Utah, 84112, United States

Location

Virginia Cancer Specialists, PC

Alexandria, Virginia, 22304, United States

Location

Virginia Cancer Specialists, PC

Arlington, Virginia, 22205, United States

Location

Virginia Cancer Specialists, PC

Fairfax, Virginia, 22031, United States

Location

Virginia Cancer Specialists, PC

Gainesville, Virginia, 20155, United States

Location

Fred Hutchinson Cancer Center

Seattle, Washington, 98109, United States

Location

University of Washington Medical Center

Seattle, Washington, 98195, United States

Location

Northwest Cancer Specialists, P.C.

Vancouver, Washington, 98684, United States

Location

1 S Park St Medical Center

Madison, Wisconsin, 53715, United States

Location

University of Wisconsin Clinical Science Center

Madison, Wisconsin, 53792, United States

Location

Grand Hopital de Charleroi

Charleroi, Hainaut, B- 6060, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Universitair Ziekenhuis Antwerpen

Edegem, 2650, Belgium

Location

AZ Groeninge

Kortrijk, 8500, Belgium

Location

CHU de Liege

Liège, 4000, Belgium

Location

AZ Sint-Maarten

Mechelen, 2800, Belgium

Location

Charite Universitatsmedizin Berlin

Berlin, 12203, Germany

Location

Divisione di Sviluppo di Nuovi Farmaci per Terapie Innovative lstituto Europeo di Oncologia

Milan, Milan, 20141, Italy

Location

Aichi Cancer Center Hospital

Nagoya, Aichi-ken, 464-8681, Japan

Location

National Cancer Center Hospital East

Kashiwa-shi, Chiba, 277-8577, Japan

Location

St. Marianna University School of Medicine Hospital

Kawasaki, Kanagawa, 216-8511, Japan

Location

Kindai University Hospital

Osakasayama-shi, Osaka, 589-8511, Japan

Location

National Cancer Center Hospital

Cho-ku, Tokyo, 104-0045, Japan

Location

The Cancer Institute Hospital of JFCR

Tokyo, 135-8550, Japan

Location

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, 13620, South Korea

Location

Severance Hospital Yonsei University Health System

Seoul, Other, 03722, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Institut Catala d'Oncologia Hospitalet

L'Hospitalet de Llobregat, Other, 8908, Spain

Location

Cetir Centre Medic

Barcelona, 08029, Spain

Location

Hospital Clínico Universitario de Valencia. Fundación Investigación Clínico de Valencia.

Valencia, 46010, Spain

Location

Ascires Eresa Campanar

Valencia, 46015, Spain

Location

Hospital Vithas Valencia 9 de Octubre

Valencia, 46015, Spain

Location

Sarah Cannon Research Institute UK

London, Budapest, W1G 6AD, United Kingdom

Location

Diagnostic Centre

London, Others, W1G 7AF, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Guy's Hospital

London, SE1 9RT, United Kingdom

Location

Jonathan Poon

London, SE1 9RT, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

London, SW3 6JJ, United Kingdom

Location

The Harley Street Clinic

London, W1G 8BJ, United Kingdom

Location

Radiology

London, W1G 8PP, United Kingdom

Location

Related Publications (2)

  • Okines AFC, Curigliano G, Mizuno N, Oh DY, Rorive A, Soliman H, Takahashi S, Bekaii-Saab T, Burkard ME, Chung KY, Debruyne PR, Fox JR, Gambardella V, Gil-Martin M, Hamilton EP, Monk BJ, Nakamura Y, Nguyen D, O'Malley DM, Olawaiye AB, Pothuri B, Reck M, Sudo K, Sunakawa Y, Van Marcke C, Yu EY, Ramos J, Tan S, Bieda M, Stinchcombe TE, Pohlmann PR. Tucatinib and trastuzumab in HER2-mutated metastatic breast cancer: a phase 2 basket trial. Nat Med. 2025 Mar;31(3):909-916. doi: 10.1038/s41591-024-03462-0. Epub 2025 Jan 17.

  • Nakamura Y, Mizuno N, Sunakawa Y, Canon JL, Galsky MD, Hamilton E, Hayashi H, Jerusalem G, Kim ST, Lee KW, Kankeu Fonkoua LA, Monk BJ, Nguyen D, Oh DY, Okines A, O'Malley DM, Pohlmann P, Reck M, Shin SJ, Sudo K, Takahashi S, Van Marcke C, Yu EY, Groisberg R, Ramos J, Tan S, Stinchcombe TE, Bekaii-Saab T. Tucatinib and Trastuzumab for Previously Treated Human Epidermal Growth Factor Receptor 2-Positive Metastatic Biliary Tract Cancer (SGNTUC-019): A Phase II Basket Study. J Clin Oncol. 2023 Dec 20;41(36):5569-5578. doi: 10.1200/JCO.23.00606. Epub 2023 Sep 26.

MeSH Terms

Conditions

Uterine NeoplasmsUterine Cervical NeoplasmsBiliary Tract NeoplasmsUrologic NeoplasmsCarcinoma, Non-Small-Cell LungBreast NeoplasmsColorectal Neoplasms

Interventions

tucatinibTrastuzumabFulvestrant

Condition Hierarchy (Ancestors)

Genital Neoplasms, FemaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesUterine Cervical DiseasesDigestive System NeoplasmsBiliary Tract DiseasesDigestive System DiseasesMale Urogenital DiseasesUrologic DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesIntestinal NeoplasmsGastrointestinal NeoplasmsGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsEstradiolEstrenesEstranesSteroidsFused-Ring CompoundsPolycyclic CompoundsEstradiol CongenersGonadal Steroid HormonesGonadal HormonesHormonesHormones, Hormone Substitutes, and Hormone Antagonists

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 1, 2020

First Posted

October 8, 2020

Study Start

January 11, 2021

Primary Completion

November 1, 2023

Study Completion

April 30, 2026

Last Updated

December 19, 2025

Results First Posted

November 13, 2024

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will not share

Locations