NCT04539938

Brief Summary

This trial studies how well the drug tucatinib works when given with trastuzumab deruxtecan (T-DXd). It will also look at what side effects happen when these drugs are given together. A side effect is anything a drug does besides treating cancer. Participants in this trial have HER2-positive (HER2+) breast cancer that has either spread to other parts of the body (metastatic) or cannot be removed completely with surgery (unresectable). All participants will get both tucatinib and T-DXd.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Dec 2020

Typical duration for phase_2

Geographic Reach
1 country

140 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 31, 2020

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 7, 2020

Completed
3 months until next milestone

Study Start

First participant enrolled

December 1, 2020

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 15, 2024

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 7, 2025

Completed
5 months until next milestone

Results Posted

Study results publicly available

July 31, 2025

Completed
Last Updated

March 23, 2026

Status Verified

March 1, 2026

Enrollment Period

3.6 years

First QC Date

August 31, 2020

Results QC Date

July 14, 2025

Last Update Submit

March 2, 2026

Conditions

Keywords

HER2+ breast cancerMetastatic breast cancerStage IV breast cancerSeattle Genetics

Outcome Measures

Primary Outcomes (1)

  • Confirmed Objective Response Rate (cORR) Per Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1 According to Investigator (INV) Assessment

    Confirmed objective response rate was defined as the percentage of participants with a confirmed complete response (CR) or partial response (PR) per investigator according to RECIST v1.1. For a response to be considered confirmed, the subsequent response had to be at least 4 weeks after the initial response. CR: disappearance of all target lesions and non-target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to less than (\<)10 millimeters (mm). PR: a greater than equal to (\>=) 30 percent (%) decrease in the sum of diameters of target lesions, taking as reference the baseline sum of diameters. 95% exact confidence interval (CI) was based on Clopper-Pearson method.

    From the first dose of study treatment until the first documented PD or before start of any new anti-cancer therapy (up to 43 months)

Secondary Outcomes (13)

  • Progression-Free Survival (PFS) Per RECIST v1.1 According to INV

    From the start of study treatment until the first documentation of PD or death due to any cause, whichever occurred first (approximately 46.2 months of treatment exposure)

  • Duration of Response (DOR) Per RECIST v1.1 According to INV

    From the first documented objective response until the first documentation of PD or death, whichever occurred first (approximately 46.2 months)

  • Disease Control Rate (DCR) Per RECIST v1.1

    From first dose of study treatment until PD or death, whichever occurred first (approximately 46.2 months)

  • Overall Survival (OS)

    From date of start of study treatment until date of death or censoring date (approximately 46.2 months)

  • Number of Participants With Treatment Emergent Adverse Events (TEAEs)

    From first dose of the study treatment (Day 1) up to 30 days after the last dose of study treatment (approximately 47.2 months)

  • +8 more secondary outcomes

Study Arms (1)

Single Arm

EXPERIMENTAL

Tucatinib + trastuzumab deruxtecan

Drug: tucatinibDrug: trastuzumab deruxtecan

Interventions

300 mg orally twice daily

Also known as: TUKYSA, ARRY-380, ONT-380, PF-07265792
Single Arm

5.4 mg/kg via intravenous (into the vein; IV) infusion on Day 1 of each of 21-day cycle

Also known as: T-DXd, Enhertu, DS-8201
Single Arm

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have confirmed HER2+ breast cancer, as defined by the current American Society of Clinical Oncology - College of American Pathologists (ASCO/CAP) guidelines, previously determined at a Clinical Laboratory Improvements Amendments (CLIA)-certified or International Organization for Standardization (ISO)-accredited laboratory.
  • History of prior treatment with a taxane and trastuzumab in the LA/M setting OR progressed within 6 months after neoadjuvant or adjuvant treatment, including a taxane and trastuzumab.
  • Have progression of unresectable LA/M breast cancer after last systemic therapy (as confirmed by investigator), or be intolerant of last systemic therapy
  • Have measurable disease assessable by RECIST v1.1
  • Have Eastern Cooperative Oncology Group Performance Status (ECOG PS) 0 or 1
  • Have a life expectancy of at least 6 months, in the opinion of the investigator
  • Untreated brain metastases not needing immediate local therapy. For participants with untreated central nervous system (CNS) lesions \>2.0 cm on screening contrast brain MRI, discussion with and approval from the medical monitor is required prior to enrollment
  • Previously treated brain metastases
  • Brain metastases previously treated with local therapy may either be stable since treatment or may have progressed since prior local CNS therapy, provided that there is no clinical indication for immediate re-treatment with local therapy in the opinion of the investigator
  • Participants treated with CNS local therapy for newly identified or previously treated progressing lesions found on contrast brain MRI performed during screening for this study may be eligible to enroll if all of the following criteria are met:
  • Time since whole brain radiation therapy (WBRT) is ≥14 days prior to first dose of study treatment, time since stereotactic radiosurgery (SRS) is ≥7 days prior to first dose of study treatment, or time since surgical resection is ≥28 days
  • Other sites of measurable disease by RECIST v1.1 are present
  • Relevant records of any CNS treatment must be available

You may not qualify if:

  • Have previously been treated with:
  • Lapatinib or neratinib within 12 months of starting study treatment (except in cases where lapatinib or neratinib was given for ≤21 days and was discontinued for reasons other than disease progression or severe toxicity)
  • Tucatinib or enrolled on a tucatinib clinical trial
  • Any investigational HER2/epidermal growth factor receptor (EGFR) or HER2 tyrosine kinase inhibitor (TKI) (eg, afatinib) at any time previously
  • Trastuzumab deruxtecan or another antibody-drug conjugate (ADC) consisting of an exatecan derivative
  • Have received treatment with:
  • Any systemic anti-cancer therapy (including hormonal therapy) or experimental agent ≤21 days of first dose of study treatment or are currently participating in another interventional clinical trial. An exception for the washout of hormonal therapies is gonadotropin releasing hormone (GnRH) agonists used for ovarian suppression in premenopausal women, which are permitted concomitant medications
  • Treatment with non-CNS radiation ≤7 days prior to first dose of study treatment
  • Major surgery \<28 days of first dose of study treatment
  • Have clinically significant cardiopulmonary disease (such as history of iterstitial lung disease (ILD)/pneumonitis that required systemic corticosteroids, or have current ILD/pneumonitis, or where suspected ILD /pneumonitis cannot be ruled out be imaging at screening)
  • Have known myocardial infarction or unstable angina within 6 months prior to first dose of study treatment
  • Known to be positive for hepatitis B by surface antigen expression. Known to be positive for hepatitis C infection. Participants who have been treated for hepatitis C infection are permitted if they have documented sustained virologic response of 12 weeks
  • Presence of known chronic liver disease
  • Active or uncontrolled clinically serious infection
  • Have inability to swallow pills or significant gastrointestinal disease which would preclude the adequate oral absorption of medications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (140)

University Of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

University of Alabama at Birmingham, IDS Pharmacy

Birmingham, Alabama, 35249, United States

Location

University Of Alabama at Birmingham

Birmingham, Alabama, 35249, United States

Location

Arizona Oncology Associates, PC - HOPE

Tucson, Arizona, 85704, United States

Location

Arizona Oncology Associates, PC - HOPE

Tucson, Arizona, 85711, United States

Location

UCLA Hematology/Oncology - Alhambra

Alhambra, California, 91801, United States

Location

UCLA Hematology/Oncology - Burbank

Burbank, California, 91505, United States

Location

City of Hope (City of Hope National Medical Center, City of Hope Medical center)

Duarte, California, 91010, United States

Location

City of Hope Investigational Drug Services (IDS)

Duarte, California, 91010, United States

Location

UCLA Hematology/Oncology - Laguna Hills

Laguna Hills, California, 92653, United States

Location

(IRB# 20-001502) Ronald Reagan UCLA Medical Center, Drug Information Center

Los Angeles, California, 90095, United States

Location

UCLA Hematology/Oncology

Los Angeles, California, 90095, United States

Location

UCLA Hematology/Oncology - Pasadena

Pasadena, California, 91105, United States

Location

Zuckerberg San Francisco General Hospital- Breast Clinic

San Francisco, California, 94110, United States

Location

Zuckerberg San Francisco General Hospital- Oncology Clinic

San Francisco, California, 94110, United States

Location

University of California, San Francisco (UCSF) Helen Diller Family Comprehensive Cancer Center

San Francisco, California, 94158, United States

Location

UCLA Hematology/Oncology - San Luis Obispo

San Luis Obispo, California, 93401, United States

Location

UCLA Hematology/Oncology - Santa Barbara

Santa Barbara, California, 93105, United States

Location

UCLA Hematology/Oncology - Santa Monica

Santa Monica, California, 90404, United States

Location

UCLA Hematology/Oncology Parkside

Santa Monica, California, 90404, United States

Location

UCLA Hematology/Oncology - Ventura

Ventura, California, 93003, United States

Location

UCLA Hematology/Oncology - Westlake

Westlake Village, California, 91361, United States

Location

University of Colorado Denver CTO/CTRC - Outpatient.

Aurora, Colorado, 80045, United States

Location

University of Colorado Hospital - Anschutz Cancer Pavilion (ACP)

Aurora, Colorado, 80045, United States

Location

University of Colorado Hospital - Anschutz Inpatient Pavilion (AIP)

Aurora, Colorado, 80045, United States

Location

University of Colorado Hospital - Anschutz Outpatient Pavilion (AOP)

Aurora, Colorado, 80045, United States

Location

UC Health Lone Tree Medical Center

Lone Tree, Colorado, 80124, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Washington Cancer Institute at MedStar Washington Hospital Center

Washington D.C., District of Columbia, 20010, United States

Location

Florida Cancer Specialists

Altamonte Springs, Florida, 32701, United States

Location

Florida Cancer Specialists

Brandon, Florida, 33511, United States

Location

Florida Cancer Specialists

Clearwater, Florida, 33761, United States

Location

Florida Cancer Specialists

Gainesville, Florida, 32605, United States

Location

Florida Cancer Specialists

Largo, Florida, 33770, United States

Location

Florida Cancer Specialists

Lecanto, Florida, 34461, United States

Location

Florida Cancer Specialists

Ocala, Florida, 34474, United States

Location

Florida Cancer Specialists

Orange City, Florida, 32763, United States

Location

Florida Cancer Specialists

Orlando, Florida, 32806, United States

Location

Florida Cancer Specialists

St. Petersburg, Florida, 33705, United States

Location

Florida Cancer Specialists

Tampa, Florida, 33607, United States

Location

Florida Cancer Specialists

Tavares, Florida, 32778, United States

Location

Florida Cancer Specialists

The Villages, Florida, 32159, United States

Location

Florida Cancer Specialists

Trinity, Florida, 34655, United States

Location

Florida Cancer Specialists

Winter Park, Florida, 32789, United States

Location

Northside Hospital, Inc - GCS/Athens

Athens, Georgia, 30606, United States

Location

Winship Cancer Institute @ Emory University Hospital Midtown

Atlanta, Georgia, 30308, United States

Location

Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

The Emory Clinic

Atlanta, Georgia, 30322, United States

Location

Winship Cancer Institute / Emory University School of Medicine

Atlanta, Georgia, 30322, United States

Location

Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Atlanta Cancer Care - Atlanta

Atlanta, Georgia, 30342, United States

Location

Northside Hospital, Inc. - Central Research Department

Atlanta, Georgia, 30342, United States

Location

Northside Hospital, Inc. - GCS/Center Pointe

Atlanta, Georgia, 30342, United States

Location

Northside Hospital, Inc - GCS/Blairsville

Blairsville, Georgia, 30512, United States

Location

Northside Hospital, Inc - GCS/Canton

Canton, Georgia, 30114, United States

Location

Atlanta Cancer Care - Cumming

Cumming, Georgia, 30041, United States

Location

Northside Hospital, Inc. - GCS/Decatur

Decatur, Georgia, 30033, United States

Location

NHCI Suburban Hematology-oncology Associates - Duluth

Duluth, Georgia, 30096, United States

Location

NHCI Suburban Hematology-oncology Associates - lawrenceville

Lawrenceville, Georgia, 30046, United States

Location

Northside Hospital, Inc - GCS/Macon

Macon, Georgia, 31217, United States

Location

Northside Hospital, Inc. - GCS/Marietta

Marietta, Georgia, 30060, United States

Location

Atlanta Cancer Care - Stockbridge

Stockbridge, Georgia, 30281, United States

Location

Harry and Jeanette Weinberg Cancer Institute at Franklin Square

Baltimore, Maryland, 21237, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Dana Farber Cancer Institute- Chestnut Hill

Newton, Massachusetts, 02459, United States

Location

Mercy Hospital

Coon Rapids, Minnesota, 55433, United States

Location

Minnesota Oncology Hematology, PA

Coon Rapids, Minnesota, 55433, United States

Location

Mercy Hospital - Unity Campus

Fridley, Minnesota, 55432, United States

Location

Minnesota Oncology Hematology, PA

Fridley, Minnesota, 55433, United States

Location

Minnesota Oncology Hematology, PA

Minneapolis, Minnesota, 55404, United States

Location

Abbott Northwestern Hospital

Minneapolis, Minnesota, 55407, United States

Location

Allina Health Cancer institute

Minneapolis, Minnesota, 55407, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Allina Health Cancer Institute

Saint Paul, Minnesota, 55102, United States

Location

Minnesota Oncology Hematology PA

Saint Paul, Minnesota, 55102, United States

Location

Minnesota Oncology Hematology, PA

Saint Paul, Minnesota, 55102, United States

Location

United Hospital

Saint Paul, Minnesota, 55102, United States

Location

Oncology Hematology West, PC dba Nebraska Cancer Specialists

Omaha, Nebraska, 68114, United States

Location

Oncology Hematology West, PC dba Nebraska Cancer Specialists

Omaha, Nebraska, 68124, United States

Location

Oncology Hematology West, PC dba Nebraska Cancer Specialists

Omaha, Nebraska, 68130, United States

Location

Oncology Hematology West, PC dba Nebraska Cancer Specialists

Papillion, Nebraska, 68046, United States

Location

MSK Basking Ridge

Basking Ridge, New Jersey, 07920, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

MSK Monmouth

Middletown, New Jersey, 07748, United States

Location

MSK Bergen

Montvale, New Jersey, 07645, United States

Location

MSK Commack

Commack, New York, 11725, United States

Location

MSK Westchester

Harrison, New York, 10604, United States

Location

Memorial Sloan Kettering Cancer Center - Investigational Drug Service Pharmacy

Long Island City, New York, 11101, United States

Location

Evelyn H. Lauder Breast and Imaging Center (BAIC).

New York, New York, 10065, United States

Location

MSK Nassau

Uniondale, New York, 11553, United States

Location

Providence Cancer Institute Franz Clinic

Portland, Oregon, 97213, United States

Location

Providence Portland Medical Center

Portland, Oregon, 97213, United States

Location

UPMC Hillman Cancer Center Passavant North

Cranberry Township, Pennsylvania, 16066, United States

Location

UPMC Hillman Cancer Center Erie

Erie, Pennsylvania, 16505, United States

Location

UPMC Hillman Cancer Center Mountainview

Greensburg, Pennsylvania, 15601, United States

Location

UPMC Hillman Cancer Center UPMC East

Monroeville, Pennsylvania, 15146, United States

Location

UPMC Hillman Cancer Center Upper Saint Clair

Pittsburgh, Pennsylvania, 15102, United States

Location

Magee-Womens Hospital of UPMC

Pittsburgh, Pennsylvania, 15213, United States

Location

University of Pittsburgh Cancer Institute Investigational Drug Service UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

UPMC Cancer Centers William M. Cooper Ambulatory Care Pavilion of the Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

UPMC Hillman Cancer Center UPMC Passavant

Pittsburgh, Pennsylvania, 15237, United States

Location

UPMC Hillman Cancer Center Uniontown

Uniontown, Pennsylvania, 15401, United States

Location

UPMC Hillman Cancer Center Washington

Washington, Pennsylvania, 15301, United States

Location

Tennessee Oncology, PLLC

Chattanooga, Tennessee, 37403, United States

Location

Sarah Cannon Research Institute

Chattanooga, Tennessee, 37404, United States

Location

Tennessee Oncology, PLLC

Chattanooga, Tennessee, 37404, United States

Location

Tennessee Oncology, PLLC

Cleveland, Tennessee, 37311, United States

Location

Tennessee Oncology, PLLC

Dickson, Tennessee, 37055, United States

Location

Tennessee Oncology, PLLC

Franklin, Tennessee, 37067, United States

Location

Tennessee Oncology, PLLC

Gallatin, Tennessee, 37066, United States

Location

Tennessee Oncology, PLLC

Hendersonville, Tennessee, 37075, United States

Location

Tennessee Oncology, PLLC

Hermitage, Tennessee, 37076, United States

Location

Tennessee Oncology, PLLC

Lebanon, Tennessee, 37909, United States

Location

Tennessee Oncology, PLLC

Murfreesboro, Tennessee, 37129, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37203, United States

Location

The Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37205, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37207, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37211, United States

Location

Tennessee Oncology, PLLC

Shelbyville, Tennessee, 37160, United States

Location

Tennessee Oncology, PLLC

Smyrna, Tennessee, 37167, United States

Location

The University of Texas M.D. Anderson Cancer Center

Houston, Texas, 77030, United States

Location

U.T. MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

US Oncology Investigational Product Center (IPC)

Irving, Texas, 75063, United States

Location

US Oncology Investigational Products Center (IPC)

Irving, Texas, 75063, United States

Location

US Oncology lnvestigational Products Center (IPC)

Irving, Texas, 75063, United States

Location

Oncology & Hematology Associates of Southwest Virginia, Inc. D.B.A Blue Ridge Cancer Care

Blacksburg, Virginia, 24060, United States

Location

Virginia Cancer Specialists, PC

Fairfax, Virginia, 22031, United States

Location

Virginia Cancer Specialists, PC

Gainesville, Virginia, 20155, United States

Location

Virginia Cancer Specialists, PC

Leesburg, Virginia, 20176, United States

Location

Oncology & Hematology Associates of Southwest Virginia, Inc. D.B.A Blue Ridge Cancer Care

Low Moor, Virginia, 24457, United States

Location

Virginia Cancer Specialists, PC

Reston, Virginia, 20190, United States

Location

Oncology & Hematology Associates of Southwest Virginia, Inc. D.B.A Blue Ridge Cancer Care

Roanoke, Virginia, 24014, United States

Location

Oncology & Hematology Associates of Southwest Virginia, Inc. D.B.A Blue Ridge Cancer Care

Salem, Virginia, 24153, United States

Location

Oncology & Hematology Associates of Southwest Virginia, Inc. D.B.A Blue Ridge Cancer Care

Wytheville, Virginia, 24382, United States

Location

Fred Hutchinson Cancer Center

Seattle, Washington, 98109, United States

Location

University of Washington Medical Center

Seattle, Washington, 98195, United States

Location

UW Health Oncology - One South Park

Madison, Wisconsin, 53715, United States

Location

University of Wisconsin Clinical Science Center

Madison, Wisconsin, 53792, United States

Location

Related Links

MeSH Terms

Conditions

Breast Neoplasms

Interventions

tucatinibtrastuzumab deruxtecan

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 31, 2020

First Posted

September 7, 2020

Study Start

December 1, 2020

Primary Completion

July 15, 2024

Study Completion

March 7, 2025

Last Updated

March 23, 2026

Results First Posted

July 31, 2025

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations