NCT04422210

Brief Summary

A study consisting of a dose-escalation phase and a dose-expansion phase to evaluate the safety, tolerability, pharmacokinetics, and efficacy of venetoclax in combination with atezolizumab, carboplatin, and etoposide.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Sep 2020

Shorter than P25 for phase_1

Geographic Reach
4 countries

5 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 5, 2020

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 9, 2020

Completed
4 months until next milestone

Study Start

First participant enrolled

September 22, 2020

Completed
2 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 6, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 6, 2020

Completed
1 year until next milestone

Results Posted

Study results publicly available

November 8, 2021

Completed
Last Updated

November 8, 2021

Status Verified

October 1, 2021

Enrollment Period

2 months

First QC Date

June 5, 2020

Results QC Date

October 8, 2021

Last Update Submit

October 8, 2021

Conditions

Outcome Measures

Primary Outcomes (2)

  • Number of Participants With Adverse Events (AEs)

    The study was terminated by the Sponsor. Only 2 participants were enrolled in this study. Based on the low enrolment number, no data is reported here in order to protect and maintain participant privacy/confidentiality.

    Baseline up until 30 days after the last dose of study drug or until initiation of new systemic anti-cancer therapy, whichever occurs first (up to a maximum of 6.5 weeks).

  • Overall Response Rate (ORR)

    The study was terminated by the Sponsor. Only 2 participants were enrolled in this study. Based on the low enrolment number, no data is reported here in order to protect and maintain participant privacy/confidentiality.

    Up to 24 months

Secondary Outcomes (9)

  • Duration of Response (DOR)

    Up to 24 months

  • Progression Free Survival (PFS)

    Up to 24 months

  • Overall Survival (OS) After Enrolment

    Up to 49 months

  • Progression Free Survival (PFS) Rate at 6 Months

    Up to 18 months

  • Overall Survival (OS) Rate at 1 Year

    Up to 18 months

  • +4 more secondary outcomes

Study Arms (8)

Dose Escalation (Arm A1) (Maintenance only)

EXPERIMENTAL

Cohort A1: Participants with ES-SCLC who completed 4-6 cycles of carboplatin and etoposide first-line induction chemotherapy, with or without atezolizumab, were administered continuous maintenance therapy with Venetoclax (400mg) once daily (QD) from Day 1 to 21 and Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1.

Drug: VenetoclaxDrug: Atezolizumab

Dose Escalation (Arm A2) (Maintenance only)

EXPERIMENTAL

Cohort A2: Participants with ES-SCLC who completed 4-6 cycles of carboplatin and etoposide first-line induction chemotherapy, with or without atezolizumab, were to be administered continuous maintenance therapy with Venetoclax (800mg) once daily (QD) from Day 1 to 21 and Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1.

Drug: VenetoclaxDrug: Atezolizumab

Dose Escalation (Arm A3) (Maintenance only)

EXPERIMENTAL

Cohort A3: Participants with ES-SCLC who completed 4-6 cycles of carboplatin and etoposide first-line induction chemotherapy, with or without atezolizumab, were to be administered continuous maintenance therapy with Venetoclax (200mg) once daily (QD) from Day 1 to 21 and Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1. This cohort maybe explored if Dose-Limiting Toxicities (DLTs) are experienced and adverse events are thought to be potentially mitigated with a lower dose of venetoclax.

Drug: VenetoclaxDrug: Atezolizumab

Dose Escalation (Arm B1) (Induction + Maintenance)

EXPERIMENTAL

Cohort B1: Participants with ES-SCLC were to be administered non-continuous induction therapy with Venetoclax (200mg) once daily (QD) from Day 1 to 7, Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1, Carboplatin (5mg/mL/min) on Day 1 and Etoposide (100mg/m\^2) on Days 1-3. Participants who tolerated study treatment without excessive toxicity, and had not undergone disease progression were to be then proceeded to maintenance treatment with venetoclax plus atezolizumab. The venetoclax dose for the maintenance setting in Arm B will be the dose that has been cleared in the maintenance only arm (Arm A) of the study (maintenance RP2D, RP2D-M).

Drug: VenetoclaxDrug: AtezolizumabDrug: CarboplatinDrug: Etoposide

Dose Escalation (Arm B2) (Induction + Maintenance)

EXPERIMENTAL

Cohort B2: Participants with ES-SCLC were to be administered non-continuous induction therapy with Venetoclax (400mg) once daily (QD) from Day 1 to 7, Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1, Carboplatin (5mg/mL/min) on Day 1 and Etoposide (100mg/m\^2) on Days 1-3. Participants who tolerated study treatment without excessive toxicity, and had not undergone disease progression were to be then proceeded to maintenance treatment with venetoclax plus atezolizumab. The venetoclax dose for the maintenance setting in Arm B will be the dose that has been cleared in the maintenance only arm (Arm A) of the study (maintenance RP2D, RP2D-M).

Drug: VenetoclaxDrug: AtezolizumabDrug: CarboplatinDrug: Etoposide

Dose Escalation (Arm B3) (Induction + Maintenance)

EXPERIMENTAL

Cohort B3: Participants with ES-SCLC were to be administered non-continuous induction therapy with Venetoclax (800mg) once daily (QD) from Day 1 to 7, Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1, Carboplatin (5mg/mL/min) on Day 1 and Etoposide (100mg/m\^2) on Days 1-3. Participants who tolerated study treatment without excessive toxicity, and had not undergone disease progression were to be then proceeded to maintenance treatment with venetoclax plus atezolizumab. The venetoclax dose for the maintenance setting in Arm B will be the dose that has been cleared in the maintenance only arm (Arm A) of the study (maintenance RP2D, RP2D-M).

Drug: VenetoclaxDrug: AtezolizumabDrug: CarboplatinDrug: Etoposide

Dose Escalation (Arm B4) (Induction + Maintenance)

EXPERIMENTAL

Cohort B4: Participants with ES-SCLC were to be administered non-continuous induction therapy with Venetoclax (800mg) once daily (QD) from Day 1 to 14, Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1, Carboplatin (5mg/mL/min) on Day 1 and Etoposide (100mg/m\^2) on Days 1-3. Participants who tolerated study treatment without excessive toxicity, and had not undergone disease progression were to be then proceeded to maintenance treatment with venetoclax plus atezolizumab. The venetoclax dose for the maintenance setting in Arm B will be the dose that has been cleared in the maintenance only arm (Arm A) of the study (maintenance RP2D, RP2D-M).

Drug: VenetoclaxDrug: AtezolizumabDrug: CarboplatinDrug: Etoposide

Dose Expansion

EXPERIMENTAL

If the Recommended Phase II Dose (RP2D) for Venetoclax during induction is established, then the dose-expansion cohort would continue to test venetoclax in both induction and maintenance. Participants would be administered non-continuous induction therapy with Venetoclax (RP2D-I/induction RP2D), Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1, Carboplatin (5mg/mL/min) on Day 1 and Etoposide (100mg/m\^2) on Days 1-3 followed by continuous maintenance therapy with Venetoclax (RP2D-M) and Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1. If significant toxicity and DLTs in induction precluded identification of an RP2D for venetoclax in induction treatment, then the safety and efficacy of venetoclax would only be investigated in dose-expansion in the maintenance setting. Participants would be administered continuous maintenance therapy with Venetoclax (RP2D-M) and Atezolizumab (1200mg) every 3 weeks (Q3W) on Day 1.

Drug: VenetoclaxDrug: AtezolizumabDrug: CarboplatinDrug: Etoposide

Interventions

Venetoclax will be administered orally at escalating doses from 200mg to 800mg as 100mg tablets as per the dosing schedules described above.

Dose Escalation (Arm A1) (Maintenance only)Dose Escalation (Arm A2) (Maintenance only)Dose Escalation (Arm A3) (Maintenance only)Dose Escalation (Arm B1) (Induction + Maintenance)Dose Escalation (Arm B2) (Induction + Maintenance)Dose Escalation (Arm B3) (Induction + Maintenance)Dose Escalation (Arm B4) (Induction + Maintenance)Dose Expansion

Atezolizumab will be administered via intravenous (IV) infusion at a fixed dose of 1200mg as per the dosing schedules described above.

Dose Escalation (Arm A1) (Maintenance only)Dose Escalation (Arm A2) (Maintenance only)Dose Escalation (Arm A3) (Maintenance only)Dose Escalation (Arm B1) (Induction + Maintenance)Dose Escalation (Arm B2) (Induction + Maintenance)Dose Escalation (Arm B3) (Induction + Maintenance)Dose Escalation (Arm B4) (Induction + Maintenance)Dose Expansion

Carboplatin will be administered via IV infusion at a dose of 5mg/mL/min as per the dosing schedules described above.

Dose Escalation (Arm B1) (Induction + Maintenance)Dose Escalation (Arm B2) (Induction + Maintenance)Dose Escalation (Arm B3) (Induction + Maintenance)Dose Escalation (Arm B4) (Induction + Maintenance)Dose Expansion

Etoposide will be administered via IV infusion at a dose of 100mg/m\^2 as per the dosing schedules described above.

Dose Escalation (Arm B1) (Induction + Maintenance)Dose Escalation (Arm B2) (Induction + Maintenance)Dose Escalation (Arm B3) (Induction + Maintenance)Dose Escalation (Arm B4) (Induction + Maintenance)Dose Expansion

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Dose Escalation, Maintenance Arm A:
  • Participants with ES-SCLC who have completed 4-6 cycles of carboplatin and etoposide induction chemotherapy, with or without atezolizumab, as their first-line therapy for extensive-stage disease and have responded (CR or PR) or have Stable Disease (SD) are eligible for the maintenance arm of the study.
  • All side effects attributed to prior anti-cancer therapy must have resolved to Grade 1 or baseline.
  • A maximum of 8 weeks (56 days) is allowed between last chemotherapy dose (Cycle 4, Day 3) given in induction and the start of maintenance therapy.
  • Dose Escalation, Induction Arm B:
  • Participants with no prior systemic treatment for ES-SCLC are eligible for this study.
  • ANC \>= 1,500 cells/µL without granulocyte colony-stimulating factor support.
  • Dose Expansion, Maintenance-Only:
  • Participants with ES-SCLC who have completed 4 cycles of carboplatin and etoposide induction chemotherapy and at least 3 cycles of atezolizumab as their first-line therapy for extensive-stage disease and have responded (CR or PR) or have SD are eligible for the maintenance arm of the study.
  • Dose Escalation (Arms A and B) and Dose Expansion:
  • Ability to comply with the study protocol, in the investigator's judgement.
  • ECOG performance status of 0 or 1.
  • Participants must be able to swallow pills.
  • Histologically or cytologically confirmed diagnosis of ES-SCLC per the Veterans Administration Lung Study Group (VALG) staging system.
  • Participants who received prior chemoradiotherapy for limited-stage SCLC must have been treated with curative intent and experienced a treatment-free interval of at least 6 months since last chemotherapy, radiotherapy or chemoradiotherapy cycle prior to diagnosis of ES-SCLC.
  • +9 more criteria

You may not qualify if:

  • Use of non-protocol-specified anti-cancer therapies or other combination partners with carboplatin/etoposide during induction.
  • Symptomatic or actively progressing CNS metastases.
  • Pregnant or breastfeeding, or intending to become pregnant during the study.
  • Spinal cord compression not definitively treated with surgery and/or radiation or previously diagnosed and treated spinal cord compression without evidence that disease has been clinically stable for \>= 1 week prior to enrollment.
  • Leptomeningeal disease.
  • Uncontrolled pleural effusion, pericardial effusion or ascites requiring recurrent drainage procedures (once a month or more frequently).
  • Uncontrolled or symptomatic hypercalcemia.
  • History of malignancy other than SCLC within 5 years prior to enrollment.
  • History of autoimmune disease.
  • History of idiopathic pulmonary fibrosis, organizing pneumonia (e.g., bronchiolitis obliterans), drug-induced pneumonitis, idiopathic pneumonitis, or evidence of active pneumonitis on screening chest CT scan.
  • Positive HIV infection.
  • Active Hepatitis B and C infection (HBV/HCV).
  • Active Tuberculosis infection.
  • Known infection with human T-cell leukemia virus 1.
  • Known active bacterial, viral, fungal, mycobacterial, parasitic, or other infection (excluding fungal infections of nail beds) at study enrollment, or any major episode of infection requiring treatment with IV antibiotics or hospitalization.
  • +19 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Emory University

Atlanta, Georgia, 30322, United States

Location

Rigshospitalet; Onkologisk Klinik

København Ø, 2100, Denmark

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

ICO I Hospitalet Hospital Duran i Reynals Instituto Catalan de Oncologia de Hospitalet ICO

L'Hospitalet de Llobregat, Barcelona, 08908, Spain

Location

START Madrid. Centro Integral Oncologico Clara Campal; CIOCC

Madrid, 28050, Spain

Location

MeSH Terms

Conditions

Small Cell Lung Carcinoma

Interventions

venetoclaxatezolizumabCarboplatinEtoposide

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPolycyclic CompoundsGlucosidesGlycosidesCarbohydrates

Limitations and Caveats

The study was terminated by the Sponsor. Only 2 participants were enrolled in this study. Based on the low enrolment number, no data is reported here in order to protect and maintain participant privacy/confidentiality.

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 5, 2020

First Posted

June 9, 2020

Study Start

September 22, 2020

Primary Completion

November 6, 2020

Study Completion

November 6, 2020

Last Updated

November 8, 2021

Results First Posted

November 8, 2021

Record last verified: 2021-10

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to individual patient level data through the clinical study data request platform (www.vivli.org). Further details on Roche's criteria for eligible studies are available here (https://vivli.org/ourmember/roche/). For further details on Roche's Global Policy on the Sharing of Clinical Information and how to request access to related clinical study documents, see here (https://www.roche.com/research\_and\_development/who\_we\_are\_how\_we\_work/clinical\_trials/our\_commitment\_to\_data\_sharing.htm).

Locations