NCT04173494

Brief Summary

MOMENTUM is a randomized, double-blind, active control Phase 3 trial intended to confirm the differentiated clinical benefits of the investigational drug momelotinib (MMB) versus danazol (DAN) in symptomatic and anemic participants who have previously received an approved Janus kinase inhibitor (JAKi) therapy for myelofibrosis (MF). The purpose of this clinical study is to compare the effectiveness and safety of MMB to DAN in treating and reducing: 1) disease related symptoms, 2) the need for blood transfusions and 3) splenomegaly, in adults with primary MF, post-polycythemia vera MF or post-essential thrombocythemia MF. The study is planned in countries including, but not limited to: Australia, Austria, Belgium, Bulgaria, Canada, Czech Republic, Denmark, France, Germany, Hungary, Israel, Italy, New Zealand, Poland, Romania, Singapore, South Korea, Spain, Sweden, Taiwan, United Kingdom (UK) and United States (US). Participants must be symptomatic with a Myelofibrosis Symptom Assessment Form (MFSAF) version (v) 4.0 Total Symptom Score of \>= 10 at screening, and be anemic with hemoglobin (Hgb) \< 10 gram/deciliter (g/dL). For participants with ongoing JAKi therapy at screening, JAKi therapy must be tapered over a period of at least 1 week, followed by a 2-week non-treatment washout interval prior to randomization. Participants will be randomized 2:1 to orally self-administer blinded treatment: MMB plus placebo or DAN plus placebo. Participants randomized to receive MMB who complete the randomized treatment period to the end of Week 24 may continue to receive MMB in the open-label extended treatment period to the end of Week 204 (a total period of treatment of approximately 4 years) if the participants tolerates and continues to benefit from MMB. Participants randomized to receive DAN may cross-over to MMB open-label treatment in the following circumstances: at the end of Week 24 if they complete the randomized treatment period; or at the end of Week 24 if they discontinue treatment with DAN but continue study assessments and do not receive prohibited medications including alternative active anti-MF therapy; or at any time during the randomized treatment period if they meet the protocol-defined criteria for radiographically confirmed symptomatic splenic progression. Participants randomized to receive DAN who are receiving clinical benefit at the end of Week 24 may choose to continue DAN therapy up to Week 48. The comparator treatment, DAN, is an approved medication in the US and in some other countries and is recommended by national guidelines as a treatment for anemia in MF.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
195

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Feb 2020

Typical duration for phase_3

Geographic Reach
21 countries

162 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 20, 2019

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 22, 2019

Completed
3 months until next milestone

Study Start

First participant enrolled

February 7, 2020

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 3, 2021

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

December 22, 2022

Completed
7 days until next milestone

Study Completion

Last participant's last visit for all outcomes

December 29, 2022

Completed
Last Updated

November 1, 2023

Status Verified

October 1, 2023

Enrollment Period

1.8 years

First QC Date

November 20, 2019

Results QC Date

December 1, 2022

Last Update Submit

October 30, 2023

Conditions

Keywords

MyelofibrosisJAK inhibitorDanazolMomelotinibFunctional Iron deficiencyActivin receptor type 1AnemiaTransfusionHepcidinMyeloproliferative DisordersBone Marrow DiseasesHematologic Diseases

Outcome Measures

Primary Outcomes (1)

  • Total Symptom Score (TSS) Response Rate at Week 24

    Myelofibrosis Symptom Assessment Form (MFSAF) TSS version (v) 4.0 response rate was defined as percentage of participants with a \>= 50 percent (%) reduction from Baseline in mean MFSAF TSS over consecutive 28-day period immediately before end of Week 24. TSS response rate was measured using MFSAF v4.0. MFSAF v4.0 comprises 7 domains representing 7 most relevant symptoms of myelofibrosis (MF) identified through existing participant and clinician-based evidence: fatigue,night sweats,pruritus,abdominal discomfort,pain under left ribs,early satietyand bone pain. Participants scored each symptom domain using an 11-point numeric rating scale ranging from 0(absent) to 10(worst imaginable). The MFSAF TSS was calculated as sum of scores of 7 domains for a possible range of scores of 0 to 70, with a higher TSS corresponding to more severe symptoms. A reduction from Baseline corresponded to a lessening of MF symptoms. Baseline was the last assessment done before or on the day of first dose date.

    Baseline and Week 24

Secondary Outcomes (20)

  • Percentage of Participants With Transfusion Independence (TI) at Week 24

    Week 24

  • Splenic Response Rate (SRR) of >=25% at Week 24

    Baseline and Week 24

  • Change From Baseline in MFSAF TSS at Week 24

    Baseline and Week 24

  • Splenic Response Rate (SRR) of >= 35% at Week 24

    Baseline and Week 24

  • Percentage of Participants With Zero RBC Units Transfused Over 24-Weeks

    Up to 24 weeks

  • +15 more secondary outcomes

Study Arms (2)

Momelotinib

EXPERIMENTAL

Participants will receive momelotinib plus placebo to match danazol

Drug: MomelotinibDrug: Placebo to match danazol

Danazol

ACTIVE COMPARATOR

Participants will receive danazol plus placebo to match momelotinib

Drug: DanazolDrug: Placebo to match momelotinib

Interventions

Momelotinib tablets will be self-administered orally once daily

Also known as: MMB, GS-0387, CYT387
Momelotinib

Danazol placebo capsules will be self-administered orally twice daily

Momelotinib

Danazol capsules will be self-administered orally twice daily

Also known as: Danocrine
Danazol

Momelotinib placebo tablets will be self-administered orally once daily

Danazol

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age \>= 18 years.
  • Confirmed diagnosis of PMF in accordance with the World Health Organization (WHO) 2016 criteria, or Post- polycythemia vera/essential thrombocythemia (PV/ET) MF in accordance with the International Working Group-Myeloproliferative Neoplasms Research and Treatment (IWG-MRT criteria).
  • Symptomatic, defined as a TSS of \>= 10 units assessed by a single MFSAF v4.0 assessment during Screening prior to Baseline period (Day BL1).
  • Anemic, defined as a Hgb \< 10 g/dL in Screening/Baseline period.
  • Previously treated with an approved JAK inhibitor for PMF or Post-PV/ET MF for \>= 90 days, or \>= 28 days if JAK inhibitor therapy is complicated by RBC transfusion requirement of \>= 4 units in 8 weeks, or Grade 3/4 AEs of thrombocytopenia, anemia, or hematoma.
  • Baseline splenomegaly, defined as having a palpable spleen at \>= 5 centimeter (cm), below the left costal margin, or with volume \>= 450 cubic centimeter (cm\^3) on imaging (ultrasound, magnetic resonance imaging \[MRI\] or computed tomography \[CT\] are acceptable), assessed during Screening at any point prior to Randomization.
  • High risk, intermediate-2, or intermediate-1 risk MF as defined by Dynamic International Prognostic Scoring System (DIPSS), or DIPSS-plus.
  • No allogeneic stem cell transplant planned.
  • Acceptable laboratory assessments:
  • Absolute neutrophil count (ANC) \>= 0.75 × 10\^9/Liter (L).
  • Platelet count (PLT) \>= 25 × 10\^9/L (without requirement for platelet transfusion).
  • Peripheral blast count \< 10%.
  • Alanine aminotransferase/ glutamic-oxaloacetic transaminase (AST/SGOT) and alanine aminotransferase/ serum glutamic-pyruvic transaminase (ALT/SGPT) \<= 3 × Upper Limit Normal (ULN) (\<= 5 × ULN if liver is involved by extramedullary hematopoiesis as judged by the investigator or if related to iron chelator therapy that was started within the prior 60 days).
  • Calculated creatinine clearance (CCr) \>= 30 milliliter per minute (mL/min) according to Cockcroft-Gault.
  • Direct bilirubin \<= 2.0 × ULN.

You may not qualify if:

  • Use of the following treatments within the time periods noted:
  • Prior momelotinib treatment at any time.
  • Approved JAK inhibitor therapy (eg, fedratinib or ruxolitinib) within 1 week prior to the first day of Baseline.
  • Active anti-MF therapy within 1 week prior to the first day of Baseline.
  • Potent Cytochrome P450 3A4 (CYP3A4) inducers within 1 week prior to Randomization.
  • Investigational agent (including investigational JAK inhibitors) within 4 weeks prior to Randomization.
  • Erythropoiesis stimulating agent (ESA) within 4 weeks prior to Randomization.
  • Danazol within 3 months prior to Randomization.
  • Splenic irradiation within 3 months prior to Randomization.
  • Current treatment with simvastatin, atorvastatin, lovastatin or rosuvastatin.
  • History of prostate cancer, with the exception of localized prostate cancer that has been treated surgically or by radiotherapy with curative intent and presumed cured.
  • Prostate specific antigen (PSA) \> 4 nanograms per milliliter (ng/mL).
  • Unsuitable for spleen volume measurements due to prior splenectomy or unwilling or unable to undergo an MRI scan or CT scan for spleen volume measurement per protocol requirements.
  • Any of the following (criteria a - k):
  • Uncontrolled intercurrent illness including, but not limited to: active uncontrolled infection (participants receiving outpatient antibacterial and/or antiviral treatments for infection that is under control or as infection prophylaxis may be included in the trial).
  • +16 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (167)

Mayo Clinic Hospital - Phoenix

Phoenix, Arizona, 85054, United States

Location

Irvine Center for Clinical Research

Irvine, California, 92614, United States

Location

Norris Comprehensive Cancer Center

Los Angeles, California, 91011, United States

Location

American Institute of Research - Whittier

Whittier, California, 90603, United States

Location

University of Colorado Hospital Anschutz Cancer Pavilion

Aurora, Colorado, 80045, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20057, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Northwest Oncology & Hematology - Rolling Meadows

Rolling Meadows, Illinois, 60008, United States

Location

Washington University School of Medicine in Saint Louis

St Louis, Missouri, 63110, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Columbia University Irving Medical Center - Presbyterian Hospital

New York, New York, 10032, United States

Location

Cleveland Clinic - Richard E. Jacobs Health Center

Avon, Ohio, 44011, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Allegheny Health Network

Pittsburgh, Pennsylvania, 15224, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

The University of Texas Health Science Center at San Antonio

San Antonio, Texas, 78229, United States

Location

Canberra Region Cancer Centre

Garran, Australian Capital Territory, 2605, Australia

Location

Calvary Mater Newcastle Hospital

Waratah, New South Wales, 2298, Australia

Location

Flinders Medical Centre

Bedford Park, South Australia, 5042, Australia

Location

The Alfred Hospital

Melbourne, Victoria, 3004, Australia

Location

Perth Radiological Clinic - Magnetic Resonance Centre

Perth, Western Australia, 6000, Australia

Location

Medizinische Universität Innsbruck

Innsbruck, Tyrol, 6020, Austria

Location

Ordensklinikum Linz Elisabethinen

Linz, Upper Austria, 4020, Austria

Location

Medizinische Universität Wien

Vienna, Vienna, 1090, Austria

Location

Oberösterreichische Gesundheitsholding GmbH

Steyr, 4400, Austria

Location

Hôpital Erasme

Brussels, Brussels Capital, 1070, Belgium

Location

Grand Hôpital de Charleroi - Notre Dame

Charleroi, Hainaut, 6000, Belgium

Location

Algemeen Ziekenhuis Sint-Jan Brugge-Oostende - Campus Sint-Jan

Bruges, West-Vlaanderen, 8000, Belgium

Location

Ziekenhuis Netwerk Antwerpen Stuivenberg

Antwerp, 2060, Belgium

Location

Centre Hospitalier Universitaire de Liège

Liège, B-4000, Belgium

Location

University Multiprofile Hospital For Active Treatment Dr. Georgi Stranski EAD

Pleven, 5800, Bulgaria

Location

University Hospital St. Ivan Rilski

Sofia, 1431, Bulgaria

Location

University Multiprofile Hospital For Active Treatment Aleksandrovska

Sofia, 1431, Bulgaria

Location

National Specialized Hospital for Active Treatment of Haematologic Diseases

Sofia, 1756, Bulgaria

Location

Saint Paul's Hospital

Vancouver, British Columbia, V6Z 1Y6, Canada

Location

Queen Elizabeth II Health Sciences Centre - Halifax Infirmary

Halifax, Nova Scotia, B3H 1V7, Canada

Location

McMaster University Medical Center

Hamilton, Ontario, L8V 5C2, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Research Institute of the McGill University Health Centre

Montreal, Quebec, H3H 2R9, Canada

Location

Hôpital de l'Enfant-Jésus

Québec, G1J 1Z4, Canada

Location

Fakultni Nemocnice Brno

Brno, Jihormoravsky Kraj, 625 00, Czechia

Location

Herlev Hospital

Herlev, Capital Region, 2730, Denmark

Location

Aalborg Universitetshospital - Syd

Aalborg, North Denmark, 9000, Denmark

Location

Sjællands Universitetshospital - Roskilde

Roskilde, Region Sjælland, 4000, Denmark

Location

Odense Universitetshospital

Odense, Region Syddanmark, 5000, Denmark

Location

Hôpital Haut-Lévêque

Pessac, Aquitaine, 33604, France

Location

Hospital Center University Of Caen Normandie

Caen, Basse-Normandie, 14033, France

Location

Hôpital Claude Huriez

Lille, Hauts-de-France, 59037, France

Location

Centre Hospitalier Universitaire Limoges

Limoges, Limousin, 87042, France

Location

Centre Hospitalier De Lens

Lens, Nord Pas-Des-Calais, 62307, France

Location

Centre Hospitalier Le Mans

Le Mans, Pays de la Loire Region, 72037, France

Location

Centre Hospitalier Universitaire Amiens-Picardie - Site Sud

Amiens, Picardie, 80054, France

Location

Hôpital l'Archet

Nice, Provence-Alpes-Côte d'Azur Region, 06200, France

Location

Centre Hospitalier Lyon-Sud

Pierre-Bénite, Rhone-Alps, 69495, France

Location

Centre Hosptitalier Universitaire Angers

Angers, 49 933, France

Location

Hôpital Saint-Vincent De Paul - Lille

Lille, 59000, France

Location

Hôpital De La Conception

Marseille, 13385, France

Location

Hôpital Emile Muller

Mulhouse, 68100, France

Location

Centre Hospitalier Universitaire Nantes - Hôtel Dieu

Nantes, 44000, France

Location

Centre Hospitalier Universitaire de Poitiers

Poitiers, 86021, France

Location

Hôpital Saint-Louis

Paris, Île-de-France Region, 75010, France

Location

Hôpital Saint-Antoine

Paris, Île-de-France Region, 75571, France

Location

Universitätsklinikum Aachen

Aachen, North Rhine-Westphalia, 52074, Germany

Location

Universitätsklinikum Essen

Essen, North Rhine-Westphalia, 45147, Germany

Location

Johannes Wesling Klinikum Minden

Minden, North Rhine-Westphalia, 32429, Germany

Location

Universitätsklinikum Carl Gustav Carus Dresden

Dresden, Saxony, 01307, Germany

Location

Universitätsklinikum Leipzig

Leipzig, Saxony, 04103, Germany

Location

Universitätsklinikum Halle

Halle, Saxony-Anhalt, 06120, Germany

Location

Universitätsklinikum Jena

Jena, Thuringia, 07747, Germany

Location

Uniklinik Köln

Cologne, 50937, Germany

Location

Universitätsklinikum Schleswig-Holstein - Campus Lübeck

Lübeck, 23538, Germany

Location

Kliniken Ostalb - Stauferklinikum Schwäbisch Gmünd

Mutlangen, 73557, Germany

Location

Pécsi Tudományegyetem Klinikai Központ

Pécs, Baranya, 7624, Hungary

Location

Debreceni Egyetem Klinikai Központ

Debrecen, Hajdú-Bihar, 4032, Hungary

Location

Szent Borbála Kórház

Tatabánya, Komárom-Esztergom, 2800, Hungary

Location

Dél-pesti Centrumkórház - Országos Hematológiai és Infektológiai Intézet - Szent László Telephely

Budapest, Pest County, 1097, Hungary

Location

Somogy Megyei Kaposi Mór Oktató Kórház

Kaposvár, Somogy County, 7400, Hungary

Location

Szabolcs-Szatmár-Bereg Megyei Kórházak És Egyetemi Oktatókórház

Nyíregyháza, Szabolcs-Szatmár-Bereg, 4400, Hungary

Location

Markusovszky Egyetemi Oktatókórház Szombathely

Szombathely, Vas County, 9700, Hungary

Location

Semmelweis Egyetem

Budapest, 1083, Hungary

Location

Petz Aladár Megyei Oktató Kórház

Győr, 9023, Hungary

Location

Yitzhak Shamir Medical Center

Be’er Ya‘aqov, Central District, 7030000, Israel

Location

Bnai Zion Medical Center

Haifa, Haifa District, 31048, Israel

Location

Hadassah University Hospital Ein Kerem

Jerusalem, Jerusalem, Israel

Location

Rambam Health Care Campus

Haifa, 3109601, Israel

Location

Carmel Medical Center

Haifa, 3436212, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 9103102, Israel

Location

Meir Medical Center

Kfar Saba, 4428164, Israel

Location

Western Galilee Hospital-Nahariya

Nahariya, Israel

Location

Rabin Medical Center - Beilinson Hospital

Petah Tikva, 4941492, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, Israel

Location

Azienda Ospedaliero - Universitaria Careggi

Florence, Florence, 50134, Italy

Location

Ospedale Casa Sollievo della Sofferenza

San Giovanni Rotondo, Foggia, 71013, Italy

Location

Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori

Meldola, Forli-Cesena, 47014, Italy

Location

Azienda Socio Sanitaria Territoriale Monza - Ospedale San Gerardo

Monza, Monza E Brianza, 20900, Italy

Location

Azienda Ospedaliera Ospedali Riuniti Marche Nord

Pesaro, Pesaro E Urbino, 61121, Italy

Location

IRCCS Centro di Riferimento Oncologico di Basilicata

Rionero in Vulture, Potenza, 85028, Italy

Location

Azienda Ospedaliero-Universitaria Citta della Salute e della Scienza di Torino

Torino, Turin, 10126, Italy

Location

Azienda Ospedaliera Ordine Mauriziano di Torino

Torino, Turin, 10128, Italy

Location

Azienda Ospedaliera Nazionale SS. Antonio e Biagio e C. Arrigo - Alessandria

Alessandria, 15121, Italy

Location

Azienda Ospedaliero-Universitaria di Bologna Policlinico Sant Orsola-Malpighi

Bologna, 40138, Italy

Location

Ospedale Policlinico San Martino

Genova, 16132, Italy

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, 20122, Italy

Location

Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

Azienda Ospedaliera Universitaria Federico II

Napoli, 80131, Italy

Location

Azienda Ospedaliero-Universitaria Maggiore della Carità di Novara

Novara, 28100, Italy

Location

Umberto I - Policlinico di Roma

Roma, 00161, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli

Roma, 20123, Italy

Location

Presidio Ospedaliero Universitario Santa Maria della Misericordia

Udine, 33100, Italy

Location

Ospedale di Circolo e Fondazione Macchi

Varese, 21100, Italy

Location

Ospedale Policlinico Giambattista Rossi Borgo Roma

Verona, 37134, Italy

Location

North Shore Hospital

Auckland, 0622, New Zealand

Location

Middlemore Clinical Trials

Auckland, 2025, New Zealand

Location

Szpital Uniwersytecki w Krakowie

Krakow, Lesser Poland Voivodeship, 31-501, Poland

Location

Szpital Specjalistyczny im. Ludwika Rydygiera w Krakowie

Krakow, Lesser Poland Voivodeship, 31-826, Poland

Location

Klinika Hematologii Nowotworów Krwi i Transplantacji Szpiku

Wroclaw, Lower Silesian Voivodeship, 50-367, Poland

Location

Samodzielny Publiczny Szpital Kliniczny nr 1 w Lublinie

Lublin, Lublin Voivodeship, 20-081, Poland

Location

Instytut Hematologii I Transfuzjologii

Warsaw, Masovian Voivodeship, 02-776, Poland

Location

Alvamed Zakład Specjalistycznej Opieki Zdrowotnej

Warsaw, Masovian Voivodeship, 03-401, Poland

Location

Szpital Wojewódzki w Opolu

Opole, Opole Voivodeship, 45-064, Poland

Location

Uniwersyteckie Centrum Kliniczne w Gdańsku

Gdansk, Pomeranian Voivodeship, 80-214, Poland

Location

Silesian Healthy Blood Clinic

Chorzów, Salskie, 41-503, Poland

Location

Wojewódzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im. M. Kopernika w Łodzi

Lodz, 93-513, Poland

Location

Spitalul Filantropia - Craiova

Craiova, Dolj, 200143, Romania

Location

Institutul Regional De Oncologie Iasi

Iași, Iaşi, 700483, Romania

Location

Spitalul Clinic Judetean De Urgenta Târgu Mureș

Târgu Mureş, Mureș County, 540136, Romania

Location

Laboratul clinic MedLife-Policlinica de Diagnostic Rapid Brasov

Brasov, 500366, Romania

Location

Coltea - Spital Clinic

Bucharest, 030 171, Romania

Location

Singapore General Hospital

Singapore, 169608, Singapore

Location

Tan Tock Seng Hospital

Singapore, 308433, Singapore

Location

Kyungpook National University Hospital

Daegu, Daegu Gwang'yeogsi, 41944, South Korea

Location

Inje University Busan Paik Hospital

Busan, 47392, South Korea

Location

Inje University Haeundae Paik Hospital

Busan, 48108, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, 13620, South Korea

Location

Severance Hospital

Seoul, 03722, South Korea

Location

The Catholic University of Korea Seoul Saint Mary's Hospital

Seoul, 06591, South Korea

Location

Samsung Medical Center

Seoul, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

Ulsan University Hospital

Ulsan, 44033, South Korea

Location

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, 33011, Spain

Location

Institut Hospital del Mar d'Investigacions Mèdiques

Barcelona, 08003, Spain

Location

Hospital Universitari Vall d'Hebrón

Barcelona, 08035, Spain

Location

Hospital Germans Trias i Pujol

Barcelona, 08916, Spain

Location

Hospital San Pedro de Alcantara

Cáceres, 10003, Spain

Location

Institut Català d'Oncologia Girona

Girona, 17007, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, 29010, Spain

Location

Complejo Asistencial Universitario de Salamanca - Hospital Clínico

Salamanca, 37007, Spain

Location

Hospital Universitario Virgen del Rocío

Seville, 41013, Spain

Location

Hospital Universitario La Fe

Valencia, 46009, Spain

Location

Hospital de Día Quirónsalud Zaragoza

Zaragoza, 50012, Spain

Location

Karolinska Universitetssjukhuset Solna

Solna, Stockholm County, 171 76, Sweden

Location

Sahlgrenska Universitetssjukhuset

Gothenburg, Västra Götaland County, 413 45, Sweden

Location

Uddevalla Sjukhus

Uddevalla, 45153, Sweden

Location

Chiayi Chang Gung Memorial Hospital

Buzi, Chaiyi, 613, Taiwan

Location

China Medical University Hospital

Taichung, Taichung, 40447, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

Chang Gung Memorial Hospital - Linkou Branch

Taoyuan District, 333, Taiwan

Location

United Lincolnshire Hospitals NHS Trust

Boston, England, PE21 9QS, United Kingdom

Location

University Hospitals Bristol NHS Foundation Trust

Bristol, England, BS2 8ED, United Kingdom

Location

University College London Hospitals NHS Foundation Trust

London, England, NW1 2PG, United Kingdom

Location

Guy's and Saint Thomas' NHS Foundation Trust

London, England, SE1 9RT, United Kingdom

Location

Imperial College Healthcare NHS Trust

London, England, W12 0HS, United Kingdom

Location

University Hospital Southampton NHS Foundation Trust

Southampton, England, SO16 6YD, United Kingdom

Location

NHS Lanarkshire

Airdrie, Scotland, ML6 0JS, United Kingdom

Location

Related Publications (6)

  • Yoon SS, Chen CC, Lee SE, Chang H, Cheong JW, Hou HA, Lee WS, Lim SN, Moon JH, Ong KH, Dai Y, Liu C, Kawashima J, Goh YT. Efficacy and safety of momelotinib in Janus kinase inhibitor-experienced Asian patients with myelofibrosis and anemia. Int J Hematol. 2025 Nov;122(5):660-670. doi: 10.1007/s12185-025-04037-6. Epub 2025 Jul 21.

  • Mesa RA, Talpaz M, Mazerolle F, Gorsh B, M'Hari M, Regnault A, Ellis C, Wang Z, Purser M, Liu T, Strouse B, Patnaik D. Time Without Transfusion Reliance (TWiTR): Integrating Survival Quality Into Myelofibrosis Treatment Strategies Based on the Phase 3 SIMPLIFY-1, SIMPLIFY-2, and MOMENTUM Trials. EJHaem. 2025 Jun 18;6(3):e70075. doi: 10.1002/jha2.70075. eCollection 2025 Jun.

  • Harrison CN, Mesa R, Talpaz M, Gupta V, Gerds AT, Perkins A, Goh YT, Fox ML, McLornan D, Palmer J, Foltz L, Vannucchi A, Koschmieder S, Passamonti F, Lee SE, Ellis C, Strouse B, Gonzalez Carreras FJ, Oh ST. Longitudinal Assessment of Transfusion Intensity in Patients With JAK Inhibitor-Naive or -Experienced Myelofibrosis Treated With Momelotinib. Clin Lymphoma Myeloma Leuk. 2025 Mar;25(3):199-211. doi: 10.1016/j.clml.2024.10.001. Epub 2024 Oct 16.

  • Gerds AT, Verstovsek S, Vannucchi AM, Al-Ali HK, Lavie D, Kuykendall AT, Grosicki S, Iurlo A, Goh YT, Lazaroiu MC, Egyed M, Fox ML, McLornan D, Perkins A, Yoon SS, Gupta V, Kiladjian JJ, Granacher N, Lee SE, Ocroteala L, Passamonti F, Harrison CN, Oh S, Klencke BJ, Yu J, Donahue R, Kawashima J, Mesa R. Momelotinib versus danazol in symptomatic patients with anaemia and myelofibrosis previously treated with a JAK inhibitor (MOMENTUM): an updated analysis of an international, double-blind, randomised phase 3 study. Lancet Haematol. 2023 Sep;10(9):e735-e746. doi: 10.1016/S2352-3026(23)00174-6. Epub 2023 Jul 27.

  • Verstovsek S, Mesa R, Gupta V, Lavie D, Dubruille V, Cambier N, Platzbecker U, Hus M, Xicoy B, Oh ST, Kiladjian JJ, Vannucchi AM, Gerds A, Egyed M, Mayer J, Sacha T, Kawashima J, Morris M, Huang M, Harrison C. Momelotinib long-term safety and survival in myelofibrosis: integrated analysis of phase 3 randomized controlled trials. Blood Adv. 2023 Jul 25;7(14):3582-3591. doi: 10.1182/bloodadvances.2022009311.

  • Verstovsek S, Gerds AT, Vannucchi AM, Al-Ali HK, Lavie D, Kuykendall AT, Grosicki S, Iurlo A, Goh YT, Lazaroiu MC, Egyed M, Fox ML, McLornan D, Perkins A, Yoon SS, Gupta V, Kiladjian JJ, Granacher N, Lee SE, Ocroteala L, Passamonti F, Harrison CN, Klencke BJ, Ro S, Donahue R, Kawashima J, Mesa R; MOMENTUM Study Investigators. Momelotinib versus danazol in symptomatic patients with anaemia and myelofibrosis (MOMENTUM): results from an international, double-blind, randomised, controlled, phase 3 study. Lancet. 2023 Jan 28;401(10373):269-280. doi: 10.1016/S0140-6736(22)02036-0.

MeSH Terms

Conditions

Primary MyelofibrosisAnemiaMyeloproliferative DisordersBone Marrow DiseasesHematologic Diseases

Interventions

N-(cyanomethyl)-4-(2-((4-(4-morpholinyl)phenyl)amino)-4-pyrimidinyl)benzamideDanazol

Condition Hierarchy (Ancestors)

Hemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

PregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Results Point of Contact

Title
GSK Response Center
Organization
Sierra Oncology LLC - a GSK company

Study Officials

  • Srdan Verstovsek, M.D., Ph.D.

    Department of Leukemia, The University of Texas MD Anderson Cancer Center

    PRINCIPAL INVESTIGATOR
  • Ruben Mesa

    UT Health San Antonio Cancer Center, San Antonio, TX, USA

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
During the 24 week randomized treatment phase of the study, participants, investigators and sponsor and relevant vendor personnel (with the exception of specified unblinded personnel, for example clinical supply) will remain blinded to the participant's treatment assignment and to aggregate data that may lead to inadvertent unblinding. Participants who continue treatment with momelotinib or danazol after Week 24 in the extended treatment phase will receive unblinded treatment.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 20, 2019

First Posted

November 22, 2019

Study Start

February 7, 2020

Primary Completion

December 3, 2021

Study Completion

December 29, 2022

Last Updated

November 1, 2023

Results First Posted

December 22, 2022

Record last verified: 2023-10

Data Sharing

IPD Sharing
Will not share

Locations