NCT03165734

Brief Summary

This study (study ID PAC203 North America; PAC303 ex-North America) is evaluating 200 mg BID of pacritinib compared to physician's choice (P/C) therapy in patients with MF and severe thrombocytopenia (platelet count \<50,000/μL). Approximately 399 patients in total will be enrolled, randomized 2:1 to either pacritinib (approximately 266 patients) or to P/C therapy (approximately 133 patients) Condition or disease: Primary Myelofibrosis/Post-Polycythemia Vera Myelofibrosis/ Post-essential Thrombocythemia Myelofibrosis Intervention/treatment: Drug-Pacritinib

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
407

participants targeted

Target at P50-P75 for phase_3

Timeline
30mo left

Started Jun 2017

Longer than P75 for phase_3

Geographic Reach
24 countries

207 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
Jun 2017Oct 2028

First Submitted

Initial submission to the registry

May 17, 2017

Completed
7 days until next milestone

First Posted

Study publicly available on registry

May 24, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

June 26, 2017

Completed
9.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 5, 2026

Expected
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 13, 2028

Last Updated

April 30, 2026

Status Verified

October 1, 2025

Enrollment Period

9.3 years

First QC Date

May 17, 2017

Last Update Submit

April 27, 2026

Conditions

Keywords

myelofibrosispacritinibPost-polycythemia Vera MyelofibrosisPost-essential Thrombocythemia MyelofibrosisRuxolitinibBone Marrow DiseaseHematologic DiseasesBlood Platelet DisordersHemorrhagic DisordersSplenomegalyAnemiaSpleen volumeSpleen

Outcome Measures

Primary Outcomes (2)

  • Spleen volume

    To compare the efficacy of pacritinib with that of physician's choice (P/C) therapy, as assessed by the proportion of patients achieving a ≥35% spleen volume reduction (SVR) as measured by magnetic resonance imaging (MRI, preferred) or computed tomography (CT) scans

    From baseline at 24 weeks

  • Total Symptom Score (TSS) (excluding tiredness)

    To compare the efficacy of pacritinib compared to P/C therapy, as assessed by the proportion of patients achieving a ≥50% reduction in Total Symptom Score (TSS). The TSS is the sum of the individual symptom scores for tiredness, early satiety, abdominal discomfort, night sweats, pruritus, bone pain, and pain under ribs on the left side. Symptoms are ranked 0 (absent) to 10 (worst imaginable)

    From baseline at Week 24

Secondary Outcomes (3)

  • Overall Survival (OS)

    until 2.5 years after the date of randomization

  • Patient Global Impression of Change (PGIC) assessed at Week 24

    End of Week 12 to 2 years following Week 24 visit

  • To compare the safety of pacritinib versus P/C therapy

    Randomization through 30 after last treatment

Other Outcomes (15)

  • SVR of ≥35%

    Up to 24 Weeks

  • Best response in SVR

    At 24 Weeks

  • >25% SVR

    From baseline and at Week 24

  • +12 more other outcomes

Study Arms (2)

Pacritinib 200 mg BID

EXPERIMENTAL

To receive pacritinib 200 mg twice daily (BID) orally, at the same time of day, with or without food

Drug: Pacritinib

Physician's Choice (P/C) therapy

ACTIVE COMPARATOR

The Physician's Choice (P/C) therapy (limited to single drugs from the following list: corticosteroids, hydroxyurea, danazol, or low-dose ruxolitinib). The proposed P/C regimen for a patient must be selected prior to randomization.

Drug: Physician's Choice medications

Interventions

Oral administration. Supplied in capsules containing 100 mg (as the free base) in red cap/gray body size 0 opaque hard gelatin capsules. The inactive ingredients are microcrystalline cellulose, magnesium stearate, and polyethylene glycol 8000. Each capsule contains 146 mg of pacritinib citrate, which is equivalent to 100 mg pacritinib free base

Pacritinib 200 mg BID

Physician's Choice medications will be selected and administered according to the investigator's judgement. Investigators can select individual P/C agents but cannot combine agents or give them sequentially.

Also known as: corticosteroids, hydroxyurea, danazol, low-dose ruxolitinib
Physician's Choice (P/C) therapy

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Primary MF, post-polycythemia vera MF, or post-essential thrombocythemia MF (as defined by Tefferi and Vardiman 2008)
  • Platelet count of \<50,000/μL at Screening (Day -35 to Day -3)
  • Dynamic International Prognostic Scoring System Intermediate-1, Intermediate-2, or High-Risk (Passamonti et al 2010)
  • Palpable splenomegaly ≥5 cm below the lower costal margin in the midclavicular line as assessed by physical examination
  • TSS of ≥10 on the MPN-SAF TSS 2.0 or a single symptom score of ≥5 or two symptoms of ≥3, including only the symptoms of left upper quadrant pain, bone pain, itching, or night sweats. The TSS criteria need only to be met on a single day.
  • Age ≥18 years
  • Eastern Cooperative Oncology Group performance status 0 to 2
  • Peripheral blast count of \<10% throughout the Screening period prior to randomization
  • Absolute neutrophil count of ≥500/µL
  • Left ventricular cardiac ejection fraction of ≥50% by echocardiogram or multigated acquisition scan
  • Adequate liver and renal function, defined by liver transaminases (aspartate aminotransferase \[AST\]/serum glutamic-oxaloacetic transaminase \[SGOT\] and alanine aminotransferase \[ALT\]/serum glutamic pyruvic transaminase \[SGPT\]) ≤3 × the upper limit of normal (ULN) (AST/ALT ≤5 × ULN if transaminase elevation is related to MF), total bilirubin ≤4 x ULN (in cases where total bilirubin is elevated, direct bilirubin ≤4 × ULN, is required) and creatinine ≤2.5 mg/dL
  • Adequate coagulation defined by prothrombin time/international normalized ratio and partial thromboplastin time ≤1.5 × ULN
  • If fertile, willing to use highly effective birth control methods during the study (see Section 7.1.2.6 for acceptable birth control methods)
  • Willing to undergo and able to tolerate frequent MRI or CT scan assessments during the study
  • Able to understand and willing to complete symptom assessments using a patient-reported outcome instrument
  • +1 more criteria

You may not qualify if:

  • Life expectancy \<6 months
  • Completed allogeneic stem cell transplant or are eligible for and willing to complete other approved available therapy including allogeneic stem cell transplant
  • History of splenectomy or planning to undergo splenectomy
  • Splenic irradiation within the last 6 months
  • Previously treated with pacritinib
  • Treatment with any MF-directed therapy within 14 days prior to treatment Day 1
  • Prior treatment with more than one JAK2 inhibitor
  • Prior treatment with with ruxolitinib, if BOTH of the following conditions are met:
  • i. exposure to higher-dose ruxolitinib (\>10 mg daily) within 120 days prior to treatment Day 1 AND ii. total duration of treatment with higher-dose ruxolitinib (\>10 mg daily) was \>90 days, from first to last exposure (i.e., this 90-day period starts on the date of first administration of ruxolitinib at a total daily dose of \>10 mg and continues for 90 calendar days, regardless of whether higher-dose ruxolitinib is administered continuously or intermittently).
  • Prior treatment with any JAK2 inhibitor other than ruxolitinib, irrespective of dose, with a duration of \>90 days. The 90-day period starts on the date of first administration of JAK2 inhibitor therapy and continues for 90 calendar days, regardless of whether therapy is administered continuously or intermittently.
  • Treatment with an experimental therapy, including MF-directed experimental therapies within 28 days prior to treatment Day 1
  • Systemic treatment with a strong cytochrome P450 3A4 (CYP 3A4) inhibitor or a strong CYP 3A4 inducer within 14 days prior to treatment Day 1. Shorter washout periods may be permitted with approval of the Medical Monitor, provided that the washout period is at least five half-lives of the drug prior to treatment Day 1
  • Significant recent bleeding history defined as National Cancer Institute Common Terminology Criteria for Adverse Events (CTCAE) grade ≥2 within 3 months prior to treatment Day 1, unless precipitated by an inciting event (eg, surgery, trauma, or injury)
  • Systemic treatment with medications that increase the risk of bleeding, including anticoagulants, antiplatelet agents (except for aspirin dosages of ≤100 mg per day),and daily use of cyclooxygenase-1 (COX-1) inhibiting non-steroidal anti-inflammatory drugs (NSAIDs) within 14 days prior to treatment Day 1. Treatment with systemic anti-vascular endothelial growth factor (anti-VEGF) agents within 28 days prior to treatment Day 1.
  • Systemic treatment with medications that can prolong the QT interval within 14 days prior to treatment Day 1. Shorter washout periods may be permitted with approval of the Medical Monitor, provided that the washout period is at least five half-lives of the drug prior to treatment Day 1
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (207)

University of Alabama at Birmingham, (UAB) Hospital, Comprehensive Cancer Center

Birmingham, Alabama, 35294, United States

Location

Mayo Clinic Hospital

Phoenix, Arizona, 85054, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

USC Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

UCLA David Geffen School of Medicine

Los Angeles, California, 90095, United States

Location

University of Colorado Cancer Center

Aurora, Colorado, 80045, United States

Location

Rocky Mountain Cancer Centers (US Oncology/McKesson)

Boulder, Colorado, 80303, United States

Location

Yale School of Medicine

New Haven, Connecticut, 06510, United States

Location

Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

George Washington University-Medical Faculty Associates

Washington D.C., District of Columbia, 20037, United States

Location

Cleveland Clinic Florida

Weston, Florida, 33331, United States

Location

Northwestern Memorial Hospital

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

The University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

University of Kansas Cancer Center and Medical Pavilion

Westwood, Kansas, 66205, United States

Location

Ochsner Medical Center

New Orleans, Louisiana, 70121, United States

Location

Saint Agnes Hospital

Baltimore, Maryland, 21229, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21287, United States

Location

American Oncology Partners of Maryland, PA

Bethesda, Maryland, 20817, United States

Location

Regional Cancer Care Associates LLC - CCBD Division

Bethesda, Maryland, 20817, United States

Location

Maryland Oncology Hematology, PA- Columbia

Columbia, Maryland, 21044, United States

Location

Michigan Medicine Hematology Clinic-Rogel Cancer Center

Ann Arbor, Michigan, 48109, United States

Location

Cancer and Hematology Centers of Western Michigan

Grand Rapids, Michigan, 49546, United States

Location

Washington University School of Medicine-Siteman Cancer Center

St Louis, Missouri, 63110, United States

Location

Comprehensive Cancer Centers of Nevada- Twain Office

Las Vegas, Nevada, 89169, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Columbia University Medical Center

New York, New York, 10017, United States

Location

Weill Cornell Medical College

New York, New York, 10021, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Memorial Sloan -Kettering Cancer Center

New York, New York, 10065, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

Duke University Hospital

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44106, United States

Location

The James Cancer Hospital and Solove Research Institute

Columbus, Ohio, 43210, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239-3098, United States

Location

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

The Sarah Cannon Research Institute-Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Mays Cancer Center

San Antonio, Texas, 78229, United States

Location

Texas Oncology- San Antonio

San Antonio, Texas, 78240, United States

Location

University of Utah - Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Westmead Hospital

Sydney, New South Wales, Australia

Location

Alfred Hospital, Malignant Hematology and Stem Cell Transplantation Service

Melbourne, Victoria, Australia

Location

The Perth Blood Institute

Perth, Western Australia, Australia

Location

Grodno University Hospital

Grodno, Belarus

Location

Republican Research Center for Radiation Medicine and Human Ecology

Homyel, Belarus

Location

Minsk Scientific and Practical Center of Surgery, Transplantology and Hematology

Minsk, Belarus

Location

University Clinical Centre of the Republic of Srpska

Banja Luka, Bosnia and Herzegovina

Location

University Clinical Center of Sarajevo

Sarajevo, Bosnia and Herzegovina

Location

Integrare Therapeutics

Fortaleza, Ceará, Brazil

Location

Hospital Sao Rafael

Salvador, Estado de Bahia, Brazil

Location

Clinics Hospital, Federal University of Goias - (UFG)

Goiânia, Goiás, Brazil

Location

Cetus Oncology Inc.

Belo Horizonte, Minas Gerais, Brazil

Location

Clinical Hospital of the Federal University of Parana (HC - UFPR)

Curitiba, Paraná, Brazil

Location

Saint Lucas Hospital of Copacabana

Rio de Janeiro, Rio de Janeiro, Brazil

Location

Humane Clinic / Atena Research Institute

Mossoró, Rio Grande do Norte, Brazil

Location

Hospital Moinhos de Vento

Porto Alegre, Rio Grande do Sul, Brazil

Location

Integrated Oncology Center of Rio Grande do Sul - Mother of God Hospital

Porto Alegre, Rio Grande do Sul, Brazil

Location

Santa Catarina Health Research and Education Center (CEPEN)

Florianópolis, Santa Catarina, Brazil

Location

State University of Campinas (UNICAMP) - Hemocenter

Campinas, São Paulo, Brazil

Location

Hospital Amaral Carvalho

Jaú, São Paulo, Brazil

Location

Jewish Hospital Albert Einstein

São Paulo, São Paulo, Brazil

Location

Samaritano Hospital

São Paulo, São Paulo, Brazil

Location

Sao Paulo University Clinical Hospital

São Paulo, São Paulo, Brazil

Location

University Multiprofile Hospital for Active Treatment "Dr. Georgi Stranski"

Pleven, Bulgaria

Location

University Multiprofile Hospital for Active Treatment "Sveti Georgi", Plovdiv

Plovdiv, Bulgaria

Location

Multiprofile Hospital for Active Treatment - Sofia, part of Military Medical Academy

Sofia, Bulgaria

Location

Specialized Hospital for Active Treatment of Hematological Diseases

Sofia, Bulgaria

Location

Multiprofile Hospital for Active Treatment "Sveta Marina"

Varna, Bulgaria

Location

Tom Baker Cancer Center, Internal Medicine/Hematology

Calgary, Alberta, Canada

Location

University of Alberta

Edmonton, Alberta, Canada

Location

Providence Hematology - Vancouver

Vancouver, British Columbia, Canada

Location

Eastern Regional Health Authority

St. John's, Newfoundland and Labrador, Canada

Location

Nova Scotia Health Authority, Centre for Clinical Research

Halifax, Nova Scotia, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Location

Jewish General Hospital; Clinical Research Unit

Montreal, Quebec, Canada

Location

University Hospital Brno

Brno, Czechia

Location

University Hospital Olomouc

Olomouc, Czechia

Location

University Hospital Plzen

Pilsen, Czechia

Location

University Hospital Kralovske Vinohrady, Clinic of Internal Hematology

Prague, Czechia

Location

CHU Hôpital Amiens Sud

Amiens, France, 80054, France

Location

CHU de Nimes - Hopital Universitaire Caremeau

Nîmes, France, 30900, France

Location

La Conception Hospital

Marseille, France

Location

Hôpital Saint-Louis

Paris, France

Location

CHU Hopitaux de Bordeaux - Hôpital Haut-Lévêque

Pessac, 33604, France

Location

Centre Hospitalier Lyon-Sud

Pierre-Bénite, France

Location

University Hospital Center of Poitiers

Poitiers, France

Location

JSC K. Eristavi National Center For Experimental and Clinical Surgery

Tbilisi, Georgia

Location

LTD M.Zodelava's Hematology Center, Department of Hematology

Tbilisi, Georgia

Location

LTD S.Khechinashvili University Hospital

Tbilisi, Georgia

Location

Malkhaz Katsiashvili Multiprofile Emergency Medicine Center LTD

Tbilisi, Georgia

Location

Tbilisi State Medical University and Ingorokva High Medical Technology University Clinic LLC

Tbilisi, Georgia

Location

Semmelweis University SE ÁOK I. sz. Belgyógyászati Klinika

Budapest, Hungary

Location

University of Debrecen Clinical Center (Debreceni Egyetem Klinikai Központ)

Debrecen, Hungary

Location

Somogy Megyei Kaposi Mór Oktató Kórház

Kaposvár, Hungary

Location

Szabolcs-Szatmar-Bereg County Hospitals and University Teaching Hospital, Department of Hematology

Nyíregyháza, Hungary

Location

Fejer County St. Gyorgy University Teaching Hospital, Department of Internal Medicine I

Székesfehérvár, Hungary

Location

Gauhati Medical College and Hospital

Guwahati, Assam, India

Location

Postgraduate Institute of Medical Education and Research (PGIMER)

Chandigarh, Chandigarh, India

Location

Nirmal Hospital Pvt Ltd

Surat, Gujarat, India

Location

Fortis Memorial Research Institute(FMRI)

Gurgaon, Haryana, India

Location

Sahyadri Super Speciality Hospital

Pune, Maharashtra, India

Location

Shri Ram Cancer Centre, Mahatma Gandhi Medical College & Hospital

Jaipur, Rajasthan, India

Location

Meenakshi Mission Hospital And Research Centre (MMHRC)

Madurai, Tamil Nadu, India

Location

Yashoda Hospitals

Hyderabad, Telangana, India

Location

All India Institute of Medical Sciences

Dehradun, Uttarakhand, India

Location

Netaji Subhash Chandra Bose Cancer Research Institute

Kolkata, West Bengal, India

Location

Tata Medical Center

Kolkata, West Bengal, India

Location

St. John's Medical College Hospital

Bengaluru, India

Location

Max Super Speciality Hospital Saket (A Unit of Max Healthcare Institute Limited)

Delhi, India

Location

Lady Davis Carmel Medical Center, Department of Hematology,

Haifa, Israel

Location

Hadassah Medical Center, Department of Hematology,

Jerusalem, Israel

Location

Meir Medical Center, Hematology Institute and Blood Bank

Kfar Saba, Israel

Location

Rabin Medical Center, Clinic for Myeloproliferative Disorders

Petah Tikva, Israel

Location

The Tel Aviv Sourasky Medical Center, Department of Internal Medicine

Tel Aviv, Israel

Location

Cancer Institute "Giovanni Paolo II", IRCCS

Bari, Italy

Location

Polyclinic S. Orsola-Malpighi

Bologna, Italy

Location

ASST Spedali Civili Brescia, Hematology Unit

Brescia, Italy

Location

Azienda Ospedaliero-Universitaria Careggi

Florence, Italy

Location

Scientific Institute of Romagna for the Study and Treatment of Cancer (IRST), IRCCS

Forlì, Italy

Location

Maggiore Polyclinic Hospital, Fondazione IRCCS Ca' Granda

Milan, Italy

Location

ASST Monza - Ospedale San Gerardo

Monza, Italy

Location

University Hospital "Federico II"

Naples, Italy

Location

University Hospital "Maggiore della Carita" of Novara

Novara, Italy

Location

United Hospitals Villa Sofia Cervello

Palermo, Italy

Location

Polyclinic San Matteo, IRCCS

Pavia, Italy

Location

Hospital "Infermi" of Rimini

Rimini, Italy

Location

Umberto I Polyclinic of Rome

Rome, Italy

Location

University Polyclinic Foundation "Agostino Gemelli"

Rome, Italy

Location

City of Health and Science of Turin

Turin, Italy

Location

Santa Maria della Misericordia University Hospital of Udine

Udine, Italy

Location

ASST Sette Laghi Hospital

Varese, Italy

Location

University of Yamanashi Hospital

Chūō, Japan

Location

Kyushu University Hospital

Fukuoka, Japan

Location

Fukushima Medical University Hospital

Fukushima, Japan

Location

Tohoku University Hospital

Miyagi, Japan

Location

University of Miyazaki Hospital

Miyazaki, Japan

Location

Juntendo University Hospital

Tokyo, Japan

Location

Nippon Medical School Hospital

Tokyo, Japan

Location

Tokyo Medical University Hospital

Tokyo, Japan

Location

Ehime University Hospital

Tōon, Japan

Location

Mie University Hospital

Tsu, Japan

Location

Aktobe Medical Center, Department of Hematology

Aktobe, Kazakhstan

Location

City Clinical Hospital #7, Hematology Department

Almaty, Kazakhstan

Location

Center for Hematology

Astana, Kazakhstan

Location

National Research Oncology, Oncohematology Center

Astana, Kazakhstan

Location

Hematology Center

Karaganda, Kazakhstan

Location

City Oncological Center

Shymkent, Kazakhstan

Location

Center for Hematology

Ust-Kamenogorsk, Kazakhstan

Location

University Teaching Hospital in Bialystok

Bialystok, Poland

Location

University Clinical Center in Gdansk

Gdansk, Poland

Location

Andrzej Mielecki Independent Public Clinical Hospital of Medical University of Silesia in Katowice, Department of Hematology and Bone Marrow Transplantation

Katowice, Poland

Location

Pratia Oncology Katowice

Katowice, Poland

Location

University Hospital in Krakow

Krakow, Poland

Location

Nicolaus Copernicus Provincial Multispecialty Oncology and Traumatology Center in Lodz

Lodz, Poland

Location

Independent Public Teaching Hospital No.1 in Lublin, Department of Hematooncology, Bone Marrow Transplantation and Chemotherapy

Lublin, Poland

Location

Jedrzej Sniadecki Specialist Hospital in Nowy Sacz, Department of Hematology

Nowy Sącz, Poland

Location

Frederic Chopin Provincial Teaching Hospital No. 1 in Rzeszow, Department of Hematology,

Rzeszów, Poland

Location

Nasz Lekarz Medical Outpatient Clinics Slawomir Jeka

Torun, Poland

Location

Institute of Hematology and Transfusion Medicine, Teaching Department of Hematology

Warsaw, Poland

Location

Jan Mikulicz Radecki University Hospital in Wroclaw, Department and Clinic of Hematology, Blood Neoplasms and Bone Marrow Transplantation

Wroclaw, Poland

Location

Onco Card Srl

Brasov, Romania

Location

Coltea Clinical Hospital

Bucharest, Romania

Location

Fundeni Clinical Institute

Bucharest, Romania

Location

Prof. Dr. Ion Chiricuta" Institute of Oncology

Cluj-Napoca, Romania

Location

City Clinical Hospital #40

Moscow, Russia

Location

City Clinical Hospital n.a. V.V. Veresaev of the Moscow City Health

Moscow, Russia

Location

S.P. Botkin City Clinical Hospital

Moscow, Russia

Location

Clinic UZI 4D, LLC

Pyatigorsk, Russia

Location

Research Institute of Hematology and Transfusiology

Saint Petersburg, Russia

Location

S.M. Kirov Military Medical Academy, Department and Clinic for Intermediate-Level Training in Internal Medicine, Hematology Division

Saint Petersburg, Russia

Location

V.A. Almazov North-West Federal Medical Research Center, Institute of Oncology and Hematology, Scientific Department of Clinical Oncology

Saint Petersburg, Russia

Location

Bashkiria State Medical University, Department of Internal Medicine

Ufa, Russia

Location

Volgograd Regional Clinical Oncology Center

Volgograd, Russia

Location

Clinical Center of Serbia, Clinic of Hematology

Belgrade, Serbia

Location

Clinical Center of Vojvodina, Clinic of Hematology

Novi Sad, Serbia

Location

Severance Hospital

Seoul, South Korea, 3722, South Korea

Location

Pusan National University Hospital

Busan, South Korea

Location

Kyungpook National University Hospital

Daegu, South Korea

Location

Samsung Medical Center

Seoul, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

The Catholic University of Korea, St. Mary's Hospital

Seoul, South Korea

Location

Hospital Clínic de Barcelona

Barcelona, Spain

Location

Hospital del Mar

Barcelona, Spain

Location

University Hospital Vall d'Hebron

Barcelona, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, Spain

Location

University Hospital 12 de Octubre, Department of Hematology

Madrid, Spain

Location

Morales Meseguer University General Hospital, Department of Hematology and Hemotherapy

Murcia, Spain

Location

University Clinical Hospital of Salamanca, Department of Hematology

Salamanca, Spain

Location

University Hospital Virgen del Rocio (HUVR)

Seville, Spain

Location

University Clinical Hospital of Valencia, Department of Hematology and Medical Oncology

Valencia, Spain

Location

Cherkasy Regional Oncology Dispensary of Cherkasy Oblast Council, Regional Treatment and Diagnostic Hematology Center, Department of Hematology

Cherkasy, Ukraine

Location

City Clinical Hospital #4" under Dnipro City Council

Dnipro, Ukraine

Location

Communal Non-profit enterprise "Regional Center of Oncology", Department of Hematology

Kharkiv, Ukraine

Location

Kyiv City Clinical Hospital #9, Hematology Department #1

Kyiv, Ukraine

Location

Kyiv Regional Oncology Center, Department of Hematology,

Kyiv, Ukraine

Location

Limited Liability Company "City Doctor"

Kyiv, Ukraine

Location

Institute of Blood Pathology and Transfusion Medicine, Department of Hematology

Lviv, Ukraine

Location

Poltava M.V. Sklifosovskyi Regional Clinical Hospital under Poltava Regional Council, Department of Hematology

Poltava, Ukraine

Location

Royal Hallamshire Hospital, Department of Hematology

Sheffield, South Yorkshire, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, United Kingdom, G12 0ZD, United Kingdom

Location

Barts Health NHS Trust - The Royal London Hospital

London, United Kingdom, E1 2ES, United Kingdom

Location

Gloucestershire Royal Hospital

Gloucester, United Kingdom

Location

Guy's and St Thomas' NHS Foundation Trust - Guy's Hospital

London, United Kingdom

Location

Imperial College Healthcare NHS Trust - Hammersmith Hospital

London, United Kingdom

Location

Oxford University Hospitals NHS Trust - Churchill Hospital

Oxford, United Kingdom

Location

Related Publications (1)

  • Gerds AT, Savona MR, Scott BL, Talpaz M, Egyed M, Harrison CN, Yacoub A, Vannucchi A, Mead AJ, Kiladjian JJ, O'Sullivan J, Garcia-Gutierrez V, Bose P, Rampal RK, Miller CB, Palmer J, Oh ST, Buckley SA, Mould DR, Ito K, Tyavanagimatt S, Smith JA, Roman-Torres K, Devineni S, Craig AR, Mascarenhas JO. Determining the recommended dose of pacritinib: results from the PAC203 dose-finding trial in advanced myelofibrosis. Blood Adv. 2020 Nov 24;4(22):5825-5835. doi: 10.1182/bloodadvances.2020003314.

MeSH Terms

Conditions

Primary MyelofibrosisBone Marrow DiseasesHematologic DiseasesBlood Platelet DisordersHemorrhagic DisordersSplenomegalyAnemia

Interventions

11-(2-pyrrolidin-1-ylethoxy)-14,19-dioxa-5,7,26-triazatetracyclo(19.3.1.1(2,6).1(8,12))heptacosa-1(25),2(26),3,5,8,10,12(27),16,21,23-decaeneAdrenal Cortex HormonesHydroxyureaDanazolruxolitinib

Condition Hierarchy (Ancestors)

Myeloproliferative DisordersHemic and Lymphatic DiseasesHypertrophyPathological Conditions, AnatomicalPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

HormonesHormones, Hormone Substitutes, and Hormone AntagonistsUreaAmidesOrganic ChemicalsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Study Officials

  • Simran Singh

    Sobi, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 17, 2017

First Posted

May 24, 2017

Study Start

June 26, 2017

Primary Completion (Estimated)

October 5, 2026

Study Completion (Estimated)

October 13, 2028

Last Updated

April 30, 2026

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will not share

Locations