NCT04074096

Brief Summary

This study evaluates the addition of stereotactic radiosurgery (SRS) to the combination of binimetinib + encorafenib + pembrolizumab in the treatment of BRAFⱽ⁶⁰⁰ mutation-positive melanoma with brain metastases (MBM).

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
10

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Sep 2022

Typical duration for phase_2

Geographic Reach
1 country

21 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 26, 2019

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 29, 2019

Completed
3 years until next milestone

Study Start

First participant enrolled

September 5, 2022

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 27, 2026

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 27, 2026

Completed
Last Updated

March 25, 2026

Status Verified

October 1, 2025

Enrollment Period

3.6 years

First QC Date

August 26, 2019

Last Update Submit

March 24, 2026

Conditions

Keywords

MelanomaBRAF V600Brain metastasesEncorafenibBinimetinibPembrolizumabStereotaxicSRS

Outcome Measures

Primary Outcomes (1)

  • Intracranial (IC) progression-free survival (PFS)

    Time from randomisation until IC-progressive disease (PD) as evaluated by centralized assessment using modified response evaluation criteria in solid tumours version 1.1 (RECIST v1.1), or death, whichever occurs first.

    From randomisation until IC-PD, or death, whichever occurs first, up to 12 months.

Secondary Outcomes (13)

  • Intracranial-response rate (RR)

    From randomisation until IC-CR or IC-PR, up to 60 months.

  • Intracranial disease control (DC)

    From randomisation until IC-CR or IC-PR or stable intracranial disease, up to 60 months.

  • Extracranial (EC) response rate

    From randomisation until confirmed EC-CR or EC-PR, up to 60 months.

  • Overall response rate (ORR)

    From randomisation until confirmed CR or PR, up to 60 months.

  • Duration of intracranial, extracranial, and overall response

    Time from first observation of, IC-, EC-, or overall response respectively (i.e. CR or PR), until disease progression (PD), up to 60 months.

  • +8 more secondary outcomes

Study Arms (2)

Encorafenib + binimetinib + pembrolizumab

EXPERIMENTAL

Encorafenib 450 mg oral route (PO) once daily (QD) + binimetinib 45 mg PO twice daily (BID) + pembrolizumab 200 mg intravenous (IV) every 3 weeks (Q3W).

Drug: Binimetinib Oral TabletDrug: Encorafenib Oral CapsuleDrug: Pembrolizumab

SRS followed by encorafenib + binimetinib + pembrolizumab

EXPERIMENTAL

Upfront SRS of all lesions ≥5 mm in diameter (or ≥3 mm if other cerebral metastases \>5 mm); followed by encorafenib 450 mg PO QD + binimetinib 45 mg PO BID + pembrolizumab 200 mg IV Q3W. The treatment should be started more than 24 hours and less than 8 days (excluded) after the SRS

Radiation: Stereotaxic radiosurgery (SRS)Drug: Binimetinib Oral TabletDrug: Encorafenib Oral CapsuleDrug: Pembrolizumab

Interventions

All patients: binimetinib 45 mg PO BID.

Also known as: Mektovi
Encorafenib + binimetinib + pembrolizumabSRS followed by encorafenib + binimetinib + pembrolizumab

All patients: encorafenib 450 mg PO QD

Also known as: Braftovi
Encorafenib + binimetinib + pembrolizumabSRS followed by encorafenib + binimetinib + pembrolizumab

All patients: pembrolizumab 200 mg IV Q3W

Also known as: Keytruda
Encorafenib + binimetinib + pembrolizumabSRS followed by encorafenib + binimetinib + pembrolizumab

For patients randomised to arm B only: Upfront SRS of all lesions ≥5 mm in diameter (or ≥3 mm if other cerebral metastases \>5 mm).

SRS followed by encorafenib + binimetinib + pembrolizumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Provided written informed consent prior to any trial specific procedures.
  • Aged ≥18 years old.
  • An Eastern Cooperative Oncology Group (ECOG) Performance Status of 0-1.
  • Histologically confirmed Stage IV M1d cutaneous melanoma or unknown primary melanoma that is metastatic to the brain.
  • Presence of BRAFV600E/K/D/R mutation according to a locally validated BRAF Assay.
  • Candidacy for SRS therapy validated by the radiation oncologist and/or neurosurgeon at the investigative centre. This should be documented in the patient file.
  • Absence of previous systemic treatment with BRAF inhibitors, MEK inhibitors or anti-PD-1 for distant metastatic melanoma. Patients having received such treatments as adjuvant therapy are allowed provided adjuvant treatment has been stopped for 6 months or more.
  • No more than one previous local intracranial therapy for one lesion (e.g. craniotomy, SRS).
  • Note: Treatment with stereotactic radiosurgery must have been completed ≥14 days prior to randomisation and this lesion cannot be target lesion for radiosurgery.
  • Able to undergo gadolinium-enhanced MRI.
  • At least one measurable intracranial lesion for which all of the following criteria have to be met:
  • Previously untreated (no local therapy including local radiotherapy, resection, radiosurgery) or progressive after previous local therapy.
  • Longest diameter ≥5 mm as determined by contrast-enhanced MRI. Longest diameter ≥3 mm is acceptable for other IC lesions provided there is at least one lesion ≥5 mm.
  • Cumulative Intracranial Target Volume ≤12 cmᵌ as determined by contrast-enhanced MRI.
  • All prior anti-cancer treatment-related toxicities (except alopecia and laboratory values) must be resolved or Grade 1 according to NCI-CTCAE v5.0.
  • +14 more criteria

You may not qualify if:

  • More than 10 intracranial metastases.
  • Presence of neurological symptoms related to intracranial metastases which induce alteration of the ECOG performance status to 2 or more or require immediate radiation treatment.
  • Ocular melanoma.
  • Brain metastases which necessitate immediate neurosurgery.
  • Any previous treatment with whole-brain radiation.
  • Presence of leptomeningeal disease or any parenchymal brain metastasis \>30 mm in longest diameter.
  • Note: On MRI, the most common finding of leptomeningeal disease is pial enhancement and nodularity, typically over the cerebral convexities, in the basal cisterns, on the tentorium, or in the ventricular ependymal surfaces.
  • Current or expected use of a strong inhibitor of CYP3A4.
  • History of malignancy other than disease under study occurring within 3 years of study enrolment with the exception of: completely resected non-melanoma skin cancer or indolent second malignancies.
  • Any serious or unstable pre-existing medical conditions (aside from malignancy exceptions specified above), psychiatric disorders, or other conditions that, in the opinion of the investigator, could interfere with the patient's safety, obtaining informed consent, or compliance with study procedures.
  • Known Human Immunodeficiency Virus (HIV), Hepatitis B Virus (HBV), or Hepatitis C Virus (HCV) infection (patients with laboratory evidence of cured HBV and/or HCV will be permitted).
  • A history or evidence of cardiovascular risk including any of the following:
  • Left ventricular ejection fraction \< local LLN as determined by a MUGA scan or echocardiogram;
  • A QT interval corrected for heart rate QTc \> 480 ms according to local standard formula;
  • A history or evidence of current clinically significant uncontrolled arrhythmias.
  • +19 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (21)

APHP - Hôpital Avicenne

Bobigny, France

Location

CHU de Bordeaux - Hôpital Saint André

Bordeaux, France

Location

GH Sud CHU Bordeaux - Hôpital Levêque

Bordeaux, France

Location

APHP - Hôpital Ambroise Paré

Boulogne-Billancourt, France

Location

CHU de Caen

Caen, France

Location

CLCC - Centre Jean François Baclesse

Caen, France

Location

APHP - Hôpital Henri Mondor

Créteil, France

Location

CHU de Dijon - Hopital Du Bocage

Dijon, France

Location

CLCC - Centre Georges François Leclerc

Dijon, France

Location

CLCC - Centre Léon Bérard

Lyon, France

Location

APHM - Hopital De La Timone

Marseille, France

Location

CHU De Montpellier - Hopital Saint Eloi

Montpellier, France

Location

CLCC - Institut de Cancerologie de Montpellier

Montpellier, France

Location

CHU Nice - Hôpital de l'Archet

Nice, France

Location

CLCC - Centre Antoine Lacassagne

Nice, France

Location

APHP - L'hôpital de la Pitié-Salpêtrière

Paris, France

Location

CHU de Nantes - Hôtel Dieu

Saint-Herblain, France

Location

CLCC - Institut de Cancerologie de l'Ouest - Nantes

Saint-Herblain, France

Location

CLCC - IUCT-0 / Institut Claudius Regaud

Toulouse, France

Location

CHU de TOURS - Hôpital Bretonneau

Tours, France

Location

CLCC - Gustave Roussy

Villejuif, France

Location

MeSH Terms

Conditions

MelanomaBrain Neoplasms

Interventions

Radiosurgerybinimetinibencorafenibpembrolizumab

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue DiseasesCentral Nervous System NeoplasmsNervous System NeoplasmsBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

RadiotherapyTherapeuticsStereotaxic TechniquesNeurosurgical ProceduresSurgical Procedures, OperativeInvestigative Techniques

Study Officials

  • Philippe Saiag, Prof

    APHP - CHU Ambroise Paré

    PRINCIPAL INVESTIGATOR
  • Marie Charissoux, MD

    Institut Régional du Cancer

    PRINCIPAL INVESTIGATOR
  • Jean Regis, Prof

    APHM - Hôpital de la Timone

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 26, 2019

First Posted

August 29, 2019

Study Start

September 5, 2022

Primary Completion

March 27, 2026

Study Completion

March 27, 2026

Last Updated

March 25, 2026

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will share

Unicancer will share de-identified individual data that underlie the results reported. A decision concerning the sharing of other study documents, including protocol and statistical analysis plan will be examined upon request.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
The data shared will be limit to that required for independent mandated verification of the published results, the applicant will need authorization from Unicancer for personal access, and data will only be transferred after signing of a data access agreement.
Access Criteria
Unicancer will consider access to study data upon written detailed request sent to Unicancer, from 6 months until 5 years after publication of summary data.

Locations