NCT03675893

Brief Summary

This research study is studying a combination of targeted therapies as a possible treatment for estrogen-receptor positive (ER+) endometrial cancer and low-grade serous ovarian cancer. The drugs involved in this study are:

  • Abemaciclib (also known as Verzenio™)
  • Letrozole (also known as Femara®)
  • Metformin (also known as Glucophage®)
  • Zotatifin (also known as eFT226)
  • Gedatolisib (also known as PF-05212384)

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
180

participants targeted

Target at P75+ for phase_2

Timeline
63mo left

Started Dec 2018

Longer than P75 for phase_2

Geographic Reach
1 country

3 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress58%
Dec 2018Aug 2031

First Submitted

Initial submission to the registry

September 14, 2018

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 18, 2018

Completed
3 months until next milestone

Study Start

First participant enrolled

December 24, 2018

Completed
9.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2028

Expected
3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2031

Last Updated

June 15, 2025

Status Verified

June 1, 2025

Enrollment Period

9.6 years

First QC Date

September 14, 2018

Last Update Submit

June 12, 2025

Conditions

Keywords

Endometrial CancerCDK4/6ER+Estrogen ReceptorLow-Grade Serous Ovarian CancereIF4API3KPAM

Outcome Measures

Primary Outcomes (2)

  • Progression Free Survival Rate

    Number of patients alive and disease progression-free per RECIST 1.1 criteria.

    6 months

  • Objective Tumor Response Rate

    Number of patients who experience objective tumor responses per RECIST 1.1 criteria.

    6 months

Secondary Outcomes (2)

  • Overall Survival Rate

    3 years

  • Treatment-related toxicities

    3 years

Study Arms (8)

Cohort 1

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * LY3023414 is administered by mouth twice daily * Letrozole is administered by mouth once daily

Drug: LetrozoleDrug: AbemaciclibDrug: LY3023414

Cohort 2

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * LY3023414 is administered by mouth twice daily

Drug: AbemaciclibDrug: LY3023414

Cohort 1A

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * Letrozole is administered by mouth once daily

Drug: LetrozoleDrug: Abemaciclib

Cohort 3

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * Letrozole is administered by mouth once daily * Metformin is administered by mouth once daily

Drug: LetrozoleDrug: AbemaciclibDrug: Metformin

Cohort 4

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * Letrozole is administered by mouth once daily * Zotatifin is administered intravenously on days 1 and 8 of a 21-day cycle

Drug: LetrozoleDrug: AbemaciclibDrug: Zotatifin

Cohort 5

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * Letrozole is administered by mouth once daily * Zotatifin is administered intravenously on days 1 and 8 of a 21-day cycle

Drug: LetrozoleDrug: AbemaciclibDrug: Zotatifin

Cohort 6

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * Letrozole is administered by mouth once daily * Gedatolisib is administered intravenously on days 1, 8 and 15 of a 28-day cycle

Drug: LetrozoleDrug: AbemaciclibDrug: Gedatolisib

Cohort 7

EXPERIMENTAL

* Abemaciclib is administered by mouth twice daily * Letrozole is administered by mouth once daily * Gedatolisib is administered intravenously on days 1, 8 and 15 of a 28-day cycle

Drug: LetrozoleDrug: AbemaciclibDrug: Gedatolisib

Interventions

Letrozole is a hormonal therapy that works by lowering the production of estrogen in the body.

Also known as: Femara
Cohort 1Cohort 1ACohort 3Cohort 4Cohort 5Cohort 6Cohort 7

Abemaciclib is a cyclin-dependent kinase (CDK) inhibitor.

Also known as: Verzenio
Cohort 1Cohort 1ACohort 2Cohort 3Cohort 4Cohort 5Cohort 6Cohort 7

LY3023414 is a potent selective inhibitor of the class I PI3K isoforms, mTOR, and DNA-PK.

Cohort 1Cohort 2

Metformin inhibits mitochondrial adenosine-5'-triphosphate (ATP) synthesis, resulting in activation of the AMPK (5' AMP-activated protein kinase) pathway through LKB1, eventually causing inhibition of the mTOR pathway and subsequent reduction in protein synthesis and cellular proliferation.

Also known as: Glucophage
Cohort 3

Zotatifin is a selective eukaryotic initiation factor 4A (eIF4A) inhibitor.

Also known as: eFT226
Cohort 4Cohort 5

Gedatolisib is a PI3K/AKT/mTOR (PAM) pathway inhibitor.

Also known as: PF-05212384
Cohort 6Cohort 7

Eligibility Criteria

Age18 Years+
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants must have cytologically or histologically confirmed endometrial cancer that is recurrent or metastatic and/or resistant to standard therapies, or for which no standard therapy is available.Participants enrolled in the second stage of Cohort 1A, or into Cohort 3, 4, 6 and 7, must have histologically confirmed either i) endometrioid endometrial cancer or ii) endometrial carcinosarcoma with endometrioid epithelial component
  • For Cohort 5: Participants must have histologically confirmed diagnosis of low-grade serous carcinoma of ovary, fallopian tube or peritoneum; original diagnosis of de novo low-grade serous carcinoma or original diagnosis of serous borderline tumor with subsequent diagnosis of low-grade serous carcinoma. Participants whose tumors contain both low-grade serous carcinoma and high-grade serous carcinoma are not eligible.
  • Participants must have ER-positive disease, defined as ≥ 1 percent of tumor cell nuclei being immunoreactive by immunohistochemistry (IHC). If multiple analyses have been performed, judgment should be based on the most recent biopsy or pathology specimen analyzed in a CLIA-certified laboratory. For Cohort 5, participants are eligible regardless of ER positive or negative status.
  • Participants must have measurable disease, defined as at least one lesion that can be accurately measured in at least one dimension (longest diameter to be recorded for non-nodal lesions and short axis for nodal lesions) as ≥20 mm with conventional techniques or as ≥10 mm with spiral CT scan, MRI, or calipers by clinical exam.
  • Age ≥ 18 years
  • ECOG performance status of 0 or 1
  • Participants must have normal organ and bone marrow function as defined below:
  • Absolute neutrophil count ≥ 1,500/mcL
  • Platelets ≥ 100,000/mcL
  • Total bilirubin ≤ 1.5 × institutional upper limit of normal (ULN). Patients with Gilbert's syndrome with a total bilirubin \</= 2.0 times ULN and direct bilirubin within normal limits are permitted.
  • AST(SGOT)/ALT(SGPT) ≤ 3× institutional ULN
  • Creatinine ≤ 1.5 × institutional ULN, OR
  • Creatinine clearance ≥ 60 mL/min/1.73 m2 for participants with creatinine levels above institutional normal.
  • For cohorts 4, 5, 6 and 7, patients must not have remaining ovarian function to be included. Women who have ovarian function are eligible but must be placed on hormonal suppression.
  • The effects of the study agents on the developing human fetus are unknown. For this reason, women of child-bearing potential must agree to use a medically approved contraceptive method during the treatment period and for 3 months following the last dose of study agent. Contraceptive methods may include an intrauterine device (IUD) or barrier method. If condoms are used as a barrier method, a spermicidal agent should be added as a double barrier protection. Should a woman become pregnant or suspect she is pregnant while she is participating in this study, she should inform her treating physician immediately. A negative serum pregnancy test is required for study entry from women of childbearing potential.
  • +7 more criteria

You may not qualify if:

  • Participants who have had chemotherapy, immune therapy, other investigational therapy, or major surgery within 4 weeks (6 weeks for nitrosoureas or mitomycin C) prior to the first dose of study medication. Previous hormonal therapy, including prior letrozole, is allowed and there is no required washout period for hormonal therapy.
  • Participants who have had tyrosine kinase inhibitor (TKI) therapy within 5 half-lives of study entry.
  • Participants who have had radiation therapy within 2 weeks of the first dose of study medication.
  • Participants who have received previous treatment with CDK4/6 inhibitors, including but not limited to previous abemaciclib therapy. For Cohorts 4 and 5, prior treatment with CDK4/6 inhibitors is allowed in up to 50% of participants for each cohort (≤8 participants in the first stage and ≤18 total in both stages for each cohort \[if the study goes to second stage\]). For Cohort 7, patients must have received prior treatment with CDK4/6 inhibitors.
  • Participants who are currently receiving metformin therapy (if enrolling to Cohort 3).
  • Participants who have impairment of gastrointestinal (GI) function or GI disease that may significantly alter the absorption of the study drugs
  • Participants with known brain metastases should be excluded from this clinical trial because of their poor prognosis and because they often develop progressive neurologic dysfunction that would confound the evaluation of neurologic and other adverse events.
  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to the study agents that the participant will be administered.
  • Participants who at the time of study enrollment are known to require concomitant therapy with moderate or strong CYP3A4 inducers, or strong inhibitors of CYP3A4. Due to potential drug interactions, concomitant use of these medications is not permitted for the duration of treatment on trial. Participants are eligible for study entry if an appropriate substitution is made prior to the first dose of study medication.
  • Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements.
  • Use of known QT-prolonging drugs during screening or expected requirement for use during study therapy.
  • Participants with histories or evidence of cardiovascular risk including any of the following: acute coronary syndromes (i.e. myocardial infarction or angina), coronary angioplasty, or stenting within 6 months prior to study enrollment.
  • Pregnant women are excluded from this study because the study agents are anti-cancer agents with the potential for teratogenic or abortifacient effects. Because there is an unknown but potential risk for adverse events in nursing infants secondary to treatment of the mother with the study agents, breastfeeding must be discontinued if the mother is treated on trial.
  • Individuals with a history of a different malignancy are ineligible with the following exceptions: individuals who have been treated and are disease-free for a minimum of 5 years prior to study enrollment, or individuals who are deemed by the treating investigator to be at low risk for disease recurrence. Additionally, individuals with the following cancers are eligible if diagnosed and treated within the past 5 years: basal or squamous cell carcinomas of the skin, and breast or cervical carcinomas in situ.
  • Known HIV-positive participants are ineligible because of the increased risk of lethal infections when treated with marrow-suppressive therapy.
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, 02214, United States

RECRUITING

Beth Israel Deaconess Medical Center (BIDMC)

Boston, Massachusetts, 02215, United States

RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

RECRUITING

Related Publications (1)

  • Konstantinopoulos PA, Lee EK, Xiong N, Krasner C, Campos S, Kolin DL, Liu JF, Horowitz N, Wright AA, Bouberhan S, Penson RT, Yeku O, Bowes B, Needham H, Hayes M, Sawyer H, Polak M, Shea M, Cheng SC, Castro C, Matulonis UA. A Phase II, Two-Stage Study of Letrozole and Abemaciclib in Estrogen Receptor-Positive Recurrent Endometrial Cancer. J Clin Oncol. 2023 Jan 20;41(3):599-608. doi: 10.1200/JCO.22.00628. Epub 2022 Sep 29.

MeSH Terms

Conditions

Endometrial NeoplasmsOvarian Neoplasms

Interventions

LetrozoleabemaciclibLY3023414Metformingedatolisib

Condition Hierarchy (Ancestors)

Uterine NeoplasmsGenital Neoplasms, FemaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesEndocrine Gland NeoplasmsOvarian DiseasesAdnexal DiseasesEndocrine System DiseasesGonadal Disorders

Intervention Hierarchy (Ancestors)

NitrilesOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsBiguanidesGuanidinesAmidines

Study Officials

  • Panagiotis Konstantininopoulos, MD

    Dana-Farber Cancer Institute

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Panagiotis Konstantinopoulos, MD

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

September 14, 2018

First Posted

September 18, 2018

Study Start

December 24, 2018

Primary Completion (Estimated)

August 1, 2028

Study Completion (Estimated)

August 1, 2031

Last Updated

June 15, 2025

Record last verified: 2025-06

Data Sharing

IPD Sharing
Will not share

Locations