NCT03555955

Brief Summary

This study evaluates the pharmacokinetics and safety of CPX-351 in patients with moderate or severe renal impairment.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
21

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Nov 2018

Typical duration for phase_1

Geographic Reach
2 countries

13 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 14, 2018

Completed
1 month until next milestone

First Posted

Study publicly available on registry

June 14, 2018

Completed
5 months until next milestone

Study Start

First participant enrolled

November 20, 2018

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 26, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 26, 2021

Completed
Last Updated

July 22, 2021

Status Verified

July 1, 2021

Enrollment Period

2.5 years

First QC Date

May 14, 2018

Last Update Submit

July 20, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Pharmacokinetics (PK) of CPX-351

    The key PK parameter AUCtau will be assessed

    Blood samples will be collected during first induction on Day 1 predose, Day 5 predose, 45 and 90 minutes post infusion start, 2, 3, 4, 6, 8, 24, 48, 96, 168, and 216 hours post Day 5 infusion start.

Secondary Outcomes (2)

  • PK parameter of the individual components of CPX-351, and their respective metabolites

    Blood samples will be collected during first induction on Day 1 predose, Day 5 predose, 45 and 90 minutes post infusion start, 2, 3, 4, 6, 8, 24, 48, 96, 168, and 216 hours post Day 5 infusion start.

  • Incidence of Treatment Emergent Adverse Events (TEAEs)

    Up to 31 months.

Study Arms (3)

Cohort 1

EXPERIMENTAL

Normal renal function

Drug: CPX-351

Cohort 2

EXPERIMENTAL

Moderate renal impairment

Drug: CPX-351

Cohort 3

EXPERIMENTAL

Severe renal impairment

Drug: CPX-351

Interventions

CPX-351 is administered as an intravenous (IV) infusion over approximately 90 minutes.

Also known as: Vyxeos™
Cohort 1

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ability to understand and voluntarily give informed consent.
  • Male or female patients, age ≥18 years at the time of consent.
  • Diagnosis of hematologic malignancy including, but not limited to, AML, ALL, and MDS. Patients may be newly diagnosed, refractory to initial treatment, or in relapse.
  • Patients with normal renal function, or moderate or severe renal impairment as categorized by creatinine clearance (CrCl)) using the Cockcroft-Gault Formula.
  • Consent of female patients to use a medically acceptable method of contraception for at least 2 months prior to the first dose of CPX-351 and consent of female patients to use a medically acceptable method of contraception throughout the entire study period and for 6 months following the last dose of CPX-351.
  • Male patients must be willing to refrain from sperm donation for 6 months following the last dose of CPX-351and must use adequate contraception throughout the entire study period and for 6 months following the last dose of CPX-351.

You may not qualify if:

  • Prior treatment with CPX-351 ≤ to 1 month before the start of CPX-351 in this study.
  • Patients with active (uncontrolled, metastatic) second malignancies are excluded.
  • Any serious medical condition, laboratory abnormality, or psychiatric illness that would prevent obtaining informed consent.
  • Patients with known hypersensitivity to cytarabine, daunorubicin, or liposomal products.
  • Female patients who are pregnant, nursing, or lactating.
  • Participation in another clinical trial of an investigational drug or medical device within 30 days or 5 half-lives (whichever is longer) prior to enrollment in this study.
  • Any other condition that would cause a risk to patients if they participate in the trial.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Northside Hospital - Blood and Bone Marrow Transplant Group of Georgia

Atlanta, Georgia, 30342, United States

Location

University of Kansas Cancer Center

Westwood, Kansas, 66205, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Weill Cornell Medical College

New York, New York, 10021, United States

Location

New York Medical/Westchester

Valhalla, New York, 10595, United States

Location

Wake Forest Baptist Health

Winston-Salem, North Carolina, 27157, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Vancouver General Hospital

Vancouver, British Columbia, V5Z 1M9, Canada

Location

University Health Network/Princess Margaret Cancer Center

Toronto, Ontaro, M5G 1Z5, Canada

Location

Related Publications (1)

  • Solomon SR, Powell BL, Koprivnikar J, Lai C, Male H, Michaelis LC, Newell LF, Sanford D, Jenkins J, Zelaya A, Coppola S, Faderl S, Walter RB. CPX-351 Pharmacokinetics and Safety in Adults with Hematologic Malignancies and Renal Function Impairment: Phase 1 Trial. Cancers (Basel). 2024 Feb 24;16(5):915. doi: 10.3390/cancers16050915.

MeSH Terms

Conditions

Hematologic NeoplasmsLeukemia, Myeloid, AcutePrecursor Cell Lymphoblastic Leukemia-LymphomaMyelodysplastic Syndromes

Interventions

CPX-351

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLeukemia, MyeloidLeukemiaNeoplasms by Histologic TypeLeukemia, LymphoidLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesBone Marrow Diseases

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 14, 2018

First Posted

June 14, 2018

Study Start

November 20, 2018

Primary Completion

May 26, 2021

Study Completion

May 26, 2021

Last Updated

July 22, 2021

Record last verified: 2021-07

Locations