NCT03454451

Brief Summary

This is a Phase 1/1b open-label, dose escalation and dose expansion study of CPI-006, a humanized monoclonal antibody (mAb) targeting the CD73 cell-surface ectonucleotidase in adult subjects with select advanced cancers. CPI-006 will be evaluated as a single agent, in combination with ciforadenant (an oral adenosine 2A receptor antagonist), in combination with pembrolizumab (an anti-PD1 antibody), and in combination with ciforadenant and pembrolizumab.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
117

participants targeted

Target at P75+ for phase_1 nonsmall-cell-lung-cancer

Timeline
Completed

Started Apr 2018

Typical duration for phase_1 nonsmall-cell-lung-cancer

Geographic Reach
2 countries

27 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 5, 2018

Completed
29 days until next milestone

First Posted

Study publicly available on registry

March 6, 2018

Completed
2 months until next milestone

Study Start

First participant enrolled

April 25, 2018

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 28, 2022

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 19, 2023

Completed
Last Updated

December 21, 2023

Status Verified

December 1, 2023

Enrollment Period

4.7 years

First QC Date

February 5, 2018

Last Update Submit

December 19, 2023

Conditions

Keywords

NSCLCRCCTNBCmCRPCCRCLung CancerKidney CancerRectal CancerBreast CancerSarcomaEndometrialPancreaticOvarianSCCHNNHL

Outcome Measures

Primary Outcomes (3)

  • Incidence of dose-limiting toxicities (DLTs) of CPI-006 as a single agent and in combination with ciforadenant and with pembrolizumab.

    From start of treatment to end of treatment, up to 36 months

  • Incidence of treatment-emergent adverse events as assessed by NCI CTCAE v.4.03, of CPI-006 as single agent and in combination with ciforadenant and with pembrolizumab.

    From start of treatment to end of treatment, up to 36 months

  • Identify the MDL(maximum dose level) of single agent CPI-006

    From start of treatment to end of treatment, up to 36 months

Secondary Outcomes (3)

  • Area under the curve (AUC) of CPI-006

    Day 1, 2, 8 , and 15 of Cycle 1 & 4 (each cycle is 21 days).

  • Maximum serum concentration (Cmax) of CPI-006

    Day 1, 2, 8 , and 15 of Cycle 1 & 4 (each cycle is 21 days).

  • Objective response rate per RECIST v.1.1 criteria of CPI-006 as single agent and in combination with ciforadenant and with pembrolizumab.

    From start of treatment to end of treatment, up to 36 months

Study Arms (6)

Cohort 1a

EXPERIMENTAL

CPI-006

Drug: CPI-006

Cohort1b

EXPERIMENTAL

CPI-006 + ciforadenant

Drug: CPI-006 + ciforadenant

Cohort 1c

EXPERIMENTAL

CPI-006 + pembrolizumab

Drug: CPI-006 + pembrolizumab

Cohort 2a

EXPERIMENTAL

CPI-006

Drug: CPI-006

Cohort 2b

EXPERIMENTAL

CPI-006 + ciforadenant

Drug: CPI-006 + ciforadenant

Cohort 2c

EXPERIMENTAL

CPI-006 + pembrolizumab

Drug: CPI-006 + pembrolizumab

Interventions

Subjects will receive escalating doses of CPI-006 administered intravenously once every 21 days until MTD is reached or until disease progression.

Cohort 1a

Subjects will receive escalating doses of CPI-006 administered intravenously once every 21 days in combination with CPI-444 orally twice daily until MTD is reached for CPI-006 or until disease progression.

Cohort1b

Subjects will receive escalating doses of CPI-006 in combination with pembrolizumab administered intravenously once every 21 days until MTD is reached for CPI-006 or until disease progression.

Cohort 1c

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Eastern Cooperative Oncology Group (ECOG) Performance Status 0-1.
  • Documented incurable cancer with one of the following histologies: nonsmall cell lung cancer, renal cell cancer, triple negative breast cancer, colorectal cancer with microsatellite instability(MSI), bladder cancer, cervical cancer, uterine cancer, sarcoma, endometrial cancer, and metastatic castration resistant prostate cancer.
  • At least 1 measurable lesion per Response Evaluation Criteria in Solid Tumors (RECIST 1.1).
  • For Escalation: At least 1 but not more than 5 prior systemic therapies for advanced/ recurrent or progressing disease. For Expansion: Subject must have progressed on, be refractory to, or intolerant to 1-3 prior systemic therapies.
  • Willingness to provide tumor biopsies.

You may not qualify if:

  • History of severe hypersensitivity reaction to monoclonal antibodies.
  • Subjects who have received prior therapy with regimens containing cytotoxicT-lymphocyte antigen-4 (CTLA-4), programmed cell death ligand 1 (PDL1), or PD1 antagonists are NOT permitted to enroll unless all adverse events (AEs) while receiving prior immunotherapy have resolved to Grade 1 or baseline prior to screening.
  • History of (non-infectious) pneumonitis that required steroids or subject has current pneumonitis.
  • The use of any investigational medication or device in the 30 days prior to screening and throughout the study is prohibited.
  • Symptomatic, untreated, or actively progressing central nervous system (CNS) metastases.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (27)

Arizona Oncology

Tucson, Arizona, 85711, United States

Location

City Of Hope

Duarte, California, 91010, United States

Location

UC San Francisco

San Francisco, California, 94143, United States

Location

Yale School of Medicine

New Haven, Connecticut, 06519, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

The University of Chicago

Chicago, Illinois, 60637, United States

Location

The John Hopkins University

Baltimore, Maryland, 21224, United States

Location

Dana Farber

Boston, Massachusetts, 02215, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169, United States

Location

NY Hematology

Albany, New York, 12206, United States

Location

Roswell Park Cancer Institute

Buffalo, New York, 14263, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Carolina BioOncology Institute

Huntsville, North Carolina, 28078, United States

Location

Oncology Hematology Care

Cincinnati, Ohio, 45242, United States

Location

University of Oklahoma - Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

UPMC Hillman

Pittsburgh, Pennsylvania, 15232, United States

Location

Greenville

Greenville, South Carolina, 29605, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Mary Crowley Cancer Research

Dallas, Texas, 75230, United States

Location

Virginia Cancer

Fairfax, Virginia, 22031, United States

Location

Froedtert Hospital & Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Lifehouse

Camperdown, New South Wales, 2050, Australia

Location

St. Vincent's Hospital

Darlinghurst, New South Wales, 2010, Australia

Location

Westmead

Westmead, New South Wales, 3168, Australia

Location

Royal Brisbane

Herston, Queensland, 4029, Australia

Location

Monash Hospital

Clayton, Victoria, 3168, Australia

Location

Related Publications (1)

  • Miller RA, Luke JJ, Hu S, Mahabhashyam S, Jones WB, Marron T, Merchan JR, Hughes BGM, Willingham SB. Anti-CD73 antibody activates human B cells, enhances humoral responses and induces redistribution of B cells in patients with cancer. J Immunother Cancer. 2022 Dec;10(12):e005802. doi: 10.1136/jitc-2022-005802.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell LungCarcinoma, Renal CellColorectal NeoplasmsTriple Negative Breast NeoplasmsUterine Cervical NeoplasmsOvarian NeoplasmsPancreatic NeoplasmsEndometrial NeoplasmsSarcomaSquamous Cell Carcinoma of Head and NeckUrinary Bladder NeoplasmsLymphoma, Non-HodgkinLung NeoplasmsKidney NeoplasmsRectal NeoplasmsBreast Neoplasms

Interventions

CPI-006ciforadenantpembrolizumab

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeUrologic NeoplasmsUrogenital NeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesKidney DiseasesUrologic DiseasesMale Urogenital DiseasesIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesUterine NeoplasmsGenital Neoplasms, FemaleUterine Cervical DiseasesUterine DiseasesGenital Diseases, FemaleGenital DiseasesEndocrine Gland NeoplasmsOvarian DiseasesAdnexal DiseasesEndocrine System DiseasesGonadal DisordersPancreatic DiseasesNeoplasms, Connective and Soft TissueCarcinoma, Squamous CellHead and Neck NeoplasmsUrinary Bladder DiseasesLymphomaLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Study Officials

  • S Mahabhashyam, MD

    Corvus Pharmaceuticals

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 5, 2018

First Posted

March 6, 2018

Study Start

April 25, 2018

Primary Completion

December 28, 2022

Study Completion

February 19, 2023

Last Updated

December 21, 2023

Record last verified: 2023-12

Locations