NCT03584516

Brief Summary

The purpose of this study is to assess the efficacy and safety of itacitinib in combination with corticosteroids as first-line treatment for moderate or severe chronic graft-versus-host disease (cGVHD).

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
155

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2019

Longer than P75 for phase_2

Geographic Reach
16 countries

133 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 29, 2018

Completed
13 days until next milestone

First Posted

Study publicly available on registry

July 12, 2018

Completed
6 months until next milestone

Study Start

First participant enrolled

January 17, 2019

Completed
4.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 3, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 3, 2023

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

January 27, 2025

Completed
Last Updated

October 20, 2025

Status Verified

October 1, 2025

Enrollment Period

4.8 years

First QC Date

June 29, 2018

Results QC Date

October 8, 2024

Last Update Submit

October 15, 2025

Conditions

Keywords

Graft-versus-host-diseaseitacitinibJanus kinase inhibitorcorticosteroids

Outcome Measures

Primary Outcomes (3)

  • Part 1: Number of Participants With Dose-limiting Toxicities (DLTs)

    A DLT was defined as the occurrence of any protocol-defined toxicity with onset up to and including Day 28, except those with a clear alternative explanation. Participants who received at least 21 of 28 doses of study drug at the level assigned or had a DLT were considered evaluable for determining tolerability of the dose. Participants who did not achieve this duration of exposure and did not have a DLT were to be replaced for purposes of toxicity identification.

    up to Day 28

  • Part 1 Expansion: Number of Participants With Any Treatment-emergent Adverse Event (TEAE)

    An adverse event (AE) was defined as any untoward medical occurrence associated with the use of a drug in humans, whether or not considered drug related. An AE could therefore have been any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of study treatment. A TEAE was defined as any AE either reported for the first time or the worsening of a pre-existing event after the first dose of study drug.

    until at least 30 days after the last dose of study treatment (up to 1103 days)

  • Part 2: Response Rate at Month 6

    Response rate was defined as the percentage of participants that had complete response (CR) or partial response (PR), per National Institutes of Health (NIH) Consensus Criteria, as determined by the investigator, within 14 days of the post-Baseline visit date until new anti-GVHD therapy or overall response-progression or relapse/progression of underlying disease. CR was defined as the complete resolution of all signs and symptoms of cGvHD in all evaluable organs. PR was defined as an improvement in at least one organ without progression in other organs.

    Month 6

Secondary Outcomes (34)

  • Part 1 Expansion: Response Rate at Months 3 and 6

    Months 3 and 6

  • Parts 1 and 1 Expansion: Cmax of Itacitinib

    Days 1, 7, and 28: predose and 1, 2, and 5 hours post-dose

  • Parts 1 and 1 Expansion: Ctau of Itacitinib

    Day 1: predose, and 1, 2, and 5 hours post-dose. Days 7 and 28: predose, and 1, 2, 5, 12 (for BID dosing), and 24 hours post-dose (for QD dosing)

  • Parts 1 and 1 Expansion: Tmax of Itacitinib

    Day 1: predose, and 1, 2, and 5 hours post-dose. Days 7 and 28: predose, and 1, 2, 5, 12 (for BID dosing), and 24 hours post-dose (for QD dosing)

  • Parts 1 and 1 Expansion: Cl/F of Itacitinib

    Day 1: predose, and 1, 2, and 5 hours post-dose. Days 7 and 28: predose, and 1, 2, 5, 12 (for BID dosing), and 24 hours post-dose (for QD dosing)

  • +29 more secondary outcomes

Study Arms (3)

Part 1 : Dose determination of itacitinib

EXPERIMENTAL

itacitinib administered in combination with corticosteroids.

Drug: ItacitinibDrug: MethylprednisoloneDrug: Prednisone

Part 1 : Dose expansion of itacitinib

EXPERIMENTAL

itacitinib administered in combination with corticosteroids or corticosteroids alone.

Drug: ItacitinibDrug: PlaceboDrug: MethylprednisoloneDrug: Prednisone

Part 2 : itacitinib recommended dose from part 1

PLACEBO COMPARATOR

itacitinib or placebo administered in combination with corticosteroids

Drug: ItacitinibDrug: MethylprednisoloneDrug: Prednisone

Interventions

In Part 1dose determination participants will receive itacitinib administered orally once daily at the protocol-defined dose according to cohort enrollment. In Part 1 expansion, participants will receive either itacitinib administered orally either once daily or twice a day or corticosteroid alone based on the assigned treatment regimen according to cohort enrollment. In Part 2, participants will receive the recommended dose from Part 1 expansion.

Also known as: INCB039110
Part 1 : Dose determination of itacitinibPart 1 : Dose expansion of itacitinibPart 2 : itacitinib recommended dose from part 1

In Part 2, participants will receive matching placebo.

Part 1 : Dose expansion of itacitinib

Administered in Parts 1 and 2 as background reference therapy at a dose level that is commensurate with institutional guidelines based on organ involvement and severity of disease.

Also known as: Medrol, Medrol Dosepak, Solu-Medrol
Part 1 : Dose determination of itacitinibPart 1 : Dose expansion of itacitinibPart 2 : itacitinib recommended dose from part 1

Administered in Parts 1 and 2 as background reference therapy at a dose level that is commensurate with institutional guidelines based on organ involvement and severity of disease.

Also known as: Deltasone, Prednicot, predniSONE Intensol, Rayos, Sterapred, Sterapred DS
Part 1 : Dose determination of itacitinibPart 1 : Dose expansion of itacitinibPart 2 : itacitinib recommended dose from part 1

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Active, clinically diagnosed, moderate or severe cGVHD per NIH Consensus Criteria
  • Underwent allogeneic stem cell transplantation (allo-HCT)
  • Karnofsky Performance Status score ≥ 60%.
  • Evidence of myeloid and platelet engraftment.
  • Willingness to avoid pregnancy or fathering children based on protocol-defined criteria.

You may not qualify if:

  • Has received more than 3 days/72 hours of systemic corticosteroid treatment for cGVHD.
  • Has received any other systemic treatment for cGVHD, including extracorporeal photopheresis (ECP).
  • Prior treatment with a Janus kinase (JAK) inhibitor for acute GVHD, unless the participant achieved complete or partial response and has been off JAK inhibitor treatment for at least 8 weeks before randomization.
  • cGVHD occurring after a nonscheduled donor lymphocyte infusion (DLI) administered for pre-emptive treatment of malignancy recurrence.
  • Evidence of relapsed primary malignancy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (133)

University of Arizona Cancer Center - Out Pt.

Tucson, Arizona, 85724, United States

Location

University of Arkansas For Medical Sciences - Winthrop P Rockefeller Cancer Institute

Little Rock, Arkansas, 72205, United States

Location

City of Hope National Medical Center

Duarte, California, 91010, United States

Location

University of California San Diego Medical Center, Moores Cancer Center

La Jolla, California, 92093, United States

Location

University of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, 33136-1002, United States

Location

Winship Cancer Institute of Emory University

Atlanta, Georgia, 30322, United States

Location

Augusta University - Medical College of Georgia

Augusta, Georgia, 30912, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Illinois Cancer Specialists

Chicago, Illinois, 60714, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153-3328, United States

Location

Advocate Lutheran General Hospital - Oncology Specislists Sc

Park Ridge, Illinois, 60028, United States

Location

Indiana University Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202-5201, United States

Location

University of Kansas Hospital Authority

Westwood, Kansas, 66160, United States

Location

Tulane University

New Orleans, Louisiana, 70112-2618, United States

Location

University of Maryland - Greenebaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111-1552, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Spectrum Health

Grand Rapids, Michigan, 49503, United States

Location

University of Minnesota, Masonic Cancer Center

Minneapolis, Minnesota, 55455, United States

Location

Saint Louis University Cancer Center

St Louis, Missouri, 63110, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601-8550, United States

Location

University of Rochester, James P. Wilmot Cancer Center

Rochester, New York, 14642-0001, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Oncology Hematology Care, Inc

Cincinnati, Ohio, 45236, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106-1716, United States

Location

University of Pennsylvania Abramson Cancer Center

Philadelphia, Pennsylvania, 19104, United States

Location

Jefferson University Hospitals

Philadelphia, Pennsylvania, 19107, United States

Location

Western Pennsylvania Hospital

Pittsburgh, Pennsylvania, 15224, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15232-1309, United States

Location

Avera Cancer Institute

Sioux Falls, South Dakota, 57105-2108, United States

Location

Tri Star Bone Marrow Transplant

Nashville, Tennessee, 37203, United States

Location

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

St David'S South Austin Medical Center

Austin, Texas, 78704, United States

Location

Texas Oncology - Medical City Dallas

Dallas, Texas, 75230, United States

Location

Texas Oncology - Baylor Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Ordensklinikum Linz Gmbh Elisabethinen

Linz, 04020, Austria

Location

Zna Stuivenberg

Antwerp, 02060, Belgium

Location

Institut Jules Bordet

Brussels, 01000, Belgium

Location

Universitair Ziekenhuis Antwerpen (Uza)

Edegem, 02650, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, 09000, Belgium

Location

Universitaire Ziekenhuis Leuven - Gasthuisberg

Leuven, 03000, Belgium

Location

CENTRE HOSPITALIER UNIVERSITAIRE DE LI�GE - SART TILMAN

Liège, 04000, Belgium

Location

AZ DELTA

Roeselare, 08800, Belgium

Location

University of Alberta

Edmonton, Alberta, T6G 2P4, Canada

Location

University Health Network

Toronto, Ontario, M5G 2M9, Canada

Location

Hospital Maisonneuve Rosemont

Montreal, Quebec, H1T 2M4, Canada

Location

Saskatchewan Cancer

Saskatoon, Saskatchewan, S7N 4H4, Canada

Location

The Finsen Centre National Hospital

Copenhagen, 02100, Denmark

Location

Turku University Hospital

Turku, 20521, Finland

Location

Chu Amiens Picardie - Hopital Sud

Amiens, 80054, France

Location

Centre Hospitalier D'Angers

Angers, 49000, France

Location

Chu de Grenoble - Hopital Albert Michallon

Grenoble, 38700, France

Location

Institut Paoli-Calmettes

Marseille, 13273, France

Location

Centre Hospitalier Universitaire de Nantes (Chu de Nantes) - Hotel-Dieu

Nantes, 44000, France

Location

Chu de Nice - Hospital L Archet

Nice, 06800, France

Location

Chu de Rennes - Hospital Pontchaillou

Rennes, 35033, France

Location

Centre Henri Becquerel

Rouen, 76038, France

Location

Chru Hopitaux de Tours Hospital Bretonneau

Tours, 37000, France

Location

Hopitaux de Brabois

Vandœuvre-lès-Nancy, 54511, France

Location

Charite Berlin

Berlin, 12200, Germany

Location

Universitatsklinikum Bonn Aoer

Bonn, 00011, Germany

Location

Universitatsklinikum Koln

Cologne, 50937, Germany

Location

University Clinic Carl Gustav Carus Technical University Dresden

Dresden, 01307, Germany

Location

Universitaetsklinikum Erlangen - Medizinische Klinik 5

Erlangen, 91054, Germany

Location

Universitatsklinikum Essen

Essen, 45147, Germany

Location

UNIVERSIT�TSKLINIKUM HALLE (SAALE)

Halle, D06120, Germany

Location

University Medical Centre Hamburg-Eppendorf Centre of Oncology

Hamburg, 20246, Germany

Location

Universitaetsklinikum Jena

Jena, 07740, Germany

Location

Selbststandige Abteilung Fur Hamatologie Und Internistische Onkologie

Leipzig, 00341, Germany

Location

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

Mainz, 55131, Germany

Location

University Hospital Mannheim

Mannheim, 68167, Germany

Location

Iii Medizinische Klinik Und Poliklinik Klinikum Rechts Der Isar Technische Universitat Munchen

Munich, 81675, Germany

Location

Universitatsklinikum Munster

Münster, 48149, Germany

Location

Universitaetsmedizin Rostock

Rostock, 18057, Germany

Location

Universitaetsklinikum in Tubingen

Tübingen, 72076, Germany

Location

University Hospital of West Attica - Attikon

Chaïdári, 124 62, Greece

Location

General Hospital of Thessaloniki G. Papanikolaou

Thessaloniki, 57010, Greece

Location

Rambam Medical Center

Haifa, 3109601, Israel

Location

Hadassah Hebrew University Medical Center Ein Karem Hadassah

Jerusalem, 91120, Israel

Location

Rabin Medical Center - Beilinson Hospital

Petach Tiqwa, 49100, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

CLINICA DI EMATOLOGIA, UNIVERSIT� POLITECNICA DELLE MARCHE

Ancona, 60126, Italy

Location

Azienda Ospedaliera Papa Giovanni Xxiii

Bergamo, 24127, Italy

Location

L AZIENDA OSPEDALIERO-UNIVERSITARIA DI BOLOGNA POLICLINICO S. ORSOLA � MALPIGHI

Bologna, 40138, Italy

Location

Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia

Brescia, 25123, Italy

Location

Azienda Policlinico Vittorio Emanuele

Catania, 95123, Italy

Location

Fondazione Irccs Ca Granda Ospedale Maggiore

Milan, 20122, Italy

Location

Istituto Di Ricovero E Cura A Carattere Scientifico (Irccs) Ospedale San Raffaele

Milan, 20132, Italy

Location

A.O.U. Di Modena - Policlinico

Modena, 41124, Italy

Location

A.O.U. Federico Ii

Napoli, 80131, Italy

Location

Azienda Ospedaliera Ospedali Riuniti "Villa Sofia - Cervello"

Palermo, 90100, Italy

Location

Comitato Di Bioetica Della Fondazione Irccs Policlinico San Matteo

Pavia, 27100, Italy

Location

Azienda Ospedaliera Bianchi-Melacrino-Morelli Ospedali Riuniti

Reggio Calabria, 89133, Italy

Location

Universita Degli Studi Di Roma La Sapienza - Umberto I Policlinico Di Roma - Centro Di Ematologia

Roma, 00161, Italy

Location

Policlinico Universitario Agostino Gemelli Universita Cattolica Del Sacro Cuore

Roma, 00168, Italy

Location

Irrcs Instituto Clinico Humanitas

Rozzano, 20089, Italy

Location

I.R.C.C.S. Casa Sollievo Della Sofferenza

San Giovanni Rotondo, 71013, Italy

Location

Azienda Ospedaliero Universitaria Citta Della Salute E Della Scienza

Torino, 10126, Italy

Location

Azienda Ospedaliero-Universitaria Santa Maria Della Misericordia

Udine, 33100, Italy

Location

Centro Ricerche Cliniche Di Verona (Crc)

Verona, 37134, Italy

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, 80-592, Poland

Location

Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy Oddzial W Gliwi

Gliwice, 44-101, Poland

Location

Szpital Kliniczny Przemienienia Panskiego

Poznan, 60-569, Poland

Location

Mtz Clinical Research Sp. Zo.O.

Warsaw, 02-106, Poland

Location

Institut Catala D Oncologia

Badalona, 08916, Spain

Location

Hospital de La Santa Creu I Sant Pau

Barcelona, 08041, Spain

Location

Hospital Universitario Virgen de Las Nieves

Granada, 18014, Spain

Location

Ico Institut Catala D Oncologia

L'Hospitalet de Llobregat, 08908, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28007, Spain

Location

Hospital Universitario Ramon Y Cajal

Madrid, 28034, Spain

Location

Hospital Regional Universitario de Malaga

Málaga, 29010, Spain

Location

Son Espases University Hospital

Palma, 07120, Spain

Location

Clinica Universidad de Navarra (Cun)

Pamplona, 31008, Spain

Location

Hospital Clinico Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Marques de Valdecilla

Santander, 39008, Spain

Location

Hospital Clinico de Santiago de Compostela

Santiago de Compostela, 15706, Spain

Location

Hospital Universitario Y Politcnico de La Fe

Valencia, 46009, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Karolinska University Hospital Huddinge

Huddinge, 141 86, Sweden

Location

Skane University Hospital Lund

Lund, 22185, Sweden

Location

Universitatsspital Zurich

Zurich, 08091, Switzerland

Location

Bristol Haematology & Oncology Centre

Bristol, BS2 8ED, United Kingdom

Location

University Hospital of Wales

Cardiff, CF14 4XW, United Kingdom

Location

Barts Health Nhs Trust - St Bartholomews Hospital

London, EC1A 7BE, United Kingdom

Location

King'S College Hospital (Nhs Foundation)

London, SE5 9RS, United Kingdom

Location

Imperial College Healthcare Nhs Trust - Hammersmith Hospital

London, W12 0HS, United Kingdom

Location

Nottingham University Hospitals Nhs Trust

Nottingham, NG5 1PB, United Kingdom

Location

The Royal Marsden Nhs Foundation Trust - Sutton

Sutton, SM2 5PT, United Kingdom

Location

St. George'S University Hospitals Nhs Foundation Trust

Tooting, SW17 0QT, United Kingdom

Location

MeSH Terms

Conditions

Bronchiolitis Obliterans SyndromeGraft vs Host Disease

Interventions

itacitinibINCB039110MethylprednisoloneMethylprednisolone HemisuccinatePrednisone

Condition Hierarchy (Ancestors)

Organizing PneumoniaBronchiolitis ObliteransBronchiolitisBronchitisBronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

PrednisolonePregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsPregnadienediols

Limitations and Caveats

Based on preliminary data, Part 2 did not enroll participants. All participants in Part 1 Expansion who were on treatment with either itacitinib 300 or 400 milligrams (mg) once daily (QD) and who were tolerating and continuing to receive benefit from itacitinib had the option to continue itacitinib treatment in the INCB 39110-801 (NCT04640025) roll-over study.

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Rodica Morariu-Zamfir, MD

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
CROSSOVER
Model Details: In Part 2 of the study, participants in the placebo group will be allowed to cross over to the experimental group after completion of the primary analysis.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 29, 2018

First Posted

July 12, 2018

Study Start

January 17, 2019

Primary Completion

November 3, 2023

Study Completion

November 3, 2023

Last Updated

October 20, 2025

Results First Posted

January 27, 2025

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will share

Incyte shares data with qualified external researchers after a research proposal is submitted. These requests are reviewed and approved by a review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. The trial data availability is according to the criteria and process described on https://www.incyte.com/our-company/compliance-and-transparency

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be shared after the primary publication or 2 years after the study has ended for market authorized products and indications.
Access Criteria
Data from eligible studies will be shared with qualified researchers according to the criteria and process described in the Data Sharing section of the www.incyteclinicaltrials.com website. For approved requests, the researchers will be granted access to anonymized data under the terms of a data sharing agreement.
More information

Locations