NCT03061656

Brief Summary

The purpose of this study is to evaluate the efficacy and toxicity of tandem HDCT/ASCT including high-dose 131I-metaiodobenzylguanidine (MIBG) treatment. In the present study, a single arm trial of tandem HDCT/ASCT will be carried out.

Trial Health

35
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
40

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jan 2009

Longer than P75 for phase_2

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2009

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2013

Completed
3.1 years until next milestone

First Submitted

Initial submission to the registry

February 20, 2017

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 23, 2017

Completed
1.9 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2018

Completed
Last Updated

September 18, 2018

Status Verified

September 1, 2018

Enrollment Period

5 years

First QC Date

February 20, 2017

Last Update Submit

September 17, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Rate of event free survival

    Event is defined as relapse, disease progression or treatment-related mortality.

    Up to 5 years

Secondary Outcomes (1)

  • Rate of treatment-related adverse events as assessed by CTCAE v4.0

    Up to 5 years

Study Arms (1)

High risk neuroblastoma

EXPERIMENTAL

1. Conventional chemotherapy (9 cycles) 2. Surgery conventional chemotherapy (after 6 cycles of chemotherapy) 3. Tandem HDCT/autoSCT * First HDCT (cyclophosphamide, etoposide, carboplatin) * Second HDCT (high-dose 131I-MIBG, thiotepa, melphalan) 4. Local radiotherapy 5. Retinoic acid, interleukin-2

Drug: CyclophosphamideDrug: CarboplatinDrug: EtoposideRadiation: 131I-MIBGDrug: ThiotepaDrug: Melphalan

Interventions

1st HDCT

High risk neuroblastoma

1st HDCT

High risk neuroblastoma

1st HDCT

High risk neuroblastoma
131I-MIBGRADIATION

2nd HDCT

High risk neuroblastoma

2nd HDCT

High risk neuroblastoma

2nd HDCT

High risk neuroblastoma

Eligibility Criteria

AgeUp to 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients with high-risk neuroblastoma

You may not qualify if:

  • Patients with progressive disease before high-dose chemotherapy
  • Patients whose parents want to stop or change the planned treatment
  • Patients with organ toxicities of NCI grade \>2 before high-dose chemotherapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Related Publications (1)

  • Lee JW, Lee S, Cho HW, Ma Y, Yoo KH, Sung KW, Koo HH, Cho EJ, Lee SK, Lim DH. Incorporation of high-dose 131I-metaiodobenzylguanidine treatment into tandem high-dose chemotherapy and autologous stem cell transplantation for high-risk neuroblastoma: results of the SMC NB-2009 study. J Hematol Oncol. 2017 May 16;10(1):108. doi: 10.1186/s13045-017-0477-0.

MeSH Terms

Interventions

CyclophosphamideCarboplatinEtoposide3-IodobenzylguanidineThiotepaMelphalan

Intervention Hierarchy (Ancestors)

Phosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsCoordination ComplexesPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicPolycyclic CompoundsGlucosidesGlycosidesCarbohydratesGuanidinesAmidinesIodobenzenesBenzene DerivativesHydrocarbons, IodinatedTriethylenephosphoramideAziridinesAzirinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and Proteins

Study Officials

  • Ki Woong Sung

    Samsung Medical Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 20, 2017

First Posted

February 23, 2017

Study Start

January 1, 2009

Primary Completion

December 31, 2013

Study Completion

December 31, 2018

Last Updated

September 18, 2018

Record last verified: 2018-09