NCT03013218

Brief Summary

A phase 1, dose escalation study of evorpacept (ALX148) in patients with advanced solid tumors and lymphoma

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
174

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Feb 2017

Longer than P75 for phase_1

Geographic Reach
2 countries

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 15, 2016

Completed
22 days until next milestone

First Posted

Study publicly available on registry

January 6, 2017

Completed
28 days until next milestone

Study Start

First participant enrolled

February 3, 2017

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2022

Completed
3.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 8, 2025

Completed
Last Updated

August 1, 2025

Status Verified

July 1, 2025

Enrollment Period

5 years

First QC Date

December 15, 2016

Last Update Submit

July 30, 2025

Conditions

Keywords

NeoplasmsCD47SIRPαALX148Evorpacept

Outcome Measures

Primary Outcomes (1)

  • Dose-limiting toxicities (Number of participants with a DLT)

    Number of participants with a DLT

    Up to 28 days

Study Arms (6)

Evorpacept (ALX148)

EXPERIMENTAL

The Part 1 Dose Escalation: Evorpacept (ALX148) infusions will be administered weekly or every two weeks.

Drug: Evorpacept (ALX148)

Evorpacept (ALX148) + Pembrolizumab

EXPERIMENTAL

The Part 2 Dose Escalation/Expansion: Evorpacept (ALX148) infusions will be administered weekly or every two weeks in combination with pembrolizumab infusions.

Drug: Evorpacept (ALX148)Drug: Pembrolizumab

Evorpacept (ALX148) + Trastuzumab

EXPERIMENTAL

The Part 2 Dose Escalation/Expansion: Evorpacept (ALX148) infusions will be administered weekly or every two weeks in combination with trastuzumab infusions.

Drug: Evorpacept (ALX148)Drug: Trastuzumab

Evorpacept (ALX148) + Rituximab

EXPERIMENTAL

The Part 2 Dose Escalation/Expansion: Evorpacept (ALX148) infusions will be administered weekly or every two weeks in combination with rituximab infusions.

Drug: Evorpacept (ALX148)Drug: Rituximab

Evorpacept (ALX148) + Pembrolizumab + 5FU + Platinum

EXPERIMENTAL

The Part 2 Dose Escalation: Evorpacept (ALX148) infusions will be administered weekly or every two weeks in combination with pembrolizumab + 5FU + platinum infusions.

Drug: Evorpacept (ALX148)Drug: PembrolizumabDrug: 5-FU + Cisplatin

Evorpacept (ALX148) + Trastuzumab + Ramucirumab + Paclitaxel

EXPERIMENTAL

The Part 2 Dose Escalation: Evorpacept (ALX148) infusions will be administered weekly or every two weeks in combination with trastuzumab + ramucirumab + paclitaxel infusions.

Drug: Evorpacept (ALX148)Drug: TrastuzumabDrug: Ramucirumab + Paclitaxel

Interventions

Evorpacept (ALX148)

Evorpacept (ALX148)Evorpacept (ALX148) + PembrolizumabEvorpacept (ALX148) + Pembrolizumab + 5FU + PlatinumEvorpacept (ALX148) + RituximabEvorpacept (ALX148) + TrastuzumabEvorpacept (ALX148) + Trastuzumab + Ramucirumab + Paclitaxel

Keytruda

Evorpacept (ALX148) + PembrolizumabEvorpacept (ALX148) + Pembrolizumab + 5FU + Platinum

Herceptin

Evorpacept (ALX148) + TrastuzumabEvorpacept (ALX148) + Trastuzumab + Ramucirumab + Paclitaxel

Rituxan

Evorpacept (ALX148) + Rituximab

Standard of care chemotherapy

Evorpacept (ALX148) + Trastuzumab + Ramucirumab + Paclitaxel

Standard of care chemotherapy

Evorpacept (ALX148) + Pembrolizumab + 5FU + Platinum

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histological or cytological diagnosis of advanced/metastatic solid tumor malignancy; or relapsed or refractory Non-Hodgkin lymphoma for whom no standard therapy is available..
  • Adequate Bone Marrow Function.
  • Adequate Renal \& Liver Function.
  • Adequate Performance Status

You may not qualify if:

  • Patients with known symptomatic CNS metastases or lepotomeningeal disease requiring steroids.
  • Previous high-dose chemotherapy requiring allogenic stem cell rescue.
  • Prior treatment with a CD47 or signal regulatory protein (SIRP) alpha targeting agent.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

University of Colorado Denver

Denver, Colorado, 80045, United States

Location

Yale University

New Haven, Connecticut, 06520, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

START-Midwest

Grand Rapids, Michigan, 49503, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

Seoul National University Bundang Hospital

Seongnam, South Korea

Location

Samsung Medical Center

Seoul, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

Severance Hospital, Yonsei University

Seoul, South Korea

Location

Related Publications (2)

  • Kim TM, Lakhani NJ, Soumerai J, Kamdar M, Gainor JF, Messersmith W, Fanning P, Guan S, Jin F, Forgie A, Wan HI, Pons J, Randolph SS, Kim WS. Evorpacept plus rituximab for the treatment of relapsed or refractory non-Hodgkin lymphoma: results from the phase I ASPEN-01 study. Haematologica. 2025 Sep 1;110(9):2102-2112. doi: 10.3324/haematol.2024.286208. Epub 2025 Apr 10.

  • Lakhani NJ, Chow LQM, Gainor JF, LoRusso P, Lee KW, Chung HC, Lee J, Bang YJ, Hodi FS, Kim WS, Santana-Davila R, Fanning P, Squifflet P, Jin F, Kuo TC, Wan HI, Pons J, Randolph SS, Messersmith WA. Evorpacept alone and in combination with pembrolizumab or trastuzumab in patients with advanced solid tumours (ASPEN-01): a first-in-human, open-label, multicentre, phase 1 dose-escalation and dose-expansion study. Lancet Oncol. 2021 Dec;22(12):1740-1751. doi: 10.1016/S1470-2045(21)00584-2. Epub 2021 Nov 15.

MeSH Terms

Conditions

Neoplasm MetastasisLymphoma, Non-HodgkinNeoplasms

Interventions

ALX148pembrolizumabTrastuzumabRituximabRamucirumabPaclitaxelFluorouracilCisplatin

Condition Hierarchy (Ancestors)

Neoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsLymphomaNeoplasms by Histologic TypeLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsAntibodies, Monoclonal, Murine-DerivedTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsChlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum Compounds

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 15, 2016

First Posted

January 6, 2017

Study Start

February 3, 2017

Primary Completion

February 1, 2022

Study Completion

July 8, 2025

Last Updated

August 1, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will not share

Locations