NCT02952534

Brief Summary

The purpose of this study is to determine how patients with metastatic castration-resistant prostate cancer, and evidence of a homologous recombination gene deficiency, respond to treatment with rucaparib.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
277

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2017

Typical duration for phase_2

Geographic Reach
12 countries

149 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 24, 2016

Completed
9 days until next milestone

First Posted

Study publicly available on registry

November 2, 2016

Completed
4 months until next milestone

Study Start

First participant enrolled

February 15, 2017

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 18, 2021

Completed
9 days until next milestone

Study Completion

Last participant's last visit for all outcomes

July 27, 2021

Completed
11 months until next milestone

Results Posted

Study results publicly available

June 8, 2022

Completed
Last Updated

June 9, 2023

Status Verified

June 1, 2023

Enrollment Period

4.4 years

First QC Date

October 24, 2016

Results QC Date

April 12, 2022

Last Update Submit

June 7, 2023

Conditions

Keywords

CRPCPARP inhibitorPARPiBRCAATMHRDTRITONhomologous recombinationDNA repairDNA defectDNA anomalyBARD1BRIP1CDK12CHEK2FANCANBNPALB2RAD51RAD51BRAD51CRAD51DRAD54LgermlinesomaticmCRPC

Outcome Measures

Primary Outcomes (1)

  • Confirmed Objective Response Rate (ORR) by Gene in Patients With Measurable Disease at Baseline Per Central Independent Radiology Review (IRR)

    The primary efficacy endpoint is confirmed radiographic ORR by central IRR. ORR is defined as the percentage of patients with a confirmed CR (complete response) or PR (partial response) by mRECIST (modified Response Evaluation Criteria in Solid Tumors) v1.1/PCWG3 (Prostate Cancer Working Group 3) criteria. The confirmed response is defined as a CR or PR on subsequent tumor assessment at least 28 days after first response documentation in the absence of confirmed progression in bone. CR is disappearance of all target and non-target lesions; any pathological lymph nodes (whether target or non-target) must have reduction in short axis to \<10 mm. PR is at least a 30% decrease in the sum of the diameters of target lesions, taking as reference the baseline sum diameters.

    Assessments every 8 weeks from study day 1 for the first 24 weeks, and then every 12 weeks until disease progression, death, or initiation of subsequent treatment. Total follow-up was up to approximately 3 years.

Secondary Outcomes (12)

  • Confirmed Objective Response Rate (ORR) by Gene in Patients With Measurable Disease at Baseline Per Investigator (INV)

    Assessments every 8 weeks from study day 1 for the first 24 weeks, and then every 12 weeks until disease progression, death, or initiation of subsequent treatment. Total follow-up was up to approximately 3 years.

  • Duration of Response (DOR) by Gene in Patients With Confirmed Response Per Central Independent Radiology Review (IRR)

    Assessments every 8 weeks from study day 1 for the first 24 weeks, and then every 12 weeks until disease progression, death, or initiation of subsequent treatment. Total follow-up was up to approximately 3 years.

  • Duration of Response (DOR) by Gene in Patients With Confirmed Response Per Investigator

    Assessments every 8 weeks from study day 1 for the first 24 weeks, and then every 12 weeks until disease progression, death, or initiation of subsequent treatment. Total follow-up was up to approximately 3 years.

  • Confirmed PSA Response (≥ 50% Decrease) by Gene as Assessed by Local Laboratory

    PSA assessments were done at baseline, Week 5, Week 9, every 4 weeks thereafter, and at Treatment Discontinuation. Total follow-up was up to approximately 39 months.

  • Confirmed PSA Response (≥ 90% Decrease) by Gene as Assessed by Local Laboratory

    PSA assessments were done at baseline, Week 5, Week 9, every 4 weeks thereafter, and at Treatment Discontinuation. Total follow-up was up to approximately 39 months.

  • +7 more secondary outcomes

Study Arms (1)

Rucaparib

EXPERIMENTAL

Oral rucaparib (monotherapy)

Drug: Rucaparib

Interventions

Rucaparib will be administered daily

Also known as: CO-338
Rucaparib

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Be 18 years old at the time the informed consent form is signed
  • Have a histologically or cytologically confirmed adenocarcinoma or poorly differentiated carcinoma of the prostate
  • Be surgically or medically castrated, with serum testosterone levels of ≤ 50 ng/dL (1.73 nM)
  • Experienced disease progression after having received at least 1 but no more than 2 prior next-generation androgen receptor-targeted therapies, and 1 prior taxane-based chemotherapy, for castration-resistant disease
  • Have a deleterious mutation in BRCA1/2 or ATM, or molecular evidence of other homologous recombination deficiency

You may not qualify if:

  • Active second malignancy, with the exception of curatively treated non-melanoma skin cancer, carcinoma in situ, or superficial bladder cancer
  • Prior treatment with any PARP inhibitor, mitoxantrone, cyclophosphamide or any platinum-based chemotherapy
  • Symptomatic and/or untreated central nervous system metastases
  • Pre-existing duodenal stent and/or any gastrointestinal disorder or defect that would, in the opinion of the investigator, interfere with absorption of rucaparib

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (149)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Mayo Clinc

Phoenix, Arizona, 85259, United States

Location

Arizona Oncology Associates

Tucson, Arizona, 85704, United States

Location

Alliance Research Centers

Laguna Hills, California, 92653, United States

Location

VA Greater Los Angeles Healthcare System

Los Angeles, California, 90073, United States

Location

University of Southern California

Los Angeles, California, 90211, United States

Location

Stanford University

Palo Alto, California, 94305, United States

Location

Sharp Memorial Hospital

San Diego, California, 92123, United States

Location

Pacific Hematology Oncology Associates

San Francisco, California, 94115, United States

Location

San Francisco VA Health Care System

San Francisco, California, 94143, United States

Location

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, 94158, United States

Location

Redwood Regional Medical Group

Santa Rosa, California, 95406, United States

Location

Kaiser Permanente Medical Center (Vallejo)

Vallejo, California, 94589, United States

Location

Rocky Mountain Cancer Centers

Aurora, Colorado, 80012, United States

Location

Yale School of Medicine

New Haven, Connecticut, 06510, United States

Location

4701 Ogletown Stanton Rd.

Newark, Delaware, 19713, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Boca Raton Community Hospital, Inc.

Boca Raton, Florida, 33486, United States

Location

Florida Cancer Specialists

Fort Myers, Florida, 33980, United States

Location

University of Florida Health Cancer Center

Orlando, Florida, 32806, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Atlanta Urological Group

Atlanta, Georgia, 30312, United States

Location

University of Chicago Comprehensive Cancer Center

Chicago, Illinois, 60637, United States

Location

Ochsner Medical Center

New Orleans, Louisiana, 70121, United States

Location

University of Maryland Greenebaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Walter Reed Hospital

Bethesda, Maryland, 48202, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

VA Ann Arbor Healthcare System

Ann Arbor, Michigan, 48105, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Fairview Hospital

Edina, Minnesota, 55435, United States

Location

Minnesota Oncology Hematology, P.A.

Minneapolis, Minnesota, 55404, United States

Location

Minnesota Veterans Research Institute

Minneapolis, Minnesota, 55417, United States

Location

HCA Midwest Division - Kansas City

Kansas City, Missouri, 64132, United States

Location

Alegent Health Bergan Mercy Hospital , GU Research Network

Omaha, Nebraska, 68130, United States

Location

Nebraska Cancer Specialists

Omaha, Nebraska, 68130, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89119, United States

Location

Premier Urology Associates dba/AdvanceMed Research

Lawrenceville, New Jersey, 08648, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08901, United States

Location

Roswell Park

Buffalo, New York, 14263, United States

Location

NYU Perlmutter Cancer Center

New York, New York, 10016, United States

Location

Memorial Sloan Kettering CC

New York, New York, 10065, United States

Location

Weill Cornell Medical College/NewYork-Presbyterian Hospital

New York, New York, 10065, United States

Location

Premier Medical Group of the Hudson Valley PC

Poughkeepsie, New York, 12301, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

Carolina Urology Partners

Concord, North Carolina, 28025, United States

Location

The Urology Group

Cincinnati, Ohio, 45212, United States

Location

Kettering Cancer Center

Kettering, Ohio, 45429, United States

Location

Clinical Research Solutions

Middleburg Heights, Ohio, 44130, United States

Location

VA Portland Health Care System

Portland, Oregon, 97219, United States

Location

Consultants in Medical Oncology Hematology

Horsham, Pennsylvania, 19044, United States

Location

SCRI - Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

Texas Oncology Medical City Dallas

Dallas, Texas, 75320, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

UT Health Science Center

Houston, Texas, 77030, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702, United States

Location

Virginia Oncology Associates

Norfolk, Virginia, 23502, United States

Location

VA Puget Sound

Seattle, Washington, 98108, United States

Location

Northern Cancer Insitute, St. Leonards

Saint Leonards, New South Wales, 2065, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Peninsula & Southeast Oncology

Frankston, Victoria, 3199, Australia

Location

Barwon Health, University Hospital Geelong

Geelong, Victoria, 3220, Australia

Location

Cabrini Hospital

Malvern, Victoria, 3144, Australia

Location

Southside Cancer Care Centre

Miranda, 2228, Australia

Location

Orange Health Services

Orange, 2800, Australia

Location

St John of God Hospital, Subiaco

Subiaco, 6008, Australia

Location

Riverina Cancer Care Centre

Wagga Wagga, 2650, Australia

Location

ZNA Middelheim

Antwerp, 2020, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, B-9000, Belgium

Location

AZ Groeninge

Kortrijk, 8500, Belgium

Location

CHU Sart-Tilman

Liège, 4000, Belgium

Location

Equipe de Recherche Clinique, Département d'Oncologie/Hématologie

Liège, 4000, Belgium

Location

AZ DELTA

Roeselare, B-8800, Belgium

Location

Juravinski Cancer Centre Hamilton Health Services

Hamilton, Ontario, L8V5C2, Canada

Location

London Health Science Center - Victoria Hospital

London, Ontario, N6A 4L6, Canada

Location

The Ottawa Hospital

Ottawa, Ontario, K1H8L6, Canada

Location

Princess Margaret Hospital

Toronto, M5G 2M9, Canada

Location

Copenhagen University Hospital

Copenhagen, 2100, Denmark

Location

Herlev Hospital

Herlev, 2730, Denmark

Location

Vejle Sygehus

Vejle, 7100, Denmark

Location

Centre François Baclesse

Caen, 14000, France

Location

Centre Georges François Leclerc

Dijon, 21079, France

Location

Clinique Victor Hugo Centre Jean Bernard

Le Mans, 72000, France

Location

Hôpital Privé La Louvière

Lille, 59800, France

Location

Polyclinique de Gentilly (Centre D'Oncologie De Gentilly)

Nancy, 54100, France

Location

Institut Curie

Paris, 75248, France

Location

Hôpital Privé des Côtes d'Armor

Plérin, 22190, France

Location

CRLCC Eugene Marquis

Rennes, 35042, France

Location

Gemeinschaftspraxis fur Hamatologie & Onkologie

Augsburg, 86150, Germany

Location

Charite Universitatsmedizin Berlin

Berlin, 12200, Germany

Location

Universitätsklinik Köln

Cologne, 50937, Germany

Location

Universitatsklinikum Carl Gustav Carus

Dresden, 01307, Germany

Location

Universitatsklinikum Dusseldorf

Düsseldorf, 40225, Germany

Location

Urologische Gemeinschaftspraxis

Emmendingen, 79312, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf (UKE)

Hamburg, 20246, Germany

Location

Universitaetsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Universitatsklinikum Jena

Jena, 07747, Germany

Location

Universitätsklinikum Schleswig-Holstein

Lübeck, 23538, Germany

Location

Medizinischen Fakultät Mannheim der Universität Heidelberg

Mannheim, 68167, Germany

Location

Studienpraxis Urologie

Nürtingen, 72622, Germany

Location

University of Tuebingen

Tübingen, 72076, Germany

Location

Die Gesundhehitsunion DGU

Wuppertal, 42103, Germany

Location

Cork University Hospital

Cork, T12 DFK4, Ireland

Location

St. Vincent's University Hospital

Dublin, D04T6F4, Ireland

Location

St James's Hospital

Dublin, D08 NHY1, Ireland

Location

Adelaide & Meath Hospital, Incorporating the National Children's Hospital

Dublin, Dublin 24, Ireland

Location

Mater Misericordiae University Hospital

Dublin, Dublin 7, Ireland

Location

Rambam Health Care Campus (RHCC), Rambam Medical Center

Haifa, 3109601, Israel

Location

Hadassah University Hospital

Jerusalem, 71120, Israel

Location

Meir Medical Center

Kfar Saba, 4428164, Israel

Location

Rabin Medical Center-Beilinson Campus

Petah Tikva, 4941492, Israel

Location

Chaim Sheba Medical Center

Ramat Gan, 52621, Israel

Location

The Tel Aviv Sourasky Medical Center (Ichilov Hospital)

Tel Aviv, 64231, Israel

Location

Ospedale San Donato, Azienda USLSUDEST

Arezzo, 52100, Italy

Location

Ospedale Santa Maria delle Croci

Faenza, 48018, Italy

Location

IRCCS Istituto Nazionale dei Tumori (INT)

Milan, 20133, Italy

Location

IEO Instituto Europeo di Oncologia

Milan, 20141, Italy

Location

University of Modena and Reggio Emilia Medical Oncology

Modena, 41124, Italy

Location

Azienda Ospedaliera San Camillo-Forlanini

Rome, 00152, Italy

Location

Azienda Opsedaliera S. Maria di Terni

Terni, 05100, Italy

Location

Santa Chiara Hospital, Dept Medical Oncology

Trento, 38122, Italy

Location

Hospital Universitari Germans Trias i Pujol

Badalona, 08916, Spain

Location

Hospital del Mar, Servicio de Oncología

Barcelona, 08003, Spain

Location

Hospital Clínic i Provincial de Barcelona-Oncology

Barcelona, 08036, Spain

Location

Instituto Catalan de Oncologia

Barcelona, 08908, Spain

Location

Hospital Universitari Germans Trias i Pujol

Barcelona, 08916, Spain

Location

Hospital General Universitario de Guadalajara

Guadalajara, 19002, Spain

Location

Hospital Universitario Lucus Augusti.

Lugo, 27003, Spain

Location

MD Anderson Cancer Center - Madrid

Madrid, 28033, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Puerta de Hierro-Majadahonda

Madrid, 28222, Spain

Location

Hospital Universitario Central de Asturias

Oviedo, 33011, Spain

Location

Corporacio Sanitaria Parc Tauli

Sabadell, 8208, Spain

Location

Marques de Valdecilla University Hospital (HUMV)

Santander, 39008, Spain

Location

Hospital Universitario Virgen del Rocío

Seville, 41013, Spain

Location

Instituto Valenciano de Oncologia IVO

Valencia, 46009, Spain

Location

Wexham Park Hospital

Slough, Berkshire, SL2 4HL, United Kingdom

Location

Mount Vernon Cancer Centre

Northwood, England, HA6 2RN, United Kingdom

Location

Royal Marsden Hospital

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Oxford University Hospitals

Headington, OC3 7LJ, United Kingdom

Location

Royal Liverpool Hospital

Liverpool, L7 8XP, United Kingdom

Location

London Health Science Center - Victoria Hospital

London, N6A 4L6, United Kingdom

Location

Guy's Hospital

London, SE1 9RT, United Kingdom

Location

Sarah Cannon Research Institutute - UK

London, W1G 6AD, United Kingdom

Location

The Clatterbridge Cancer Centre NHS Foundation Trust

Metropolitan Borough of Wirral, CH63 4JY, United Kingdom

Location

Southampton General Hospital

Southampton, SO16 6YD, United Kingdom

Location

Musgrove Park Hospital

Taunton, TA1 5DA, United Kingdom

Location

Related Publications (4)

  • Abida W, Campbell D, Patnaik A, Bryce AH, Shapiro J, Bambury RM, Zhang J, Burke JM, Castellano D, Font A, Ganju V, Hardy-Bessard AC, McDermott R, Sautois B, Spaeth D, Voog E, Piulats JM, Pintus E, Ryan CJ, Merseburger AS, Daugaard G, Heidenreich A, Fizazi K, Loehr A, Despain D, Simmons AD, Dowson M, Go J, Watkins SP, Chowdhury S. Rucaparib for the Treatment of Metastatic Castration-resistant Prostate Cancer Associated with a DNA Damage Repair Gene Alteration: Final Results from the Phase 2 TRITON2 Study. Eur Urol. 2023 Sep;84(3):321-330. doi: 10.1016/j.eururo.2023.05.021. Epub 2023 Jun 3.

  • Collins K, Cheng L. Reprint of: morphologic spectrum of treatment-related changes in prostate tissue and prostate cancer: an updated review. Hum Pathol. 2023 Mar;133:92-101. doi: 10.1016/j.humpath.2023.02.007. Epub 2023 Mar 8.

  • Green ML, Ma SC, Goble S, Giordano H, Maloney L, Simmons AD, Beltman J, Harding TC, Xiao JJ. Population pharmacokinetics of rucaparib in patients with advanced ovarian cancer or other solid tumors. Cancer Chemother Pharmacol. 2022 May;89(5):671-682. doi: 10.1007/s00280-022-04413-7. Epub 2022 Apr 10.

  • Maia MC, Salgia M, Pal SK. Harnessing cell-free DNA: plasma circulating tumour DNA for liquid biopsy in genitourinary cancers. Nat Rev Urol. 2020 May;17(5):271-291. doi: 10.1038/s41585-020-0297-9. Epub 2020 Mar 17.

MeSH Terms

Conditions

Mental Retardation, X-Linked, With Or Without Seizures, Arx-Related

Interventions

rucaparib

Results Point of Contact

Title
Medical Information Department
Organization
Clovis Oncology, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 24, 2016

First Posted

November 2, 2016

Study Start

February 15, 2017

Primary Completion

July 18, 2021

Study Completion

July 27, 2021

Last Updated

June 9, 2023

Results First Posted

June 8, 2022

Record last verified: 2023-06

Data Sharing

IPD Sharing
Will share

De-identified datasets for study results will be made available to qualified researchers in compliance with applicable privacy laws and data protection regulations. Data will be provided by Clovis Oncology.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be made available to qualified researchers after the primary, secondary, and/or exploratory outcomes of the study are reported or published and for 1 year thereafter.
Access Criteria
Requests for de-identified datasets will be made available to qualified researchers following submission of a methodologically sound proposal to medinfo@clovisoncology.com.

Locations