NCT02975934

Brief Summary

The purpose of this study is to determine how participants with metastatic castration-resistant prostate cancer, and evidence of a homologous recombination gene deficiency, respond to treatment with rucaparib versus treatment with physician's choice of abiraterone acetate, enzalutamide, or docetaxel.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
405

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jun 2017

Longer than P75 for phase_3

Geographic Reach
12 countries

150 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 19, 2016

Completed
10 days until next milestone

First Posted

Study publicly available on registry

November 29, 2016

Completed
7 months until next milestone

Study Start

First participant enrolled

June 13, 2017

Completed
5.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 25, 2022

Completed
12 months until next milestone

Results Posted

Study results publicly available

August 16, 2023

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 8, 2024

Completed
Last Updated

July 25, 2025

Status Verified

July 1, 2025

Enrollment Period

5.2 years

First QC Date

November 19, 2016

Results QC Date

June 2, 2023

Last Update Submit

July 24, 2025

Conditions

Keywords

CRPCPARP inhibitorPARPiBRCAATMHRDTRITONhomologous recombinationDNA repairDNA defectDNA anomalygermlinesomaticmCRPC

Outcome Measures

Primary Outcomes (2)

  • Radiographic Progression-free Survival (rPFS) by IRR in Participants With a BRCA Alteration

    The primary efficacy endpoint for the study is rPFSirr, defined as the time from randomization to the first objective evidence of radiographic progression, or death due to any cause (whichever occurs first). Radiographic disease progression includes confirmed soft tissue disease progression and confirmed bone disease progression as per modified RECIST Version 1.1 (at least a 20% increase in the sum of the LD of target lesions or appearance of one or more new extra-skeletal lesions and/or unequivocal progression of existing nontarget lesions) or PCWG3 criteria Progression by bone is determined by PCWG3 criteria in which at least two new lesions appearing during the first 12-week flare window followed by 2 additional new lesions in the confirmatory scan appearing after the 12-week flare window, or after the 12-week flare window, at least 2 new lesions relative to the first post-treatment scan confirmed on a subsequent scan).

    From enrollment to primary completion of study (Total follow-up was up to approximately 4 years)

  • Radiographic Progression-free Survival (rPFS) by IRR in Participants With a BRCA or ATM Alteration Combined

    The primary efficacy endpoint for the study is rPFSirr, defined as the time from randomization to the first objective evidence of radiographic progression, or death due to any cause (whichever occurs first). Radiographic disease progression includes confirmed soft tissue disease progression and confirmed bone disease progression as per modified RECIST Version 1.1 (at least a 20% increase in the sum of the LD of target lesions or appearance of one or more new extra-skeletal lesions and/or unequivocal progression of existing nontarget lesions) or PCWG3 criteria (Progression by bone is determined by PCWG3 criteria in which at least two new lesions appearing during the first 12-week flare window followed by 2 additional new lesions in the confirmatory scan appearing after the 12-week flare window, or after the 12-week flare window, at least 2 new lesions relative to the first post-treatment scan confirmed on a subsequent scan).

    From enrollment to primary completion of study (Total follow-up was up to approximately 4 years)

Secondary Outcomes (16)

  • Overall Survival in Participants With a BRCA Alteration

    From enrollment to completion of study (up to approximately 7 years)

  • Overall Survival in Participants With a BRCA or ATM Alteration Combined

    From enrollment to completion of study (up to approximately 7 years)

  • Objective Response Rate (ORR) by IRR in Participants With a BRCA Alteration

    From enrollment to primary completion of study (Total follow-up was up to approximately 4 years)

  • Objective Response Rate (ORR) by IRR in Participants With a BRCA or ATM Alteration Combined

    From enrollment to primary completion of study (Total follow-up was up to approximately 4 years)

  • Duration of Response (DOR) by IRR in Participants With a BRCA Alteration

    From enrollment to primary completion of study (Total follow-up was up to approximately 4 years)

  • +11 more secondary outcomes

Study Arms (2)

Rucaparib

EXPERIMENTAL

Oral rucaparib (monotherapy).

Drug: Rucaparib

Abiraterone acetate or Enzalutamide or Docetaxel

ACTIVE COMPARATOR

Oral abiraterone acetate (monotherapy, given in combination with prednisone). Oral enzalutamide (monotherapy). Intravenous docetaxel (monotherapy, given in combination with prednisone or prednisolone).

Drug: Abiraterone acetate or Enzalutamide or Docetaxel

Interventions

Rucaparib will be administered daily.

Also known as: CO-338
Rucaparib

Abiraterone acetate and enzalutamide will be administered daily. Docetaxel will be administered every 3 weeks.

Also known as: Zytiga (abiraterone acetate) or Xtandi (enzalutamide) or Taxotere (docetaxel)
Abiraterone acetate or Enzalutamide or Docetaxel

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Be 18 years old at the time the informed consent is signed
  • Have a histologically or cytologically confirmed adenocarcinoma or poorly differentiated carcinoma of the prostate that is metastatic
  • Be surgically or medically castrated, with serum testosterone levels of ≤ 50 ng/dL (1.73 nM)
  • Be eligible for treatment with physician's choice of comparator treatment (abiraterone acetate, enzalutamide or docetaxel)
  • Experienced disease progression after having received 1 prior next generation androgen receptor-targeted therapy
  • Have a deleterious mutation in a BRCA1/2 or ATM gene

You may not qualify if:

  • Active second malignancy, with the exception of curatively treated non melanoma skin cancer, carcinoma in situ, or superficial bladder cancer
  • Prior treatment with any PARP inhibitor
  • Prior treatment with chemotherapy for metastatic castration-resistant prostate cancer
  • Symptomatic and/or untreated central nervous system metastases
  • Pre-existing duodenal stent and/or any gastrointestinal disorder or defect that would, in the opinion of the investigator, interfere with absorption of study drug

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (150)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Mayo Clinic - Arizona

Phoenix, Arizona, 85054, United States

Location

Arizona Oncology Associates - USOR

Tucson, Arizona, 85704, United States

Location

University of Southern California

Beverly Hills, California, 90210, United States

Location

Alliance Research Centers

Laguna Hills, California, 92653, United States

Location

VA Greater Los Angeles Healthcare System

Los Angeles, California, 90073, United States

Location

San Bernardino Urological Associates

San Bernardino, California, 92404, United States

Location

Sharp Memorial Hospital

San Diego, California, 92123, United States

Location

Pacific Hematology Oncology Associates

San Francisco, California, 94115, United States

Location

San Francisco VA Health Care System

San Francisco, California, 94121, United States

Location

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, 94158, United States

Location

St. Joseph Heritage Healthcare

Santa Rosa, California, 95403, United States

Location

Kaiser Permanente, Northern CA

Vallejo, California, 94589, United States

Location

Rocky Mountain Cancer Centers

Aurora, Colorado, 80012, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06510, United States

Location

Medical Oncology Hematology Consultants - USOR

Newark, Delaware, 19713, United States

Location

Boca Raton Community Hospital, Inc.

Boca Raton, Florida, 33486, United States

Location

University of Florida Health Cancer Center

Orlando, Florida, 32806, United States

Location

Atlanta Urological Group

Atlanta, Georgia, 30312, United States

Location

Kaiser Permanente Medical Group

Honolulu, Hawaii, 96819, United States

Location

Ochsner Medical Center

New Orleans, Louisiana, 70121, United States

Location

University of Maryland Greenebaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Walter Reed National Military Medical Center

Bethesda, Maryland, 20889, United States

Location

Maryland Oncology Hematology P.A.

Columbia, Maryland, 21044, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

VA Ann Arbor Healthcare System

Ann Arbor, Michigan, 48105, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Minnesota Oncology Hematology, P.A.

Minneapolis, Minnesota, 55404, United States

Location

Minnesota Veterans Research Institute

Minneapolis, Minnesota, 55417, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Mayo Clinic - Rochester, MN

Rochester, Minnesota, 55902, United States

Location

Alegent Health Bergan Mercy Hospital , GU Research Network

Omaha, Nebraska, 68130, United States

Location

Nebraska Cancer Specialists

Omaha, Nebraska, 68130, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169, United States

Location

Premier Urology Associates

Lawrenceville, New Jersey, 08648, United States

Location

Roswell Park

Buffalo, New York, 14263, United States

Location

NYU Perlmutter Cancer Center

New York, New York, 10016, United States

Location

Memorial Sloan Kettering CC

New York, New York, 10065, United States

Location

Weill Cornell Medical College

New York, New York, 10065, United States

Location

Premier Medical Group of the Hudson Valley PC

Poughkeepsie, New York, 12601, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

University of North Carolina Lineberger Cancer Center

Chapel Hill, North Carolina, 27599, United States

Location

Carolina Urology Partners

Concord, North Carolina, 28025, United States

Location

Durham VA Medical Center

Durham, North Carolina, 27705, United States

Location

Oncology Hematology Care

Cincinnati, Ohio, 45211, United States

Location

The Urology Group

Cincinnati, Ohio, 45212, United States

Location

Kettering Medical Center

Kettering, Ohio, 45429, United States

Location

Clinical Research Solutions

Middleburg Heights, Ohio, 44130, United States

Location

VA Portland Health Care System

Portland, Oregon, 97219, United States

Location

Northwest Cancer Specialist DBA Compass Oncology

Portland, Oregon, 97227, United States

Location

Knight Cancer Institute

Portland, Oregon, 97239, United States

Location

Urology Associates Clinical Research

Nashville, Tennessee, 37209, United States

Location

Urology Clinics of North Texas

Dallas, Texas, 75231, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

UT Health Science Center

Houston, Texas, 77030, United States

Location

Texas Oncology Cancer Center-Round Rock

Round Rock, Texas, 78681, United States

Location

Urology of Virginia

Virginia Beach, Virginia, 23462, United States

Location

MultiCare Regional Cancer Center - Gig Harbor

Gig Harbor, Washington, 98335, United States

Location

VA Puget Sound HCS

Seattle, Washington, 98108, United States

Location

University of Washington Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Southside Cancer Care Centre

Miranda, New South Wales, 2228, Australia

Location

Orange Health Service

Orange, New South Wales, 2800, Australia

Location

Northern Cancer Insitute, St. Leonards

Saint Leonards, New South Wales, 2065, Australia

Location

St John of God Hospital, Subiaco

Subiaco, Western Australia, 6008, Australia

Location

Peninsula & Southeast Oncology

Frankston, 3199, Australia

Location

Barwon Health, University Hospital Geelong

Geelong, 3220, Australia

Location

Royal Hobart Hospital

Hobart, 7000, Australia

Location

Riverina Cancer Care Centre

Wagga Wagga, 2650, Australia

Location

ZNA Middelheim

Antwerp, 2020, Belgium

Location

AZ Groeninge

Kortrijk, 8500, Belgium

Location

CHU Sart-Tilman

Liège, 4000, Belgium

Location

Clinique et Maternité Sainte-Elisabeth

Namur, 5000, Belgium

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

Cancer Care Manitoba

Winnipeg, Manitoba, R3E 0V9, Canada

Location

Centre Hospitalier Universitaire Dr-Georges-L.-Dumont

Moncton, New Brunswick, E1C 8X3, Canada

Location

London Health Sciences Centre

London, Ontario, N6A 4L6, Canada

Location

The Ottawa Hospital

Ottawa, Ontario, K1H8L6, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Lakeridge Health Medical Specialty Medical Oncology

Oshawa, L1G 2B9, Canada

Location

Sunnybrook Odette Cancer Centre

Toronto, M4N3M5, Canada

Location

Copenhagen University Hospital

Copenhagen, 2100, Denmark

Location

Herlev Hospital

Herlev, 2730, Denmark

Location

Vejle Sygehus

Vejle, 7100, Denmark

Location

Centre Georges François Leclerc

Dijon, 21079, France

Location

Clinique Victor Hugo Centre Jean Bernard

Le Mans, 72000, France

Location

Hôpital Privé La Louvière

Lille, 59000, France

Location

Centre Léon Bérard

Lyon, 69008, France

Location

Polyclinique de Gentilly (Centre D'Oncologie De Gentilly)

Nancy, 54000, France

Location

Institut Curie

Paris, 75248, France

Location

Centre Armoricain de Radiotherapie, Imagerie medicale et Oncologie, CARIO

Plérin, 22190, France

Location

CRLCC Eugene Marquis

Rennes, 35042, France

Location

Institut Gustave-Roussy

Villejuif, 94805, France

Location

Gemeinschaftspraxis für Hämatologie&Onkologie

Augsburg, 86150, Germany

Location

Charite - Universitaetsmedizin Berlin

Berlin, 12200, Germany

Location

Apotheke des Städtischen Klinikums Braunschweig

Braunschweig, 38102, Germany

Location

Universitätsklinikum Köln

Cologne, 50937, Germany

Location

University Hospital Carl Gustav Carus

Dresden, 01307, Germany

Location

Universitatsklinikum Dusseldorf

Düsseldorf, 40225, Germany

Location

Urologische Gemeinschaftspraxis

Emmendingen, 79312, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf (UKE)

Hamburg, 20246, Germany

Location

Universitatsklinikum Jena

Jena, 07747, Germany

Location

Universitätsklinikum Schleswig-Holstein

Lübeck, 23538, Germany

Location

Medizinischen Fakultät Mannheim der Universität Heidelberg

Mannheim, 68167, Germany

Location

Studienpraxis Urologie

Nürtingen, 72622, Germany

Location

University of Tuebingen

Tübingen, 72076, Germany

Location

Die GesundheitsUnion (DGU)

Wuppertal, 42103, Germany

Location

Cork University Hospital

Cork, Ireland

Location

Adelaide & Meath Hospital, Incorporating the National Children's Hospital

Dublin, Ireland

Location

Mater Misericordiae University Hospital

Dublin, Ireland

Location

Mater Private Hospital (MPH)

Dublin, Ireland

Location

St James's Hospital

Dublin, Ireland

Location

St. Vincent's University Hospital

Dublin, Ireland

Location

Rambam Health Care Campus (RHCC), Rambam Medical Center

Haifa, 3109601, Israel

Location

Hadassah University Hospital

Jerusalem, 91120, Israel

Location

Meir Medical Center

Kfar Saba, 4428164, Israel

Location

Rabin Medical Center-Beilinson Campus

Petah Tikva, 4941492, Israel

Location

The Tel Aviv Sourasky Medical Center (Ichilov Hospital)

Tel Aviv, 6423, Israel

Location

Chaim Sheba Medical Center

Tel Litwinsky, 5262000, Israel

Location

Ospedale San Donato, Azienda USLSUDEST

Arezzo, 52100, Italy

Location

Ospedale Santa Maria delle Croci

Faenza, 48018, Italy

Location

Romagnolo per lo Studio e la Cura dei Tumori IRST-IRCCS - Oncologia medica

Meldola, 47014, Italy

Location

IEO Instituto Europeo di Oncologia

Milan, 20141, Italy

Location

University of Modena and Reggio Emilia

Modena, 41124, Italy

Location

Azienda Ospedaliera San Camillo-Forlanini

Roma, 00152, Italy

Location

Azienda Opsedaliera S. Maria di Terni

Terni, 05100, Italy

Location

Presidio Ospedaliero Santa Chiara di Trento

Trento, 38122, Italy

Location

Hospital Universitari Germans Trias i Pujol

Barcelona, 08916, Spain

Location

Hospital Universitario Reina Sofia

Córdoba, 14004, Spain

Location

Hospital General Universitario de Guadalajara

Guadalajara, 19002, Spain

Location

Hospital Universitario Lucus Augusti.

Lugo, 27004, Spain

Location

MD Anderson Cancer Center - Madrid

Madrid, 28033, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Clinico Universitario Virgen de la Victoria

Málaga, 29010, Spain

Location

Hospital Universitario Central de Asturias

Oviedo, 33011, Spain

Location

Corporacio Sanitaria Parc Tauli

Sabadell, 08208, Spain

Location

Marques de Valdecilla University Hospital (HUMV)

Santander, 39008, Spain

Location

Hospital Universitario Virgen del Rocío

Seville, 41013, Spain

Location

Instituto Valenciano de Oncología

Valencia, 46009, Spain

Location

Guy's and St Thomas' NHS Foundation Trust

London, England, SE1 9RT, United Kingdom

Location

Royal Marsden Hospital

London, England, SM2 5PT, United Kingdom

Location

Oxford Cancer Centre, Medical Oncology Unit

Oxford, England, OX3 7LE, United Kingdom

Location

Royal Preston Hospital

Preston, England, PR2 9HT, United Kingdom

Location

Wexham Park Hospital

Slough, England, SL2 4HL, United Kingdom

Location

Velindre Hospital

Cardiff, CF14 2TL, United Kingdom

Location

Royal Marsden Hospital

London, SM2 5PT, United Kingdom

Location

The Clatterbridge Cancer Centre NHS Foundation Trust

Metropolitan Borough of Wirral, CH63 4JY, United Kingdom

Location

Musgrove Park Hospital

Taunton, TA15DA, United Kingdom

Location

Related Publications (3)

  • Fizazi K, Piulats JM, Reaume MN, Ostler P, McDermott R, Gingerich JR, Pintus E, Sridhar SS, Bambury RM, Emmenegger U, Lindberg H, Morris D, Nole F, Staffurth J, Redfern C, Saez MI, Abida W, Daugaard G, Heidenreich A, Krieger L, Sautois B, Loehr A, Despain D, Heyes CA, Watkins SP, Chowdhury S, Ryan CJ, Bryce AH; TRITON3 Investigators. Rucaparib or Physician's Choice in Metastatic Prostate Cancer. N Engl J Med. 2023 Feb 23;388(8):719-732. doi: 10.1056/NEJMoa2214676. Epub 2023 Feb 16.

  • Collins K, Cheng L. Reprint of: morphologic spectrum of treatment-related changes in prostate tissue and prostate cancer: an updated review. Hum Pathol. 2023 Mar;133:92-101. doi: 10.1016/j.humpath.2023.02.007. Epub 2023 Mar 8.

  • Maia MC, Salgia M, Pal SK. Harnessing cell-free DNA: plasma circulating tumour DNA for liquid biopsy in genitourinary cancers. Nat Rev Urol. 2020 May;17(5):271-291. doi: 10.1038/s41585-020-0297-9. Epub 2020 Mar 17.

MeSH Terms

Interventions

rucaparibAbiraterone AcetateenzalutamideDocetaxel

Intervention Hierarchy (Ancestors)

AndrostenesAndrostanesSteroidsFused-Ring CompoundsPolycyclic CompoundsTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenes

Results Point of Contact

Title
Medical Information Department
Organization
pharmaand GmbH

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 19, 2016

First Posted

November 29, 2016

Study Start

June 13, 2017

Primary Completion

August 25, 2022

Study Completion

August 8, 2024

Last Updated

July 25, 2025

Results First Posted

August 16, 2023

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

De-identified datasets for study results will be made available to qualified researchers in compliance with applicable privacy laws and data protection regulations. Data will be provided by pharmaand GmbH.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be made available to qualified researchers after the primary, secondary, and/or exploratory outcomes of the study are reported or published and for 1 year thereafter.
Access Criteria
Requests for de-identified datasets will be made available to qualified researchers following submission of a methodologically sound proposal to medinfo@pharmaand.com.

Locations