NCT04171700

Brief Summary

A Phase 2, open-label, single-arm trial to evaluate the response of rucaparib in participants with various solid tumors and with deleterious mutations in Homologous Recombination Repair (HRR) genes.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
83

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2020

Geographic Reach
1 country

19 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 19, 2019

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 21, 2019

Completed
2 months until next milestone

Study Start

First participant enrolled

January 16, 2020

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 8, 2022

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

July 15, 2022

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

October 2, 2023

Completed
Last Updated

October 2, 2023

Status Verified

September 1, 2023

Enrollment Period

2.4 years

First QC Date

November 19, 2019

Results QC Date

May 31, 2023

Last Update Submit

September 29, 2023

Conditions

Keywords

rucaparibPARPirare tumorsolid tumorCO-338ovarian cancerprostate cancerpancreatic cancerbreast cancerlung cancercolon cancergastric cancerbladder cancercolorectal cancerPARP inhibitorhomologous recombinationDNA repairLODESTARgermlinesomaticBRCA1BRCA2PALB2RAD51CRAD51DBARD1BRIP1FANCARAD51RAD51BsarcomaHRRHRDplatinum sensitiveplatinum resistantprimary peritoneal cancerfallopian tube cancertumor agnosticbasket studybasket trialmetastaticlocally advancedesophageal cancerleiomyosarcomaampullary carcinomacarcinosarcomaendometrial cancercervical cancer

Outcome Measures

Primary Outcomes (1)

  • Best Overall Response Rate by Investigator

    Best overall response rate as assessed by the investigator by RECIST v1.1 (or by RECIST v1.1 and PCWG3 in participants with advanced prostate cancer).

    From first dose of study drug until disease progression (up to approximately 2 years)

Secondary Outcomes (7)

  • Overall Response Rate by Independent Radiology Review

    From first dose of study drug until disease progression (up to approximately 2 years)

  • Duration of Response

    From first dose of study drug until disease progression (up to approximately 2 years)

  • Disease Control Rate

    From first dose of study drug until disease progression (up to approximately 2 years)

  • Progression-free Survival

    From first dose of study drug until disease progression (up to approximately 2 years)

  • Overall Survival

    From first dose of study drug until disease progression (up to approximately 2 years)

  • +2 more secondary outcomes

Study Arms (1)

Rucaparib

EXPERIMENTAL

Eligible participants will be enrolled in either Cohort A or Cohort B. Cohort A: Up to 200 participants with deleterious mutations in BRCA1, BRCA2, PALB2, RAD51C or RAD51D. Cohort B (Exploratory): Up to 20 participants with deleterious mutations in BARD1, BRIP1, FANCA, NBN, RAD51 or RAD51B.

Drug: Rucaparib

Interventions

Oral rucaparib will be administered twice daily. The starting dose will be 600 mg daily (BID).

Also known as: Rubraca, Rucaparib camsylate, Rucaparib tablets, CO-338, PF 01367338, AG 014447
Rucaparib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Unresectable, locally advanced or metastatic solid tumor and relapsed/progressive disease
  • Measurable disease per RECIST v1.1 or modified RECIST v1.1 and PCWG3 (for prostate cancer)
  • Have a deleterious mutation (germline or somatic) in BRCA1, BRCA2, PALB2, RAD51C, RAD51D, BARD1, BRIP1, FANCA, NBN, RAD51 or RAD51B. Note: Breast cancer patients that are HER2 negative and have germline BRCA1 or BRCA2 mutations AND patients with epithelial ovarian cancer, fallopian tube cancer, primary peritoneal cancer or metastatic castration-resistant prostate cancer with BRCA1 or BRCA2 mutations are ineligible for this trial.

You may not qualify if:

  • ECOG 0 or 1
  • Tumor tissue available for genomic analysis, or must be willing to have a biopsy if no archival tumor tissue available
  • Adequate organ function
  • Life expectancy of 4 months
  • Active central nervous system brain metastases, leptomeningeal disease or primary tumor of CNS origin
  • Active second malignancy (Exceptions: Successfully treated malignancy with no active disease for 1 year, surgically cured and/or low-risk tumors, or patients receiving ongoing anticancer hormonal therapy for a previously treated cancer)
  • Pre-existing gastrointestinal disorders/conditions interfering with ingestion/absorption of rucaparib
  • Prior treatment with a PARP inhibitor
  • More than 3 prior lines of chemotherapy in the locally advanced/metastatic setting
  • History of myelodysplastic syndrome or acute myeloid leukemia

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (19)

UCLA Medicine Hematology and Oncology

Los Angeles, California, 90024, United States

Location

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, 94158, United States

Location

Florida Cancer Specialists

Fort Myers, Florida, 33901, United States

Location

Florida Cancer Specialists

St. Petersburg, Florida, 33705, United States

Location

H. Lee Moffitt Cancer Center & Research Institute

Tampa, Florida, 33612, United States

Location

Robert H. Lurie Comprehensive Cancer Center of Northwestern University

Chicago, Illinois, 60611, United States

Location

University of Iowa Hospital and Clinics

Iowa City, Iowa, 52242, United States

Location

Beth Israel Deaconess Medical Cancer Surgical Pavilion

Boston, Massachusetts, 02215, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Columbia University Irving Medical Center

New York, New York, 10032, United States

Location

New York Cancer and Blood Specialists

Port Jefferson Station, New York, 11776, United States

Location

New York Cancer And Blood Specialists

The Bronx, New York, 10469, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

Stephenson Cancer Center - The University of Oklahoma

Oklahoma City, Oklahoma, 73104, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

SCRI/Tennessee Oncology - Chattanooga

Chattanooga, Tennessee, 37404, United States

Location

Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

Seattle Cancer Care Alliance/University of Washington

Seattle, Washington, 98109, United States

Location

Related Publications (1)

  • Anbil S, Seewald NJ, Chiorean EG, Hussein M, Kasi PM, Laux DE, Schwartz GK, Shapiro GI, Lin KK, Craib M, Maloney L, McLachlan K, Tukachinsky H, Schrock AB, Wang S, Sokol ES, Decker B, Nathanson KL, Domchek SM, Reiss KA. LODESTAR: A Single-Arm Phase II Study of Rucaparib in Solid Tumors With Pathogenic Germline or Somatic Variants in Homologous Recombination Repair Genes. JCO Precis Oncol. 2025 Jul;9:e2500090. doi: 10.1200/PO-25-00090. Epub 2025 Jul 9.

MeSH Terms

Conditions

Ovarian NeoplasmsProstatic NeoplasmsPancreatic NeoplasmsBreast NeoplasmsLung NeoplasmsColonic NeoplasmsStomach NeoplasmsUrinary Bladder NeoplasmsColorectal NeoplasmsSarcomaFallopian Tube NeoplasmsNeoplasm MetastasisEsophageal NeoplasmsLeiomyosarcomaCarcinosarcomaEndometrial NeoplasmsUterine Cervical Neoplasms

Interventions

rucaparib

Condition Hierarchy (Ancestors)

Endocrine Gland NeoplasmsNeoplasms by SiteNeoplasmsOvarian DiseasesAdnexal DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital Neoplasms, FemaleUrogenital NeoplasmsGenital DiseasesEndocrine System DiseasesGonadal DisordersGenital Neoplasms, MaleGenital Diseases, MaleProstatic DiseasesMale Urogenital DiseasesDigestive System NeoplasmsDigestive System DiseasesPancreatic DiseasesBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesIntestinal NeoplasmsGastrointestinal NeoplasmsGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesStomach DiseasesUrologic NeoplasmsUrinary Bladder DiseasesUrologic DiseasesRectal DiseasesNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeFallopian Tube DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsHead and Neck NeoplasmsEsophageal DiseasesNeoplasms, Muscle TissueNeoplasms, Complex and MixedUterine NeoplasmsUterine DiseasesUterine Cervical Diseases

Results Point of Contact

Title
Kim Reiss Binder
Organization
University of Pennsylvania

Study Officials

  • Kim Reiss-Binder, MD

    University of Pennsylvania

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 19, 2019

First Posted

November 21, 2019

Study Start

January 16, 2020

Primary Completion

June 8, 2022

Study Completion

July 15, 2022

Last Updated

October 2, 2023

Results First Posted

October 2, 2023

Record last verified: 2023-09

Data Sharing

IPD Sharing
Will share

De-identified datasets for study results will be made available to qualified researchers in compliance with applicable privacy laws and data protection regulations. Data will be provided by Clovis Oncology.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be made available to qualified researchers after the primary, secondary, and/or exploratory outcomes of the study are reported or published and for 1 year thereafter.
Access Criteria
Requests for de-identified datasets will be made available to qualified researchers following submission of a methodologically sound proposal to medinfo@clovisoncology.com.

Locations