NCT02914938

Brief Summary

A Three-Arm Study of ME-401 in Subjects with Relapsed/Refractory CLL/SLL or FL, of ME-401 in Combination with Rituximab in Subjects with Relapsed/Refractory CLL/SLL or B-cell NHL, and of ME-401 in Combination with Zanubrutinib in Subjects with Relapsed/Refractory CLL/SLL or B-cell NHL

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
97

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Oct 2016

Longer than P75 for phase_1

Geographic Reach
2 countries

24 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 12, 2016

Completed
14 days until next milestone

First Posted

Study publicly available on registry

September 26, 2016

Completed
5 days until next milestone

Study Start

First participant enrolled

October 1, 2016

Completed
6.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 29, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 29, 2023

Completed
Last Updated

May 9, 2023

Status Verified

December 1, 2022

Enrollment Period

6.5 years

First QC Date

September 12, 2016

Last Update Submit

May 5, 2023

Conditions

Outcome Measures

Primary Outcomes (7)

  • Minimum Biologically Effective Dose (mBED) of ME-401 alone

    The mBED will be defined as the dose that is safe and that achieves an objective response rate that is not less than 30%.

    1 year

  • Maximally Tolerated Dose (MTD) of ME-401 alone

    The MTD will be determined as the maximum dose that is safe. DLT rate closest to .25 and not to exceed 2 DLTs in 6 subjects

    1 year

  • Dose Limiting Toxicities (DLTs) of ME-401 alone

    DLTs will be measured by the number of treatment related AEs that occur within the first 56 days of ME-401 administration, is considered clinically significant by the P.I. and occurs in the presence of supportive care

    within the first 56 days

  • Evaluate the safety and tolerability of ME-401 plus rituximab

    Safety and tolerability will be measured by the number of treatment related AEs

    1 year

  • Determine the MTD of ME-401 plus zanubrutinib

    The MTD of ME-401 is defined as the dose level with a DLT rate closest to 0.25.

    1 year

  • Determine the DLTs of ME-401 plus zanubrutinib

    DLTs will be measured by the number of treatment related AEs that occur within the first 56 days of ME-401 plus zanubrutinib

    within the first 56 days

  • Evaluate the safety and tolerability of ME-401 plus zanubrutinib

    Safety and tolerability will be measured by the number of treatment related AEs

    1 year

Secondary Outcomes (10)

  • Safety profile of ME-401 alone

    1 year

  • Efficacy of ME-401 alone as assessed by (OR)

    2 years

  • Evaluate the (AUC) PK of ME-401 alone

    2 years

  • Evaluate the PK (Cmax) of ME-401 alone

    2 years

  • Efficacy of ME-401 with rituximab

    2 years

  • +5 more secondary outcomes

Study Arms (3)

ME-401 Alone

EXPERIMENTAL

This arm is an open-label, dose escalation study to determine the safety, efficacy and pharmacokinetics of ME-401 along with the mBED, MTD, and DLTs. There are 4 planned cohorts which may enroll up to 61 subjects.

Drug: ME-401

ME-401 in Combination with Rituximab

EXPERIMENTAL

The second arm is an open label study to evaluate the safety, efficacy, and pharmacokinetics of ME-401 in combination with rituximab in subjects with various B-cell malignancies. There are two planned cohorts which may enroll up to 30 subjects.

Drug: ME-401Drug: Rituximab

ME-401 in Combination with Zanubrutinib

EXPERIMENTAL

The third arm is an open label study evaluating the safety, efficacy, MTD, DLT and pharmacokinetics of ME-401 in combination with zanubrutinib in subjects with various B-cell malignancies. This arm will include 2 stages: a safety evaluation stage (cohort of 6-12 subjects) and a disease-specific expansion cohort stage (up to 74 subjects).

Drug: ME-401Drug: Zanubrutinib

Interventions

ME-401DRUG

60 mg

ME-401 AloneME-401 in Combination with RituximabME-401 in Combination with Zanubrutinib

IV infusion 375 mg/m2

Also known as: Rituxan
ME-401 in Combination with Rituximab

80 and 160 mg bid

ME-401 in Combination with Zanubrutinib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of relapsed/refractory CLL and/or relapsed/refractory SLL or FL
  • No prior therapy with PI3Kd inhibitors
  • No prior therapy with Bruton tyrosine kinase (BTK) inhibitors unless the subject was intolerant of BTK therapy or subject had disease progression
  • Subjects with CLL/SLL must have prior treatment with BTK inhibitor and must have had progression or recurrence while on treatment of within 12 mos from BTK treatment
  • Subject must have failed at least 1 prior systemic therapy
  • QT-interval corrected according to Fridericia's formula (QTcF) ≤ 450 milliseconds (ms)
  • Left ventricular ejection fraction \> 50%
  • For subjects, except those with CLL, must have at least one bi-dimensionally measurable nodal lesion \>1.5 cm, as defined by Lugano Classification
  • Willingness to participate in collection of pharmacokinetic samples
  • A negative serum pregnancy test within 14 days of study Day 0, for females of childbearing potential
  • Diagnosis of relapsed/refractory CLL SLL or FL, MZL, DLBCL and high-grade B-cell lymphoma. Subjects must meet the following criteria for relapsed or refractory disease:
  • No prior therapy with PI3Kδ inhibitors
  • No prior therapy with Bruton tyrosine kinase (BTK) inhibitors unless the subject was intolerant of BTK therapy or subject had disease progression
  • Subjects with CLL, SLL, FL, and MZL must have a failure of at least 1 prior systemic therapy and be considered by the investigator a candidate for therapy with a rituximab-based regimen; subjects with DLBCL and high-grade B-cell lymphoma must have a failure of at least 2 prior therapies.
  • QT-interval corrected according to Fridericia's formula (QTcF) ≤450 milliseconds (ms)
  • +13 more criteria

You may not qualify if:

  • Known histological transformation from CLL to an aggressive lymphoma
  • Uncontrolled autoimmune hemolytic anemia or immune thrombocytopenia
  • Subjects who have tested positive for hepatitis B surface antigen and/or hepatitis B core antibody
  • Positive for hepatitis C virus antibody (HCV Ab) or human immunodeficiency virus (HIV) antibody
  • Ongoing drug-induced pneumonitis
  • History of clinically significant cardiovascular abnormalities
  • History of severe bleeding disorders (ME-401 plus zanubrutinib arm only)
  • Known central nervous system (CNS) hemorrhage or stroke within 6 months prior to start of study drugs (ME-401 plus zanubrutinib arm only)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

University of Arizona

Tucson, Arizona, 85724, United States

Location

Compassionate Care

Corona, California, 92708, United States

Location

Sylvester Comprehensive Cancer Center (Univ of Miami School of Med)

Miami, Florida, 33136, United States

Location

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, 02114, United States

Location

Dana Farber

Boston, Massachusetts, 02215, United States

Location

Memorial Sloan Kettering

Basking Ridge, New Jersey, 07920, United States

Location

Memorial Sloan Kettering

Middletown, New Jersey, 07748, United States

Location

Memorial Sloan Kettering

Montvale, New Jersey, 07645, United States

Location

Memorial Sloan Kettering

Commack, New York, 11725, United States

Location

Memorial Sloan Kettering

Harrison, New York, 10604, United States

Location

NYU Langone Laura & Isaac - Perlmutter Cancer Center

New York, New York, 10016, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Stony Brook

Stony Brook, New York, 11794, United States

Location

Memorial Sloan Kettering

Uniondale, New York, 11553, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

Vanderbilt

Nashville, Tennessee, 37240, United States

Location

University of Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Swedish Cancer Institute

Edmonds, Washington, 98026, United States

Location

Swedish Cancer Institute

Issaquah, Washington, 98029, United States

Location

Swedish Cancer Center

Seattle, Washington, 98104, United States

Location

Carbone Cancer Center

Madison, Wisconsin, 53792, United States

Location

lstituto Oncologico della Svizzera ltaliana Ospedale Regionale Bellinzona e Valli CH

Bellinzona, Switzerland

Location

Related Publications (1)

  • Pagel JM, Soumerai JD, Reddy N, Jagadeesh D, Stathis A, Asch A, Salman H, Kenkre VP, Iasonos A, Llorin-Sangalang J, Li J, Zelenetz AD. Zandelisib with continuous or intermittent dosing as monotherapy or in combination with rituximab in patients with relapsed or refractory B-cell malignancy: a multicentre, first-in-patient, dose-escalation and dose-expansion, phase 1b trial. Lancet Oncol. 2022 Aug;23(8):1021-1030. doi: 10.1016/S1470-2045(22)00333-3. Epub 2022 Jul 11.

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-CellLymphoma, FollicularLymphoma, B-Cell, Marginal ZoneLymphoma, Large B-Cell, DiffuseLymphoma, Mantle-Cell

Interventions

ME-401Rituximabzanubrutinib

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsLymphoma, Non-HodgkinLymphomaLymphoma, B-Cell

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: This is a three-arm study of ME-401 alone, of ME-401 in combination with rituximab, and of ME-401 in combination with zanubrutinib in subjects with relapsed/refractory CLL/SLL or B cell NHL. The 3 arms of the study will be conducted in parallel, with subject allocation to ME 401 alone, ME-401 plus rituximab, or ME 401 plus zanubrutinib based on disease type and availability of an open enrollment slot.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 12, 2016

First Posted

September 26, 2016

Study Start

October 1, 2016

Primary Completion

March 29, 2023

Study Completion

March 29, 2023

Last Updated

May 9, 2023

Record last verified: 2022-12

Locations