NCT02706951

Brief Summary

The study objective of Period 1 of this study is to compare the safety and efficacy (signs and symptoms) of upadacitinib 30 mg once daily (QD) alone and upadacitinib 15 mg QD alone versus continuing MTX alone adults with moderately to severely active rheumatoid arthritis (RA) with an inadequate response to MTX. The study objective of Period 2 is to evaluate the long term safety, tolerability, and efficacy of upadacitinib 30 mg QD and 15 mg QD in adults with RA who had completed Period 1.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
648

participants targeted

Target at P75+ for phase_3 rheumatoid-arthritis

Timeline
Completed

Started Mar 2016

Longer than P75 for phase_3 rheumatoid-arthritis

Geographic Reach
23 countries

147 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 18, 2016

Completed
22 days until next milestone

First Posted

Study publicly available on registry

March 11, 2016

Completed
12 days until next milestone

Study Start

First participant enrolled

March 23, 2016

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 2, 2017

Completed
2 years until next milestone

Results Posted

Study results publicly available

October 7, 2019

Completed
2.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 10, 2022

Completed
Last Updated

January 30, 2024

Status Verified

January 1, 2024

Enrollment Period

1.5 years

First QC Date

February 18, 2016

Results QC Date

September 13, 2019

Last Update Submit

January 3, 2024

Conditions

Keywords

Musculoskeletal DiseaseArthritisJoint DiseaseAnti-inflammatory agentsAntirheumatic agentsUpadacitinibABT-494

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants With an American College of Rheumatology 20% (ACR20) Response at Week 14

    The primary endpoint for United States (US)/Food and Drug Administration (FDA) regulatory purposes was ACR 20% response (ACR20) at Week 14. Participants who met the following 3 conditions for improvement from baseline were classified as meeting the ACR20 response criteria: 1. ≥ 20% improvement in 68-tender joint count; 2. ≥ 20% improvement in 66-swollen joint count; and 3. ≥ 20% improvement in at least 3 of the 5 following parameters: * Physician global assessment of disease activity * Patient global assessment of disease activity * Patient assessment of pain * Health Assessment Questionnaire - Disability Index (HAQ-DI) * High-sensitivity C-reactive protein (hsCRP).

    Baseline and week 14

  • Percentage of Participants Achieving Low Disease Activity (LDA) Based on DAS28(CRP) at Week 14

    The primary endpoint for European Union (EU)/European Medicines Agency (EMA) regulatory purposes was low disease activity, based on a Disease Activity Score 28 (DAS28)-CRP score of ≤ 3.2 at Week 14. The DAS28 is a composite index used to assess rheumatoid arthritis disease activity, calculated based on the tender joint count (out of 28 evaluated joints), swollen joint count (out of 28 evaluated joints), Patient's Global Assessment of Disease Activity (0-100 mm), and hsCRP (in mg/L). Scores on the DAS28 range from 0 to approximately 10, where higher scores indicate more disease activity. A DAS28 score less than or equal to 3.2 indicates low disease activity.

    Week 14

Secondary Outcomes (7)

  • Change From Baseline in in Disease Activity Score 28 (CRP) at Week 14

    Baseline to week 14

  • Change From Baseline in Heath Assessment Questionnaire and Disability Index (HAQ-DI) at Week 14

    Baseline to week 14

  • Change From Baseline in Short-Form 36 (SF-36) Physical Component Score (PCS) at Week 14

    Baseline to week 14

  • Percentage of Participants Achieving Clinical Remission (CR) Based on DAS28(CRP) at Week 14

    Week 14

  • Change From Baseline in Duration of Morning Stiffness at Week 14

    Baseline to week 14

  • +2 more secondary outcomes

Study Arms (4)

Upadacitinib 30 mg

EXPERIMENTAL

Period 1: Participants receive upadacitnib 30 mg once daily and placebo to methotrexate once weekly for 14 weeks. Period 2: Participants receive upadacitinib 30 mg once daily until implementation of Protocol Amendment 5 when participants begin to receive upadacitinib 15 mg once daily up to Week 260.

Drug: UpadacitinibDrug: Placebo Methotrexate

Upadacitinib 15 mg

EXPERIMENTAL

Period 1: Participants receive upadacitnib 15 mg once daily and placebo to methotrexate once weekly for 14 weeks. Period 2: Participants receive upadacitinib 15 mg once daily up to Week 260.

Drug: UpadacitinibDrug: Placebo Methotrexate

Methotrexate / Upadacitinib 30 mg

EXPERIMENTAL

Period 1: Participants receive methotrexate once weekly and placebo to upadacitinib once daily for 14 weeks. Period 2: Participants receive upadacitinib 30 mg once daily until implementation of Protocol Amendment 5 when participants begin to receive upadacitinib 15 mg once daily up to Week 260.

Drug: MethotrexateDrug: UpadacitinibDrug: Placebo UpadacitinibDrug: Placebo Methotrexate

Methotrexate / Upadacitinib 15 mg

EXPERIMENTAL

Period 1: Participants receive methotrexate once weekly and placebo to upadacitinib for 14 weeks. Period 2: Participants receive upadacitinib 15 mg once daily up to Week 260.

Drug: MethotrexateDrug: UpadacitinibDrug: Placebo UpadacitinibDrug: Placebo Methotrexate

Interventions

Capsule; Oral

Methotrexate / Upadacitinib 15 mgMethotrexate / Upadacitinib 30 mg

Tablet; Oral

Also known as: ABT-494, Rinvoq
Methotrexate / Upadacitinib 15 mgMethotrexate / Upadacitinib 30 mgUpadacitinib 15 mgUpadacitinib 30 mg

Tablet; Oral

Methotrexate / Upadacitinib 15 mgMethotrexate / Upadacitinib 30 mg

Capsule; Oral

Methotrexate / Upadacitinib 15 mgMethotrexate / Upadacitinib 30 mgUpadacitinib 15 mgUpadacitinib 30 mg

Eligibility Criteria

Age18 Years - 99 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of RA for \>= 3 months.
  • Subjects must have been on oral or parenteral MTX therapy \>= 3 months and on a stable dose for \>= 4 weeks prior to first dose of study drug.
  • Must have discontinued all conventional synthetic disease-modifying anti-rheumatic drugs (csDMARDs) (other than MTX) \>= 4 weeks prior to first dose of study drug.
  • Meets the following minimum disease activity criteria: \>= 6 swollen joints (based on 66 joint counts) and \>= 6 tender joints (based on 68 joint counts) at Screening and Baseline Visits.

You may not qualify if:

  • Prior exposure to any Janus kinase (JAK) inhibitor (including but not limited to tofacitinib, baricitinib, and filgotinib).
  • Prior exposure to any biological disease-modifying anti-rheumatic drugs (bDMARDs).
  • Current diagnosis of inflammatory joint disease other than RA. Current diagnosis of secondary Sjogren's Syndrome is permitted.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (153)

Rheum Assoc of North Alabama /ID# 146009

Huntsville, Alabama, 35801, United States

Location

Alabama Medical Group, PC /ID# 153941

Mobile, Alabama, 36608-1787, United States

Location

ArthroCare Arthritis Care & Re /ID# 143751

Gilbert, Arizona, 85234, United States

Location

Elite Clinical Studies, LLC /ID# 143760

Phoenix, Arizona, 85018, United States

Location

University of Arizona Cancer Center - North Campus /ID# 147175

Tucson, Arizona, 85719-1478, United States

Location

NEA Baptist Womens Clinic /ID# 148904

Jonesboro, Arkansas, 72401, United States

Location

C.V. Mehta MD, Med Corporation /ID# 143762

Hemet, California, 92543, United States

Location

Arthritis Assoc & Osteo Ctr /ID# 147176

Colorado Springs, Colorado, 80920, United States

Location

Ctr Rheum, Immuno, Arthritis /ID# 143766

Fort Lauderdale, Florida, 33309, United States

Location

South Florida Research Ph I-IV /ID# 151983

Miami Springs, Florida, 33166-7225, United States

Location

Advent Clinical Research /ID# 143767

Pinellas Park, Florida, 33781, United States

Location

Sarasota Arthritis Center /ID# 146011

Sarasota, Florida, 34239, United States

Location

W. Broward Rheum Assoc Inc. /ID# 146010

Tamarac, Florida, 33321, United States

Location

Clinical Research West FL /ID# 148726

Tampa, Florida, 33603, United States

Location

SW FL Clin Res Ctr, Tampa, FL /ID# 143763

Tampa, Florida, 33609, United States

Location

University of South Florida /ID# 146004

Tampa, Florida, 33612, United States

Location

BayCare Medical Group, Inc. /ID# 151985

Tampa, Florida, 33614-7101, United States

Location

BayCare Medical Group, Inc. /ID# 163595

Tampa, Florida, 33614-7101, United States

Location

Jefrey D. Lieberman, MD, P.C. /ID# 151816

Decatur, Georgia, 30033, United States

Location

Great Lakes Clinical Trials /ID# 150935

Chicago, Illinois, 60640, United States

Location

PRN Professional Research Network of Kansas, LLC /ID# 143761

Wichita, Kansas, 67205, United States

Location

Ochsner Clinic Foundation /ID# 153573

Baton Rouge, Louisiana, 70836-6455, United States

Location

The Arthritis & Diabetes Clinic, Inc. /ID# 160809

Monroe, Louisiana, 71203, United States

Location

Vanguard Medical Research, LLC /ID# 153124

Shreveport, Louisiana, 71011, United States

Location

Mansfield Health Center /ID# 161627

Mansfield, Massachusetts, 02048, United States

Location

Quality Clinical Research Inc. /ID# 156415

Omaha, Nebraska, 68114, United States

Location

Dartmouth-Hitchcock Medical Center /ID# 146008

Lebanon, New Hampshire, 03756, United States

Location

Albuquerque Clinical Trials, Inc /ID# 147618

Albuquerque, New Mexico, 87102, United States

Location

Arthritis and Osteo Assoc /ID# 147177

Las Cruces, New Mexico, 88011, United States

Location

Coastal Carolina Health Care /ID# 149275

New Bern, North Carolina, 28562, United States

Location

STAT Research, Inc. /ID# 143770

Vandalia, Ohio, 45377-9464, United States

Location

Health Research Oklahoma /ID# 159550

Oklahoma City, Oklahoma, 73103-2400, United States

Location

Healthcare Research Consultant /ID# 147632

Tulsa, Oklahoma, 74135, United States

Location

Innovative Clinical Research /ID# 143757

Greenville, South Carolina, 29601, United States

Location

Nashville Arthritis and Rheumatology /ID# 162641

Nashville, Tennessee, 37203, United States

Location

Tekton Research, Inc. /ID# 159554

Austin, Texas, 78745, United States

Location

Diagnostic Group Integrated He /ID# 148725

Beaumont, Texas, 77701, United States

Location

Trinity Universal Res Assoc /ID# 150138

Carrollton, Texas, 75007, United States

Location

Arth and Osteo Clin Brazo Valley /ID# 160810

College Station, Texas, 77845, United States

Location

Adriana Pop-Moody MD Clinic PA /ID# 147627

Corpus Christi, Texas, 78404, United States

Location

Accurate Clinical Management /ID# 143768

Houston, Texas, 77004, United States

Location

Accurate Clinical Research /ID# 143769

Houston, Texas, 77089, United States

Location

Pioneer Research Solutions, Inc. /ID# 143765

Houston, Texas, 77098-5294, United States

Location

P&I Clinical Research /ID# 151358

Lufkin, Texas, 75904-3132, United States

Location

SW Rheumatology Res. LLC /ID# 147620

Mesquite, Texas, 75150, United States

Location

Sun Research Institute /ID# 159553

San Antonio, Texas, 78215, United States

Location

Arthritis Clinic of Central TX /ID# 149266

San Marcos, Texas, 78666, United States

Location

Adv Rheumatology of Houston /ID# 162609

The Woodlands, Texas, 77382, United States

Location

DM Clinical Research /ID# 151359

Tomball, Texas, 77375, United States

Location

Arthritis & Osteoporosis Clinic /ID# 143752

Waco, Texas, 76710, United States

Location

Ctr for Arth and Rheum Disease /ID# 143759

Chesapeake, Virginia, 23320, United States

Location

Aurora Rheumatology and Immunotherapy Center /ID# 160811

Franklin, Wisconsin, 53132, United States

Location

Mautalen Salud e Investigacion /ID# 145980

Buenos Aires, 1128, Argentina

Location

Ctr Privado Med Familiar /ID# 149183

Buenos Aires, 1417, Argentina

Location

Consultorio Reumatologic Pampa /ID# 145979

Buenos Aires, 1428, Argentina

Location

Centro de Educación Médica e Investigaciones Clínicas "Norberto Quimo" - CEMIC /ID# 149176

Buenos Aires, 1431, Argentina

Location

Cordis S.A. /Id# 152621

Salta, 4400, Argentina

Location

Centro de Enfermedades /ID# 153543

Santa Fe, 2000, Argentina

Location

Royal Prince Alfred Hospital /ID# 146028

Camperdown, New South Wales, 2050, Australia

Location

Rheuma-Zentrum Wien-Oberlaa /ID# 144728

Vienna, 1100, Austria

Location

Algemeen Stedelijk Ziekenhuis /ID# 148720

Aalst, Oost-Vlaanderen, 9300, Belgium

Location

ReumaClinic Genk /ID# 146030

Genk, 3600, Belgium

Location

Diag Consult Ctr 17 Sofia EOOD /ID# 144730

Sofia, 1505, Bulgaria

Location

UMHAT Sv. Ivan Rilski /ID# 147351

Sofia, 1612, Bulgaria

Location

Reg. Clinical Hosptial Concepcion /ID# 151267

Concepción, 4070038, Chile

Location

Quantum Research LTDA. /ID# 145984

Puerto Varas, 5550170, Chile

Location

Quantum Research Stgo. /ID# 145983

Santiago, 7500588, Chile

Location

CTCenter MaVe, s.r.o. /ID# 144823

Olomouc, Olomoucký kraj, 779 00, Czechia

Location

Nuselská poliklinika, Revmatologie /ID# 145986

Prague, Praha 4, 140 00, Czechia

Location

Thomayerova nemocnice /ID# 144736

Prague, Praha 4, 140 00, Czechia

Location

RHEUMA s.r.o. /ID# 144737

Břeclav, 690 02, Czechia

Location

Medical Plus, s.r.o. /ID# 144821

Uherské Hradište, 686 01, Czechia

Location

MediTrials /ID# 159745

Tartu, Tartu, 50406, Estonia

Location

North Estonian Medical Centre /ID# 145455

Tallinn, 13419, Estonia

Location

General Hospital of Athens "Ippokratio" /ID# 144739

Athens, 11527, Greece

Location

Vital Medical Center Orvosi es /ID# 144740

Veszprém, Veszprém megye, 8200, Hungary

Location

Magyar Honvedseg Egeszsegugyi Kozpont /ID# 144743

Budapest, 1134, Hungary

Location

Pest Megyei Flor Ferenc Korhaz /ID# 144742

Kistarcsa, 2143, Hungary

Location

Fejer Megyei Szent Gyorgy Korh /ID# 144741

Székesfehérvár, 8000, Hungary

Location

Barzilai Medical Center /ID# 144744

Ashkelon, 78278, Israel

Location

Bnai Zion Medical Center /ID# 144745

Haifa, 3339419, Israel

Location

The Lady Davis Carmel MC /ID# 147174

Haifa, 3436212, Israel

Location

Sheba Medical Center /ID# 144824

Ramat Gan, 5262100, Israel

Location

Universita di Catanzaro Magna Graecia /ID# 144747

Catanzaro, Calabria, 88100, Italy

Location

A.O.U.I. di Verona Policlinico /ID# 144746

Verona, 37134, Italy

Location

Kondo Clinic for Rheum & Ortho /ID# 148268

Fukuoka, Fukuoka, 810-0001, Japan

Location

NHO Kyushu Medical Center /ID# 148279

Fukuoka, Fukuoka, 810-8563, Japan

Location

NHO Kyushu Medical Center /ID# 148280

Fukuoka, Fukuoka, 810-8563, Japan

Location

Aso Iizuka Hospital /ID# 148272

Iizuka-shi, Fukuoka, 820-8505, Japan

Location

Inoue Hospital /ID# 148069

Takasaki, Gunma, 3700053, Japan

Location

Bay Side Misato Medical Center /ID# 148281

Kochi, Kochi, 781-0112, Japan

Location

Center for Arthritis and Clinical Rheumatology Matsubara Clinic /ID# 148269

Kumamoto, Kumamoto, 862-0920, Japan

Location

Kumamoto Shinto General Hospital /ID# 148286

Kumamoto, Kumamoto, 8628655, Japan

Location

Nagasaki University Hospital /ID# 149859

Nagasaki, Nagasaki, 852-8501, Japan

Location

Sasebo Chuo Hospital /ID# 148275

Sasebo, Nagasaki, 857-1195, Japan

Location

Osaka Red Cross Hospital /ID# 148267

Osaka, Osaka, 543-8555, Japan

Location

Seirei Hamamatsu General Hosp /ID# 148270

Hamamatsu, 430-8558, Japan

Location

Ohira Orthopaedic Hospital /ID# 157944

Hyūga, 883-0043, Japan

Location

Shirahama Hamayu Hospital /ID# 148277

Nishimura, 649-2211, Japan

Location

Sanuki Municipal Hospital /ID# 158080

Sanuki, 769-2321, Japan

Location

Hokkaido University Hospital /ID# 148285

Sapporo, 060-8648, Japan

Location

Hokkaido Medical Center for Rheumatic Diseases /ID# 148274

Sapporo, 063-0811, Japan

Location

Miyasato Clinic /ID# 148271

Shūnan, 745-0824, Japan

Location

Takaoka Rheumatic Orthopedic Clinic /ID# 148068

Takaoka, 933-0874, Japan

Location

Matsuta Clinic /ID# 148278

Tokyo, 155-0032, Japan

Location

National Hospital Organization Shimoshizu National Hospital /ID# 148273

Yotsukaidō, 284-0003, Japan

Location

Desarrollos Biomedicos y Biotc /ID# 147379

Monterrey, Nuevo León, 64060, Mexico

Location

Cryptex Investigación Clínica S.A de C.V /ID# 147095

Mexico City, 06100, Mexico

Location

Medyczne Centrum Hetmanska /ID# 144751

Poznan, Greater Poland Voivodeship, 60-218, Poland

Location

WroMedica I. Bielicka, A. Strzalkowska s.c. /ID# 157622

Wroclaw, Lower Silesian Voivodeship, 51-685, Poland

Location

REUMED Sp.z o.o. Filia nr 1 /ID# 144752

Lublin, Lublin Voivodeship, 20-607, Poland

Location

Centralny Szpital Kliniczny MSWiA w Warszawie /ID# 149521

Warsaw, Masovian Voivodeship, 02-507, Poland

Location

Osteo-Medic spolka cywilna /ID# 144753

Bialystok, Podlaskie Voivodeship, 15-351, Poland

Location

Centrum Badań Klinicznych Pi-House /ID# 149520

Gdansk, Pomeranian Voivodeship, 80-546, Poland

Location

NZOZ Centrum Reumatologiczne /ID# 144749

Elblag, Warmian-Masurian Voivodeship, 82-300, Poland

Location

Instituto Portugues De Reumatologia /ID# 149281

Lisbon, Lisbon District, 1050-034, Portugal

Location

Centro Hospitalar De Vila Nova /ID# 146036

Vila Nova de Gaia, Porto District, 4434-502, Portugal

Location

Centro Hospitalar Lisboa Norte, EPE /ID# 146035

Lisbon, 1649-035, Portugal

Location

Centro Hospitalar Baixo Vouga /ID# 152916

Porto, 4050-111, Portugal

Location

Dr. Ramon L. Ortega-Colon, MD /ID# 145989

Carolina, 00983, Puerto Rico

Location

Ponce School of Medicine /ID# 145990

Ponce, 00716, Puerto Rico

Location

Spitalul Municipal Ploiesti /ID# 144756

Ploieşti, 100337, Romania

Location

Clinical Hospital No.1 n.a. N.I.Pirogov /ID# 147255

Moscow, Moscow, 119049, Russia

Location

LLC Medical Center /ID# 144758

Novosibirsk, Novosibirsk Oblast, 630099, Russia

Location

Perm Clinical Center of FMBA /ID# 145993

Perm, Permskiy Kray, 614109, Russia

Location

Tver Regional Clinical Hosp. /ID# 147254

Tver', Tver Oblast, 170036, Russia

Location

Сity Clinical Hospital 4 /ID# 145994

Ivanovo, 153005, Russia

Location

City Clinical Hospital Botkina /ID# 145995

Moscow, 125284, Russia

Location

City Clinical Hospital #5 /ID# 149832

Nizhny Novgorod, 603005, Russia

Location

Orenburg State Medical Academy /ID# 145992

Orenburg, 460000, Russia

Location

Republican Clin Hos n.a. Baran /ID# 147251

Petrozavodsk, 185019, Russia

Location

Samara Regional Clinical Hosp /ID# 150934

Samara, 443095, Russia

Location

Reg Clin Hosp n.a. Kuvatova G. /ID# 144757

Ufa, 450005, Russia

Location

Yaroslavi State Medical Univer /ID# 147253

Yaroslavl, 150000, Russia

Location

Institute for Rheumatology /ID# 144759

Belgrade, Beograd, 11000, Serbia

Location

Institute for Rheumatology /ID# 144761

Belgrade, Beograd, 11000, Serbia

Location

Institute for Rheumatology /ID# 144762

Belgrade, Beograd, 11000, Serbia

Location

Special Hospital for Rheuma /ID# 144760

Novi Sad, Vojvodina, 21000, Serbia

Location

Wits Clinical Research Site /ID# 149835

Johannesburg, Gauteng, 2193, South Africa

Location

University of Pretoria /ID# 148740

Pretoria, Gauteng, 0001, South Africa

Location

Synexus Helderberg Clinical Tr /ID# 148724

Cape Town, Western Cape, 7130, South Africa

Location

Tiervlei Trial Centre /ID# 153086

Cape Town, Western Cape, 7530, South Africa

Location

Hospital Plató /ID# 145999

Barcelona, 08006, Spain

Location

Hospital Univ Germans Trias I /ID# 146037

Barcelona, 08916, Spain

Location

Hospital Infanta Luisa /ID# 144771

Seville, 41010, Spain

Location

Hospital Universitario de Valm /ID# 144770

Seville, 41014, Spain

Location

Hospital Universitario La Fe /ID# 158013

Valencia, 46026, Spain

Location

Uludağ Üniversitesi Atatürk Rehabilitasyon Uygulama ve Araştırma Merkezi /ID# 144772

Osmangazi, Bursa, 16080, Turkey (Türkiye)

Location

Lviv Regional Clinical Hospita /ID# 154448

Lviv, Lviv Oblast, 79013, Ukraine

Location

Vinnytsia Regional Clinical Hospital n.a. M.I.Pyrogov /ID# 146002

Vinnytsia, Vinnytsia Oblast, 21018, Ukraine

Location

Regional Clinical Hospital /ID# 152007

Ivano-Frankivsk, 76018, Ukraine

Location

NSC-Strazhesko Ist Cardiology /ID# 152004

Kiev, 03680, Ukraine

Location

Zaporizhzhia Regional Clinical /ID# 146000

Zaporizhia, 69600, Ukraine

Location

Related Publications (15)

  • Smolen JS, Pangan AL, Emery P, Rigby W, Tanaka Y, Vargas JI, Zhang Y, Damjanov N, Friedman A, Othman AA, Camp HS, Cohen S. Upadacitinib as monotherapy in patients with active rheumatoid arthritis and inadequate response to methotrexate (SELECT-MONOTHERAPY): a randomised, placebo-controlled, double-blind phase 3 study. Lancet. 2019 Jun 8;393(10188):2303-2311. doi: 10.1016/S0140-6736(19)30419-2. Epub 2019 May 23.

    PMID: 31130260BACKGROUND
  • Burmester GR, Deodhar A, Irvine AD, Panaccione R, Winthrop KL, Vleugels RA, Levy G, Suravaram S, Palac H, Wegrzyn L, Ford S, Meerwein S, Guttman-Yassky E. Safety Profile of Upadacitinib: Descriptive Analysis in Over 27,000 Patient-Years Across Rheumatoid Arthritis, Psoriatic Arthritis, Axial Spondyloarthritis, Atopic Dermatitis, and Inflammatory Bowel Disease. Adv Ther. 2025 Oct;42(10):5215-5237. doi: 10.1007/s12325-025-03328-y. Epub 2025 Aug 28.

  • Smolen JS, Emery P, Rigby W, Tanaka Y, Vargas JI, Jain M, Kato K, Carter KM, Khan N, Phillips C, Meerwein S, Cohen SB. Upadacitinib as monotherapy in patients with rheumatoid arthritis and prior inadequate response to methotrexate: results at 260 weeks from the SELECT-MONOTHERAPY randomised study. RMD Open. 2025 May 11;11(2):e005051. doi: 10.1136/rmdopen-2024-005051.

  • Rubbert-Roth A, Kakehasi AM, Takeuchi T, Schmalzing M, Palac H, Coombs D, Liu J, Anyanwu SI, Lippe R, Curtis JR. Malignancy in the Upadacitinib Clinical Trials for Rheumatoid Arthritis, Psoriatic Arthritis, Ankylosing Spondylitis, and Non-radiographic Axial Spondyloarthritis. Rheumatol Ther. 2024 Feb;11(1):97-112. doi: 10.1007/s40744-023-00621-6. Epub 2023 Nov 20.

  • Charles-Schoeman C, Choy E, McInnes IB, Mysler E, Nash P, Yamaoka K, Lippe R, Khan N, Shmagel AK, Palac H, Suboticki J, Curtis JR. MACE and VTE across upadacitinib clinical trial programmes in rheumatoid arthritis, psoriatic arthritis and ankylosing spondylitis. RMD Open. 2023 Nov;9(4):e003392. doi: 10.1136/rmdopen-2023-003392.

  • Fleischmann R, Curtis JR, Charles-Schoeman C, Mysler E, Yamaoka K, Richez C, Palac H, Dilley D, Liu J, Strengholt S, Burmester G. Safety profile of upadacitinib in patients at risk of cardiovascular disease: integrated post hoc analysis of the SELECT phase III rheumatoid arthritis clinical programme. Ann Rheum Dis. 2023 Sep;82(9):1130-1141. doi: 10.1136/ard-2023-223916. Epub 2023 Jun 12.

  • Conaghan PG, Pavelka K, Hsieh SC, Bonnington TL, Kent TC, Marchbank K, Edwards CJ. Evaluating the efficacy of upadacitinib in patients with moderate rheumatoid arthritis: a post-hoc analysis of the SELECT phase 3 trials. Rheumatol Adv Pract. 2023 Feb 8;7(1):rkad017. doi: 10.1093/rap/rkad017. eCollection 2023.

  • Burmester GR, Cohen SB, Winthrop KL, Nash P, Irvine AD, Deodhar A, Mysler E, Tanaka Y, Liu J, Lacerda AP, Palac H, Shaw T, Mease PJ, Guttman-Yassky E. Safety profile of upadacitinib over 15 000 patient-years across rheumatoid arthritis, psoriatic arthritis, ankylosing spondylitis and atopic dermatitis. RMD Open. 2023 Feb;9(1):e002735. doi: 10.1136/rmdopen-2022-002735.

  • Kakehasi AM, Radominski SC, Baravalle MD, Palazuelos FCI, Garcia-Garcia C, Arruda MS, Curi M, Liu J, Qiao M, Velez-Sanchez P, Vargas JI. Safety of upadacitinib in Latin American patients with rheumatoid arthritis: an integrated safety analysis of the SELECT phase 3 clinical program. Clin Rheumatol. 2023 May;42(5):1249-1258. doi: 10.1007/s10067-023-06513-y. Epub 2023 Jan 30.

  • Bergman M, Buch MH, Tanaka Y, Citera G, Bahlas S, Wong E, Song Y, Zueger P, Ali M, Strand V. Routine Assessment of Patient Index Data 3 (RAPID3) in Patients with Rheumatoid Arthritis Treated with Long-Term Upadacitinib Therapy in Five Randomized Controlled Trials. Rheumatol Ther. 2022 Dec;9(6):1517-1529. doi: 10.1007/s40744-022-00483-4. Epub 2022 Sep 20.

  • Bergman M, Tundia N, Yang M, Orvis E, Clewell J, Bensimon A. Economic Benefit from Improvements in Quality of Life with Upadacitinib: Comparisons with Tofacitinib and Methotrexate in Patients with Rheumatoid Arthritis. Adv Ther. 2021 Dec;38(12):5649-5661. doi: 10.1007/s12325-021-01930-4. Epub 2021 Oct 12.

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Related Links

MeSH Terms

Conditions

Arthritis, RheumatoidMusculoskeletal DiseasesArthritisJoint Diseases

Interventions

Methotrexateupadacitinib

Condition Hierarchy (Ancestors)

Rheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

AminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Global Medical Services
Organization
AbbVie

Study Officials

  • AbbVie Inc.

    AbbVie

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 18, 2016

First Posted

March 11, 2016

Study Start

March 23, 2016

Primary Completion

October 2, 2017

Study Completion

August 10, 2022

Last Updated

January 30, 2024

Results First Posted

October 7, 2019

Record last verified: 2024-01

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible data sharing regarding the clinical trials we sponsor. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information (e.g., protocols and clinical study reports), as long as the trials are not part of an ongoing or planned regulatory submission. This includes requests for clinical trial data for unlicensed products and indications.

Shared Documents
STUDY PROTOCOL, SAP, CSR, ANALYTIC CODE
Time Frame
Data requests can be submitted at any time and the data will be accessible for 12 months, with possible extensions considered.
Access Criteria
Access to this clinical trial data can be requested by any qualified researchers who engage in rigorous, independent scientific research, and will be provided following review and approval of a research proposal and Statistical Analysis Plan (SAP) and execution of a Data Sharing Agreement (DSA). For more information on the process, or to submit a request, visit the following link.
More information

Locations