NCT02600949

Brief Summary

This phase I trial studies the side effects and best way to give personalized peptide vaccine in patients with pancreatic or colorectal cancer that has spread to other places in the body and usually cannot be cured or controlled with treatment (advanced). Personalized peptide vaccine is a vaccine developed from patient's own tumor cells and blood in order to use as a biological therapy. Biological therapies, such as personalized peptide vaccine may attack tumor cells and stop them from growing or kill them.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
300

participants targeted

Target at P75+ for phase_1

Timeline
12mo left

Started May 2016

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress91%
May 2016May 2027

First Submitted

Initial submission to the registry

November 6, 2015

Completed
3 days until next milestone

First Posted

Study publicly available on registry

November 9, 2015

Completed
6 months until next milestone

Study Start

First participant enrolled

May 11, 2016

Completed
11.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 31, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 31, 2027

Last Updated

April 24, 2026

Status Verified

April 1, 2026

Enrollment Period

11.1 years

First QC Date

November 6, 2015

Last Update Submit

April 21, 2026

Conditions

Outcome Measures

Primary Outcomes (3)

  • Proportion of enrolled patients for whom a personalized vaccine is developed and ready to administer (cohorts A and B)

    Up to 12 weeks post-enrollment

  • Proportion of enrolled patients who receive at least 1 dose of vaccine at any time post-enrollment (cohorts A and B)

    Up to 44 weeks

  • Incidence of adverse events (AEs)

    Defined as the proportion of subjects who experience at least one toxicity event per National Cancer Institute Common Toxicity Criteria for Adverse Events version 4.0. A toxicity event is defined as at least one grade 3 or 4 non-hematologic or grade 4 hematologic toxicity. Proportion of patients with AEs will be estimated, along with the Bayesian 95% credible interval.

    Up to 24 weeks

Secondary Outcomes (12)

  • Proportion of patients who have received at least one dose of vaccine that is alive and progression free defined based on response criteria according to Response Evaluation Criteria in Solid Tumors (RECIST) 1.1

    At 12 weeks post-vaccination (second re-staging scan)

  • Progression-free survival (cohorts A and B and C)

    The time between the date of first vaccination and evidence of progression on computed tomography scan or the date of death due to any cause, assessed up to 6 months after the last dose of vaccine

  • Response rate (cohort A and B)

    Up to 12 weeks

  • Change in tumor biomarker (CA19-9, carcinoembryonic antigen [CEA] or circulating free deoxyribonucleic acid [cfDNA] mutation)

    Up to 6 months

  • Overall survival

    The time from first vaccination to death, assessed up to 6 months after the last dose of vaccine

  • +7 more secondary outcomes

Study Arms (3)

Cohort A (personalized vaccine, imiquimod)

EXPERIMENTAL

Patients receive personalized synthetic tumor-associated peptide vaccine therapy SC on day 1 of weeks 0, 1, 3, 4, 6, 12, and 24. Beginning 15 minutes after each vaccine is administered, patients then receive imiquimod cream topically in the absence of disease progression or unacceptable toxicity. Patients also undergo CT or MRI scans at baseline and at weeks 0 and 6, then every 3 months, and at week 39.

Drug: ImiquimodBiological: Synthetic Tumor-Associated Peptide Vaccine TherapyProcedure: Computed TomographyProcedure: Magnetic Resonance Imaging

Cohort B (personalized vaccine, imiquimod, pembrolizumab)

EXPERIMENTAL

Patients receive personalized synthetic tumor-associated peptide vaccine therapy SC on day 1 of weeks 0, 1, 3, 4, 6, 12, and 24. Beginning 15 minutes after each vaccine is administered, patients receive imiquimod cream topically. Patients also receive pembrolizumab IV over 30 minutes every 3 weeks until week 24 in the absence of disease progression or unacceptable toxicity. Patients also undergo CT or MRI scans at baseline and at weeks 0 and 6, then every 3 months, and at week 39.

Drug: ImiquimodBiological: PembrolizumabBiological: Synthetic Tumor-Associated Peptide Vaccine TherapyProcedure: Computed TomographyProcedure: Magnetic Resonance Imaging

Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)

EXPERIMENTAL

Patients receive personalized synthetic tumor-associated peptide vaccine therapy SC on day 1 of weeks 0, 1, 3, 4, 6, 9, 12, 15, 18, 21, and 24. Beginning 15 minutes after each vaccine is administered, patients receive imiquimod cream topically. Patients also receive pembrolizumab IV over 30 minutes every 3 weeks until week 24 in the absence of disease progression or unacceptable toxicity. Beginning about 1 hour after each vaccine, patients also receive sotigalimab IV over 60 minutes on day 1 of weeks 0, 1, 3, 4, 6, 12, and 24 in the absence of disease progression or unacceptable toxicity. Patients also undergo CT or MRI scans at baseline and weeks 6,12, and 24, then every 3 months, and at week 39.

Drug: ImiquimodBiological: PembrolizumabBiological: SotigalimabBiological: Synthetic Tumor-Associated Peptide Vaccine TherapyProcedure: Computed TomographyProcedure: Magnetic Resonance Imaging

Interventions

Undergo MRI

Also known as: Magnetic Resonance Imaging Scan, Medical Imaging, Magnetic Resonance / Nuclear Magnetic Resonance, MR Imaging, MRI, MR, MRI Scan, Nuclear Magnetic Resonance Imaging, NMR, NMRI, NMR Imaging
Cohort A (personalized vaccine, imiquimod)Cohort B (personalized vaccine, imiquimod, pembrolizumab)Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)

Applied topically

Also known as: Aldara, R 837, S 26308, Zyclara
Cohort A (personalized vaccine, imiquimod)Cohort B (personalized vaccine, imiquimod, pembrolizumab)Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)
PembrolizumabBIOLOGICAL

Given IV

Also known as: Keytruda, Lambrolizumab, MK-3475, SCH 900475
Cohort B (personalized vaccine, imiquimod, pembrolizumab)Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)
SotigalimabBIOLOGICAL

Given IV

Also known as: APX 005, APX 005M, APX-005M, APX005M, CD40 Agonistic Monoclonal Antibody APX005M, EPI-0050
Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)

Undergo CT

Also known as: CAT, CAT Scan, Computed Axial Tomography, CT
Cohort A (personalized vaccine, imiquimod)Cohort B (personalized vaccine, imiquimod, pembrolizumab)Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)

Given SC

Cohort A (personalized vaccine, imiquimod)Cohort B (personalized vaccine, imiquimod, pembrolizumab)Cohort C and D (vaccine, imiquimod, pembrolizumab, APX005M)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Metastatic CRC or PDA planned to or have undergone complete surgical resection (metastatectomy) and also for PDA participants with localized disease planned for primary tumor resection.
  • Any lines (including zero) of therapy prior to tissue harvest.
  • Adequate tumor tissue availability
  • Adults (age ≥ 18)
  • ECOG PS 0-1
  • Life expectancy \>12 months for Cohort C and \>9 months for Cohort D
  • Adequate organ and marrow function
  • Ability to understand and the willingness to sign a written informed consent document.
  • As the effects of a peptide based vaccine, pembrolizumab or APX005M on the developing human fetus are unknown, women of child-bearing potential and men must agree to use adequate contraception at study entry and for the duration of study participation. Should a woman become pregnant or suspect she is pregnant, she should inform her treating physician immediately. Unless surgically sterile by bilateral tubal ligation or vasectomy of partner(s), sexually active participants must use birth control during and for \>120 days after the study. Abstinence is also an acceptable form of birth control.
  • For Cohort C only: participants must have metastatic CRC and are planned to or have undergone complete metastecomy/ies and agree to have post-operative blood draw for ctDNA testing within 6 weeks following surgical resection.

You may not qualify if:

  • History of HIV or AIDS
  • Patients with brain metastasis
  • Serious autoimmune conditions
  • Use of chronic immune suppressive medications.
  • Uncontrolled concurrent illness including, but not limited to ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements.
  • Women of child bearing potential who are pregnant or breastfeeding. Women with a positive pregnancy test at enrollment or prior to administration of vaccine. .
  • Has history of (non-infectious) pneumonitis that required steroids, evidence of interstitial lung disease or active, non-infectious pneumonitis.
  • Known history of active TB (Bacillus Tuberculosis).
  • Hypersensitivity to therapy drugs or their components.
  • Has a known additional malignancy that is progressing or requires active treatment.
  • Active coagulopathy.
  • History of arterial thrombosis within 3 months prior to starting study treatment.
  • History of New York Heart Association Class 3-4 heart failure or myocardial infarction within 6 months prior to starting therapy.
  • Known history of Hepatitis B or known active Hepatitis C.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

M D Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Colorectal Neoplasms

Interventions

ImiquimodpembrolizumabsotigalimabMagnetic Resonance SpectroscopyX-Rays

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Intervention Hierarchy (Ancestors)

AminoquinolinesQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsSpectrum AnalysisChemistry Techniques, AnalyticalInvestigative TechniquesElectromagnetic RadiationElectromagnetic PhenomenaMagnetic PhenomenaPhysical PhenomenaRadiationRadiation, Ionizing

Study Officials

  • Michael J Overman

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 6, 2015

First Posted

November 9, 2015

Study Start

May 11, 2016

Primary Completion (Estimated)

May 31, 2027

Study Completion (Estimated)

May 31, 2027

Last Updated

April 24, 2026

Record last verified: 2026-04

Locations