NCT02117479

Brief Summary

Determining the efficacy, based upon overall survival, of ruxolitinib added to capecitabine for the treatment of advanced or metastatic pancreatic cancer.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
321

participants targeted

Target at P50-P75 for phase_3 pancreatic-cancer

Timeline
Completed

Started Mar 2014

Shorter than P25 for phase_3 pancreatic-cancer

Geographic Reach
12 countries

230 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2014

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

April 16, 2014

Completed
5 days until next milestone

First Posted

Study publicly available on registry

April 21, 2014

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2016

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2016

Completed
7 months until next milestone

Results Posted

Study results publicly available

July 11, 2017

Completed
Last Updated

March 26, 2019

Status Verified

March 1, 2019

Enrollment Period

1.9 years

First QC Date

April 16, 2014

Results QC Date

February 9, 2017

Last Update Submit

March 14, 2019

Conditions

Keywords

Metastatic pancreatic cancerMetastatic pancreatic adenocarcinoma that is recurrent

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    Overall survival is reported here based on the number of deaths from randomization up to 6-months or to the data cutoff 11FEB2016.

    Randomization until death due to any cause; up to the data cutoff 11FEB2016.

Secondary Outcomes (5)

  • Progression-free Survival (PFS)

    Randomization to disease progression, or death due to any cause if sooner; up to 6-months or to the data cutoff 11FEB2016.

  • Percentage of Participants Achieving Progression Free Survival (PFS)

    Randomization to disease progression, or death due to any cause if sooner; up to 6-months or to the data cutoff 11FEB2016.

  • Objective Response Rate (ORR)

    Baseline through end of study; up to 6-months or to the data cutoff 11FEB2016.

  • Duration of Response

    Baseline through end of study; up to 6-months or to the data cutoff 11FEB2016.

  • Participants With Treatment-Emergent Adverse Events (TEAEs)

    Baseline through approximately 30 days post treatment discontinuation; up to 6-months or to the data cutoff 11FEB2016.

Study Arms (2)

Ruxolitinib plus capecitabine

EXPERIMENTAL
Drug: RuxolitinibDrug: Capecitabine

Placebo plus capecitabine

ACTIVE COMPARATOR
Drug: PlaceboDrug: Capecitabine

Interventions

5 mg tablets to be administered by mouth twice daily (BID)

Also known as: Jakafi ®, Jakavi ®
Ruxolitinib plus capecitabine

5 mg tablets to be administered by mouth twice daily (BID)

Placebo plus capecitabine

150 and 500 mg tablets to be administered by mouth twice daily (BID)

Placebo plus capecitabineRuxolitinib plus capecitabine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the pancreas.
  • Advanced adenocarcinoma of the pancreas that is inoperable or metastatic.
  • Eastern Cooperative Oncology Group (ECOG) performance status 0 to 2
  • Received 1 prior chemotherapy regimen for advanced or metastatic disease (not including neoadjuvant and/or adjuvant therapy).
  • ≥ 2 weeks elapsed from the completion of previous treatment regimen and participants must have recovered or be at a new stable baseline from any related toxicities.
  • Radiographically measurable or evaluable disease
  • Modified Glasgow Prognostic Score (mGPS) of 1 or 2 as defined below:
  • mGPS of 1: C-reactive protein \>10 mg/L and albumin ≥35 g/L
  • mGPS of 2: C-reactive protein \>10 mg/L and albumin \<35 g/L

You may not qualify if:

  • Received more than 1 prior regimen for advanced or metastatic disease.
  • Ongoing radiation therapy, radiation therapy administered within 30 days of enrollment.
  • Concurrent anticancer therapy (eg, chemotherapy, radiation therapy, surgery, immunotherapy, biologic therapy, hormonal therapy, investigational therapy, or tumor embolization).
  • Prior severe reaction to fluoropyrimidines, known dihydropyrimidine dehydrogenase deficiency (DPD), or other known hypersensitivity to active substances, including fluorouracil (5-FU), or ruxolitinib, or any of their excipients.
  • Prior treatment with a JAK inhibitor for any indication.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (230)

Unknown Facility

Avondale, Arizona, United States

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Chandler, Arizona, United States

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Gilbert, Arizona, United States

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Glendale, Arizona, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Surprise, Arizona, United States

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Tucson, Arizona, United States

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Hot Springs, Arkansas, United States

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Jonesboro, Arkansas, United States

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Anaheim, California, United States

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Bakersfield, California, United States

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Berkeley, California, United States

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Beverly Hills, California, United States

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Chula Vista, California, United States

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Covina, California, United States

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Downey, California, United States

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El Cajon, California, United States

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Fullerton, California, United States

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Gilroy, California, United States

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Glendale, California, United States

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La Mesa, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Lynwood, California, United States

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Modesto, California, United States

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Montebello, California, United States

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Northridge, California, United States

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Oceanside, California, United States

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Orange, California, United States

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Redondo Beach, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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San Luis Obispo, California, United States

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Santa Ana, California, United States

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Santa Maria, California, United States

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Santa Monica, California, United States

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Torrance, California, United States

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Whittier, California, United States

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Aurora, Colorado, United States

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Boulder, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Grand Junction, Colorado, United States

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Longmont, Colorado, United States

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Thornton, Colorado, United States

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New Britain, Connecticut, United States

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New Haven, Connecticut, United States

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Southington, Connecticut, United States

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Trumbull, Connecticut, United States

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Newark, Delaware, United States

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Boca Raton, Florida, United States

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Hollywood, Florida, United States

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Miami, Florida, United States

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Pembroke Pines, Florida, United States

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Atlanta, Georgia, United States

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Austell, Georgia, United States

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Carrollton, Georgia, United States

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Cartersville, Georgia, United States

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Douglasville, Georgia, United States

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Marietta, Georgia, United States

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Newnan, Georgia, United States

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Rome, Georgia, United States

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Thomasville, Georgia, United States

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Arlington Heights, Illinois, United States

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Chicago, Illinois, United States

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Hinsdale, Illinois, United States

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Niles, Illinois, United States

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Urbana, Illinois, United States

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Goshen, Indiana, United States

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Indianapolis, Indiana, United States

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Topeka, Kansas, United States

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Ashland, Kentucky, United States

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Louisville, Kentucky, United States

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Metairie, Louisiana, United States

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New Orleans, Louisiana, United States

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Scarborough, Maine, United States

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Annapolis, Maryland, United States

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Baltimore, Maryland, United States

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Bethesda, Maryland, United States

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Rockville, Maryland, United States

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Worcester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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Kalamazoo, Michigan, United States

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Lansing, Michigan, United States

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Woodbury, Minnesota, United States

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Bolivar, Missouri, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Kalispell, Montana, United States

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Hastings, Nebraska, United States

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Omaha, Nebraska, United States

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Papillion, Nebraska, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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East Orange, New Jersey, United States

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Farmington, New Mexico, United States

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Binghamton, New York, United States

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Fresh Meadows, New York, United States

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Hudson, New York, United States

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Johnson City, New York, United States

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New York, New York, United States

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Nyack, New York, United States

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Rochester, New York, United States

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The Bronx, New York, United States

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Durham, North Carolina, United States

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Wake Forest, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Canton, Ohio, United States

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Columbus, Ohio, United States

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Middletown, Ohio, United States

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Oregon, Ohio, United States

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Toledo, Ohio, United States

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Eugene, Oregon, United States

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Portland, Oregon, United States

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Springfield, Oregon, United States

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Tualatin, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Seneca, South Carolina, United States

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Spartanburg, South Carolina, United States

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Chattanooga, Tennessee, United States

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Knoxville, Tennessee, United States

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Memphis, Tennessee, United States

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Nashville, Tennessee, United States

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Arlington, Texas, United States

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Austin, Texas, United States

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Beaumont, Texas, United States

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Bedford, Texas, United States

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Cedar Park, Texas, United States

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Dallas, Texas, United States

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Denton, Texas, United States

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El Paso, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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Plano, Texas, United States

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Round Rock, Texas, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Tyler, Texas, United States

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Waco, Texas, United States

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Ogden, Utah, United States

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Salt Lake City, Utah, United States

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Blacksburg, Virginia, United States

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Richmond, Virginia, United States

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Roanoke, Virginia, United States

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Salem, Virginia, United States

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Wytheville, Virginia, United States

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Seattle, Washington, United States

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Vancouver, Washington, United States

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Madison, Wisconsin, United States

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Australian Capital Territory, Australia

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New South Wales, Australia

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South Australia, Australia

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Victoria, Australia

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Aalst, Belgium

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Bruges, Belgium

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Brussels, Belgium

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Edegem, Belgium

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Ghent, Belgium

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Gilly, Belgium

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Kortrijk, Belgium

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Leuven, Belgium

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Calgary, Alberta, Canada

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Oshawa, Ontario, Canada

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Sault Ste. Marie, Ontario, Canada

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Toronto, Ontario, Canada

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Greenfield Park, Quebec, Canada

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Laval, Quebec, Canada

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Montreal, Quebec, Canada

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Aschaffenburg, Germany

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Berlin, Germany

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Bochum, Germany

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Cologne, Germany

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Essen, Germany

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Frankford, Germany

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Velbert, Germany

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Aviano, Italy

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Bari, Italy

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Bergamo, Italy

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Brescia, Italy

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Cremona, Italy

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Florence, Italy

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Genova, Italy

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Lido di Camaiore, Italy

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Milan, Italy

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Napoli, Italy

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Pisa, Italy

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Rimini, Italy

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Roma, Italy

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Auckland, New Zealand

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Christchurch, New Zealand

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Hamilton, New Zealand

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Hwasun-gun, South Korea

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Seongnam-si, South Korea

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Seoul, South Korea

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Badajoz, Spain

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Barcelona, Spain

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Madrid, Spain

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Málaga, Spain

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Seville, Spain

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Taichung, Taiwan

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Tainan, Taiwan

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Taipei, Taiwan

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Patumwan, Thailand

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Ratchathewi, Thailand

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Seetatarom, Thailand

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Aberdeen, United Kingdom

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Bangor, United Kingdom

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Birmingham, United Kingdom

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Boston, United Kingdom

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Bristol, United Kingdom

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Cardiff, United Kingdom

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Glasgow, United Kingdom

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Guildford, United Kingdom

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Harlow, United Kingdom

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Huddersfield, United Kingdom

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Lancaster, United Kingdom

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Leeds, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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Metropolitan Borough of Wirral, United Kingdom

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Newcastle upon Tyne, United Kingdom

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Nottingham, United Kingdom

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Plymouth, United Kingdom

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Southampton, United Kingdom

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Sutton, United Kingdom

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Welwyn Garden City, United Kingdom

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Related Publications (1)

  • Hurwitz H, Van Cutsem E, Bendell J, Hidalgo M, Li CP, Salvo MG, Macarulla T, Sahai V, Sama A, Greeno E, Yu KH, Verslype C, Dawkins F, Walker C, Clark J, O'Reilly EM. Ruxolitinib + capecitabine in advanced/metastatic pancreatic cancer after disease progression/intolerance to first-line therapy: JANUS 1 and 2 randomized phase III studies. Invest New Drugs. 2018 Aug;36(4):683-695. doi: 10.1007/s10637-018-0580-2. Epub 2018 Mar 6.

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

ruxolitinibCapecitabine

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

DeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsFluorouracilUracilPyrimidinonesDeoxyribonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Limitations and Caveats

The study was terminated as other related studies of ruxolitinib did not provide sufficient efficacy to warrant continuation at the recommendation of the Data Monitoring Committee.

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Fitzroy Dawkins, M.D.

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 16, 2014

First Posted

April 21, 2014

Study Start

March 1, 2014

Primary Completion

February 1, 2016

Study Completion

December 1, 2016

Last Updated

March 26, 2019

Results First Posted

July 11, 2017

Record last verified: 2019-03

Locations