NCT01423604

Brief Summary

The purpose of this study was to determine whether ruxolitinib added to capecitabine is effective in improving the overall survival of patients with metastatic pancreatic cancer.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
136

participants targeted

Target at P75+ for phase_2 pancreatic-cancer

Timeline
Completed

Started Jul 2011

Typical duration for phase_2 pancreatic-cancer

Geographic Reach
1 country

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

August 22, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 26, 2011

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2013

Completed
3.2 years until next milestone

Results Posted

Study results publicly available

August 29, 2016

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2016

Completed
Last Updated

February 12, 2018

Status Verified

January 1, 2018

Enrollment Period

1.9 years

First QC Date

August 22, 2011

Results QC Date

April 1, 2016

Last Update Submit

January 15, 2018

Conditions

Keywords

Metastatic pancreatic cancer

Outcome Measures

Primary Outcomes (1)

  • Overall Survival

    Overall survival was measured as the length of time (in days) between the randomization date and the date of death.

    Primary analysis includes study data from the start of the study (first dose for that subject) until the death of the subject (up to 8 months).

Secondary Outcomes (4)

  • Progression-Free Survival (PFS)

    Analysis includes study data from the start of the study (first dose for that subject) until death or PD, whichever was earlier up to 8 months.

  • Objective Response Rate

    Measured every 4 weeks for duration of study treatment (up to 8 months)

  • Durable Response Rate

    Measured every 4 weeks until death or PD, whichever was earlier (up to 8 months)

  • Summary of Clinical Benefit

    Measured every 4 weeks until death or PD, whichever was earlier (up to 8 months)

Study Arms (2)

Capecitabine and ruxolitinib

EXPERIMENTAL
Drug: CapecitabineDrug: Ruxolitinib

Capecitabine and placebo

PLACEBO COMPARATOR
Drug: CapecitabineDrug: Placebo

Interventions

Capecitabine starting dose - 2000 mg/m\^2 (1000 mg/m\^2 twice a day (BID)) (NOTE: Frequency of administration may be adjusted during the study.)

Capecitabine and placeboCapecitabine and ruxolitinib

Ruxolitinib starting dose - 15 mg BID (NOTE: Starting dose of randomized study drug may be 10 mg BID based on results from safety run-in study. Dose of ruxolitinib may be increased during randomized study.)

Capecitabine and ruxolitinib

Placebo matching ruxolitinib

Capecitabine and placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • years of age or older
  • Diagnosis of metastatic pancreatic cancer; subjects must have had measurable, or evaluable disease that was histologically confirmed
  • Karnofsky performance status of ≥ 60
  • Subjects must have failed 1st-line gemcitabine treatment for metastatic pancreatic cancer:
  • o An alternate chemotherapeutic agent was an acceptable substitute as 1st-line therapy in the event that the subject was intolerant to or ineligible to receive gemcitabine
  • ≥ 2 weeks elapsed from the completion of previous chemotherapy, and subjects must have recovered or been at new stable baseline from any related toxicities

You may not qualify if:

  • More than 1 prior chemotherapy regimen (not including adjuvant therapy) for metastatic disease
  • Evidence of central nervous system (CNS) metastases (unless stable for \> 3 months) or history of uncontrolled seizures
  • Ongoing radiation therapy or prior radiation therapy administered as a second-line treatment
  • Other active malignancy except basal or squamous carcinoma of the skin
  • Inability to swallow food or any condition of the upper GI tract that precluded administration of oral medications
  • Inadequate renal, hepatic and bone marrow function demonstrated by clinical observations and/or laboratory assessments

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Unknown Facility

Birmingham, Alabama, United States

Location

Unknown Facility

Hot Springs, Arkansas, United States

Location

Unknown Facility

Burbank, California, United States

Location

Unknown Facility

Los Angeles, California, United States

Location

Unknown Facility

Santa Monica, California, United States

Location

Unknown Facility

Denver, Colorado, United States

Location

Unknown Facility

Stamford, Connecticut, United States

Location

Unknown Facility

Boynton Beach, Florida, United States

Location

Unknown Facility

Fort Myers, Florida, United States

Location

Unknown Facility

St. Petersburg, Florida, United States

Location

Unknown Facility

Arlington Heights, Illinois, United States

Location

Unknown Facility

Elks Grove Village, Illinois, United States

Location

Unknown Facility

Indianapolis, Indiana, United States

Location

Unknown Facility

Sioux City, Iowa, United States

Location

Unknown Facility

Lexington, Kentucky, United States

Location

Unknown Facility

Louisville, Kentucky, United States

Location

Unknown Facility

Worcester, Massachusetts, United States

Location

Unknown Facility

Ann Arbor, Michigan, United States

Location

Unknown Facility

Detroit, Michigan, United States

Location

Unknown Facility

Grand Rapids, Michigan, United States

Location

Unknown Facility

Novi, Michigan, United States

Location

Unknown Facility

Minneapolis, Minnesota, United States

Location

Unknown Facility

St Louis, Missouri, United States

Location

Unknown Facility

Voorhees Township, New Jersey, United States

Location

Unknown Facility

Albuquerque, New Mexico, United States

Location

Unknown Facility

Lake Success, New York, United States

Location

Unknown Facility

Durham, North Carolina, United States

Location

Unknown Facility

Hickory, North Carolina, United States

Location

Unknown Facility

Canton, Ohio, United States

Location

Unknown Facility

Dayton, Ohio, United States

Location

Unknown Facility

Tulsa, Oklahoma, United States

Location

Unknown Facility

Bend, Oregon, United States

Location

Unknown Facility

Portland, Oregon, United States

Location

Unknown Facility

Danville, Pennsylvania, United States

Location

Unknown Facility

Pittsburgh, Pennsylvania, United States

Location

Unknown Facility

Knoxville, Tennessee, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Unknown Facility

Richmond, Virginia, United States

Location

Unknown Facility

Green Bay, Wisconsin, United States

Location

Related Publications (1)

  • Hurwitz HI, Uppal N, Wagner SA, Bendell JC, Beck JT, Wade SM 3rd, Nemunaitis JJ, Stella PJ, Pipas JM, Wainberg ZA, Manges R, Garrett WM, Hunter DS, Clark J, Leopold L, Sandor V, Levy RS. Randomized, Double-Blind, Phase II Study of Ruxolitinib or Placebo in Combination With Capecitabine in Patients With Metastatic Pancreatic Cancer for Whom Therapy With Gemcitabine Has Failed. J Clin Oncol. 2015 Dec 1;33(34):4039-47. doi: 10.1200/JCO.2015.61.4578. Epub 2015 Sep 8.

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

Capecitabineruxolitinib

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

DeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsFluorouracilUracilPyrimidinonesDeoxyribonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • William Williams, MD

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 22, 2011

First Posted

August 26, 2011

Study Start

July 1, 2011

Primary Completion

June 1, 2013

Study Completion

November 1, 2016

Last Updated

February 12, 2018

Results First Posted

August 29, 2016

Record last verified: 2018-01

Locations