NCT00789633

Brief Summary

The objective of this study is to compare the efficacy and safety of masitinib in combination with gemcitabine to placebo in combination with gemcitabine in patients with advanced/metastatic pancreatic cancer.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
353

participants targeted

Target at P50-P75 for phase_3 pancreatic-cancer

Timeline
Completed

Started Nov 2008

Geographic Reach
5 countries

68 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 12, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 13, 2008

Completed
12 days until next milestone

Study Start

First participant enrolled

November 25, 2008

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 23, 2011

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 31, 2012

Completed
Last Updated

December 17, 2018

Status Verified

December 1, 2018

Enrollment Period

3.1 years

First QC Date

November 12, 2008

Last Update Submit

December 13, 2018

Conditions

Keywords

Pancreatic cancerAdvanced pancreatic cancerMetastatic pancreatic cancerGemcitabineChemo-naive

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    Overall survival is defined as time in months from the randomization date to the date of death due to any cause. If a patient is not known to have died, then OS will be censored at the date of last known date patient alive.

    From day of randomization to the date of death, assessed up to 60 months

Secondary Outcomes (2)

  • Survival rate

    Every 24 weeks, assessed up to 60 months

  • Progression Free Survival (PFS)

    From day of randomization to disease progression or death, whichever came first, assessed up to 60 months

Study Arms (2)

Masitinib & gemcitabine

EXPERIMENTAL

Participants receive masitinib (9 mg/kg/day), given orally twice daily, plus gemcitabine at 1000mg/m2 by intravenous infusion during 30 minutes, once every 7 days, for up to 7 weeks, followed by a week of rest. Subsequent cycles should consist of an IV infusion, once every 7 days, for 3 consecutive weeks out of every 4 weeks, until disease progression, death, limiting toxicity or patient consent withdrawal.

Drug: MasitinibDrug: Gemcitabine

Placebo & gemcitabine

PLACEBO COMPARATOR

Participants receive matching placebo, given orally twice daily, plus gemcitabine at 1000mg/m2 by intravenous infusion during 30 minutes, once every 7 days, for up to 7 weeks, followed by a week of rest. Subsequent cycles should consist of an IV infusion, once every 7 days, for 3 consecutive weeks out of every 4 weeks, until disease progression, death, limiting toxicity or patient consent withdrawal.

Drug: PlaceboDrug: Gemcitabine

Interventions

Masitinib at 9 mg/kg/day given orally twice daily

Also known as: AB1010
Masitinib & gemcitabine

Matching placebo given orally twice daily

Placebo & gemcitabine

Gemcitabine at 1000 mg/m2 by intravenous infusion

Also known as: Gemzar
Masitinib & gemcitabinePlacebo & gemcitabine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the pancreas
  • Chemo naïve patients with advanced/metastatic disease
  • Documented decision justifying non eligibility for surgical resection. The documentation of the non eligibility for surgical resection will be reviewed by an independent committee.
  • Men and women, age \>18 years
  • Men and women of childbearing potential (entering the study after a confirmed menstrual period and who have a negative pregnancy test), must agree to use two methods (one for the patient and one for the partner) of medically acceptable forms of contraception during the study and for 3 months after the last treatment intake.
  • Patient should be able and willing to comply with study visits and procedures as per protocol.
  • Patient should understand, sign, and date the written voluntary informed consent form at the screening visit prior to any protocol-specific procedures performed.

You may not qualify if:

  • Patient treated for a cancer other than pancreatic cancer within 5 years before enrollment, with the exception of basal cell carcinoma or in situ cervical cancer
  • Any condition that the physician judges could be detrimental to subjects participating in this study; including any clinically important deviations from normal clinical laboratory values or concurrent medical events Previous treatment
  • Any anti-tumor therapy (any chemotherapy, radiotherapy, immunotherapy, biologic or hormonal therapy) within 6 months prior to baseline
  • Treatment with any investigational agent within 4 weeks prior to baseline

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (68)

Eastern Connecticut Hematology and Oncology (ECHO)

Norwich, Connecticut, 06360, United States

Location

MD Anderson

Orlando, Florida, 32806, United States

Location

The Emory Clinic

Atlanta, Georgia, 30322, United States

Location

Decatur Memorial Hospital

Decatur, Illinois, 62526, United States

Location

Medical & Surgical Specialists

Galesburg, Illinois, 61401, United States

Location

Berkshire Hematology Oncology

Pittsfield, Massachusetts, 01201, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Metro MN CCOP

Saint Louis Park, Minnesota, 55416, United States

Location

Saint Luke's Cancer Institute

Kansas City, Missouri, 64111, United States

Location

The Valley Hospital

Paramus, New Jersey, 07652, United States

Location

Southeastern Medical Oncology Center

Goldsboro, North Carolina, 27534, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Teaching Hospital Brno-Bohunice

Brno, 625 00, Czechia

Location

Hospital Chomutov

Chomutov, 430 12, Czechia

Location

Oncology Surgery

Kutná Hora, 284 30, Czechia

Location

Department of Oncology Teaching Hospital Olomouc

Olomouc, 775 20, Czechia

Location

Teaching Hospital Královské

Prague, 100 34, Czechia

Location

Teaching Hospital Na Bulovce

Prague, 180 81, Czechia

Location

Hospital na Homolce

Prague, 5 150 30, Czechia

Location

CHU Amiens

Amiens, 80000, France

Location

Hôpital Privé d'Antony

Antony, 92160, France

Location

Institut Sainte-Catherine

Avignon, 84000, France

Location

Hôpital Jean Minjoz

Besançon, France

Location

Hôpital Saint-André

Bordeaux, France

Location

CHU de la Cavale Blanche

Brest, 29600, France

Location

CHU de Caen

Caen, 14000, France

Location

CHU Hôtel Dieu

Clermont-Ferrand, 63000, France

Location

Groupement Hospitalier Universitaire Nord - Beaujon

Clichy, 92, France

Location

CHU Henri Mondor

Créteil, 94000, France

Location

CHU Henri Mondor

Créteil, France

Location

Hôpital Victor Jousselin

Dreux, France

Location

Centre Gastro-Loire

Gien, 45500, France

Location

Institut Daniel Hollard

Grenoble, 38000, France

Location

CHD Les Oudairies

La Roche-sur-Yon, 85925, France

Location

Hôpital André Mignot

Le Chesnay, 78150, France

Location

Hôpital Robert Boulin

Libourne, 33500, France

Location

Hôpital Claude Huriez

Lille, 59000, France

Location

Centre Hospitalier de Longjumeau

Longjumeau, 91164, France

Location

Hôpital Privé Jean Mermoz

Lyon, 69000, France

Location

Hôpital Edouard Herriot

Lyon, 69003, France

Location

Centre Léon Bérard

Lyon, France

Location

Assistance Publique des Hôpitaux de Marseille

Marseille, 13000, France

Location

Hôpital Saint Joseph

Marseille, 13000, France

Location

Centre Hospitalier Belfort - Montbéliard

Montbéliard, 25200, France

Location

CHU Hôtel Dieu

Nantes, 44000, France

Location

Centre Catherine de Sienne

Nantes, 44200, France

Location

Hôpital de la Source

Orléans, 45000, France

Location

Groupe Hospitalier Diaconesse Croix Saint Simon

Paris, 75000, France

Location

Hôpital Tenon

Paris, 75020, France

Location

Hôpital Hôtel Dieu

Paris, France

Location

Hôpital Saint-Joseph

Paris, France

Location

Hôpital Haut-Lévêque

Pessac, 33600, France

Location

Polyclinique Francheville

Périgueux, 24000, France

Location

Hôpital Hautepierre

Strasbourg, 67200, France

Location

CHU Brabois

Vandœuvre-lès-Nancy, 54500, France

Location

Hôpital Paul Brousse

Villejuif, 94800, France

Location

Hotel Dieu de France

Beirut, Lebanon

Location

Makassed General Hospital Tarik Jadide

Beirut, Lebanon

Location

Rafik Hariri University Hospital

Beirut, Lebanon

Location

Saint Georges Hospital UMC

Beirut, Lebanon

Location

Middle East Institute of Health- Bsaleem

Metn, Lebanon

Location

Saint Joseph Hospital Baouchrieh

Metn, Lebanon

Location

Hammoud Hospital University Medical Center

Saida, Lebanon

Location

Municipal Clinical Hospital

Arad, 310013, Romania

Location

County Hospital

Baia Mare, 430031, Romania

Location

Emergency Clinical Hospital

Constanța, 900591, Romania

Location

Pelica Impex SRL Hospital

Pelica Impex, 410548, Romania

Location

County Hospital

Satu Mare, 440056, Romania

Location

Related Publications (1)

  • Deplanque G, Demarchi M, Hebbar M, Flynn P, Melichar B, Atkins J, Nowara E, Moye L, Piquemal D, Ritter D, Dubreuil P, Mansfield CD, Acin Y, Moussy A, Hermine O, Hammel P. A randomized, placebo-controlled phase III trial of masitinib plus gemcitabine in the treatment of advanced pancreatic cancer. Ann Oncol. 2015 Jun;26(6):1194-1200. doi: 10.1093/annonc/mdv133. Epub 2015 Apr 9.

Related Links

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

masitinibGemcitabine

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

Heterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Study Officials

  • Gaël Deplanque, MD

    Hôpital Saint Joseph, Paris, France

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 12, 2008

First Posted

November 13, 2008

Study Start

November 25, 2008

Primary Completion

December 23, 2011

Study Completion

August 31, 2012

Last Updated

December 17, 2018

Record last verified: 2018-12

Locations