NCT02044822

Brief Summary

The primary objective of this study is to evaluate overall response rate (ORR) following treatment with idelalisib plus rituximab in participants with previously untreated chronic lymphocytic leukemia (CLL) with 17p deletion. An increased rate of deaths and serious adverse events (SAEs) among participants with front-line CLL and early-line indolent non-Hodgkin lymphoma (iNHL) treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated those studies in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA). All front-line studies of idelalisib, including this study, were also terminated.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
102

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Aug 2014

Geographic Reach
13 countries

51 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 22, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 24, 2014

Completed
6 months until next milestone

Study Start

First participant enrolled

August 6, 2014

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 27, 2016

Completed
20 days until next milestone

Study Completion

Last participant's last visit for all outcomes

May 17, 2016

Completed
12 months until next milestone

Results Posted

Study results publicly available

May 11, 2017

Completed
Last Updated

November 19, 2018

Status Verified

March 1, 2017

Enrollment Period

1.7 years

First QC Date

January 22, 2014

Results QC Date

March 30, 2017

Last Update Submit

October 19, 2018

Conditions

Keywords

Chronic Lymphocytic LeukemiaCLL

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate

    Overall response rate (ORR) was defined as the proportion of participants who achieve a confirmed complete or partial response. ORR was to be assessed by an independent review committee (IRC).

Secondary Outcomes (6)

  • Duration of Response

  • Nodal Response Rate

  • Complete Response Rate

  • Progression-Free Survival

  • Overall Survival

  • +1 more secondary outcomes

Study Arms (1)

Idelalisib + rituximab

EXPERIMENTAL

Participants will receive rituximab for 8 weeks and Idelalisib continuously throughout the study (up to 10 years).

Drug: IdelalisibDrug: Rituximab

Interventions

150 mg tablets administered orally twice daily

Also known as: GS-1101, CAL-101, Zydelig®
Idelalisib + rituximab

375 mg/m\^2 administered intravenously once weekly x 8 weeks

Also known as: Rituxan
Idelalisib + rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Documented diagnosis of B-cell CLL, according to International Workshop on Chronic Lymphocytic Leukemia 2008
  • Presence of 17p deletion in CLL cells as demonstrated by fluorescence in-situ hybridization (FISH) testing
  • No prior therapy for CLL other than corticosteroids for disease complications
  • CLL that warrants treatment
  • Presence of measurable lymphadenopathy
  • Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2

You may not qualify if:

  • Known histological transformation from CLL to an aggressive lymphoma (ie, Richter transformation)
  • Known presence of myelodysplastic syndrome
  • History of a non-CLL malignancy except for the following:
  • the malignancy has been in remission without treatment for ≥ 5 years prior to enrollment, or
  • carcinoma in situ of the cervix, or
  • adequately treated basal or squamous cell skin cancer or other localized non-melanoma skin cancer, or
  • asymptomatic prostate cancer without known metastatic disease and with no current requirement for therapy or requiring only hormonal therapy and with normal prostate specific antigen for ≥ 1 year prior to enrollment, or
  • ductal carcinoma in situ (DCIS) of the breast treated with lumpectomy alone, or
  • other adequately treated Stage 1 or 2 cancer currently in complete remission
  • Evidence of ongoing systemic bacterial, fungal, or viral infection at the time of enrollment
  • Ongoing liver injury
  • History of noninfectious pneumonitis
  • Ongoing inflammatory bowel disease
  • History of prior allogeneic bone marrow progenitor cell or solid organ transplantation
  • Ongoing immunosuppressive therapy other than corticosteroids
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (56)

Arizona Oncology Associates, PC - HOPE

Tucson, Arizona, 85710, United States

Location

Innovative Clinical Research Institute

Whittier, California, 90603, United States

Location

Rocky Mountain Cancer Centers

Boulder, Colorado, 80303, United States

Location

The University of Chicago Medicine

Chicago, Illinois, 60637, United States

Location

Illinois Cancer Specialists

Niles, Illinois, 60714, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Duke University

Durham, North Carolina, 27705, United States

Location

GHS Cancer Institute

Greenville, North Carolina, 29615, United States

Location

Compass Oncology

Portland, Oregon, 97213, United States

Location

Willamette Valley Cancer Center and Research Institute

Springfield, Oregon, 97477, United States

Location

Hospital of the University of Pennsylvania, Abramson Cancer Center

Philadelphia, Pennsylvania, 19104, United States

Location

St Vincent's Hospital, Sydney

Darlinghurst, New South Wales, 2010, Australia

Location

St George Hospital

Kogarah, New South Wales, 2217, Australia

Location

Icon Cancer Foundation

South Brisbane, Queensland, 4101, Australia

Location

St Vincent's Hospital, Melbourne

Fitzroy, Victoria, 3065, Australia

Location

Liverpool Hospital

Liverpool, NSW 2170, Australia

Location

Innsbruck University Hospital, Inner Medicine,

Innsbruck, A-6020, Austria

Location

Univ. Klinik für Innere Medizin III LKH

Salzburg, 5020, Austria

Location

Medizinische Universität Wien, Univ. Klinik f. Innere Med. I, Abteilung für Hämatologie und Hämostaseologie

Vienna, 1090, Austria

Location

AZ Sint-Jan AV Brugge-Oostende

Bruges, 8000, Belgium

Location

University Hospital Leuven

Leuven, 3000, Belgium

Location

University Hospital

Brno, Czechia

Location

Faculty Hospital Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

Hemato-Onkologicka Klinika Fn

Olomuc, Czechia

Location

Faculty hospital Ostrava

Ostrava-Poruba, 70852, Czechia

Location

Faculty Hospital Kralovske Vinohrady

Prague, 10034, Czechia

Location

Vseobecna Fakultim Nemocnice

Prague, 12808, Czechia

Location

Aalborg University Hospital

Aalborg, 9100, Denmark

Location

Centre Hospitalier Universitaire Hôpital Avicenne

Bobigny, 93009, France

Location

CHRU de Lille, Hopital Claude Huriez

Lille, 59037, France

Location

Centre Hospitalier Universitaire Nancy

Nancy, 54511, France

Location

Hopital Pitie-Salpetriere

Paris, 75651, France

Location

University of Debrecen HSC Institute of internal Medicine, Department of Hematology

Debrecen, 4032, Hungary

Location

Institute of Hematology "L. e A. Seràgnoli"

Bologna, 40138, Italy

Location

A.O.Spedali Civili Brescia

Brescia, 25123, Italy

Location

A.O.Niguarda Ca' Granda

Milan, 20162, Italy

Location

Azienda Ospedaliero Universitaria Policlinico di Modena

Modena, 41124, Italy

Location

SCDU Medicina II ed Ematologia, A.O.U. San Luigi Gonzaga

Orbassano, 10043, Italy

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, 80-952, Poland

Location

Szpital Specjalistyczny w Brzozowie

Brzozów, 36-200, Poland

Location

Malopolskie Centrum Medyczne s.c.

Krakow, 30-510, Poland

Location

Wojewodzki Szpital Specjalistyczny

Lodz, 93-510, Poland

Location

Centrum Onkologii-Instytut Marii Sklodowskiej -Curie klinika Nowotworow Ukladu Chlonnego

Warsaw, 02-781, Poland

Location

Samodzielny Publiczny Szpital Kliniczny

Wroclaw, 50-367, Poland

Location

Centro Hospitalar De Lisboa Norte, E.P.E. - Hospital Santa Maria

Lisbon, 1649-035, Portugal

Location

IPO Porto Francisco Gentil, E.P.E

Porto, 4200-072, Portugal

Location

Emergency County Clinical Hospital Brasov

Brasov, 500326, Romania

Location

Spitalul Clinic Colentina

Bucharest, 20125, Romania

Location

Institutul Regional de Oncologie Iasi

Iași, 700348, Romania

Location

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, 39008, Spain

Location

Hospital Clinic

Barcelona, Catalonia, 08036, Spain

Location

Hospital Universitario Puerta De Hierro

Madrid, 28222, Spain

Location

Hospital Clinico Universitario De Valencia (Chuv)

Valencia, 46010, Spain

Location

Saint James's University Hospital

Leeds, LS9 7TF, United Kingdom

Location

Royal Liverpool & Broadgreen Univ. Hospitals

Liverpool, L7 8XP, United Kingdom

Location

University Hospital Southampton NHS Trust

Southampton, 16, United Kingdom

Location

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-Cell

Interventions

idelalisibRituximab

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Limitations and Caveats

Due to the early termination of the study, efficacy data were not available for all participants, and therefore the prespecified analyses were not conducted.

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 22, 2014

First Posted

January 24, 2014

Study Start

August 6, 2014

Primary Completion

April 27, 2016

Study Completion

May 17, 2016

Last Updated

November 19, 2018

Results First Posted

May 11, 2017

Record last verified: 2017-03

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations