NCT01282424

Brief Summary

The primary objective will be to assess the overall response rate and to evaluate the efficacy and safety of idelalisib (IDELA; GS-1101) in participants with previously treated indolent Non-Hodgkin Lymphoma (iNHL) that is refractory both to rituximab and to alkylating-agent-containing chemotherapy. Eligible participants will initiate oral therapy with idelalisib at a starting dose of 150 mg taken twice per day. Treatment with idelalisib can continue in compliant participants as long as the study is still ongoing and the participants appear to be benefiting from treatment with acceptable safety.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
125

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2011

Longer than P75 for phase_2

Geographic Reach
6 countries

41 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 21, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 25, 2011

Completed
2 months until next milestone

Study Start

First participant enrolled

March 18, 2011

Completed
3.5 years until next milestone

Results Posted

Study results publicly available

September 4, 2014

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 2, 2018

Completed
14 days until next milestone

Study Completion

Last participant's last visit for all outcomes

May 16, 2018

Completed
Last Updated

July 11, 2019

Status Verified

June 1, 2019

Enrollment Period

7.1 years

First QC Date

January 21, 2011

Results QC Date

August 22, 2014

Last Update Submit

June 14, 2019

Conditions

Keywords

indolent Non-Hodgkin LymphomaNon-Hodgkin LymphomaiNHLNHLGS-1101CAL-101PI3KPhosphatidylinositol 3-kinaseFollicular Lymphoma (FL)Small lymphocytic lymphoma (SLL)Lymphoplasmacytoid lymphoma (LPL)Marginal zone lymphoma (MZL)

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate

    Overall response rate (ORR) was assessed based on the International Working Group Revised Response Criteria for Malignant Lymphoma (Cheson, 2007), and was defined as the percentage of participants achieving a complete response (CR) or partial response (PR; or minor response \[MR\] for participants with WM) as assessed by the study independent review committee (IRC). CR was defined as the complete resolution of all disease-related radiological abnormalities and the disappearance of all signs and symptoms related to the disease. PR was defined as a ≥ 50% reduction in the sum of the products of the longest perpendicular diameters of all index lesions, with no new lesions. For WM only, response was defined as a reduction in immunoglobulin M (IgM) of ≥ 50% decrease for PR, and ≥ 25% decrease for MR; no increase from baseline in the sum of the products of the longest perpendicular diameters of all index lesions, with no new lesions or signs and symptoms of active disease (Owen, 2013)

    Start of Treatment to End of Treatment (up to 81 months)

Secondary Outcomes (14)

  • Duration of Response

    Start of Treatment to End of Treatment (up to 81 months)

  • Lymph Node Response Rate

    Start of Treatment to End of Treatment (up to 81 months)

  • Time to Response

    Start of Treatment to End of Treatment (up to 81 months)

  • Progression-Free Survival

    Start of Treatment to End of Treatment (up to 81 months)

  • Overall Survival

    Start of Treatment to Last Long-Term Follow-Up Visit (up to maximum of 7 years)

  • +9 more secondary outcomes

Study Arms (1)

Idelalisib

EXPERIMENTAL

Treatment with idelalisib will be continued until tumor progression or development of unacceptable toxicity.

Drug: Idelalisib

Interventions

Idelalisib 150 mg tablet administered orally twice daily

Also known as: Zydelig®, GS-1101, CAL-101, IDELA
Idelalisib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Karnofsky performance status of ≥ 60 (Eastern Cooperative Oncology Group \[ECOG\] performance score of 0, 1, or 2)
  • Histologically confirmed diagnosis of B-cell iNHL, with histological subtype limited to the following:
  • Follicular lymphoma (FL)
  • Small lymphocytic lymphoma (SLL) with absolute lymphocyte count \< 5 x 10\^9/L at the time of diagnosis and on baseline laboratory assessment performed within 4 weeks prior to the start of study drug administration
  • Lymphoplasmacytic lymphoma (LPL), with or without associated Waldenstroms Macroglobulinemia (WM)
  • Marginal zone lymphoma (MZL) (splenic, nodal, or extranodal)
  • Prior treatment with ≥ 2 prior chemotherapy-based or immunotherapy-based regimens for iNHL
  • Presence of radiographically measurable lymphadenopathy or extranodal lymphoid malignancy
  • Prior treatment with rituximab and with an alkylating agent (eg, bendamustine, cyclophosphamide, ifosfamide, chlorambucil, melphalan, busulfan, nitrosoureas) for iNHL
  • Lymphoma that is refractory to rituximab and to an alkylating agent
  • Discontinuation of all other therapies for treatment of iNHL ≥ 3 weeks before Visit 2
  • For men and women of childbearing potential, willingness to abstain from sexual intercourse or employ an effective method of contraception during the study drug administration and follow-up periods
  • Willingness and ability to provide written informed consent and to comply with the protocol requirements

You may not qualify if:

  • Central nervous system or leptomeningeal lymphoma
  • Known histological transformation from iNHL to diffuse large B-cell lymphoma
  • History of a non-lymphoma malignancy except for the following: adequately treated local basal cell or squamous cell carcinoma of the skin, cervical carcinoma in situ, superficial bladder cancer, localized prostate cancer, other adequately treated Stage 1 or 2 cancer currently in complete remission, or any other cancer that has been in complete remission for ≥ 5 years
  • Evidence of ongoing systemic bacterial, fungal, or viral infection (excluding viral upper respiratory tract infections) at the time of initiation of study treatment
  • Pregnancy or breastfeeding
  • Ongoing alcohol or drug addiction
  • Known history of drug-induced liver injury, chronic active hepatitis B infection, chronic active hepatitis C infection, alcoholic liver disease, non-alcoholic steatohepatitis, primary biliary cirrhosis, ongoing extrahepatic obstruction caused by stones, cirrhosis of the liver, or portal hypertension
  • History of prior allogeneic bone marrow progenitor cell or solid organ transplantation
  • Ongoing immunosuppressive therapy, including systemic corticosteroids. Participant may be using topical or inhaled corticosteroids.
  • Prior therapy with idelalisib
  • Exposure to another investigational drug within 3 weeks prior to start of study treatment
  • Concurrent participation in another therapeutic treatment trial
  • Prior or ongoing clinically significant illness, medical condition, surgical history, physical finding, ECG finding, or laboratory abnormality that, in the investigator's opinion, could affect the safety of the participant, alter the absorption, distribution, metabolism or excretion of the study drug, or impair the assessment of study results

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

St. Jude Medical Center

Fullerton, California, 92835, United States

Location

Pacific Shores Medical Group

Long Beach, California, 90813-3244, United States

Location

UCLA

Los Angeles, California, 90095, United States

Location

Central Coast Medical Oncology

Santa Maria, California, 93454, United States

Location

Stanford Cancer Center

Stanford, California, 94035-5796, United States

Location

Collaborative Research Group, LLC

Boynton Beach, Florida, 33435, United States

Location

Winship Cancer Institute

Atlanta, Georgia, 30322-1013, United States

Location

Northwestern University Robert H. Lurie Comprehensive Cancer Center

Chicago, Illinois, 60611, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

John Theurer Cancer Center Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

University of Medicine and Dentistry of NJ

New Brunswick, New Jersey, 08901-1914, United States

Location

Weill Cornell -New York Presbyterian Hospital

New York, New York, 10002, United States

Location

Montefiore Medical Center

New York, New York, 10467, United States

Location

The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

South Carolina Oncology Associates

Columbia, South Carolina, 29210, United States

Location

Chattanooga Hem/Oncology Ass (SCRI)

Chattanooga, Tennessee, 37404, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

University of Virginia Medical Center

Charlottesville, Virginia, 22908, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

University of Wisconsin

Madison, Wisconsin, 53792-5156, United States

Location

CHU Morvan

Brest, 29609, France

Location

Centre Hospitalier de Lyon Sud

Pierre-Bénite, 69310, France

Location

Centre Henri Bequerel

Rouen, 76038, France

Location

CHU Bretonneau - Centre Kaplan

Tours, 37044, France

Location

Charité Campus Virchow Klinikum

Berlin, 13353, Germany

Location

Universitätsklinikum Essen

Essen, 45147, Germany

Location

Klinikum der Universität München-Großhadern

München, 81377, Germany

Location

Universitatsklinikum Ulm

Ulm, 89081, Germany

Location

Azienda Ospedaliera di Bologna - Policlinico S. Orsola Malpighi

Bologna, 40138, Italy

Location

A.O.U. San Martino

Genova, 16132, Italy

Location

Fondazione Centro San Raffaele del Monte Tabor

Milan, 20132, Italy

Location

Università "Sapienza"

Rome, 00161, Italy

Location

Małopolskie Centrum Medyczne

Krakow, 30-510, Poland

Location

Centrum Onkologii w Warszawie

Warsaw, 02-781, Poland

Location

St James's Institute of Oncology

Leeds, LS9 7TF, United Kingdom

Location

St Bartholemews Hospital

London, EC1M 6BQ, United Kingdom

Location

Sarah Cannon Institute

London, W1G 6AD, United Kingdom

Location

The Christie Hospital

Manchester, M20 4BX, United Kingdom

Location

Southampton General Hospital

Southampton, SO16 6YD, United Kingdom

Location

Related Publications (4)

  • Salles GA, Kahl, BS, Wagner-Johnston ND, et al. Interim results from a phase 2 study of PI3Kδ inhibitor idelalisib in patients with relapsed indolent non-Hodgki lymphoma (iNHL) refractory to both rituximab and an alkylating agent. 12th International Conference on Malignant Lymphoma, Palazzo dei Congressi, Lugano, Switzerland, June 19-22, 2013 Abstract No: 064bis.

    RESULT
  • Gopal AK, Kahl BS, de Vos S, Wagner-Johnston ND, Schuster SJ, Jurczak WJ, Flinn IW, Flowers CR, Martin P, Viardot A, Blum KA, Goy AH, Davies AJ, Zinzani PL, Dreyling M, Johnson D, Miller LL, Holes L, Li D, Dansey RD, Godfrey WR, Salles GA. PI3Kdelta inhibition by idelalisib in patients with relapsed indolent lymphoma. N Engl J Med. 2014 Mar 13;370(11):1008-18. doi: 10.1056/NEJMoa1314583. Epub 2014 Jan 22.

  • Ma S, Chan RJ, Gu L, Xing G, Rajakumaraswamy N, Ruzicka BB, Wagner-Johnston ND. Retrospective Analysis of the Impact of Adverse Event-Triggered Idelalisib Interruption and Dose Reduction on Clinical Outcomes in Patients With Relapsed/Refractory B-Cell Malignancies. Clin Lymphoma Myeloma Leuk. 2021 May;21(5):e432-e448. doi: 10.1016/j.clml.2020.12.016. Epub 2020 Dec 24.

  • Barrientos JC, Hillmen P, Salles G, Sharman J, Stilgenbauer S, Gurtovaya O, Xing G, Ruzicka B, Bhargava P, Ghia P, Pagel JM. No increased bleeding events in patients with relapsed chronic lymphocytic leukemia and indolent non-Hodgkin lymphoma treated with idelalisib. Leuk Lymphoma. 2021 Apr;62(4):837-845. doi: 10.1080/10428194.2020.1845339. Epub 2020 Dec 10.

MeSH Terms

Conditions

Lymphoma, FollicularLeukemia, Lymphocytic, Chronic, B-CellLymphoma, B-Cell, Marginal ZoneLymphoma, Non-HodgkinWaldenstrom Macroglobulinemia

Interventions

idelalisib

Condition Hierarchy (Ancestors)

LymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLeukemia, B-CellLeukemia, LymphoidLeukemiaHematologic DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsLymphoma, B-CellNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic Disorders

Results Point of Contact

Title
Gilead Clinical Study Information Center
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 21, 2011

First Posted

January 25, 2011

Study Start

March 18, 2011

Primary Completion

May 2, 2018

Study Completion

May 16, 2018

Last Updated

July 11, 2019

Results First Posted

September 4, 2014

Record last verified: 2019-06

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations