NCT01980888

Brief Summary

The primary objective of this study is to evaluate the progression-free survival in participants with previously untreated chronic lymphocytic leukemia (CLL) who would otherwise be suitable for bendamustine and rituximab treatment as standard of care. An increased rate of deaths and serious adverse events (SAEs) among participants with front-line CLL and early-line indolent non-Hodgkin lymphoma (iNHL) treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated this study in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA).

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
311

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Feb 2014

Geographic Reach
13 countries

91 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 5, 2013

Completed
6 days until next milestone

First Posted

Study publicly available on registry

November 11, 2013

Completed
3 months until next milestone

Study Start

First participant enrolled

February 5, 2014

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 30, 2016

Completed
17 days until next milestone

Study Completion

Last participant's last visit for all outcomes

June 16, 2016

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

October 11, 2017

Completed
Last Updated

November 19, 2018

Status Verified

September 1, 2017

Enrollment Period

2.3 years

First QC Date

November 5, 2013

Results QC Date

March 30, 2017

Last Update Submit

October 19, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival

    Progression-free survival (PFS) is defined as the interval from randomization to the first documentation of definitive disease progression or death from any cause. Definitive disease progression is CLL progression based on standard criteria, excluding lymphocytosis alone. PFS was to be assessed by an independent review committee (IRC).

    Up to 22 months

Secondary Outcomes (5)

  • Overall Response Rate

    Up to 22 months

  • Nodal Response Rate

    Up to 22 months

  • Complete Response Rate

    Up to 22 months

  • Overall Survival

    Up to 22 months

  • Minimal Residual Disease Negativity Rate at Week 36

    Up to 22 months

Study Arms (2)

Idelalisib+bendamustine+rituximab

EXPERIMENTAL

Participants will receive idelalisib for 96 weeks plus bendamustine+rituximab for 21 weeks.

Drug: IdelalisibDrug: BendamustineDrug: Rituximab

Placebo+bendamustine+rituximab

PLACEBO COMPARATOR

Participants will receive placebo to match idelalisib for 96 weeks plus bendamustine+rituximab for 21 weeks.

Drug: BendamustineDrug: RituximabDrug: Placebo

Interventions

150 mg tablet administered orally twice daily

Also known as: Zydelig®, GS-1101, CAL-101
Idelalisib+bendamustine+rituximab

Administered intravenously at a starting dose of 90 mg/m\^2 for up to 6 cycles. Dosing will be based on mg/m\^2 of body surface area.

Idelalisib+bendamustine+rituximabPlacebo+bendamustine+rituximab

Single-use vials administered intravenously weekly starting at 375 mg/m\^2 on Day 1 (Week 0) and 500 mg/m\^2 thereafter for a total of 6 infusions

Idelalisib+bendamustine+rituximabPlacebo+bendamustine+rituximab

Placebo to match idelalisib administered orally twice daily

Placebo+bendamustine+rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Documented diagnosis of B-cell CLL, with diagnosis established according to International Workshop on Chronic Lymphocytic Leukemia (IWCLL)
  • No prior therapy for CLL other than corticosteroids for disease complications
  • CLL that warrants treatment
  • Presence of measurable lymphadenopathy
  • Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2

You may not qualify if:

  • Known histological transformation from CLL to an aggressive lymphoma (ie, Richter transformation)
  • Known presence of myelodysplastic syndrome
  • Evidence of ongoing systemic bacterial, fungal, or viral infection at the time of randomization
  • Ongoing liver injury
  • History of non-infectious pneumonitis
  • Ongoing inflammatory bowel disease
  • History of prior allogeneic bone marrow progenitor cell or solid organ transplantation
  • Ongoing immunosuppressive therapy other than corticosteroids
  • Received last dose of study drug on another therapeutic clinical trial within 30 days prior to randomization

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (91)

St. Jude Heritage Healthcare Virginia K. Crosson Cancer Center

Fullerton, California, 92835, United States

Location

UCSD Moores Cancer Center

La Jolla, California, 92093, United States

Location

Central Coast Medical Oncology

Santa Maria, California, 93454, United States

Location

Georgetown University

Washington D.C., District of Columbia, 20007, United States

Location

Memorial Healthcare System

Hollywood, Florida, 33021, United States

Location

Cancer Specialists of North Florida

Jacksonville, Florida, 32256, United States

Location

Florida Cancer Specialists-South

Sarasota, Florida, 34236, United States

Location

Franciscan Physician Network Oncology & Hematology

Indianapolis, Indiana, 46237, United States

Location

Siouxland Hematology-Oncology Associates, LLP

Sioux City, Iowa, 51101, United States

Location

Center for Cancer and Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89074, United States

Location

Hematology /Oncology Associates of Northern New Jersey

Morristown, New Jersey, 07962, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

Gabrail Cancer Center Research

Canton, Ohio, 44718, United States

Location

Sarah Cannon Research Institute

Cincinnati, Ohio, 45242, United States

Location

Signal Point Clinical Research Center

Middletown, Ohio, 45042, United States

Location

Saint Francis Hospital

Greenville, South Carolina, 29601, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Texas Oncology-Austin Midtown

Austin, Texas, 78705, United States

Location

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Utah Cancer Specialists

Salt Lake City, Utah, 84103, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

St Vincent's Hospital, Sydney

Darlinghurst, New South Wales, 2010, Australia

Location

Jarrett Street Specialist Centre

North Gosford, New South Wales, 2250, Australia

Location

Calvary Mater Newcastle

Waratah, New South Wales, 2298, Australia

Location

Haematology and Bone Marrow Transplant Unit, Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Flinders Medical Centre, Department of Haematology, Level 6

Bedford Park, South Australia, 5042, Australia

Location

Ashford Cancer Centre Research

Kurralta Park, South Australia, 5037, Australia

Location

Queen Elizabeth Hospital

Woodville South, South Australia, 5011, Australia

Location

Frankston Hospital

Frankston, Victoria, 3199, Australia

Location

Barwon Health, University Hospital Geelong

Geelong, Victoria, 3220, Australia

Location

Z N A Stuivenberg

Antwerp, 2060, Belgium

Location

AZ Sint-Jan AV Brugge-Oostende

Bruges, 8000, Belgium

Location

University Hospital Leuven

Leuven, 3000, Belgium

Location

Cancercare Manitoba - Maccharles Unit

Winnipeg, Manitoba, R3E 0V9, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3M5, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2C9, Canada

Location

Hôpital du Sacré-Coeur de Montréal

Montreal, Quebec, H4J 1C5, Canada

Location

CHU de Québec - Hôpital de l'Enfant-Jésus

Québec, Quebec, G1J 1Z4, Canada

Location

Klinicka bolnica Dubrava

Zagreb, 10000, Croatia

Location

Klinicka bolnica Merkur

Zagreb, 10000, Croatia

Location

UHC Zagreb

Zagreb, 10000, Croatia

Location

Faculty hospital Ostrava

Ostrava-Poruba, Moravian-Silesian, 70852, Czechia

Location

University Hospital

Brno, 62500, Czechia

Location

Faculty Hospital Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

Faculty Hospital Plzen

Pilsen, 304 60, Czechia

Location

Faculty Hospital Kralovske Vinohrady

Prague, 10034, Czechia

Location

CHRU de Lille, Hopital Claude Huriez

Lille, 59037, France

Location

Hospital Saint-Louis

Paris, 75010, France

Location

CHU Bretonneau

Tours, 37044, France

Location

Szent Borbála Hospital

Tatabánya, Komárom-Esztergom, 2800, Hungary

Location

Kaposi Mor Oktato Korhaz, Intezeti Gyogyszertar,

Kaposvár, Somogy County, 7400, Hungary

Location

Semmelweis University

Budapest, 1083, Hungary

Location

National Institute of Oncology

Budapest, 1122, Hungary

Location

University of Debrecen HSC Institute of internal Medicine, Department of Hematology

Debrecen, 4032, Hungary

Location

Pandy Kalman Hospital

Gyula, 5700, Hungary

Location

University Of Pecs, Medical School

Pécs, 7624, Hungary

Location

Szegedi Tudomanyegyetem AOK - Szent-Gyorgyi Albert Klinikai Kozpont, II. Belgyógyászati Klinika

Szeged, 6725, Hungary

Location

IRCCS Istituto Tumori

Bari, Apulia, 70024, Italy

Location

Ospedale Oncologico Armando Businco

Cagliari, 09121, Italy

Location

Ospedale San Raffaele

Milan, 20132, Italy

Location

Azienda Ospedaliero Universitaria Policlinico di Modena

Modena, 41124, Italy

Location

AOU Maggiore della Carità

Novara, 28100, Italy

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, 80-952, Poland

Location

Malopolskie Centrum Medyczne s.c.

Krakow, 30-510, Poland

Location

Wojewodzki Szpital Specjalistyczny im. M. Kopernika Klinika Hematologii

Lodz, 93-510, Poland

Location

Centralny Szpital Kliniczny MSW w Warszawie Klinika Onkologii i Hematologii

Warsaw, 02-507, Poland

Location

Centrum Onkologii-Instytut Marii Sklodowskiej -Curie klinika Nowotworow Ukladu Chlonnego

Warsaw, 02-781, Poland

Location

Samodzielny Publiczny Szpital Kliniczny nr 1 we Wroclawiu Klinika i Katedra Hematologii,Nowotworow Krwi i Transplantacji Szpiku

Wroclaw, 50-367, Poland

Location

Dolnoslakie Centrum Transplantacji Komorkowych z Krajowym Bankiem Dawcow Szpiku

Wroclaw, 53-439, Poland

Location

Emergency County Clinical Hospital Brasov

Brasov, 500326, Romania

Location

Spitalul Clinic Colentina

Bucharest, 20125, Romania

Location

Hospital Vall de Hebron

Barcelona, Catalonia, 08035, Spain

Location

Hospital Clinic

Barcelona, Catalonia, 08036, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, 8041, Spain

Location

ICO, Hospitalet de Llobregat

Barcelona, 8908, Spain

Location

Hospital Universitario La Princesa

Madrid, 28006, Spain

Location

Hospital Gregorio Marañon

Madrid, 28007, Spain

Location

Hospital Universitario Ramón Y Cajal

Madrid, 28033, Spain

Location

Hospital 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario Puerta De Hierro

Madrid, 28222, Spain

Location

University College London

London, England, WC1E 6BT, United Kingdom

Location

East Kent Hospitals University NHS Foundation Trust

Canterbury, Kent, CT1 3NG, United Kingdom

Location

Royal Marsden NHS Trust

Sutton, Surrey, SM2 5PT, United Kingdom

Location

University Hospital of Wales

Cardiff, CF14 4XW, United Kingdom

Location

Royal Liverpool & Broadgreen Univ. Hospitals NHS Trust

Liverpool, L7 8XP, United Kingdom

Location

Hammersmith Hospitals NHS Trust

London, W12 0HS, United Kingdom

Location

Oxford University Hospitals

Oxford, OX37LE, United Kingdom

Location

University Hospital Southampton NHS Trust

Southampton, SO16 6YD, United Kingdom

Location

Royal Wolverhampton Hospital NHS Trust, New Cross Hospital

Wolverhampton, WV10 0QP, United Kingdom

Location

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-Cell

Interventions

idelalisibBendamustine HydrochlorideRituximab

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

ButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsBenzimidazolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Limitations and Caveats

The study was terminated in agreement with the FDA due to urgent safety measures. Due to early study termination, the prespecified efficacy analyses were not conducted. The PFS data presented are investigator assessments rather than IRC assessments.

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 5, 2013

First Posted

November 11, 2013

Study Start

February 5, 2014

Primary Completion

May 30, 2016

Study Completion

June 16, 2016

Last Updated

November 19, 2018

Results First Posted

October 11, 2017

Record last verified: 2017-09

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations