NCT01569295

Brief Summary

The primary objective of this study is to evaluate the effect of the addition of idelalisib (formerly GS-1101) to bendamustine + rituximab (BR) on progression-free survival (PFS) in participants with previously treated chronic lymphocytic leukemia (CLL)

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
416

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jun 2012

Longer than P75 for phase_3

Geographic Reach
18 countries

106 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 27, 2012

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 3, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

June 15, 2012

Completed
5.7 years until next milestone

Results Posted

Study results publicly available

February 27, 2018

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 10, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 10, 2019

Completed
Last Updated

March 10, 2020

Status Verified

March 1, 2020

Enrollment Period

7 years

First QC Date

March 27, 2012

Results QC Date

December 18, 2017

Last Update Submit

March 2, 2020

Conditions

Keywords

ZydeligCLLCAL-101GS 1101GS-1101PI3KRituxanRituximabBendamustineLeukemiaidelalisib

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival (PFS)

    PFS was defined as the interval from randomization to the earlier of the first documentation of definitive disease progression or death from any cause. PFS (months) = (minimum (date of disease progression, date of death) - date of randomization + 1)/30.4375.

    Up to 84 months

Secondary Outcomes (4)

  • Overall Response Rate (ORR)

    Up to 84 months

  • Lymph Node Response Rate

    Up to 84 months

  • Overall Survival

    Up to 84 months

  • Complete Response Rate

    Up to 84 months

Study Arms (2)

Idelalisib+bendamustine+rituximab

EXPERIMENTAL

Participants will receive idelalisib plus bendamustine and rituximab

Drug: IdelalisibDrug: RituximabDrug: Bendamustine

Placebo to match idelalisib+bendamustine+rituximab

PLACEBO COMPARATOR

Participants will receive placebo to match idelalisib plus bendamustine and rituximab

Drug: RituximabDrug: BendamustineDrug: Placebo to match idelalisib

Interventions

Idelalisib 150 mg administered orally twice daily

Also known as: GS-1101, CAL-101, Zydelig®
Idelalisib+bendamustine+rituximab

Rituximab 375 mg/m\^2 on Day 1, then 500 mg/m\^2 every 28 days administered intravenously for a maximum of 6 infusions

Also known as: Rituxan®, MabThera
Idelalisib+bendamustine+rituximabPlacebo to match idelalisib+bendamustine+rituximab

Bendamustine 70 mg/mg\^2/day on 2 consecutive days every 28 days administered intravenously for a maximum of 12 infusions

Also known as: Ribomustin, Treanda®
Idelalisib+bendamustine+rituximabPlacebo to match idelalisib+bendamustine+rituximab

Placebo to match idelalisib administered orally twice daily

Placebo to match idelalisib+bendamustine+rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Previously treated recurrent CLL
  • Measurable lymphadenopathy
  • Requires therapy for CLL
  • Has experienced CLL progression \< 36 months since the completion of the last prior therapy

You may not qualify if:

  • Recent history of a major non-CLL malignancy
  • Evidence of an ongoing infection
  • CLL refractory to bendamustine
  • Concurrent participation in another therapeutic clinical trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (106)

Clearview Cancer Institute

Huntsville, Alabama, 35805, United States

Location

UCLA Medical Center

Los Angeles, California, 90095, United States

Location

Stanford Cancer Center

Palo Alto, California, 94035, United States

Location

Rocky Mountain Cancer Center

Denver, Colorado, 80218, United States

Location

University of Florida

Gainesville, Florida, 32603, United States

Location

Winship Cancer Institute at Emory University

Atlanta, Georgia, 30322, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02115, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198, United States

Location

Summit Medical Group, P.A.

Morristown, New Jersey, 07962, United States

Location

North Shore University Hospital

Manhasset, New York, 11030, United States

Location

Long Island Jewish Medical Center

New Hyde Park, New York, 11042, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10021, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Willamette Valley Cancer Center

Eugene, Oregon, 97477, United States

Location

Charleston Hematology Oncology

Charleston, South Carolina, 29414, United States

Location

Texas Oncology

Austin, Texas, 78731, United States

Location

Texas Oncology PA

Dallas, Texas, 75246, United States

Location

Texas Oncology

Fort Worth, Texas, 76104, United States

Location

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

Cancer Care Northwest, US Oncology

Spokane, Washington, 99202, United States

Location

Virginia Cancer Specialists, PC

Vancouver, Washington, 98684, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

St Vincent's Hospital - Sydney

Darlinghurst, New South Wales, 2010, Australia

Location

Gosford Hospital

Gosford, New South Wales, 2250, Australia

Location

Princess Alexandra Hospital

Woolloongabba, Queensland, 4102, Australia

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Monash Medical Centre - Clayton Campus

Clayton, Victoria, 3168, Australia

Location

Sir Charles Gairdner Hospital

Nedlands, Western Australia, 6009, Australia

Location

Princess Alexandra Hospital

Woolloongabba, 4102, Australia

Location

Ziekenhuisnetwerk Antwerpen - AZ Stuivenberg

Antwerp, 2060, Belgium

Location

UZ Gent

Ghent, 9000, Belgium

Location

UZ Leuven

Leuven, 3000, Belgium

Location

Cancer Care Manitoba

Winnipeg, Manitoba, R3E 0V9, Canada

Location

Clinical Hospital "Dubrava"

Zagreb, 10000, Croatia

Location

Klinichki Bolnicki Centar-Zagreb

Zagreb, 10000, Croatia

Location

University Hospital Merkur

Zagreb, 10000, Croatia

Location

Fakultni nemocnice Brno

Brno, 625 00, Czechia

Location

Fakultní nemocnice Hradec Králové

Hradec Králové, 500 05, Czechia

Location

Fakultni nemocnice Ostrava

Ostrava, 708 52, Czechia

Location

Hopital Henri Mondor

Créteil, 94010, France

Location

Centre Jean Bernard - Clinique Victor Hugo

Le Mans, 72015, France

Location

CHRU Lille-Hôpital Claude Huriez

Lille, 59045, France

Location

Centre Léon Bérard - Centre régional de lutte contre le cancer Rhône-Alpes

Lyon, 69373, France

Location

Centre Hospitalier de Mulhouse

Mulhouse, 68100, France

Location

CHU Hôtel-Dieu-Service Hématologie

Nantes, 44 093, France

Location

Centre Hospitalier Lyon Sud

Pierre-Bénite, Pierre Bénite, France

Location

Hopital Purpan

Toulouse, 31059, France

Location

Hôpitaux de Brabois

Vandoeuvre-lés-Nancy, 54511, France

Location

G. Genimatas Hospital

Athens, 11527, Greece

Location

University General Hospital of Patras

Pátrai, 26500, Greece

Location

Semmelweis Egyetem

Budapest, 1083, Hungary

Location

Országos Onkológiai Intézet

Budapest, 1122, Hungary

Location

Debreceni Egyetem Orvos- és Egészségtudományi Centrum

Debrecen, 4032, Hungary

Location

Tallian Gyula utca 20-32

Kaposvár, 7400, Hungary

Location

Szegedi Tudományegyetem Szent-Györgyi Albert Klinikai Központ

Szeged, 6720, Hungary

Location

Mater Misericordiae Hospital

Dublin, Ireland

Location

Spedali Civili di Brescia

Brescia, 25123, Italy

Location

Ospedale Oncologico Regionale A. Businco

Cagliari, 9121, Italy

Location

IRCCS Ospedale San Raffaele

Milan, 20132, Italy

Location

Azienda Ospedaliera Universitaria San Giovanni Battista-Molinette

Torino, 10126, Italy

Location

Szpital Specjalistyczny w Brzozowie

Brzozów, 36-200, Poland

Location

Malopolskie Centrum Medyczne

Krakow, 30-510, Poland

Location

Wojewodzki Szpital Specjalistyczny im. M. Kopernika w Lodzi

Lodz, 93-510, Poland

Location

Samodzielny Publiczny Szpital Kliniczny Nr 1

Lublin, 20-081, Poland

Location

Wojewodzki Szpital w Opolu

Opole, 43-372, Poland

Location

Centralny Szpital Kliniczny MSW w Warszawie

Warsaw, 02-507, Poland

Location

Centrum Onkologii Instytut im. Marii Sklodowskiej-Curie

Warsaw, 02-781, Poland

Location

Hospital Santa Maria

Lisbon, 1649-035, Portugal

Location

"Instituto Portugues de Oncologia do Porto Francisco Gentil (IPOPFG, EPE)

Porto, 4200-072, Portugal

Location

Emergency County Clinical Hospital Brasov

Brasov, 500152, Romania

Location

"Colentina" Clinical Hospital

Bucharest, 20125, Romania

Location

"Fundeni" Clinical Institute

Bucharest, 22328, Romania

Location

Regional Oncology Institute Iasi

Iași, 700483, Romania

Location

Russian Oncology Research Center (N.N. Blokhin)

Moscow, 115478, Russia

Location

Nizhegorodskaya Regional Clinical Hospital n.a. N.A. Semashko

Nizhny Novgorod, 603126, Russia

Location

Novosibirsk State Regional Clinical Hospital

Novosibirsk, Russia

Location

Ryazan Regional Clinical Hospital

Ryazan, 390039, Russia

Location

Research Institute of Hematology and Blood Transfusion

Saint Petersburg, 193024, Russia

Location

Saratov State Medical University

Saratov, 410028, Russia

Location

State Budgetary Healthcare Institution Volgograd Regional Clinical Oncology Dispensary #1

Volgograd, 400138, Russia

Location

Hospital Universitario Germans Trias i Pujol

Badalona, Catalonia, 08916, Spain

Location

Hospital Clinic de Barcelona

Barcelona, Catalonia, 8036, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, Catalonia, 8041, Spain

Location

Hospital 12 de Octubre

Madrid, Madrid, Communidad de, 28041, Spain

Location

Hospital Universitario Puerta de Hierro

Majadahonda, Madrid, Communidad de, 28222, Spain

Location

Hospital Universitario de La Princesa

Madrid, 28033, Spain

Location

Gazi University Medical Faculty Gazi Hospital

Ankara, 06500, Turkey (Türkiye)

Location

Ankara University Medical Faculty

Ankara, 6590, Turkey (Türkiye)

Location

Istanbul University Istanbul Medical Faculty

Istanbul, 34093, Turkey (Türkiye)

Location

Ondokuz Mayis University Faculty of Medicine

Samsun, 55239, Turkey (Türkiye)

Location

Birmingham Heartlands Hospital

Birmingham, B9 5SS, United Kingdom

Location

Kent and Canterbury Hospital

Canterbury, CT1 3NG, United Kingdom

Location

University Hospital of Wales

Cardiff, CF14 4XW, United Kingdom

Location

Dorset County Hospital

Dorchester, DT1 2JY, United Kingdom

Location

St. James University Hospital

Leeds, LS9 7TF, United Kingdom

Location

Royal Liverpool University Hospital

Liverpool, L7 8XP, United Kingdom

Location

St Bartholomews Hospital

London, EC1A 7BE, United Kingdom

Location

King's College Hospital

London, SE5 9RS, United Kingdom

Location

Hammersmith Hospital

London, W12 0NN, United Kingdom

Location

University College London

London, WC1E 6BT, United Kingdom

Location

Christie Hospital

Manchester, M20 4BX, United Kingdom

Location

Nottingham University Hospitals NHS Trust

Nottingham, NG5 1PB, United Kingdom

Location

Churchill Hospital

Oxford, OX3 7LE, United Kingdom

Location

Royal Cornwall Hospital

Truro, TR1 3LJ, United Kingdom

Location

New Cross Hospital

Wolverhampton, WV10 0QP, United Kingdom

Location

Related Publications (6)

  • Zelenetz AD, Robak T, et al. Idelalisib Plus Bendamustine and Rituximab (BR) Is Superior to BR Alone in Patients with Relapsed/Refractory Chronic Lymphocytic Leukemia: Results of a Phase 3 Randomized Double-Blind Placebo-Controlled Study. American Society ofHematology (ASH) 57th Annual Meeting & Exposition; 5-8 December 2015; Orlando, FL.

    BACKGROUND
  • Barrientos JC, Brown JR, et al. Results of a Randomized Double-Blind Placebo-Controlled Phase 3 study Evaluating Idelalisib in Combination with Bendamustine and Rituximab in Patients with Relapsed/Refractory CLL and Adverse Prognostic Features. American Society of Clinical Oncology (ASCO) 2016 Annual Meeting; 3-7 June 2016; Chicago, IL.

    BACKGROUND
  • Hillmen, P, Ferra C, et al. Idelalisib in Combination with Bendamustine and Rituximab Improves Overall Survival in Patients with Relapsed/Refractory CLL: Interim Results of a Phase 3 Randomized Double-Blind Placebo-Controlled Study. European Hematology Association (EHA) 21st Annual Meeting; 9-12 June 2016; Copenhagen, Denmark.

    BACKGROUND
  • Zelenetz AD, Brown JR et al. Updated Analysis of Overall Survival in Randomized Phase III Study of Idelalisib in Combination with Bendamustine and Rituximab in Patients with Relapsed/Refractory CLL. American Society of Hematology (ASH) 58th Annual Meeting & Exposition; 3-6 December 2016; San Diego, CA

    BACKGROUND
  • Zelenetz AD, Barrientos JC, Brown JR, Coiffier B, Delgado J, Egyed M, Ghia P, Illes A, Jurczak W, Marlton P, Montillo M, Morschhauser F, Pristupa AS, Robak T, Sharman JP, Simpson D, Smolej L, Tausch E, Adewoye AH, Dreiling LK, Kim Y, Stilgenbauer S, Hillmen P. Idelalisib or placebo in combination with bendamustine and rituximab in patients with relapsed or refractory chronic lymphocytic leukaemia: interim results from a phase 3, randomised, double-blind, placebo-controlled trial. Lancet Oncol. 2017 Mar;18(3):297-311. doi: 10.1016/S1470-2045(16)30671-4. Epub 2017 Jan 28.

    PMID: 28139405BACKGROUND
  • Montillo M, Illes A, Robak T, Pristupa AS, Wach M, Egyed M, Delgado J, Jurczak W, Morschhauser F, Schuh A, Eradat H, Shreay S, Barrientos JC, Zelenetz AD. Idelalisib addition has neutral to beneficial effects on quality of life in bendamustine/rituximab-treated patients: results of a phase 3, randomized, controlled trial. Health Qual Life Outcomes. 2019 Nov 15;17(1):173. doi: 10.1186/s12955-019-1232-8.

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-CellLeukemia

Interventions

idelalisibRituximabBendamustine Hydrochloride

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsBenzimidazolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Gilead Clinical Study Information Center
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 27, 2012

First Posted

April 3, 2012

Study Start

June 15, 2012

Primary Completion

June 10, 2019

Study Completion

June 10, 2019

Last Updated

March 10, 2020

Results First Posted

February 27, 2018

Record last verified: 2020-03

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at https://www.gilead.com/science-and-medicine/research/clinical-trials-transparency-and-data-sharing-policy.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations