NCT01539512

Brief Summary

This Phase 3, randomized, double-blind, placebo-controlled study is to evaluate the effect of idelalisib in combination with rituximab on the onset, magnitude, and duration of tumor control in participants previously treated for chronic lymphocytic leukemia (CLL). Eligible patients will be randomized with a 1:1 ratio into 1 of the 2 treatment arms to receive either idelalisib plus rituximab or placebo plus rituximab. Participants who are tolerating primary study therapy but experience definitive CLL progression are eligible to receive active idelalisib therapy in the extension study, GS-US-312-0117.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
220

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Apr 2012

Geographic Reach
5 countries

72 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 12, 2012

Completed
15 days until next milestone

First Posted

Study publicly available on registry

February 27, 2012

Completed
1 month until next milestone

Study Start

First participant enrolled

April 1, 2012

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2013

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2014

Completed
7 months until next milestone

Results Posted

Study results publicly available

October 16, 2014

Completed
Last Updated

May 14, 2019

Status Verified

April 1, 2015

Enrollment Period

1.5 years

First QC Date

February 12, 2012

Results QC Date

October 9, 2014

Last Update Submit

May 1, 2019

Conditions

Keywords

CLLCAL-101GS 1101PI3KGS-US-312-0117idelalisib

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival

    Progression-free survival was defined as the interval from randomization to the earlier of the first documentation of definitive disease progression or death from any cause. Definitive disease progression was CLL progression based on standard criteria (other than lymphocytosis alone) as defined by the 2008 update of the International Workshop on CLL guidelines, ie, appearance of any new lesion; increase by ≥ 50% in the sum of the products of the perpendicular diameters of measured lymph nodes (SPD); new or ≥ 50% enlargement of liver or spleen; transformation to a more aggressive histology (eg, Richter's or prolymphocytic transformation); reduction in the number of blood cells (cytopenia) attributable to CLL.

    Up to 17 months

Secondary Outcomes (4)

  • Overall Response Rate

    Up to 17 months

  • Lymph Node Response Rate

    Up to 17 months

  • Overall Survival

    Up to 17 months

  • Complete Response Rate

    Up to 17 months

Study Arms (2)

Idelalisib + rituximab

ACTIVE COMPARATOR

Participants will receive idelalisib plus rituximab

Drug: IdelalisibDrug: Rituximab

Placebo + rituximab

PLACEBO COMPARATOR

Participants will receive placebo to match idelalisib plus rituximab

Drug: RituximabDrug: Placebo to match idelalisib

Interventions

Idelalisib 150 mg tablet administered orally twice daily

Also known as: Zydelig®, GS-1101, CAL 101
Idelalisib + rituximab

Rituximab administered intravenously 8 times through Week 20: Day 1: 375 mg/m\^2, and 500 mg/m\^2 thereafter

Also known as: Rituxan®
Idelalisib + rituximabPlacebo + rituximab

Placebo to match idelalisib administered orally twice daily

Placebo + rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Adult subjects with previously treated recurrent CLL who have measurable lymphadenopathy
  • Require therapy for CLL
  • Have experienced CLL progression \< 24 months since the completion of the last prior therapy
  • Currently not sufficiently fit to receive cytotoxic therapy because of chemotherapy-induced bone marrow damage or comorbidities.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (72)

Clearview Cancer Institute

Huntsville, Alabama, 35805, United States

Location

Arizona Oncology Associates

Tucson, Arizona, 85704, United States

Location

University of California, San Diego- Moores Cancer Center

La Jolla, California, 92093, United States

Location

Ventura County Hematology Oncology Specialists

Oxnard, California, 93030, United States

Location

UCLA

Santa Monica, California, 90404, United States

Location

Stanford Cancer Center

Stanford, California, 94305, United States

Location

Rocky Mountain Blood and Marrow Transplant Program

Denver, Colorado, 80218, United States

Location

Rocky Mountain Cancer Center

Denver, Colorado, 80218, United States

Location

Georgetown University Medical Center Lombardi Cancer Center

Washington D.C., District of Columbia, 20057, United States

Location

Collaborative Medical Research Corporation

Boynton Beach, Florida, 33435, United States

Location

Collaborative Research Group LLC

Boynton Beach, Florida, 33435, United States

Location

Florida Cancer Specialists

Fort Myers, Florida, 33916, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Florida Cancer Specialists

St. Petersburg, Florida, 33705, United States

Location

Winship Cancer Institute at Emory University

Atlanta, Georgia, 30322, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Hematology Oncology Associates of Northern New Jersey

Morristown, New Jersey, 07962, United States

Location

Long Island Jewish Medical Center

New Hyde Park, New York, 11042, United States

Location

Weill Cornell Medical College

New York, New York, 10021, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Willamette Valley Cancer Center

Springfield, Oregon, 97477, United States

Location

Northwest Cancer Specialists, PC

Tualatin, Oregon, 97062, United States

Location

Cancer Centers of the Carolinas

Greenville, South Carolina, 29605, United States

Location

Sarah Cannon Cancer Center

Nashville, Tennessee, 37203, United States

Location

Texas Oncology, P.A.

Fort Worth, Texas, 76104, United States

Location

M.D. Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Cancer Care Network of South Texas

San Antonio, Texas, 78217, United States

Location

Virginia Cancer Specialists, PC

Fairfax, Virginia, 22031, United States

Location

Oncology and Hematology Associates of Southwest Virginia, Inc

Roanoke, Virginia, 24014, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109-1024, United States

Location

Yakima Valley Memorial Hospital / North Star Lodge

Yakima, Washington, 98902, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Hôpital Henri Mondor

Créteil, 94010, France

Location

Centre Hospitalier Régional Universitaire de Lille (CHRU)

Lille, 59045, France

Location

Hôpital Emile Muller

Mulhouse, 68100, France

Location

Centre Hospitalier Lyon Sud

Pierre-Bénite, 69495, France

Location

Hôpital Pontchaillou

Rennes, 35019, France

Location

Centre Henri Becquerel

Rouen, 76038, France

Location

Hopital Purpan

Toulouse, 31059, France

Location

Universitätsklinikum Köln

Cologne, 50937, Germany

Location

Gemeinschaftspraxis Hämatologie-Onkologie

Dresden, 1307, Germany

Location

Internistische Gemeinschaftspraxis

Erlangen, 91052, Germany

Location

Stauferklinikum Schwäb. Gmünd

Mutlangen, 73557, Germany

Location

Hämatologische/Onkologische Gemeinschaftspraxis Dr. Peter Schmidt / Dr. Holger Klaproth

Neunkirchen, 66538, Germany

Location

Universitätsklinikum Ulm

Ulm, 89081, Germany

Location

Ospedale Oncologico Regionale A. Businco

Cagliari, 9121, Italy

Location

Ospedale San Raffaele S.r.l.

Milan, 20132, Italy

Location

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

Royal Bournemouth Hospital

Bournemouth, BH7 7DW, United Kingdom

Location

Addenbrooke's Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

University Hospital of Wales

Cardiff, CF14 4XW, United Kingdom

Location

Castle Hill Hospital

Cottingham, HU10 6ED, United Kingdom

Location

Dorset County Hospital

Dorchester, DT1 2JY, United Kingdom

Location

Western General Hospital

Edinburgh, EH4 2XU, United Kingdom

Location

Northwick Park Hospital

Harrow, HA1 3UJ, United Kingdom

Location

St James's University Hospital

Leeds, LS9 7TF, United Kingdom

Location

Royal Liverpool University Hospital

Liverpool, L7 8XP, United Kingdom

Location

King's College Hospital

London, SE5 9RS, United Kingdom

Location

Hammersmith Hospital

London, W12 0NN, United Kingdom

Location

Sarah Cannon Research Institute UK

London, W1G 6AD, United Kingdom

Location

Freeman Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Princess Royal University Hospital

Orpington, BR6 8ND, United Kingdom

Location

Salisbury District Hospital

Salisbury, SP2 8BJ, United Kingdom

Location

Southampton General Hospital

Southampton, SO16 6YD, United Kingdom

Location

Royal Marsden Hospital

Sutton, SM2 5PT, United Kingdom

Location

Great Western Hospital

Swindon, SN3 6BB, United Kingdom

Location

Torbay District General Hospital

Torquay, TQ2 7AA, United Kingdom

Location

Royal Cornwall Hospital

Truro, TR1 3LJ, United Kingdom

Location

New Cross Hospital

Wolverhampton, WV10 0QP, United Kingdom

Location

Yeovil District Hospital

Yeovil, BA21 4AT, United Kingdom

Location

Related Publications (3)

  • Barrientos JC, Hillmen P, Salles G, Sharman J, Stilgenbauer S, Gurtovaya O, Xing G, Ruzicka B, Bhargava P, Ghia P, Pagel JM. No increased bleeding events in patients with relapsed chronic lymphocytic leukemia and indolent non-Hodgkin lymphoma treated with idelalisib. Leuk Lymphoma. 2021 Apr;62(4):837-845. doi: 10.1080/10428194.2020.1845339. Epub 2020 Dec 10.

  • Gordon MJ, Huang J, Chan RJ, Bhargava P, Danilov AV. Medical comorbidities in patients with chronic lymphocytic leukaemia treated with idelalisib: analysis of two large randomised clinical trials. Br J Haematol. 2021 Feb;192(4):720-728. doi: 10.1111/bjh.16879. Epub 2020 Jun 29.

  • Furman RR, Sharman JP, Coutre SE, Cheson BD, Pagel JM, Hillmen P, Barrientos JC, Zelenetz AD, Kipps TJ, Flinn I, Ghia P, Eradat H, Ervin T, Lamanna N, Coiffier B, Pettitt AR, Ma S, Stilgenbauer S, Cramer P, Aiello M, Johnson DM, Miller LL, Li D, Jahn TM, Dansey RD, Hallek M, O'Brien SM. Idelalisib and rituximab in relapsed chronic lymphocytic leukemia. N Engl J Med. 2014 Mar 13;370(11):997-1007. doi: 10.1056/NEJMoa1315226. Epub 2014 Jan 22.

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-Cell

Interventions

idelalisibRituximab

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Limitations and Caveats

Following a recommendation by an independent Data Monitoring Committee (DMC), the study was stopped early due to highly statistically significant results for the primary efficacy endpoint of progression-free survival.

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences, Inc.

Study Officials

  • Thomas Jahn, MD

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 12, 2012

First Posted

February 27, 2012

Study Start

April 1, 2012

Primary Completion

October 1, 2013

Study Completion

April 1, 2014

Last Updated

May 14, 2019

Results First Posted

October 16, 2014

Record last verified: 2015-04

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations