NCT01972568

Brief Summary

This is a multi-center, double-blind, randomized, Phase 2b trial to evaluate the efficacy of atacicept in subjects with systemic lupus erythematosus (SLE).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
306

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2013

Typical duration for phase_2

Geographic Reach
18 countries

138 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 24, 2013

Completed
6 days until next milestone

First Posted

Study publicly available on registry

October 30, 2013

Completed
1 month until next milestone

Study Start

First participant enrolled

December 1, 2013

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2016

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2016

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

October 26, 2017

Completed
Last Updated

January 2, 2018

Status Verified

December 1, 2017

Enrollment Period

2.3 years

First QC Date

October 24, 2013

Results QC Date

September 29, 2017

Last Update Submit

December 4, 2017

Conditions

Keywords

AtaciceptPlacebo

Outcome Measures

Primary Outcomes (2)

  • Percentage of Subjects With Systemic Lupus Erythematosus (SLE) Responder Index (SRI) Response at Week 24 Using Screening Visit as Baseline

    SRI response, a composite measure of reduced SLE disease activity, was defined as a reduction in Systemic Lupus Erythematosus Disease Activity Index 2000 (SLEDAI-2K) disease activity score of greater than or equal to (\>=) 4 points; no significant worsening in Physician's Global Assessment (PGA) score (\<10 % increase, defined as \<0.3 point increase for statistical analyses); no new British Isles Lupus Assessment Group (BILAG) A organ domain scores and \<=1 (defined as no more than one) new BILAG B organ domain score.

    Week 24

  • Percentage of Subjects With Systemic Lupus Erythematosus (SLE) Responder Index (SRI) Response at Week 24 Using Day 1 as Baseline

    SRI response, a composite measure of reduced SLE disease activity, was defined as a reduction in Systemic Lupus Erythematosus Disease Activity Index 2000 (SLEDAI-2K) disease activity score of greater than or equal to (\>=) 4 points; no significant worsening in Physician's Global Assessment (PGA) score (\<10 % increase, defined as \<0.3 point increase for statistical analyses); no new British Isles Lupus Assessment Group (BILAG) A organ domain scores and \<=1 (defined as no more than one) new BILAG B organ domain score.

    Week 24

Secondary Outcomes (7)

  • Percentage of Subjects at Week 24 Whose Prednisone-Equivalent Corticosteroid (CS) Dose Reduced From Screening by >=25% and to a Dose of =<7.5mg/Day, and no British Isles Lupus Assessment Group (BILAG) A or 2B Flare in Disease Activity

    Week 24

  • Percentage of Subjects With Patient Global Impression of Change (PGIC) Categories at Week 24

    Week 24

  • Change From Screening in Prednisolone-Equivalent Corticosteroid (CS) Daily Dose at Week 24

    Screening and Week 24

  • Time From Randomization to First SRI Response During Treatment Period

    Baseline up to 24 Weeks

  • Percentage of Subjects With British Isles Lupus Assessment Group (BILAG)-Based Combined Lupus Assessment (BICLA) Response at Week 24

    Week 24

  • +2 more secondary outcomes

Study Arms (3)

Atacicept 75 mg

EXPERIMENTAL
Drug: Atacicept 75 milligram (mg)

Atacicept 150 mg

EXPERIMENTAL
Drug: Atacicept 150 mg

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Atacicept 75 mg will be administered as subcutaneous injection once weekly for 24 weeks.

Atacicept 75 mg

Atacicept 150 mg will be administered as subcutaneous injection once weekly for 24 weeks.

Atacicept 150 mg

Placebo matched to atacicept will be administered as subcutaneous injection once weekly for 24 weeks.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Eligible male and female subjects, aged 18 years or older
  • Must have at least moderately active SLE, as defined as SLE Disease Activity Index-2000 (SLEDAI-2K) score greater than or equal to \[\>=\] 6 at screening visit
  • At least 4 of the 11 American college of rheumatology (ACR) classification criteria for SLE (diagnosed \>= 6 months prior to the screening visit)
  • Be seropositive for anti-nuclear antibodies (ANA) and/or anti-double-stranded deoxyribonucleic acid (anti-dsDNA) antibodies

You may not qualify if:

  • Subjects have demyelinating disorder
  • Severe central nervous system SLE
  • Use of cyclophosphamide within 3 months of the screening visit
  • Urine protein:creatinine ratio (UPCr) \>= 2 milligram per milligram (mg/mg) per day

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (138)

Pinnacle Research Group LLC

Anniston, Alabama, 36207, United States

Location

Achieve Clinical Research, LLC

Birmingham, Alabama, 35216, United States

Location

University of Alabama at Birmingham - (UAB)

Birmingham, Alabama, 35294, United States

Location

Southern California Permanente Medical Group

Anaheim, California, 92806, United States

Location

Wallace Rheumatic Study Center

Los Angeles, California, 90048, United States

Location

East Bay Rheumatology Medical Group, Inc.

San Leandro, California, 94578, United States

Location

Clinical Research of West Florida - Corporate

Dunedin, Florida, 34698, United States

Location

Center for Rheumatology, Immunology & Arthritis

Fort Lauderdale, Florida, 33309, United States

Location

University of Miami Miller School of Medicine

Miami, Florida, 33136, United States

Location

Clinical Research of West Florida, Inc.

Tampa, Florida, 33603, United States

Location

Goldpoint Clinical Research, LLC

Indianapolis, Indiana, 46260, United States

Location

AA MRC LLC Ahmed Arif Medical Research Center

Grand Blanc, Michigan, 48439, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

North MS Medical Clinics, Inc.

Tupelo, Mississippi, 38801, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Rutgers New Jersey Medical School

Newark, New Jersey, 07103, United States

Location

The Feinstein Institute for Medical Research

Manhasset, New York, 11031, United States

Location

Hospital for Special Surgery

New York, New York, 10021, United States

Location

Box Arthritis & Rheumatology of the Carolinas PLLC

Charlotte, North Carolina, 28210, United States

Location

MetroHealth System

Cleveland, Ohio, 44109, United States

Location

Ohio State University Medical Center

Columbus, Ohio, 43210, United States

Location

STAT Research, Inc.

Dayton, Ohio, 45417, United States

Location

Arthritis & Rheumatology Center of Oklahoma

Oklahoma City, Oklahoma, 73103, United States

Location

OMRF

Oklahoma City, Oklahoma, 73104, United States

Location

Lynn Health Science Institute

Oklahoma City, Oklahoma, 73112, United States

Location

Clinical Research Center of Reading LLC

Wyomissing, Pennsylvania, 19610, United States

Location

Medical University of South Carolina (MUSC)

Charleston, South Carolina, 29425, United States

Location

UTMB Pathology Clinical Services

Galveston, Texas, 77555, United States

Location

Arthritis & Osteoporosis Clinic

Waco, Texas, 76708, United States

Location

Danville Orthopedic Clinic, Inc.

Danville, Virginia, 24541, United States

Location

APRILLUS

Ciudad Autonoma Buenos Aires, Argentina

Location

Atencion Integral en Reumatologia (AIR)

Ciudad Autonoma Buenos Aires, Argentina

Location

Hospital Italiano

Ciudad Autonoma Buenos Aires, Argentina

Location

Organizacion Medica de Investigacion (OMI)

Ciudad Autonoma Buenos Aires, Argentina

Location

Policlìnica Red Omip S.A - Ensayos Clinicos GC

Mar del Plata, Argentina

Location

Centro de Investigacion Pergamino SA

Pergamino, Argentina

Location

Cordis S.A.

Salta, Argentina

Location

Centro Polivalente de Asistencia e Inv. Clinica CER

San Juan, Argentina

Location

Centro Integral de Reumatologia

San Miguel de Tucumán, Argentina

Location

Centro Medico Privado de Reumatologia

San Miguel de Tucumán, Argentina

Location

Investigaciones Clinicas Tucuman

San Miguel de Tucumán, Argentina

Location

CPD - Centro de Pesquisas em Diabetes

Porto Alegre, Brazil

Location

CLION - Clínica de Oncologia da Bahia

Salvador, Brazil

Location

Clínica de Neoplasias Litoral Ltda.

Santa Catarina, Brazil

Location

Fundação Faculdade Regional de Medicina de São José do Rio Preto

São José do Rio Preto, Brazil

Location

MHAT "Eurohospital" - Plovdiv, OOD

Plovdiv, Bulgaria

Location

Medical Center "Teodora", EOOD

Rousse, Bulgaria

Location

DCC "Sveta Anna", EOOD

Sofia, Bulgaria

Location

UMHAT "Sv. Ivan Rilski", EAD

Sofia, Bulgaria

Location

Medical Center "Nov Rehabilitatsionen Tsentar", EOOD

Stara Zagora, Bulgaria

Location

MHAT-Targovishte, AD

Targovishte, Bulgaria

Location

Biomedica

Santiago, Chile

Location

Centro de Estudios Reumatologicos

Santiago, Chile

Location

Centro Medico Prosalud

Santiago, Chile

Location

SOMEAL

Santiago, Chile

Location

CINVEC - Centro de Investigacion Clinica V Region

Viña del Mar, Chile

Location

A-Shine, s.r.o.

Pilsen, Czechia

Location

Revmatologicky Ustav

Prague, Czechia

Location

Vseobecna fakultni nemocnice v Praze

Prague, Czechia

Location

MEDICAL PLUS s.r.o.

Uherské Hradiště, Czechia

Location

Kerckhoff-Klinik gGmbH

Bad Nauheim, Germany

Location

Charite Universitaetsmedizin Berlin - Campus Charite Mitte

Berlin, Germany

Location

Klinikum der Johann Wolfgang Goethe-Universitaet

Frankfurt, Germany

Location

Universitaetsklinikum Freiburg

Freiburg im Breisgau, Germany

Location

Rheumazentrum Ruhrgebiet

Herne, Germany

Location

Universitaetsklinikum Schleswig-Holstein - Campus Kiel

Kiel, Germany

Location

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, Germany

Location

Azienda Ospedaliero-Universitaria Consorziale Pol. di Bari

Bari, Italy

Location

Presidio Ospedaliero Vittorio Emanuele

Catania, Italy

Location

Azienda Ospedaliera Universitaria Careggi

Florence, Italy

Location

Azienda Ospedaliero Universitaria San Martino

Genova, Italy

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Italy

Location

Fondazione IRCCS Policlinico San Matteo

Pavia, Italy

Location

St. Luke's International Hospital

Chūōku, Japan

Location

NHO Kyushu Medical Center

Fukuoka, Japan

Location

Toho University Ohashi Medical Center

Meguro-ku, Japan

Location

Okayama University Hospital

Okayama, Japan

Location

Kitasato University Hospital

Sagamihara-shi, Japan

Location

Hokkaido University Hospital

Sapporo, Japan

Location

Sapporo City General Hospital

Sapporo, Japan

Location

Hakujujikai Sasebochuo Hospital

Sasebo-shi, Japan

Location

Tohoku University Hospital

Sendai, Japan

Location

Jichi Medical University Hospital

Shimotsuke-shi, Japan

Location

National Center for Global Health and Medicine Hospital

Shinjuku, Japan

Location

Yuaikai Tomishiro Chuo Hospital

Tomigusuku-shi, Japan

Location

Tsukuba University Hospital

Tsukuba, Japan

Location

Investigacion y Biomedicina de Chihuahua, S.C.

Chihuahua City, Mexico

Location

Icle S.C.

Guadalajara, Mexico

Location

Unidad de Investigacion en Enfermedades Cronico Degenerativas SC

Guadalajara, Mexico

Location

Investigacion Clinica de Leon S.C.

León, Mexico

Location

Morales Vargas Centro de Investigacion, S.C.

León, Mexico

Location

Centro de Estudios Clinicos Especializados

Mérida, Mexico

Location

Accelerium S. de R.L. de C.V.

Monterrey, Mexico

Location

ALIVIA Clínica de Alta Especialidad S.A. de C.V.

Monterrey, Mexico

Location

Clinica de Enfermedades Cronicas y de Procedimientos Especiales, S.C.

Morelia, Mexico

Location

Hospital Universitario de Saltillo "Dr. Gonzalo Valdés Valdés"

Saltillo, Mexico

Location

Clinica El Golf

Lima, Peru

Location

Clinica Medica Cayetano Heredia

Lima, Peru

Location

Clinica Vesalio

Lima, Peru

Location

HMA - Hospital Maria Auxiliadora

Lima, Peru

Location

Angeles University Foundation Medical Center

Angeles City, Philippines

Location

Mary Mediatrix Medical Center

Batangas, Philippines

Location

Davao Doctors Hospital

Davao City, Philippines

Location

Iloilo Doctors Hospital

Iloilo City, Philippines

Location

St. Luke's Medical Center

Quezon City, Philippines

Location

Szpital Uniwersytecki nr 2 im.dr J. Biziela

Bydgoszcz, Poland

Location

Niepubliczny Zaklad Opieki Zdrowotnej "Nasz Lekarz" Praktyka Grupowa Lekarzy Rodzinnych z

Torun, Poland

Location

Rheuma Medicus Zaklad Opieki Zdrowotnej

Warsaw, Poland

Location

Wojskowy Instytut Medyczny

Warsaw, Poland

Location

SBEI HPE Altai State Medical University of MoH and SD

Barnaul, Russia

Location

SBHI of Kem. "Regional Clinical Hospital for War Veterans"

Kemerovo, Russia

Location

First Moscow State Medical University n.a. I.M. Sechenov

Moscow, Russia

Location

Municipal City Hospital #2

Omsk, Russia

Location

Republican Hospital n.a. V.A. Baranov

Petrozavodsk, Russia

Location

Clinical Rheumatology Hospital #25

Saint Petersburg, Russia

Location

Out - patient Clinic # 107

Saint Petersburg, Russia

Location

City Clinical Hospital #12

Saratov, Russia

Location

Regional Clinical Hospital

Saratov, Russia

Location

Regional Clinical Hospital

Vladimir, Russia

Location

Yaroslavl State Medical University

Yaroslavl, Russia

Location

Dr CE Spargo and Dr RB Bhorat

Cape Town, South Africa

Location

Naidoo, A

Durban, South Africa

Location

Winelands Medical Research Centre

Stellenbosch, South Africa

Location

Gachon University Gil Medical Center

Incheon, South Korea

Location

Konkuk University Medical Center

Seoul, South Korea

Location

Kyung Hee University Hospital

Seoul, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

Ajou University Hospital

Suwon, South Korea

Location

Hospital General Universitario Gregorio Marañon

Madrid, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, Spain

Location

Hospital de Sagunto

Sagunto, Spain

Location

Hospital Clínico Universitario de Valladolid

Valladolid, Spain

Location

Royal National Hospital for Rheumatic Diseases

Bath, United Kingdom

Location

Royal Sussex County Hospital

Brighton, United Kingdom

Location

University Hospital Coventry

Coventry, United Kingdom

Location

Guy's Hospital

London, United Kingdom

Location

University College London Hospitals

London, United Kingdom

Location

Wrightington Hospital

Wigan, United Kingdom

Location

Related Publications (3)

  • Pitsiu M, Yalkinoglu O, Farrell C, Girard P, Vazquez-Mateo C, Papasouliotis O. Population pharmacokinetics of atacicept in systemic lupus erythematosus: An analysis of three clinical trials. CPT Pharmacometrics Syst Pharmacol. 2023 Aug;12(8):1157-1169. doi: 10.1002/psp4.12982. Epub 2023 Jun 18.

  • Morand EF, Isenberg DA, Wallace DJ, Kao AH, Vazquez-Mateo C, Chang P, Pudota K, Aranow C, Merrill JT. Attainment of treat-to-target endpoints in SLE patients with high disease activity in the atacicept phase 2b ADDRESS II study. Rheumatology (Oxford). 2020 Oct 1;59(10):2930-2938. doi: 10.1093/rheumatology/keaa029.

  • Merrill JT, Wallace DJ, Wax S, Kao A, Fraser PA, Chang P, Isenberg D; ADDRESS II Investigators. Efficacy and Safety of Atacicept in Patients With Systemic Lupus Erythematosus: Results of a Twenty-Four-Week, Multicenter, Randomized, Double-Blind, Placebo-Controlled, Parallel-Arm, Phase IIb Study. Arthritis Rheumatol. 2018 Feb;70(2):266-276. doi: 10.1002/art.40360.

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

TACI receptor-IgG Fc fragment fusion protein

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Merck KGaA Communication Center
Organization
Merck Healthcare, a business of Merck KGaA, Darmstadt, Germany

Study Officials

  • Medical Responsible

    EMD Serono, Inc., Rockland MA, a subsidiary of Merck KGaA, Darmstadt, Germany

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 24, 2013

First Posted

October 30, 2013

Study Start

December 1, 2013

Primary Completion

April 1, 2016

Study Completion

September 1, 2016

Last Updated

January 2, 2018

Results First Posted

October 26, 2017

Record last verified: 2017-12

Locations