NCT00137969

Brief Summary

This is a Phase II/III, randomized, double-blind, placebo-controlled, multicenter study to evaluate the efficacy and safety of rituximab compared with placebo when combined with a single stable background immunosuppressive medication in subjects with moderate to severe systemic lupus erythematosus (SLE). The primary efficacy endpoint of the trial will be evaluated at 52 weeks.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
262

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2005

Typical duration for phase_2

Geographic Reach
2 countries

65 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 10, 2005

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

August 26, 2005

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 30, 2005

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 25, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 25, 2008

Completed
2.3 years until next milestone

Results Posted

Study results publicly available

December 10, 2010

Completed
Last Updated

August 20, 2019

Status Verified

June 1, 2017

Enrollment Period

3.3 years

First QC Date

August 26, 2005

Results QC Date

June 5, 2009

Last Update Submit

August 2, 2019

Conditions

Keywords

RituxanSLELupus

Outcome Measures

Primary Outcomes (1)

  • Number of Participants Who Achieved a Major Clinical Response (MCR), Partial Clinical Response (PCR), or Nonclinical Response (NCR) Defined by British Isles Lupus Assessment Group (BILAG) Scores Over The 52-week Treatment Period

    The BILAG Index measures clinical disease activity in Systemic Lupus Erythematosus (SLE). A single alphabetic score (A through E) is used to denote disease severity for each of the 8 domains. The global BILAG score is the sum of a converted numerical score (A=9, B=3, C=1, D=0, E=0) over 8 domains. MCR = participants who achieved BILAG C scores or better at 24 weeks, maintained this response without developing a flare to 52 weeks, and did not experience a severe flare from Day 1 to Week 24; PCR = participants who achieved BILAG C score or better at 24 wks and maintained response without a flare for 16 consecutive weeks, or maximum of one BILAG B score at 24 weeks and maintained response without a flare to 52 wks, or maximum of 2 BILAG B scores at 24 wks without development of BILAG scores of A or B until Week 52 if the baseline BILAG score was 1A+\>=2Bs, or\>=2 As, or\>=4 Bs, or participants who enrolled with scores of severe disease and did not achieve a single BILAG B at Month 6.

    From baseline to 52 weeks

Secondary Outcomes (7)

  • Time-adjusted Area Under The Curve Minus Baseline (AUCMB) of BILAG Score Over The 52-week Treatment Period

    From baseline to 52 weeks

  • Number of Participants Who Achieved an MCR (Excluding PCR)

    From baseline to 52 weeks

  • Number of Participants Who Achieved a PCR (Including MCR)

    From baseline to 52 Weeks

  • Number of Participants Who Achieved a BILAG C or Better in All Domains

    24 weeks

  • Time to First Moderate or Severe Flare

    52 weeks

  • +2 more secondary outcomes

Study Arms (2)

Rituximab 1000 mg + prednisone

EXPERIMENTAL

Participants will receive rituximab 1000 mg intravenously on Days 1, 15, 168, and 182. Participants will also receive an initial dose of prednisone (0.5, 0.75, or 1.0 mg/kg orally once a day) with tapering beginning at Day 16 for 10 weeks to a dose of ≤ 10 mg/day. Participants will also receive acetaminophen 1000 mg orally and diphenhydramine 50 mg orally prior to study drug infusion.

Drug: RituximabDrug: PrednisoneDrug: AcetaminophenDrug: Diphenhydramine

Placebo + prednisone

PLACEBO COMPARATOR

Participants will receive placebo intravenously on Days 1, 15, 168, and 182. Participants will also receive an initial dose of prednisone (0.5, 0.75, or 1.0 mg/kg orally once a day) with tapering beginning at Day 16 for 10 weeks to a dose of ≤ 10 mg/day. Participants will also receive acetaminophen 1000 mg orally and diphenhydramine 50 mg orally prior to study drug infusion.

Drug: PlaceboDrug: PrednisoneDrug: AcetaminophenDrug: Diphenhydramine

Interventions

Rituximab will be supplied as a sterile liquid for IV administration.

Also known as: Rituxan, MabThera, Zytux
Rituximab 1000 mg + prednisone

Placebo will be supplied as a sterile liquid for IV administration.

Placebo + prednisone
Placebo + prednisoneRituximab 1000 mg + prednisone
Placebo + prednisoneRituximab 1000 mg + prednisone
Placebo + prednisoneRituximab 1000 mg + prednisone

Eligibility Criteria

Age16 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of systemic lupus erythematosus (SLE).
  • Active disease at screening.
  • Stable use of one immunosuppressive drug.
  • Use of an antimalarial drug.
  • For subjects of reproductive potential (males and females), use of a reliable means of contraception throughout their study participation.

You may not qualify if:

  • Unstable patients with thrombocytopenia experiencing or at high risk for developing clinically significant bleeding or organ dysfunction requiring therapies such as plasmapheresis or acute blood or platelet transfusions.
  • Active moderate to severe glomerulonephritis.
  • Retinitis, poorly controlled seizure disorder, acute confusional state, myelitis, stroke or stroke syndrome, cerebellar ataxia, or dementia that is currently active and resulting from SLE.
  • Lack of peripheral venous access.
  • Pregnant women or nursing (breast feeding) mothers.
  • History of severe, allergic, or anaphylactic reactions to humanized or murine monoclonal antibodies.
  • Significant, uncontrolled medical disease in any organ system not related to SLE that in the investigator's opinion would preclude subject participation.
  • Concomitant conditions that require oral or systemic corticosteroid use.
  • Known human immunodeficiency virus (HIV) infection.
  • Known active infection of any kind (excluding fungal infection of nail beds) or any major episode of infection requiring hospitalization or treatment with intravenous (IV) antibiotics.
  • History of deep space infection.
  • History of serious recurrent or chronic infection.
  • History of cancer, including solid tumors, hematological malignancies, and carcinoma in situ.
  • Active alcohol or drug abuse, or history of alcohol or drug abuse.
  • Major surgery.
  • +10 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (65)

Univ of Alabama School of Med; Clinical Immun Rheumatology

Birmingham, Alabama, 35294, United States

Location

Rheumatology Assoc of North AL

Huntsville, Alabama, 35801, United States

Location

Arizona Arthritis & Rheumatology Research, Pllc

Paradise Valley, Arizona, 85253, United States

Location

Univ of California, San Diego

La Jolla, California, 92037, United States

Location

Univ of Calif., Los Angeles; Rheumatology

Los Angeles, California, 90025, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Stanford University Med Ctr;Div of Immunology/Rheumatology

Palo Alto, California, 94304, United States

Location

Univ of Calif, San Francisco; Rheumatology

San Francisco, California, 94143-0111, United States

Location

Eden Medical Center San Leandro Hospital

San Leandro, California, 94578, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

Arthritis & Rheumatism; Disease Specialities

Aventura, Florida, 33180, United States

Location

Family Arthritis Center

Jupiter, Florida, 33458, United States

Location

Emory Uni ; Division of Rheumatology

Atlanta, Georgia, 30303, United States

Location

Intermountain Research Center

Boise, Idaho, 83702, United States

Location

Coeur D'Alene Arthritis Clinic

Coeur d'Alene, Idaho, 83814, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Rheumatology Associates

Chicago, Illinois, 60612, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Tri-State Arth & Rheum Center

Evansville, Indiana, 47714, United States

Location

Univ of Kansas Medical Center; Allergy/Clin Imm/Rheum

Kansas City, Kansas, 66160, United States

Location

Kentuckiana Cancer Institute

Louisville, Kentucky, 40202, United States

Location

LA State Univ; Medicine

Shreveport, Louisiana, 71103, United States

Location

Johns Hopkins Uni

Baltimore, Maryland, 21205, United States

Location

Center For Rheumatology & Bone Research

Wheaton, Maryland, 20902, United States

Location

Tufts - New England Medical Center

Boston, Massachusetts, 02111, United States

Location

Dana-Farber Cancer Institute; Rheumatology

Boston, Massachusetts, 02215-5501, United States

Location

University Of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Michigan Arthritis Rsrch Ctr

Brighton, Michigan, 48116, United States

Location

Washington University; Rheumatology Division

St Louis, Missouri, 63110, United States

Location

Center for Rheumatology, State Uni. of New York

Albany, New York, 12206, United States

Location

SUNY Downstate Medical Center.

Brooklyn, New York, 11203, United States

Location

NS-LIJ Health Systems; Rheum-Allergy Clin Immu

Lake Success, New York, 11042, United States

Location

Feinstein Institute for Medical Research

Manhasset, New York, 11030, United States

Location

NYU-Hosp for Joint Diseases; Rheum and Med

New York, New York, 10003, United States

Location

Hospital for Special Surgery

New York, New York, 10021, United States

Location

Buffalo Rheumatology Associates

Orchard Park, New York, 14127, United States

Location

Long Island Osteo/Arth Center

Plainview, New York, 11803, United States

Location

University of Rochester - Strong Memorial Hospital

Rochester, New York, 14642, United States

Location

University of North Carolina Hospitals Department of Pharmacy; Investigational Drug Services

Chapel Hill, North Carolina, 27514, United States

Location

Duke Medical Center

Durham, North Carolina, 27710, United States

Location

Physicians East Pa

Greenville, North Carolina, 27834, United States

Location

Ohio State University; Division of Nephrology

Columbus, Ohio, 43210, United States

Location

Bone and Joint Hospital at St. Anthony Research Department

Oklahoma City, Oklahoma, 73103, United States

Location

Oklahoma Medical Research Foundation

Oklahoma City, Oklahoma, 73104, United States

Location

Oklahoma Center For Arthritis Therapy & Research

Tulsa, Oklahoma, 74104, United States

Location

Portland Medical Associates

Portland, Oregon, 97224, United States

Location

East Penn Rheumatology Associates, Pc

Bethlehem, Pennsylvania, 18015, United States

Location

Altoona Arthritis & Osteo Center

Duncansville, Pennsylvania, 16635, United States

Location

Uni of Pennslyvania Medical Center

Philadelphia, Pennsylvania, 19104, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, 19141, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

Medical Univ of South Carolina

Charleston, South Carolina, 29425, United States

Location

Arthritis Associates PLLC

Chattanooga, Tennessee, 37404, United States

Location

Metroplex Clinical Research

Dallas, Texas, 75231, United States

Location

Arthritis Centers of Texas

Dallas, Texas, 75246, United States

Location

Houston Inst. For Clinical Research

Houston, Texas, 77074, United States

Location

Arthritis & Osteoporosis Associates, LLP

Lubbock, Texas, 79424, United States

Location

Texas Research Center

Sugar Land, Texas, 77479, United States

Location

University of Virginia Med Ctr; Div of Ped Respiratory Med

Charlottesville, Virginia, 22908, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Seattle Rheumatology Assoc; Swedish Rheumatology Research

Seattle, Washington, 98104, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

Arthritis Northwest, Spokane

Spokane, Washington, 99204, United States

Location

Univ of Manitoba, Health Scien; Arthritis Centre

Winnipeg, Manitoba, R3A1M4, Canada

Location

St. Joseph'S Health Care Centre

London, Ontario, N6A 4V2, Canada

Location

Related Publications (1)

  • Merrill JT, Neuwelt CM, Wallace DJ, Shanahan JC, Latinis KM, Oates JC, Utset TO, Gordon C, Isenberg DA, Hsieh HJ, Zhang D, Brunetta PG. Efficacy and safety of rituximab in moderately-to-severely active systemic lupus erythematosus: the randomized, double-blind, phase II/III systemic lupus erythematosus evaluation of rituximab trial. Arthritis Rheum. 2010 Jan;62(1):222-33. doi: 10.1002/art.27233.

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

RituximabPrednisoneAcetaminophenDiphenhydramine

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsPregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsAcetanilidesAnilidesAmidesOrganic ChemicalsAniline CompoundsAminesEthylaminesBenzhydryl CompoundsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbons

Results Point of Contact

Title
Medical Communications
Organization
Hoffman-LaRoche

Study Officials

  • Paul Brunetta, M.D.

    Genentech, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 26, 2005

First Posted

August 30, 2005

Study Start

May 10, 2005

Primary Completion

August 25, 2008

Study Completion

August 25, 2008

Last Updated

August 20, 2019

Results First Posted

December 10, 2010

Record last verified: 2017-06

Locations