NCT00624338

Brief Summary

This study is to evaluate the efficacy and safety of atacicept compared to placebo in preventing new flares in subjects with systemic lupus erythematosus (SLE) and to confirm the optimal dose of atacicept for treatment of subjects with SLE and gain information on the effect of atacicept on markers specific to its mechanism of action (MoA) and their correlation to disease activity/progression. Study medication will be administered through subcutaneous (under the skin) injections, beginning with twice weekly injections for the first 4 weeks, followed by once weekly doses for 48 weeks. Following the last treatment, a safety follow-up period of 24 weeks will be conducted.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
461

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2008

Longer than P75 for phase_2

Geographic Reach
28 countries

112 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2008

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

February 15, 2008

Completed
12 days until next milestone

First Posted

Study publicly available on registry

February 27, 2008

Completed
4.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2012

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2012

Completed
3.5 years until next milestone

Results Posted

Study results publicly available

March 14, 2016

Completed
Last Updated

March 14, 2016

Status Verified

March 1, 2016

Enrollment Period

4.3 years

First QC Date

February 15, 2008

Results QC Date

January 19, 2016

Last Update Submit

March 11, 2016

Conditions

Keywords

Atacicept 75 and 150 mgPlacebo

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Experiencing a New Flare as Defined by British Isles Lupus Assessment Group (BILAG) Score A or B

    A flare was defined as having an adjudicated BILAG A or B score in any of the 8 organ systems during treatment, or imputed for participants who had premature treatment discontinuation. Discontinuations due to sponsor termination of the atacicept 150 mg group were not imputed as flares in this analysis. The BILAG disease activity index evaluates systemic lupus erythematosus (SLE) activity in 8 organ systems, using a separate alphabetic score (A to E) assigned to each organ system defined as follows. BILAG A: Disease sufficiently active requiring disease-modifying treatment (prednisone greater than 20 mg daily or immunosuppressants); BILAG B: Disease less active than in "A", mild reversible problems requiring only symptomatic therapy such as antimalarials, non-steroidal anti-inflammatory drugs (NSAIDs), or prednisone less than 20 mg day; BILAG C: Stable mild disease; BILAG D: System previously affected but now inactive; BILAG E: System never involved.

    From screening up to Week 52

Secondary Outcomes (4)

  • Time to First New Flare as Defined by BILAG Score A or B

    From screening up to Week 52

  • Percentage of Participants Experiencing a New Flare as Defined by BILAG Score A or B During Initial 24 Weeks

    From screening up to Week 24

  • Percentage of Participants Within Ordinal Response Categories for British Isles Lupus Assessment Group (BILAG) Flares

    Week 52

  • Mean Cumulative Corticosteroid Dose

    Randomization up to Week 52

Study Arms (3)

Atacicept 75 mg

EXPERIMENTAL
Drug: Atacicept 75 mg

Atacicept 150 mg

EXPERIMENTAL
Drug: Atacicept 150 mg

Placebo

PLACEBO COMPARATOR
Other: Placebo Comparator

Interventions

75 milligram (mg) atacicept injection will be administered subcutaneously twice weekly during initial loading period for 4 weeks followed by once weekly during maintenance period for subsequent 48 weeks.

Atacicept 75 mg

150 mg atacicept injection will be administered subcutaneously twice weekly during initial loading period for 4 weeks followed by once weekly during maintenance period for subsequent 48 weeks.

Atacicept 150 mg

Placebo matched to atacicept injection will be administered subcutaneously twice weekly during initial loading period for 4 weeks followed by once weekly during maintenance period for subsequent 48 weeks.

Placebo

Eligibility Criteria

Age16 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female 16 years of age or older
  • Disease history of at least six months meeting at least 4 out of the 11 American College of Rheumatology (ACR) criteria for SLE
  • Active SLE with at least one British Isles Lupus Assessment Group (BILAG) flare A or B at screening requiring a change in the dose of corticosteroids
  • Positive antinuclear antibody (ANA) or anti-double-stranded deoxyribonucleic acid (dsDNA) at screening
  • Female subjects must be willing to avoid pregnancy by using an adequate method of contraception for 4 weeks prior to Study Day 1, during the trial and 24 weeks after the last dose of study medication

You may not qualify if:

  • Active moderate to severe glomerulonephritis (kidney impairment) as defined in the protocol
  • Active central nervous system SLE deemed to be severe/progressive and/or associated with significant cognitive impairment leading to inability to provide informed consent and/or comply with the protocol
  • Previous treatment with rituximab, abatacept, or belimumab
  • History of demyelinating disease such as multiple sclerosis (MS) or optic neuritis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (113)

Division of Clinical Immunology and Rheumatology - UAB

Birmingham, Alabama, 35249-7201, United States

Location

Stanford University

Palo Alto, California, United States

Location

Research Site

San Diego, California, United States

Location

Inland Rheumatology Clinical Trials Inc

Upland, California, United States

Location

Research Site

Jacksonville, Florida, United States

Location

Research Site

Boise, Idaho, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

US Local Medical Information

Rockland, Massachusetts, 02370, United States

Location

Wayne State University

Detroit, Michigan, 48201, United States

Location

Justus J. Fiechtner, MD, MPH

Lansing, Michigan, 48910, United States

Location

SUNY Health Science Center at Brooklyn

Brooklyn, New York, United States

Location

Feinstein Institute for Medical Research

Manhasset, New York, 11030, United States

Location

Hospital for Special Surgey

New York, New York, 10021, United States

Location

Research Site

New York, New York, United States

Location

Research Site

Cincinnati, Ohio, United States

Location

University of Cincinnati Medical Center, Division of Immunology

Cincinnati, Ohio, United States

Location

Research Site

Temple, Texas, United States

Location

Virginia Mason Medical Center

Seattle, Washington, United States

Location

Research Site

Buenos Aires, Argentina

Location

Research Site

Córdoba, Argentina

Location

Research Site

Quilmes, Argentina

Location

Research Site

San Juan, Argentina

Location

Research Site

San Miguel de Tucumán, Argentina

Location

Research Site

Cairns, Australia

Location

Research Site

Clayton, Victoria, Australia

Location

Research Site

Sunshine Coast, Queensland, Australia

Location

Research Site

Woodville S.A., Australia

Location

Research Site

Wein, Austria

Location

Research Site

Sofia, Bulgaria

Location

Research Site

Osijek, Croatia

Location

Research Site

Rijeka, Croatia

Location

Research Site

Split, Croatia

Location

Research Site

Zagreb, Croatia

Location

Research Site

Prague, Czechia

Location

Research Site

Bordeaux Pessac, France

Location

Research Site

Lille, France

Location

Research Site

Montpelier Cedex, France

Location

Research Site

Paris, France

Location

Research Site

Strasbourg, France

Location

Research Site

Toulouse, France

Location

Research Site

Berlin, Germany

Location

Research Site

Erlangen, Germany

Location

Research Site

Hanover, Germany

Location

Research Site

Heidelberg, Germany

Location

Research Site

Herne, Germany

Location

Research Site

München, Germany

Location

Research Site

Münster, Germany

Location

Research Site

Athens, Greece

Location

Research Site

Thessaloniki, Greece

Location

Research Site

Secunderabad, Andhra Pradesh, India

Location

Research Site

Haifa, Israel

Location

Research Site

Jerasalem, Israel

Location

Research Site

Petah Tikva, Israel

Location

Research Site

Tel Aviv, Israel

Location

Research Site

Riga, Latvia

Location

Research Site

Beirut, Lebanon

Location

Research Site

Kaunas, Lithuania

Location

Research Site

Vilnius, Lithuania

Location

Research Site

Kuala Lumpur, Malaysia

Location

Research Site

Perak, Malaysia

Location

Research Site

Seremban, Malaysia

Location

Research Site

Guadalajara Jalisco, Mexico

Location

Research Site

Tijuana, BC, Mexico

Location

Research Site

Amsterdam, Netherlands

Location

Research Site

Leiden, Netherlands

Location

Research Site

Maastricht, Netherlands

Location

Research Site

Angeles City, Pampanga, Philippines

Location

Research Site

Davao City, Philippines

Location

Research Site

Iloilo City, Philippines

Location

Research Site

Las Piñas, Philippines

Location

Research Site

Manila, Philippines

Location

Research Site

Bialystok, Poland

Location

Research Site

Gdansk, Poland

Location

Research Site

Krakow, Poland

Location

Research Site

Lublin, Poland

Location

Research Site

Szczecin, Poland

Location

Research Site

Torun, Poland

Location

Research Site

Warsaw, Poland

Location

Research Site

Kemerovo, Russia

Location

Research Site

Petrozavodsk, Russia

Location

Research Site

Ryazan, Russia

Location

Research Site

Saint Petersburg, Russia

Location

Research Site

Saratov, Russia

Location

Research Site

Tula, Russia

Location

Research Site

Yaroslavl, Russia

Location

Research Site

Belgrade, Serbia

Location

Research Site

New Belgrade, Serbia

Location

Research Site

Niška Banja, Serbia

Location

Research Site

Cape Town, South Africa

Location

Research Site

Durban, South Africa

Location

Research Site

Panorama, Western Cape, South Africa

Location

Research Site

Parlow, Western Cape, South Africa

Location

Research Site

Pinelands, South Africa

Location

Research Site

Stellenbosch, Western Cape, South Africa

Location

Research Site

Gyeonggi-do, South Korea

Location

Research Site

Seoul, South Korea

Location

Research Site

Barcelona, Spain

Location

Research Site

Madrid, Spain

Location

Research Site

Málaga, Spain

Location

Research Site

Santiago de Compostela, Spain

Location

Research Site

Sankt Gallen, Switzerland

Location

Research Site

Taichung, Taiwan

Location

Research Site

Taipei, Taiwan

Location

Research Site

Taoyuan District, Taiwan

Location

Research Site

Donetsk, Ukraine

Location

Research Site

Kharkiv, Ukraine

Location

Research Site

Kyiv, Ukraine

Location

Research Site

Lviv, Ukraine

Location

Research Site

Ternopil, Ukraine

Location

Research Site

Vinnytsia, Ukraine

Location

Research Site

Zhytomyr, Ukraine

Location

Research Site

London, United Kingdom

Location

Research Site

Manchester, United Kingdom

Location

Related Publications (3)

  • Pitsiu M, Yalkinoglu O, Farrell C, Girard P, Vazquez-Mateo C, Papasouliotis O. Population pharmacokinetics of atacicept in systemic lupus erythematosus: An analysis of three clinical trials. CPT Pharmacometrics Syst Pharmacol. 2023 Aug;12(8):1157-1169. doi: 10.1002/psp4.12982. Epub 2023 Jun 18.

  • Eslami M, Willen D, Papasouliotis O, Schuepbach-Mallpell S, Willen L, Donze O, Yalkinoglu O, Schneider P. Kinetics of free and ligand-bound atacicept in human serum. Front Immunol. 2022 Dec 2;13:1035556. doi: 10.3389/fimmu.2022.1035556. eCollection 2022.

  • Isenberg D, Gordon C, Licu D, Copt S, Rossi CP, Wofsy D. Efficacy and safety of atacicept for prevention of flares in patients with moderate-to-severe systemic lupus erythematosus (SLE): 52-week data (APRIL-SLE randomised trial). Ann Rheum Dis. 2015 Nov;74(11):2006-15. doi: 10.1136/annrheumdis-2013-205067. Epub 2014 Jun 20.

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

TACI receptor-IgG Fc fragment fusion protein

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Limitations and Caveats

Atacicept 150 mg group was discontinued on 2 February 2011 based on the recommendation from the Independent Data Monitoring Committee.

Results Point of Contact

Title
Merck KGaA Communication Center
Organization
Merck Healthcare, a business of Merck KGaA, Darmstadt, Germany

Study Officials

  • Medical Responsible

    Merck KGaA, Darmstadt, Germany

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 15, 2008

First Posted

February 27, 2008

Study Start

January 1, 2008

Primary Completion

April 1, 2012

Study Completion

October 1, 2012

Last Updated

March 14, 2016

Results First Posted

March 14, 2016

Record last verified: 2016-03

Locations