NCT01668784

Brief Summary

The purpose of the study is to compare the clinical benefit, as measured by duration of overall survival, of Nivolumab vs. Everolimus in subjects with advanced or metastatic clear-cell renal cell carcinoma who have received prior anti-angiogenic therapy

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
821

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2012

Longer than P75 for phase_3

Geographic Reach
23 countries

163 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 16, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 20, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

October 9, 2012

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 6, 2015

Completed
12 months until next milestone

Results Posted

Study results publicly available

April 29, 2016

Completed
5.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 19, 2021

Completed
Last Updated

August 9, 2022

Status Verified

July 1, 2022

Enrollment Period

2.6 years

First QC Date

August 16, 2012

Results QC Date

March 28, 2016

Last Update Submit

July 15, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS) at Primary Endpoint

    Overall Survival (OS) was defined as the time from randomization to the date of death. Participants that had not died were censored at last known date alive. Median OS time was calculated using Kaplan-Meier Estimates. Interim analysis for the Primary Endpoint occurred after 398 deaths (70% of the total OS events needed for final analysis). At that time the data monitoring committee noted that the pre-specified boundary for OS (nominal significance level p \< 0.0148) was crossed while no new safety signals that would affect continuation of the study were found. The study was stopped early by the Sponsor, Bristol-Myers Squibb (BMS) and the interim analysis became the final analysis. As a result, participants in the everolimus groups could be assessed for a crossover to nivolumab treatment if they met all inclusion criteria.

    Randomization until 398 deaths, up to May 2015 (approximately 30 months)

Secondary Outcomes (9)

  • Investigator-assessed Objective Response Rate (ORR)

    from randomization up to disease progression or death (approximately up to 105 Months)

  • Investigator-assessed Duration of Objective Response

    From randomization to date of disease progression or death or censoring if no progression or death occurred (approximately 105 months)

  • Investigator-assessed Time to Objective Response

    Randomization to date of first response (approximately 105 months)

  • Investigator-assessed Time of Progression-free Survival (PFS)

    from randomization up to disease progression or death (approximately up to 105 Months)

  • Overall Survival (OS) by Programmed Death-Ligand 1 (PD-L1) Expression Level

    Randomization to date of death or date of last contact for patients without documentation of death, up to May 2015 (approximately 30 months)

  • +4 more secondary outcomes

Study Arms (2)

Arm 1: Nivolumab

EXPERIMENTAL

Nivolumab 3 mg/kg solution intravenously every 2 weeks until documented disease progression, discontinuation due to toxicity, withdrawal of consent or the study ends

Biological: Nivolumab

Arm 2: Everolimus

ACTIVE COMPARATOR

Everolimus 10 mg tablets by mouth daily until documented disease progression, discontinuation due to toxicity, withdrawal of consent or the study ends

Drug: Everolimus

Interventions

NivolumabBIOLOGICAL
Also known as: BMS-936558
Arm 1: Nivolumab
Also known as: Afinitor
Arm 2: Everolimus

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Men \& women ≥18 years of age
  • Histologic confirmation of renal cell carcinoma (RCC) with clear-cell component
  • Advanced/metastatic RCC
  • Measurable disease per Response Evaluation Criteria in Solid Tumors (RECIST) 1.1 criteria
  • Received 1 or 2 prior anti-angiogenic therapy regimens in advanced or metastatic setting
  • No more than 3 total prior systemic treatment regimens in the advanced or metastatic setting, and evidence of progression on or after last treatment regimen received and within 6 months of enrollment
  • Karnofsky Performance Score ≥70%

You may not qualify if:

  • Any Central Nervous System (CNS) metastases or history of CNS metastases
  • Prior therapy with an Mammalian target of rapamycin (mTOR) inhibitor
  • Any active known or suspected autoimmune disease
  • Uncontrolled adrenal insufficiency
  • Active chronic liver disease
  • Prior malignancy active within past 3 years, except for locally curable cancers

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (168)

Local Institution - 0182

Fayetteville, Arkansas, 72703, United States

Location

UCSD Moores Cancer Center

La Jolla, California, 92093-0698, United States

Location

Local Institution - 0024

Los Angeles, California, 90033, United States

Location

University Of Southern California

Los Angeles, California, 90033, United States

Location

Cedars Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Ucsf Helen Diller Family Comprehensive Cancer Center

San Francisco, California, 94115, United States

Location

Stanford Cancer Institute

Stanford, California, 94305, United States

Location

University Of Colorado

Aurora, Colorado, 80045, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Local Institution - 0027

Washington D.C., District of Columbia, 20007, United States

Location

H. Lee Moffitt Cancer Center & Research Institute

Tampa, Florida, 33612-9497, United States

Location

Winship Cancer Institute.

Atlanta, Georgia, 30322, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Loyola University Chicago

Maywood, Illinois, 60153, United States

Location

Indiana University Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

University Of Iowa Hospitals And Clinics

Iowa City, Iowa, 52242, United States

Location

Sidney Kimmel Comprehensive Cancer Center At Johns Hopkins

Baltimore, Maryland, 21231-1000, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

University Of Michigan Comprehensive Cancer Center

Ann Arbor, Michigan, 48109-5946, United States

Location

Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Roswell Park Cancer Institute

Buffalo, New York, 14263, United States

Location

Memorial Sloan Kettering Nassau

New York, New York, 10065, United States

Location

Weill Cornell Medical College

New York, New York, 10065, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

The Ohio State University

Columbus, Ohio, 43210, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, 19140, United States

Location

Medical University Of South Carolina

Charleston, South Carolina, 29425, United States

Location

St Francis Hospital

Greenville, South Carolina, 29601, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37203, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232-6307, United States

Location

Ut Southwestern Medical Center

Dallas, Texas, 75390-9133, United States

Location

Local Institution - 0139

Houston, Texas, 77030-4009, United States

Location

CTRC at UTHSC San Antonio

San Antonio, Texas, 78229, United States

Location

Local Institution - 0076

Richmond, Virginia, 23229, United States

Location

Local Institution - 0009

Seattle, Washington, 98109, United States

Location

University Of Washington

Seattle, Washington, 98109, United States

Location

COIBA

Berazategui, Buenos Aires, 1880, Argentina

Location

Local Institution

Capital Federal, Buenos Aires, 1431, Argentina

Location

Centro Para La Atencion Integral Del Paciente Oncologico

San Miguel de Tucumán, Tucumán Province, 4000, Argentina

Location

Local Institution

Buenos Aires, C1280AEB, Argentina

Location

Local Institution

Buenos Aires, C1426ANZ, Argentina

Location

Instituto Oncologico De Cordoba

Córdoba, X5006HBF, Argentina

Location

Local Institution - 0095

Westmead, New South Wales, 2145, Australia

Location

Local Institution

Woodville South, South Australia, 5011, Australia

Location

Local Institution

Box Hill, Victoria, 3128, Australia

Location

Local Institution

Clayton, Victoria, 3168, Australia

Location

Local Institution

Melbourne, Victoria, 3000, Australia

Location

Local Institution

Linz, 4020, Austria

Location

Local Institution

Vienna, 1090, Austria

Location

Local Institution

Vienna, 1130, Austria

Location

Local Institution

Brussels, 1090, Belgium

Location

Local Institution

Brussels, 1200, Belgium

Location

Local Institution

Ghent, 9000, Belgium

Location

Local Institution

Leuven, 3000, Belgium

Location

Local Institution - 0125

Ijuí, Rio Grande do Sul, 98700-000, Brazil

Location

Local Institution - 0124

São Paulo, 01246-000, Brazil

Location

Local Institution

São Paulo, 01321-001, Brazil

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

BC Cancer Agency - Vancouver Centre

Vancouver, British Columbia, V5Z 4E6, Canada

Location

Centre D'Oncologie Dr-Leon-Richard

Moncton, New Brunswick, E1C 8X3, Canada

Location

QEII Health Sciences Centre

Halfax, Nova Scotia, B3H 2Y9, Canada

Location

Local Institution - 0143

Oshawa, Ontario, L1G 2B9, Canada

Location

Princess Margaret Hospital

Toronto, Ontario, M5G 2M9, Canada

Location

Chum, Hopital Notre-Dame

Montreal, Quebec, H2L 4M1, Canada

Location

Local Institution - 0145

Montreal, H3T 1E2, Canada

Location

Local Institution

Hradec Králové, 500 05, Czechia

Location

Local Institution

Olomouc, 779 00, Czechia

Location

Local Institution

Prague, 150 06, Czechia

Location

Local Institution

Aarhus N, 8200, Denmark

Location

Local Institution

Herlev, 2730, Denmark

Location

Local Institution - 0137

Odense, 5000, Denmark

Location

Local Institution

Helsinki, 00029, Finland

Location

Local Institution - 0006

Vandœuvre-lès-Nancy, Lorraine, 54519, France

Location

Local Institution - 0008

Bordeaux, 33075, France

Location

Local Institution

Bordeaux, 33075, France

Location

Local Institution - 0007

Lyon, 69373, France

Location

Local Institution

Lyon, 69373, France

Location

Local Institution - 0004

Marseille, 13009, France

Location

Local Institution

Marseille, 13009, France

Location

Local Institution - 0118

Paris, 75908, France

Location

Local Institution - 0003

Poitiers, 86000, France

Location

Local Institution

Poitiers, 86000, France

Location

Local Institution - 0005

Saint-Herblain, 44805, France

Location

Local Institution

Saint-Herblain, 44805, France

Location

Local Institution - 0012

Toulouse, 31059, France

Location

Local Institution

Toulouse, 31059, France

Location

Local Institution

Vandœuvre-lès-Nancy, 54511, France

Location

Local Institution - 0002

Villejuif, 94805, France

Location

Local Institution

Villejuif, 94805, France

Location

Local Institution

Aachen, 52074, Germany

Location

Local Institution

Dresden, 01307, Germany

Location

Local Institution

Erlangen, 91054, Germany

Location

Local Institution

Essen, 45122, Germany

Location

Local Institution

Hanover, 30625, Germany

Location

Local Institution - 0126

Heidelberg, 69120, Germany

Location

Local Institution

Munich, 81675, Germany

Location

Local Institution

Tübingen, 72076, Germany

Location

Alexandra General Hospital Of Athens

Athens, 12462, Greece

Location

Euromedica General Clinic of Thessaloniki

Thessaloniki, 54645, Greece

Location

Local Institution

Tallaght, Dublin, DUBLIN 24, Ireland

Location

Local Institution - 0087

Dublin, 7, Ireland

Location

Local Institution

Dublin, Dublin 7, Ireland

Location

Local Institution

Haifa, 31096, Israel

Location

Local Institution - 0148

Petah Tikva, 49100, Israel

Location

Local Institution

Ramat Gan, 52621, Israel

Location

Local Institution

Tel Aviv, 64239, Israel

Location

Local Institution

Arezzo, 52100, Italy

Location

Local Institution

Meldola (fc), 47014, Italy

Location

Local Institution - 0082

Milan, 20133, Italy

Location

Local Institution

Rimini, 47900, Italy

Location

Local Institution

Roma, 00144, Italy

Location

Local Institution

Roma, 00152, Italy

Location

Local Institution - 0102

Rozzano, 20089, Italy

Location

Local Institution

Siena, 53100, Italy

Location

Local Institution

Terni, 05100, Italy

Location

Local Institution

Akita, Akita, 0108543, Japan

Location

Local Institution

Chiba, Chiba, 2608717, Japan

Location

Local Institution

Higashiku, Fukuoka, 812-8582, Japan

Location

Local Institution

Sapporo, Hokkaido, 0608543, Japan

Location

Local Institution

Sapporo, Hokkaido, 0608648, Japan

Location

Local Institution

Morioka, Iwate, 0208505, Japan

Location

Local Institution

Yokohama, Kanagawa, 2360004, Japan

Location

Local Institution

Kyoto, Kyoto, 602-8566, Japan

Location

Local Institution

Osaka-sayama-shi, Osaka, 5898511, Japan

Location

Local Institution - 0169

Suita, Osaka, 5650871, Japan

Location

Local Institution - 0167

Hamamatsu, Shizuoka, 4313192, Japan

Location

Local Institution

Tokushima, Tokushima, 7708503, Japan

Location

Local Institution

Yamagata, Yamagata, 9909585, Japan

Location

Local Institution

Kobe-city, Hyogo, 650-0017, Japan

Location

Local Institution

Kumamoto, 860-8556, Japan

Location

Local Institution

Tokyo, 1138603, Japan

Location

Local Institution

Tokyo, 1138655, Japan

Location

Local Institution

Tokyo, 1358550, Japan

Location

Local Institution

Tokyo, 1608582, Japan

Location

Local Institution

Tokyo, 1628666, Japan

Location

Local Institution

Tokyo, 1738606, Japan

Location

Local Institution

Bergen, 5021, Norway

Location

Local Institution

Lorenskog, 1478, Norway

Location

Local Institution

Gdansk, 80-219, Poland

Location

Local Institution

Lodz, 93-513, Poland

Location

Local Institution

Poznan, 60-569, Poland

Location

Local Institution

Rybnik, 44-200, Poland

Location

Local Institution

Warsaw, 00-909, Poland

Location

Local Institution

Wroclaw, 50-556, Poland

Location

Local Institution

Bucharest, 022328, Romania

Location

Local Institution

Craiova, 200385, Romania

Location

Local Institution

Iași, 700106, Romania

Location

Local Institution

Timișoara, 300167, Romania

Location

Local Institution

Moscow, 115478, Russia

Location

Local Institution

Moscow, 121309, Russia

Location

Local Institution

Saint Petersburg, 198255, Russia

Location

Local Institution

Pamplona, Navarre, 31008, Spain

Location

Local Institution

Barcelona, 08035, Spain

Location

Local Institution - 0064

L'Hospitalet de Llobregat, 08907, Spain

Location

Local Institution

Madrid, 28007, Spain

Location

Local Institution

Madrid, 28040, Spain

Location

Local Institution

Madrid, 28041, Spain

Location

Local Institution

Gothenberg, 413 45, Sweden

Location

Local Institution

Solna, 171 64, Sweden

Location

Local Institution

Cambridge, Cambridgeshire, CB2 0QQ, United Kingdom

Location

Local Institution - 0048

Swansea, Carmarthenshire, SA2 8QA, United Kingdom

Location

Local Institution

Swansea, Carmarthenshire, SA2 8QA, United Kingdom

Location

Local Institution

London, Greater London, HA6 2RN, United Kingdom

Location

Local Institution

London, Greater London, SW3 6JJ, United Kingdom

Location

Related Publications (8)

  • Klijn SL, Fenwick E, Kroep S, Johannesen K, Malcolm B, Kurt M, Kiff C, Borrill J. What Did Time Tell Us? A Comparison and Retrospective Validation of Different Survival Extrapolation Methods for Immuno-Oncologic Therapy in Advanced or Metastatic Renal Cell Carcinoma. Pharmacoeconomics. 2021 Mar;39(3):345-356. doi: 10.1007/s40273-020-00989-1. Epub 2021 Jan 11.

  • Ambavane A, Yang S, Atkins MB, Rao S, Shah A, Regan MM, McDermott DF, Michaelson MD. Clinical and economic outcomes of treatment sequences for intermediate- to poor-risk advanced renal cell carcinoma. Immunotherapy. 2020 Jan;12(1):37-51. doi: 10.2217/imt-2019-0199. Epub 2020 Jan 29.

  • Shah R, Botteman M, Solem CT, Luo L, Doan J, Cella D, Motzer RJ. A Quality-adjusted Time Without Symptoms or Toxicity (Q-TWiST) Analysis of Nivolumab Versus Everolimus in Advanced Renal Cell Carcinoma (aRCC). Clin Genitourin Cancer. 2019 Oct;17(5):356-365.e1. doi: 10.1016/j.clgc.2019.05.010. Epub 2019 May 31.

  • Long GV, Tykodi SS, Schneider JG, Garbe C, Gravis G, Rashford M, Agrawal S, Grigoryeva E, Bello A, Roy A, Rollin L, Zhao X. Assessment of nivolumab exposure and clinical safety of 480 mg every 4 weeks flat-dosing schedule in patients with cancer. Ann Oncol. 2018 Nov 1;29(11):2208-2213. doi: 10.1093/annonc/mdy408.

  • Escudier B, Motzer RJ, Sharma P, Wagstaff J, Plimack ER, Hammers HJ, Donskov F, Gurney H, Sosman JA, Zalewski PG, Harmenberg U, McDermott DF, Choueiri TK, Richardet M, Tomita Y, Ravaud A, Doan J, Zhao H, Hardy H, George S. Treatment Beyond Progression in Patients with Advanced Renal Cell Carcinoma Treated with Nivolumab in CheckMate 025. Eur Urol. 2017 Sep;72(3):368-376. doi: 10.1016/j.eururo.2017.03.037. Epub 2017 Apr 12.

  • Escudier B, Sharma P, McDermott DF, George S, Hammers HJ, Srinivas S, Tykodi SS, Sosman JA, Procopio G, Plimack ER, Castellano D, Gurney H, Donskov F, Peltola K, Wagstaff J, Gauler TC, Ueda T, Zhao H, Waxman IM, Motzer RJ; CheckMate 025 investigators. CheckMate 025 Randomized Phase 3 Study: Outcomes by Key Baseline Factors and Prior Therapy for Nivolumab Versus Everolimus in Advanced Renal Cell Carcinoma. Eur Urol. 2017 Dec;72(6):962-971. doi: 10.1016/j.eururo.2017.02.010. Epub 2017 Mar 3.

  • Cella D, Grunwald V, Nathan P, Doan J, Dastani H, Taylor F, Bennett B, DeRosa M, Berry S, Broglio K, Berghorn E, Motzer RJ. Quality of life in patients with advanced renal cell carcinoma given nivolumab versus everolimus in CheckMate 025: a randomised, open-label, phase 3 trial. Lancet Oncol. 2016 Jul;17(7):994-1003. doi: 10.1016/S1470-2045(16)30125-5. Epub 2016 Jun 6.

  • Motzer RJ, Escudier B, McDermott DF, George S, Hammers HJ, Srinivas S, Tykodi SS, Sosman JA, Procopio G, Plimack ER, Castellano D, Choueiri TK, Gurney H, Donskov F, Bono P, Wagstaff J, Gauler TC, Ueda T, Tomita Y, Schutz FA, Kollmannsberger C, Larkin J, Ravaud A, Simon JS, Xu LA, Waxman IM, Sharma P; CheckMate 025 Investigators. Nivolumab versus Everolimus in Advanced Renal-Cell Carcinoma. N Engl J Med. 2015 Nov 5;373(19):1803-13. doi: 10.1056/NEJMoa1510665. Epub 2015 Sep 25.

Related Links

MeSH Terms

Conditions

Neoplasm MetastasisCarcinoma, Renal Cell

Interventions

NivolumabEverolimus

Condition Hierarchy (Ancestors)

Neoplastic ProcessesNeoplasmsPathologic ProcessesPathological Conditions, Signs and SymptomsAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeKidney NeoplasmsUrologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesKidney DiseasesUrologic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsSirolimusMacrolidesLactonesOrganic Chemicals

Results Point of Contact

Title
Bristol-Myers Squibb Study Director
Organization
Bristol-Myers Squibb

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

August 16, 2012

First Posted

August 20, 2012

Study Start

October 9, 2012

Primary Completion

May 6, 2015

Study Completion

July 19, 2021

Last Updated

August 9, 2022

Results First Posted

April 29, 2016

Record last verified: 2022-07

Locations