NCT01408576

Brief Summary

The primary objective of the study is assess the safety and tolerability of long-term epratuzumab treatment in subjects with Systemic Lupus Erythematosus (SLE)

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,250

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jul 2011

Longer than P75 for phase_3

Geographic Reach
24 countries

227 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

August 1, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 3, 2011

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2016

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

October 3, 2018

Completed
Last Updated

October 3, 2018

Status Verified

March 1, 2016

Enrollment Period

4.6 years

First QC Date

August 1, 2011

Results QC Date

July 20, 2018

Last Update Submit

September 3, 2018

Conditions

Keywords

LupusMonoclonal antibodyB-Cell immunotherapyEpratuzumab

Outcome Measures

Primary Outcomes (4)

  • Number of Subjects Prematurely Discontinuing Due to a Treatment-emergent Adverse Event (TEAE) During the Treatment Period (Maximum 96 Weeks)

    A TEAE is any untoward medical occurrence in a patient or clinical investigation subject administered a pharmaceutical product, which does not necessarily have a causal relationship with this treatment.

    During the treatment period (through Week 96)

  • Percentage of Subjects Prematurely Discontinuing Due to a Treatment-emergent Adverse Event (TEAE) During the Treatment Period (Maximum 96 Weeks)

    A TEAE is any untoward medical occurrence in a patient or clinical investigation subject administered a pharmaceutical product, which does not necessarily have a causal relationship with this treatment.

    During the treatment period (through Week 96)

  • Number of Subjects Reporting at Least 1 Serious Adverse Event (SAE) During the Treatment Period (Maximum 96 Weeks)

    A SAE is a treatment-emergent adverse event (TEAE) that the investigator classifies as serious. This includes: * Death * Life-threatening * Significant or persistent disability/incapacity * Congenital anomaly/birth defect (including that occurring in a fetus) * Important medical event that, based upon appropriate medical judgment, may jeopardize the patient or subject and may require medical or surgical intervention to prevent 1 of the other outcomes listed in the definition of serious * Initial inpatient hospitalization or prolongation of hospitalization

    During the treatment period (through Week 96)

  • Percentage of Subjects Reporting at Least 1 Serious Adverse Event (SAE) During the Treatment Period (Maximum 96 Weeks)

    A SAE is a treatment-emergent adverse event (TEAE) that the investigator classifies as serious. This includes: * Death * Life-threatening * Significant or persistent disability/incapacity * Congenital anomaly/birth defect (including that occurring in a fetus) * Important medical event that, based upon appropriate medical judgment, may jeopardize the patient or subject and may require medical or surgical intervention to prevent 1 of the other outcomes listed in the definition of serious * Initial inpatient hospitalization or prolongation of hospitalization

    During the treatment period (through Week 96)

Secondary Outcomes (4)

  • Number of Subjects Meeting Treatment Response Criteria According to a Combined Response Index

    At Week 48

  • Percentage of Subjects Meeting Treatment Response Criteria According to a Combined Response Index

    Week 48

  • Number of Subjects Meeting Treatment Response Criteria According to a Combined Response Index

    Week 96

  • The Percent of Subjects Meeting Treatment Response Criteria According to a Combined Response Index

    Week 96

Study Arms (2)

Epratuzumab 600 mg per week

EXPERIMENTAL

600 mg infusions delivered weekly for a total of 4 consecutive weeks (cumulative dose 2400 mg) over sixteen 12-week treatment cycles

Drug: Epratuzumab

Epratuzumab 1200 mg every other week

EXPERIMENTAL

1200 mg infusions delivered every other week for a total of 4 weeks (cumulative dose 2400 mg) over sixteen 12 week treatment cycles

Drug: Epratuzumab

Interventions

600 mg infusions delivered weekly for a total of 4 consecutive weeks (cumulative dose 2400 mg) over eight 12-week treatment cycles

Epratuzumab 600 mg per week

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject has completed the double-blind study SL0009 (NCT01262365) or SL0010 (NCT01261793) or terminated prematurely at Week 16 or later in SL0009 or SL0010 due to lack of efficacy and would, in the opinion of the investigator, continue to benefit from continued epratuzumab treatment
  • Subject has completed open-label study SL0006 (NCT00383513) or SL0008 (NCT00660881), and would, in the opinion of the investigator, continue to benefit from continued epratuzumab treatment
  • Women of childbearing potential must agree to use an acceptable method of birth control

You may not qualify if:

  • Subjects with active, severe, neuropsychiatric SLE, defined as any neuropsychiatric element scoring British Isles Lupus Assessment Group Index (BILAG) level A disease
  • Subjects with active, severe SLE disease activity which involves the renal system
  • Subjects with concurrent relevant medical conditions like defined chronic infections or high risk of new significant infections
  • Substance abuse or dependence
  • History of malignant cancer

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (228)

539

Birmingham, Alabama, United States

Location

557

Little Rock, Arkansas, United States

Location

515

Hemet, California, United States

Location

544

Huntington Beach, California, United States

Location

550

La Jolla, California, United States

Location

031

Los Angeles, California, United States

Location

051

Los Angeles, California, United States

Location

089

Los Angeles, California, United States

Location

531

San Leandro, California, United States

Location

594

Thousand Oaks, California, United States

Location

558

Torrance, California, United States

Location

048

Aurora, Colorado, United States

Location

037

Colorado Springs, Colorado, United States

Location

532

Denver, Colorado, United States

Location

511

Bridgeport, Connecticut, United States

Location

039

Farmington, Connecticut, United States

Location

042

Aventura, Florida, United States

Location

514

Brandon, Florida, United States

Location

090

Clearwater, Florida, United States

Location

092

DeBary, Florida, United States

Location

533

Fort Lauderdale, Florida, United States

Location

064

Jupiter, Florida, United States

Location

070

Ormond Beach, Florida, United States

Location

084

Palm Harbor, Florida, United States

Location

518

Plantation, Florida, United States

Location

585

Port Orange, Florida, United States

Location

050

Tampa, Florida, United States

Location

538

Tampa, Florida, United States

Location

087

Vero Beach, Florida, United States

Location

537

Atlanta, Georgia, United States

Location

044

Duluth, Georgia, United States

Location

590

Idaho Falls, Idaho, United States

Location

052

Chicago, Illinois, United States

Location

096

Indianapolis, Indiana, United States

Location

060

Shreveport, Louisiana, United States

Location

513

Lansing, Michigan, United States

Location

599

Lansing, Michigan, United States

Location

047

Saint Clair Shores, Michigan, United States

Location

575

Florissant, Missouri, United States

Location

549

St Louis, Missouri, United States

Location

596

Nashua, New Hampshire, United States

Location

568

Freehold, New Jersey, United States

Location

593

Trenton, New Jersey, United States

Location

067

Las Cruces, New Mexico, United States

Location

551

Brooklyn, New York, United States

Location

553

Great Neck, New York, United States

Location

545

Manhasset, New York, United States

Location

053

New York, New York, United States

Location

577

Roslyn, New York, United States

Location

077

Charlotte, North Carolina, United States

Location

559

Charlotte, North Carolina, United States

Location

058

Durham, North Carolina, United States

Location

075

Wilmington, North Carolina, United States

Location

061

Columbus, Ohio, United States

Location

071

Middleburg Heights, Ohio, United States

Location

041

Oklahoma City, Oklahoma, United States

Location

076

Oklahoma City, Oklahoma, United States

Location

097

Oklahoma City, Oklahoma, United States

Location

547

Tulsa, Oklahoma, United States

Location

032

Duncansville, Pennsylvania, United States

Location

093

Philadelphia, Pennsylvania, United States

Location

073

Pittsburgh, Pennsylvania, United States

Location

094

Pittsburgh, Pennsylvania, United States

Location

535

Charleston, South Carolina, United States

Location

598

Myrtle Beach, South Carolina, United States

Location

571

Jackson, Tennessee, United States

Location

057

Memphis, Tennessee, United States

Location

574

Amarillo, Texas, United States

Location

078

Austin, Texas, United States

Location

098

Austin, Texas, United States

Location

570

Austin, Texas, United States

Location

079

Dallas, Texas, United States

Location

541

Houston, Texas, United States

Location

563

Houston, Texas, United States

Location

036

Mesquite, Texas, United States

Location

066

San Antonio, Texas, United States

Location

562

San Antonio, Texas, United States

Location

534

Seattle, Washington, United States

Location

429

Camperdown, Australia

Location

427

Clayton, Australia

Location

430

Liverpool, Australia

Location

425

Malvern, Australia

Location

426

Maroochydore, Australia

Location

106

Brussels, Belgium

Location

107

Brussels, Belgium

Location

105

Leuven, Belgium

Location

104

Liège, Belgium

Location

954

Belo Horizonte, Brazil

Location

956

Campinas, Brazil

Location

955

Goiânia, Brazil

Location

950

Juiz de Fora, Brazil

Location

453

Porto Alegre, Brazil

Location

451

Recife, Brazil

Location

450

Rio de Janeiro, Brazil

Location

952

Rio de Janeiro, Brazil

Location

452

Salvador, Brazil

Location

454

São Paulo, Brazil

Location

200

Sofia, Bulgaria

Location

202

Sofia, Bulgaria

Location

203

Sofia, Bulgaria

Location

204

Sofia, Bulgaria

Location

205

Sofia, Bulgaria

Location

500

London, Ontario, Canada

Location

502

Hamilton, Canada

Location

507

Mississauga, Canada

Location

508

Rimouski, Canada

Location

506

St. John's, Canada

Location

504

Toronto, Canada

Location

218

Olomouc, Czechia

Location

216

Prague, Czechia

Location

215

Zlín, Czechia

Location

226

Tallinn, Estonia

Location

113

Lille, France

Location

618

Limoges, France

Location

617

Montpellier, France

Location

614

Paris, France

Location

116

Pessac, France

Location

616

Toulouse, France

Location

127

Berlin, Germany

Location

628

Berlin, Germany

Location

633

Berlin, Germany

Location

625

Cologne, Germany

Location

128

Frankfurt, Germany

Location

126

Freiburg im Breisgau, Germany

Location

637

Hamburg, Germany

Location

632

Herne, Germany

Location

626

Leipzig, Germany

Location

634

Mainz, Germany

Location

627

Münster, Germany

Location

129

Plochingen, Germany

Location

636

Roßlau, Germany

Location

631

Zerbst, Germany

Location

349

Shatin, Hong Kong

Location

712

Budapest, Hungary

Location

716

Budapest, Hungary

Location

718

Budapest, Hungary

Location

717

Debrecen, Hungary

Location

711

Szeged, Hungary

Location

715

Szeged, Hungary

Location

713

Zalaegerszeg, Hungary

Location

378

Ashkelon, Israel

Location

376

Beersheba, Israel

Location

375

Haifa, Israel

Location

377

Haifa, Israel

Location

381

Jerusalem, Israel

Location

382

Kfar Saba, Israel

Location

380

Rehovot, Israel

Location

379

Tel Aviv, Israel

Location

383

Tel Litwinsky, Israel

Location

149

Ferrara, Italy

Location

648

Milan, Italy

Location

148

Padua, Italy

Location

647

Pisa, Italy

Location

646

Roma, Italy

Location

147

Torino, Italy

Location

242

Kaunas, Lithuania

Location

244

Klaipėda, Lithuania

Location

243

Vilnius, Lithuania

Location

478

Guadalajara, Mexico

Location

976

Mexico City, Mexico

Location

982

Mexico City, Mexico

Location

480

Mérida, Mexico

Location

981

Torreón, Mexico

Location

743

Bydgoszcz, Poland

Location

744

Częstochowa, Poland

Location

752

Elblag, Poland

Location

754

Elblag, Poland

Location

746

Katowice, Poland

Location

748

Lublin, Poland

Location

750

Lublin, Poland

Location

742

Poznan, Poland

Location

747

Szczecin, Poland

Location

751

Ustroń, Poland

Location

749

Warsaw, Poland

Location

263

Brasov, Romania

Location

260

Bucharest, Romania

Location

262

Bucharest, Romania

Location

264

Bucharest, Romania

Location

757

Bucharest, Romania

Location

758

Bucharest, Romania

Location

261

Cluj-Napoca, Romania

Location

759

Constanța, Romania

Location

756

Galati, Romania

Location

761

Iași, Romania

Location

779

Moscow, Russia

Location

285

Petrozavodsk, Russia

Location

284

Saint Petersburg, Russia

Location

281

Yekaterinburg, Russia

Location

901

Cape Town, South Africa

Location

902

Durban, South Africa

Location

903

Stellenbosch, South Africa

Location

306

Busan, South Korea

Location

303

Daegu, South Korea

Location

308

Daejeon, South Korea

Location

301

Incheon, South Korea

Location

307

Seoul, South Korea

Location

302

Suwon, South Korea

Location

161

Barcelona, Spain

Location

661

Barcelona, Spain

Location

164

Bilbao, Spain

Location

660

Getafe, Spain

Location

662

Las Palmas de Gran Canaria, Spain

Location

162

Madrid, Spain

Location

163

Madrid, Spain

Location

664

Madrid, Spain

Location

166

Málaga, Spain

Location

165

San Cristóbal de La Laguna, Spain

Location

177

Santander, Spain

Location

663

Santiago de Compostela, Spain

Location

160

Seville, Spain

Location

659

Vigo, Spain

Location

325

Changhua, Taiwan

Location

326

Chiayi City, Taiwan

Location

328

Kaohsiung City, Taiwan

Location

330

Taipei, Taiwan

Location

791

Donetsk, Ukraine

Location

799

Ivano-Frankivsk, Ukraine

Location

790

Kiev, Ukraine

Location

794

Kiev, Ukraine

Location

797

Kiev, Ukraine

Location

792

Luhansk, Ukraine

Location

793

Odesa, Ukraine

Location

796

Vinnytsia, Ukraine

Location

677

Birmingham, United Kingdom

Location

178

Brighton, United Kingdom

Location

182

Doncaster, United Kingdom

Location

179

Leeds, United Kingdom

Location

181

Romford, United Kingdom

Location

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

epratuzumab

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
UCB
Organization
Cares

Study Officials

  • UCB Clinical Trial Call Center

    UCB Pharma

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 1, 2011

First Posted

August 3, 2011

Study Start

July 1, 2011

Primary Completion

February 1, 2016

Study Completion

February 1, 2016

Last Updated

October 3, 2018

Results First Posted

October 3, 2018

Record last verified: 2016-03

Locations