NCT01262365

Brief Summary

The primary objective of the study is to confirm the clinical efficacy of epratuzumab in the treatment of subjects with Systemic Lupus Erythematosus (SLE)

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
793

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Dec 2010

Typical duration for phase_3

Geographic Reach
20 countries

133 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2010

Completed
13 days until next milestone

First Submitted

Initial submission to the registry

December 14, 2010

Completed
3 days until next milestone

First Posted

Study publicly available on registry

December 17, 2010

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2015

Completed
3.2 years until next milestone

Results Posted

Study results publicly available

June 29, 2018

Completed
Last Updated

September 28, 2018

Status Verified

June 1, 2018

Enrollment Period

4.4 years

First QC Date

December 14, 2010

Results QC Date

May 30, 2018

Last Update Submit

August 31, 2018

Conditions

Keywords

LupusMonoclonal antibodyB-Cell immunotherapyEpratuzumab

Outcome Measures

Primary Outcomes (1)

  • The Percent of Subjects Meeting Treatment Response Criteria at Week 48 According to a Combined Response Index

    Percentages are based on the number of subjects in the relevant treatment group within the Full Analysis Set. The combined response index incorporated criteria for achievement of responder status from the: British Isles Lupus Assessment Group Index (BILAG-2004)- improvement from study entry or no worsening in other organ systems, Systemic Lupus Erythematosus Disease Activity Index (SLEDAI; Version 2000, also known as SLEDAI-2K) - no worsening compared to study entry, physician's global assessment of disease activity(PGA)- no worsening compared to study entry, and concomitant medications- no changes.

    At Week 48

Secondary Outcomes (5)

  • The Percent of Subjects Meeting Treatment Response Criteria at Week 24 According to a Combined Response Index

    At Week 24

  • The Percent of Subjects Meeting Treatment Response Criteria at Week 12 According to a Combined Response Index

    At Week 12

  • The Percent of Subjects Meeting Treatment Response Criteria at Week 36 According to a Combined Response Index

    At Week 36

  • Change From Baseline in Daily Corticosteroid Dose at Week 24

    At Week 24

  • Change From Baseline in Daily Corticosteroid Dose at Week 48

    At Week 48

Study Arms (3)

Placebo (Weekly infusion)

PLACEBO COMPARATOR

Placebo infusions delivered weekly for a total of 4 weeks over four 12-week treatment cycles

Drug: Placebo

Epratuzumab 600 mg per week

EXPERIMENTAL

600 mg infusions delivered weekly for a total of 4 weeks (cumulative dose 2400 mg) over four 12-week treatment cycles

Drug: Epratuzumab

Epratuzumab 1200 mg every other week

EXPERIMENTAL

1200 mg infusions delivered every other week for a total of 4 weeks (cumulative dose 2400 mg) over four 12-week treatment cycles and placebo infusions delivered every other week for a total of 4 weeks over four 12-week treatment cycles

Drug: EpratuzumabDrug: Placebo

Interventions

600 mg infusions delivered weekly for a total of 4 weeks (cumulative dose 2400 mg) over four 12- week treatment cycles

Epratuzumab 600 mg per week

Placebo infusions delivered weekly for 4 weeks over four 12-week treatment cycles

Epratuzumab 1200 mg every other weekPlacebo (Weekly infusion)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Positive antinuclear antibodies (ANA) at Screening (Visit 1)
  • Current clinical diagnosis of Systemic Lupus Erythematosus (SLE) by American College of Rheumatology (ACR) criteria such that at least 4 of the 11 criteria are met
  • Active moderate to severe SLE activity as demonstrated by the British Isles Lupus Assessment Group Index (BILAG)
  • Active moderate to severe SLE disease as demonstrated by SLEDAI total score.
  • On stable SLE treatment regimen, including mandatory corticosteroids and immunosuppressants or antimalarials

You may not qualify if:

  • Subjects who are breastfeeding, pregnant, or plan to become pregnant
  • Subjects with active, severe SLE disease activity which involves the renal system
  • Subjects with active, severe, neuropsychiatric SLE, defined as any neuropsychiatric element scoring BILAG level A disease.
  • Subjects with the evidence of an immunosuppressive state
  • Subjects who, in the opinion of the investigator, are at a particularly high risk of significant infection
  • History of malignant cancer, except the following treated cancers: cervical carcinoma in situ, basal cell carcinoma, or dermatological squamous cell carcinoma.
  • Subjects receiving any live vaccination within the 8 weeks prior to screening (Visit 1).
  • Subjects with history of infections, including but not limited to concurrent acute or chronic viral hepatitis B or C
  • Subjects with substance abuse or dependence or other relevant concurrent medical condition
  • Subjects with history of thromboembolic events within 1 year of screening Visit.
  • Subjects with significant hematologic abnormalities
  • Subject has received treatment with other anti- B cell antibodies within 12 months prior to screening (visit 1)
  • Subject use of oral anticoagulant (not including) nonsteroidal anti-inflammatory drugs (NSAIDs) within 12 weeks prior to screening (Visit 1)
  • Subject has previously participated in this study or has previously received epratuzumab treatment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (141)

069

Birmingham, Alabama, United States

Location

063

Little Rock, Arkansas, United States

Location

085

Escondido, California, United States

Location

031

Los Angeles, California, United States

Location

051

Los Angeles, California, United States

Location

089

Los Angeles, California, United States

Location

074

San Diego, California, United States

Location

80

San Gabriel, California, United States

Location

048

Aurora, Colorado, United States

Location

037

Colorado Springs, Colorado, United States

Location

039

Farmington, Connecticut, United States

Location

042

Aventura, Florida, United States

Location

090

Clearwater, Florida, United States

Location

092

DeBary, Florida, United States

Location

064

Jupiter, Florida, United States

Location

082

Miami, Florida, United States

Location

070

Ormond Beach, Florida, United States

Location

084

Palm Harbor, Florida, United States

Location

062

Tamarac, Florida, United States

Location

050

Tampa, Florida, United States

Location

087

Vero Beach, Florida, United States

Location

044

Lawrenceville, Georgia, United States

Location

052

Chicago, Illinois, United States

Location

096

Indianapolis, Indiana, United States

Location

060

Shreveport, Louisiana, United States

Location

040

Baltimore, Maryland, United States

Location

047

Saint Clair Shores, Michigan, United States

Location

067

Las Cruces, New Mexico, United States

Location

053

New York, New York, United States

Location

077

Charlotte, North Carolina, United States

Location

058

Durham, North Carolina, United States

Location

061

Columbus, Ohio, United States

Location

071

Middleburg Heights, Ohio, United States

Location

041

Oklahoma City, Oklahoma, United States

Location

076

Oklahoma City, Oklahoma, United States

Location

097

Oklahoma City, Oklahoma, United States

Location

032

Duncansville, Pennsylvania, United States

Location

093

Philadelphia, Pennsylvania, United States

Location

073

Pittsburgh, Pennsylvania, United States

Location

094

Pittsburgh, Pennsylvania, United States

Location

099

Charleston, South Carolina, United States

Location

001

Columbia, South Carolina, United States

Location

034

Simpsonville, South Carolina, United States

Location

057

Memphis, Tennessee, United States

Location

078

Austin, Texas, United States

Location

098

Austin, Texas, United States

Location

079

Dallas, Texas, United States

Location

055

Houston, Texas, United States

Location

036

Mesquite, Texas, United States

Location

066

San Antonio, Texas, United States

Location

426

Maroochydore, Queensland, Australia

Location

425

Malvern, Victoria, Australia

Location

429

Camperdown, Australia

Location

427

Clayton, Australia

Location

430

Liverpool, Australia

Location

106

Brussels, Belgium

Location

107

Brussels, Belgium

Location

105

Leuven, Belgium

Location

104

Liège, Belgium

Location

455

Campinas, Brazil

Location

453

Porto Alegre, Brazil

Location

451

Recife, Brazil

Location

450

Rio de Janeiro, Brazil

Location

452

Salvador, Brazil

Location

454

São Paulo, Brazil

Location

201

Plovdiv, Bulgaria

Location

200

Sofia, Bulgaria

Location

202

Sofia, Bulgaria

Location

203

Sofia, Bulgaria

Location

204

Sofia, Bulgaria

Location

205

Sofia, Bulgaria

Location

218

Olomouc, Czechia

Location

216

Prague, Czechia

Location

215

Zlín, Czechia

Location

226

Tallinn, Estonia

Location

113

Lille, France

Location

114

Nantes, France

Location

112

Paris, France

Location

116

Pessac, France

Location

127

Berlin, Germany

Location

128

Frankfurt, Germany

Location

126

Freiburg im Breisgau, Germany

Location

130

Hanover, Germany

Location

129

Plochingen, Germany

Location

351

Bangalore, India

Location

352

Hyderabad, India

Location

350

Lucknow, India

Location

378

Ashkelon, Israel

Location

376

Beersheba, Israel

Location

375

Haifa, Israel

Location

377

Haifa, Israel

Location

381

Jerusalem, Israel

Location

382

Kfar Saba, Israel

Location

380

Rehovot, Israel

Location

379

Tel Aviv, Israel

Location

383

Tel Litwinsky, Israel

Location

149

Ferrara, Italy

Location

148

Padua, Italy

Location

147

Torino, Italy

Location

155

Kaunas, Lithuania

Location

156

Klaipėda, Lithuania

Location

475

Guadalajara, Mexico

Location

476

Guadalajara, Mexico

Location

478

Guadalajara, Mexico

Location

480

Mérida, Mexico

Location

091

Cidra, Puerto Rico

Location

086

San Juan, Puerto Rico

Location

263

Brasov, Romania

Location

260

Bucharest, Romania

Location

262

Bucharest, Romania

Location

264

Bucharest, Romania

Location

261

Cluj-Napoca, Romania

Location

285

Petrozavodsk, Russia

Location

284

Saint Petersburg, Russia

Location

281

Yekaterinburg, Russia

Location

306

Busan, South Korea

Location

303

Daegu, South Korea

Location

309

Daegu, South Korea

Location

308

Daejeon, South Korea

Location

304

Incheon, South Korea

Location

310

Jeonju, South Korea

Location

301

Junggu, South Korea

Location

307

Seoul, South Korea

Location

302

Suwon, South Korea

Location

165

San Cristóbal de La Laguna, Santa Cruz De Tenerife, Spain

Location

164

Bilbao, Vizcaya, Spain

Location

161

Barcelona, Spain

Location

162

Madrid, Spain

Location

163

Madrid, Spain

Location

166

Málaga, Spain

Location

177

Santander, Spain

Location

160

Seville, Spain

Location

325

Changhua, Taiwan

Location

326

Chiayi City, Taiwan

Location

328

Kaohsiung City, Taiwan

Location

329

Taichung, Taiwan

Location

330

Taipei, Taiwan

Location

178

Brighton, United Kingdom

Location

182

Doncaster, United Kingdom

Location

179

Leeds, United Kingdom

Location

181

Romford, United Kingdom

Location

Related Publications (2)

  • Gottenberg JE, Dorner T, Bootsma H, Devauchelle-Pensec V, Bowman SJ, Mariette X, Bartz H, Oortgiesen M, Shock A, Koetse W, Galateanu C, Bongardt S, Wegener WA, Goldenberg DM, Meno-Tetang G, Kosutic G, Gordon C. Efficacy of Epratuzumab, an Anti-CD22 Monoclonal IgG Antibody, in Systemic Lupus Erythematosus Patients With Associated Sjogren's Syndrome: Post Hoc Analyses From the EMBODY Trials. Arthritis Rheumatol. 2018 May;70(5):763-773. doi: 10.1002/art.40425. Epub 2018 Apr 12.

  • Clowse ME, Wallace DJ, Furie RA, Petri MA, Pike MC, Leszczynski P, Neuwelt CM, Hobbs K, Keiserman M, Duca L, Kalunian KC, Galateanu C, Bongardt S, Stach C, Beaudot C, Kilgallen B, Gordon C; EMBODY Investigator Group. Efficacy and Safety of Epratuzumab in Moderately to Severely Active Systemic Lupus Erythematosus: Results From Two Phase III Randomized, Double-Blind, Placebo-Controlled Trials. Arthritis Rheumatol. 2017 Feb;69(2):362-375. doi: 10.1002/art.39856.

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

epratuzumab

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
UCB
Organization
Cares

Study Officials

  • UCb Clinical Trial Call Center

    +1 877 822 9493 (UCB)

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 14, 2010

First Posted

December 17, 2010

Study Start

December 1, 2010

Primary Completion

May 1, 2015

Study Completion

May 1, 2015

Last Updated

September 28, 2018

Results First Posted

June 29, 2018

Record last verified: 2018-06

Locations