NCT00624351

Brief Summary

The primary objective of the study is to assess the dose response and the dose frequency of epratuzumab in patients with SLE.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
227

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2008

Geographic Reach
11 countries

53 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2008

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

February 15, 2008

Completed
12 days until next milestone

First Posted

Study publicly available on registry

February 27, 2008

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2009

Completed
Last Updated

September 12, 2011

Status Verified

July 1, 2011

Enrollment Period

1.6 years

First QC Date

February 15, 2008

Last Update Submit

September 2, 2011

Conditions

Keywords

LupusMonoclonal antibodyB-Cell immunotherapy

Outcome Measures

Primary Outcomes (1)

  • Response at Week 12 according to a combined response index

    The combined response index incorporates the Bristish Isles Lupus Assessment Group (BILAG) assessment, the Systemic Lupus Eyrthematosus Disease Activity Index (SLEDAI), a physician's global assessment of disease activity, and treatment failure status.

    Week 12

Secondary Outcomes (28)

  • Response at Week 4 according to a combined response index

    Week 4

  • Response at Week 8 according to a combined response index

    Week 8

  • Response at Week 4 according to a combined response index involving Short Form-36 (SF-36) response

    Week 4

  • Response at Week 8 according to a combined response index involving Short Form-36 (SF-36) response

    Week 8

  • Response at Week 12 according to a combined response index involving Short Form-36 (SF-36) response

    Week 12

  • +23 more secondary outcomes

Study Arms (6)

Placebo

PLACEBO COMPARATOR

Phosphate-buffered Saline (PBS) infusions at study weeks 0, 1, 2, and 3.

Other: Placebo

EMAB 600mg

EXPERIMENTAL

600 mg Epratuzumab infusions at study weeks 0, 1, 2, and 3.

Biological: Epratuzumab

EMAB 100mg

EXPERIMENTAL

100 mg Epratuzumab infusions at study weeks 0, and 2, and placebo at study weeks 1 and 3.

Biological: EpratuzumabOther: Placebo

EMAB 400mg

EXPERIMENTAL

400 mg Epratuzumab infusions at study weeks 0, and 2, and placebo at study weeks 1 and 3.

Biological: EpratuzumabOther: Placebo

EMAB 1200mg

EXPERIMENTAL

1200 mg Epratuzumab infusions at study weeks 0, and 2, and placebo at study weeks 1 and 3.

Biological: EpratuzumabOther: Placebo

EMAB 1800mg

EXPERIMENTAL

1800 mg Epratuzumab infusions at study weeks 0, and 2, and placebo at study weeks 1 and 3.

Biological: EpratuzumabOther: Placebo

Interventions

EpratuzumabBIOLOGICAL

Epratuzumab at a concentration of 10 mg/mL prepared in 17.5 ml vials for slow intravenous infusion using only Phosphate buffered Saline (PBS) as a vehicle/buffer for the infusion procedure.

EMAB 100mgEMAB 1200mgEMAB 1800mgEMAB 400mgEMAB 600mg
PlaceboOTHER

Phosphate-buffered Saline (PBS) infusion.

EMAB 100mgEMAB 1200mgEMAB 1800mgEMAB 400mgPlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Positive ANA result at visit 1
  • Current diagnosis of systemic lupus erythematosus (SLE) by American College of Rheumatology revised criteria such that at least 4 of the 11 criteria are met
  • Active moderate or severe SLE disease activity as demonstrated by British Isles Lupus Assessment Group (BILAG) A level disease activity in at least one body/organ system or BILAG B level disease activity in at least two body/organ systems if no BILAG A level disease is present
  • If on antimalarials, dose regimen must be stable for 4 weeks prior to study entry.

You may not qualify if:

  • Patients receiving any live vaccination within 2 weeks prior to visit 1 or during the course of the study
  • Active severe SLE disease activity which involves the central nervous system (CNS) (defined by BILAG neurologic A level activity) including transverse myelitis, psychosis and seizures
  • Active severe SLE disease activity which involves the Renal system (defined by BILAG renal level A activity or Grade III or higher World Health Organization (WHO) nephritis) or serum creatinine \>2.5mg/dL or clinically significant serum creatinine increase within the prior 4 weeks or proteinuria \>3.5gm/day
  • Patients with a history of anti-phospholipid antibody syndrome AND use of oral anticoagulants or anti-platelet treatment
  • Patients with a history of chronic infection, recent significant infection, or any current sign of symptom that may indicate an infection

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (53)

Unknown Facility

Birmingham, Alabama, United States

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Tucson, Arizona, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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San Leandro, California, United States

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Denver, Colorado, United States

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Farmington, Connecticut, United States

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Aventura, Florida, United States

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Tampa, Florida, United States

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Baltimore, Maryland, United States

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Brooklyn, New York, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Wilmington, North Carolina, United States

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Oklahoma City, Oklahoma, United States

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Dallas, Texas, United States

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Arlington, Virginia, United States

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Milwaukee, Wisconsin, United States

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Brussels, Belgium

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Leuven, Belgium

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Curitiba, Brazil

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Goiânia, Brazil

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Porto Alegre, Brazil

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Rio de Janeiro, Brazil

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São Paulo, Brazil

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Sorocaba, Brazil

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Chai Wan, Hong Kong

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Shatin, Hong Kong

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Debrecen, Hungary

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Zalaegerszeg, Hungary

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Bangalore, India

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Hyderabad, India

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Ludhiana, India

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Madurai, India

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Manipal, India

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Nagpur, India

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Kaunas, Lithuania

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Klaipėda, Lithuania

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Vilnius, Lithuania

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Elblag, Poland

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Gmina Końskie, Poland

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Lublin, Poland

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Poznan, Poland

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Torun, Poland

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Barcelona, Spain

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Santander, Spain

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Valencia, Spain

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Donetsk, Ukraine

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Ivano-Frankivsk, Ukraine

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Kiev, Ukraine

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Lviv, Ukraine

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Unknown Facility

Birmingham, United Kingdom

Location

Related Publications (2)

  • Hannon CW, McCourt C, Lima HC, Chen S, Bennett C. Interventions for cutaneous disease in systemic lupus erythematosus. Cochrane Database Syst Rev. 2021 Mar 9;3(3):CD007478. doi: 10.1002/14651858.CD007478.pub2.

  • Wallace DJ, Kalunian K, Petri MA, Strand V, Houssiau FA, Pike M, Kilgallen B, Bongardt S, Barry A, Kelley L, Gordon C. Efficacy and safety of epratuzumab in patients with moderate/severe active systemic lupus erythematosus: results from EMBLEM, a phase IIb, randomised, double-blind, placebo-controlled, multicentre study. Ann Rheum Dis. 2014 Jan;73(1):183-90. doi: 10.1136/annrheumdis-2012-202760. Epub 2013 Jan 12.

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

epratuzumab

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • UCB Clinical Trial Call Center

    +1 877 822 9493 (UCB)

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 15, 2008

First Posted

February 27, 2008

Study Start

January 1, 2008

Primary Completion

August 1, 2009

Study Completion

August 1, 2009

Last Updated

September 12, 2011

Record last verified: 2011-07

Locations