NCT01232556

Brief Summary

The purpose of this study is to evaluate the efficacy of inotuzumab ozogamicin plus rituximab in relapsed/refractory aggressive Non-Hodgkin lymphoma patients who are not candidates for intensive high-dose chemotherapy. Specifically, the goal is to demonstrate the superiority of this combination compared with an active comparator arm (investigator's choice of rituximab+bendamustine or rituximab+gemcitabine) using the primary endpoint of overall survival.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
338

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Apr 2011

Typical duration for phase_3

Geographic Reach
25 countries

177 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 27, 2010

Completed
6 days until next milestone

First Posted

Study publicly available on registry

November 2, 2010

Completed
5 months until next milestone

Study Start

First participant enrolled

April 4, 2011

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 28, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 28, 2014

Completed
4.4 years until next milestone

Results Posted

Study results publicly available

August 21, 2018

Completed
Last Updated

January 8, 2019

Status Verified

December 1, 2018

Enrollment Period

3 years

First QC Date

October 27, 2010

Results QC Date

July 17, 2017

Last Update Submit

December 19, 2018

Conditions

Keywords

inotuzumab ozogamicinaggressive Non-Hodgkin lymphomadiffuse large b-cell lymphomarelapsed/refractory lymphoma

Outcome Measures

Primary Outcomes (2)

  • Overall Survival

    Overall Survival (OS) was defined as the time from randomization to death due to any cause, censoring at the date of last contact or the end of the study. The Kaplan-Meier method was used to determine OS. The hazard ratio and corresponding 95% 2-sided confidence interval were calculated using stratified Cox proportional hazard regression.

    From randomization up to 5 years after last dose or up to final study visit, whichever occurs first.

  • Percentage of Participants With a Treatment Emergent Adverse Event (TEAE) (Safety Population)

    Includes all TEAEs: Any event that occurred after the first dose of study drug and was not present prior to study drug administration or worsened in severity after study drug administration..

    Up to 20 weeks after the first dose of study drug

Secondary Outcomes (6)

  • Progression-Free Survival (PFS)

    From randomization up to 2 years or final study visit, whichever occurs first, including but not limited to planned assessments scheduled approximately every 12 weeks.

  • Percentage of Participants With A Best Overall Response of CR or Partial Response (PR) Per NCI International Response Criteria for NHL

    Up to 2 years from first study drug dose or up to final study visit, whichever occurs first, including but not limited to planned assessments scheduled approximately every 12 weeks.

  • Percentage of Participants With A Best Overall Response of CR, Unconfirmed CR (unCR), PR, or Unconfirmed PR (unPR) Per NCI International Response Criteria for NHL

    Up to 2 years from first study drug dose or up to final study visit, whichever occurs first, including but not limited to planned assessments scheduled approximately every 12 weeks.

  • Duration of Response

    Up to 2 years from first study drug dose or up to final study visit, whichever occurs first, including but not limited to planned assessments scheduled approximately every 12 weeks.

  • Health Status as Assessed by the European Quality of Life 5 Dimension (EQ-5D) Questionnaire

    Assessed at Day 1 of each cycle and 6-9 weeks after the last dose, Cycle 3 (Week 12) reported

  • +1 more secondary outcomes

Study Arms (2)

1

EXPERIMENTAL

Inotuzumab ozogamicin+rituximab

Drug: Inotuzumab ozogamicinDrug: Rituximab

2

ACTIVE COMPARATOR

Investigator's choice of (1) rituximab+gemcitabine, or (2) rituximab+bendamustine

Drug: rituximab + gemcitabineDrug: rituximab +bendamustine

Interventions

1.8 mg/m2 on day 2 every 28 days by IV infusion, 3 to 6 cycles

Also known as: CMC-544
1

375 mg/m2 on day 1 every 28 days by IV infusion, 3 to 6 cycles

1

rituximab 375 mg/m2 on days 1, 8, 15, and 22 of cycle 1, and day 1 of cycles 2 to 6, every 28 days by IV infusion, 3 to 6 cycles; gemcitabine 1000 mg/m2 on days 1, 8, and 15 every 28 days, 3 to 6 cycles

2

rituximab 375 mg/m2 on day 1 every 28 days by IV infusion, 3 to 6 cycles; bendamustine 120 mg/m2 on days 1 and 2 by IV infusion every 28 days, 3 to 6 cycles

2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (177)

Disney Family Cancer Center at Providence St Joseph Medical Center

Burbank, California, 91505, United States

Location

Providence St Joseph Medical Center

Burbank, California, 91505, United States

Location

Hematology-Oncology Medical Group of Fresno Inc

Fresno, California, 93720, United States

Location

Ronald Reagan UCLA Medical Center Drug Information Center Department of Pharmaceutical Services

Los Angeles, California, 90095-6981, United States

Location

Clinical Research Unit

Los Angeles, California, 90095, United States

Location

Peter Morton Medical Plaza

Los Angeles, California, 90095, United States

Location

Ronald Reagan UCLA Medical Center

Los Angeles, California, 90095, United States

Location

Sansum Clinic

Santa Barbara, California, 93105, United States

Location

UCLA Santa Monica Hematology Oncology

Santa Monica, California, 90404, United States

Location

Sansum Clinic

Solvang, California, 93463, United States

Location

Howard University Hospital

Washington D.C., District of Columbia, 20060, United States

Location

Mount Sinai Comprehensive Cancer Center at Aventura

Aventura, Florida, 33180, United States

Location

University Cancer Institute

Boynton Beach, Florida, 33426, United States

Location

21st Century Oncology of Jacksonville, LLC

Fernandina Beach, Florida, 32034, United States

Location

Davis Cancer Pavilion and Shands Medical Plaza

Gainesville, Florida, 32608, United States

Location

Shands Cancer Hospital at the University of Florida

Gainesville, Florida, 32608, United States

Location

UF Health Davis Cancer Pavillion and Shands Med Plaza

Gainesville, Florida, 32608, United States

Location

UF Health Shands Cancer Hospital

Gainesville, Florida, 32608, United States

Location

Shands Hospital at the University of Florida

Gainesville, Florida, 32610, United States

Location

UF Health Shands Hospital

Gainesville, Florida, 32610, United States

Location

21st Century Oncology of Jacksonville, LLC

Jacksonville, Florida, 32205, United States

Location

21st Century Oncology of Jacksonville, LLC

Jacksonville, Florida, 32207, United States

Location

Baptist Cancer Institute

Jacksonville, Florida, 32207, United States

Location

Baptist Medical Center

Jacksonville, Florida, 32207, United States

Location

21st Century Oncology of Jacksonville, LLC

Jacksonville, Florida, 32256, United States

Location

21st Century Oncology of Jacksonville, Inc.

Jacksonville, Florida, 32258, United States

Location

Medical Specialists Of The Palm Beaches

Lake Worth, Florida, 33467, United States

Location

Advanced Medical Specialties

Miami, Florida, 33133, United States

Location

Mercy Hospital

Miami, Florida, 33133, United States

Location

Mercy Research Institute

Miami, Florida, 33133, United States

Location

Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, 33140, United States

Location

Mount Sinai Medical Center

Miami Beach, Florida, 33140, United States

Location

21st Century Oncology of Jacksonville, LLC

Orange Park, Florida, 32073, United States

Location

Georgia Regents Medical Cancer Pharmacy

Augusta, Georgia, 30912, United States

Location

Georgia Regents University

Augusta, Georgia, 30912, United States

Location

Kootenai Cancer Center

Coeur d'Alene, Idaho, 83814, United States

Location

Kootenai Cancer Center

Post Falls, Idaho, 083854, United States

Location

Decatur Memorial Hospital (DMH)

Decatur, Illinois, 62526, United States

Location

Floyd Memorial Cancer Center of Indiana

New Albany, Indiana, 47150, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Kansas Cancer Center and Medical Pavilion

Westwood, Kansas, 66205, United States

Location

University of Kentucky A.B. Chandler Medical Center

Lexington, Kentucky, 40536, United States

Location

University of Kentucky Markey Cancer Center

Lexington, Kentucky, 40536, United States

Location

Tulane University Hospital and Clinic

New Orleans, Louisiana, 70112, United States

Location

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Barbara Ann Karmanos Cancer Institute at farmington Hills

Farmington Hills, Michigan, 48334, United States

Location

Park Nicollet Frauenshuh Cancer Center

Saint Louis Park, Minnesota, 55426, United States

Location

Barnes-Jewish St. Peters

City of Saint Peters, Missouri, 63376, United States

Location

Barnes-Jewish Hospital

St Louis, Missouri, 63110, United States

Location

Washington University in St Louis

St Louis, Missouri, 63110, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

Southeast Nebraska Hematology & Oncology Consultants, P.C. d/b/a Southeast Nebraska Cancer Center

Lincoln, Nebraska, 68510, United States

Location

Beth Israel Medical Center;

New York, New York, 10003, United States

Location

Beth Israel Comprehensive Cancer Center

New York, New York, 10011-5903, United States

Location

St Luke's- Roosevelt Hospital Center

New York, New York, 10019, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Stony Brook University Medical Center, The Cancer Center

Stony Brook, New York, 11794, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

University Hospital

Cincinnati, Ohio, 45219, United States

Location

West Chester Hospital Medical Building

West Chester, Ohio, 45069, United States

Location

OU Medical Center Presbyterian Professional Building

Oklahoma City, Oklahoma, 73104, United States

Location

OU Medical Center Presbyterian Tower

Oklahoma City, Oklahoma, 73104, United States

Location

Peggy and Charles Stephenson Cancer Center (chemo & infusion)

Oklahoma City, Oklahoma, 73104, United States

Location

Peggy and Charles Stephenson Cancer Center (clinic location)

Oklahoma City, Oklahoma, 73104, United States

Location

Good Samaritan Hospital Corvallis

Corvallis, Oregon, 97330, United States

Location

Good Samaritan Hospital, Corvallis

Corvallis, Oregon, 97330, United States

Location

Samaritan Ambulatory Infusion Services

Corvallis, Oregon, 97330, United States

Location

Samaritan Pacific Coast Hospital

Newport, Oregon, 97365, United States

Location

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Guthrie Clinic, Ltd.

Sayre, Pennsylvania, 18840, United States

Location

Robert Packer Hospital

Sayre, Pennsylvania, 18840, United States

Location

Thompson Oncology Group

Knoxville, Tennessee, 37916, United States

Location

Thompson Oncology Group

Knoxville, Tennessee, 37932, United States

Location

Thompson Oncology Group

Maryville, Tennessee, 37804, United States

Location

Thompson Oncology Group

Sevierville, Tennessee, 37862, United States

Location

University Hospital - St. Paul

Dallas, Texas, 75235, United States

Location

University Hospital - Zale Lipshy

Dallas, Texas, 75235, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Baylor: Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Simmons Comprehensive Cancer Center

Dallas, Texas, 75390, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Universitaire Ziekenhuizen Leuven

Leuven, Vlaams Brabant, 3000, Belgium

Location

Institut Jules Bordet

Brussels, 1000, Belgium

Location

Grand Hopital de Charleroi

Charleroi, 6000, Belgium

Location

H.-Hartziekenhuis Roeselare-Menen

Roeselare, 8800, Belgium

Location

St Augustinus Ziekenhuis

Wilrijk, 2610, Belgium

Location

Cliniques universitaires UCL de Mont-Godinne,

Yvoir, 5530, Belgium

Location

UMBAL Sveti Georgi, Klinika po hematologia

Plovdiv, 4002, Bulgaria

Location

SBAL na Hematologichnichni Zabolyavania,CTH Sofia

Sofia, 1756, Bulgaria

Location

Spetsializirana Bolnitsa za Aktivno Lechenie na Hematologichni Zabolyavania, CTH Sofia

Sofia, 1756, Bulgaria

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3 M5, Canada

Location

Centre Hospitalier Universitaire de Sherbrooke (CHUS), Hopital Fleurimont

Sherbrooke, Quebec, J1H 5N4, Canada

Location

University Hospital Zagreb

Zagreb, 10000, Croatia

Location

University Hospital Dubrava Department of Internal Medicine Division of Hematology

Zagreb, 10010, Croatia

Location

Fakultni nemocnice Kralovske Vinohrady

Prague, Czech Republic, 100 34, Czechia

Location

Fakultni nemocnice Brno

Brno, 62500, Czechia

Location

Département Pharmacie

Marseille, Bouches-du-rhône, Cedex 09 13273, France

Location

Institut Paoli Calmettes

Marseille, Cedex 09, 13273, France

Location

Hopital Andre Mignot

Le Chesnay, Yvelines, 78157, France

Location

Hospital Universitaire Andre Mignot

Le Chesnay, Yvelines, 78157, France

Location

Centre Leon Berard

Lyon, 69373, France

Location

CHU Saint Eloi

Montpellier, 34295Cedex5, France

Location

Hopital du haut Leveque

Pessac, 33600, France

Location

Centre Henri Becquerel

Rouen, 76038, France

Location

Universitaetsklinikum Aachen

Aachen, 52074, Germany

Location

Sozialstiftung Bamberg

Bamberg, 96049, Germany

Location

Charite Campus Benjamin Franklin

Berlin, 10117, Germany

Location

Charite Campus Virchow-Klinikum

Berlin, 13353, Germany

Location

Universitaetsklinikum Mainz

Mainz, 55101, Germany

Location

TU Muenchen III. Medizinische Klinik

München, 81675, Germany

Location

Universitaetsklinik Ulm

Ulm, 89081, Germany

Location

Egyesitett Szent Istvan es Szent Laszlo Korhaz /

Budapest, 1097, Hungary

Location

DEOEC, Belgyogyaszati Intezet

Debrechen, 4032, Hungary

Location

Somongy Megyei Kaposi Mor Okato Korhaz/ Belgyogyaszati osztaly

Kaposvár, 7400, Hungary

Location

Kodlikeri Memorial Hospital

Aurangabad, Maharashtra, 431 005, India

Location

Sahyadri Clinical Research and Development Center

Pune, Maharashtra, 411 004, India

Location

OEC Record Management Company Pvt. Ltd.,

Pune, Maharashtra, 411004, India

Location

Sahyadri Speciality Hospital

Pune, Maharashtra, 411004, India

Location

Bon Secours Hospital

Cork, Ireland

Location

Nagoya Daini Red Cross Hospital

Nagoya, Aichi-ken, 4668650, Japan

Location

National Cancer Center Hospital East

Kashiwa, Chiba, 277-8577, Japan

Location

Ehime University Hospital

Toon-shi, Ehime, 791-0295, Japan

Location

Gunma University Hospital

Maebashi, Gunma, 371-8511, Japan

Location

Tohoku University Hospital

Sendai, Miyagi, 980-8574, Japan

Location

Matsushita Memorial Hospital

Moriguchi, Osaka, 570-8540, Japan

Location

Shizuoka Cancer Center

Sunto-gun, Shizuoka, 411-8777, Japan

Location

National Cancer Center Hospital

Chuo-ku, Tokyo, 104-0045, Japan

Location

Cancer Institute Hospital, Japanese Foundation For Cancer Research

Koto-Ku, Tokyo, 135-8550, Japan

Location

Akita University Hospital

Akita, 010-8543, Japan

Location

National Kyushu Cancer Center

Fukuoka, 811-1395, Japan

Location

Tokai University Hospital

Kanagawa, 259-1193, Japan

Location

University Hospital, Kyoto Prefectural University of Medicine

Kyoto, 602-8566, Japan

Location

Klaipeda Seamen's Hospital, Public Institution, department of Oncology

Klaipėda, 92288, Lithuania

Location

Instituto Biomédico de Investigación A.C.

Aguascalientes, Aguascalientes. Mexico, 20127, Mexico

Location

Niepubliczny Zaklad Opieki Zdrowotnej AVI Diagnostyka Obrazowa

Warsaw, 00-728, Poland

Location

Klinika Nowotworow Ukladu Chlonnego

Warsaw, 02-781, Poland

Location

Advanced Infusion Services

Cataño, 00962, Puerto Rico

Location

Hospital Espanol Auxilio Mutuo de Puerto Rico Inc

San Juan, 00918, Puerto Rico

Location

Federal State Budgetary Institution Hematology Scientific Centre of Ministry of

Moscow, 125167, Russia

Location

Moscow State Healthcare Institution City clinical hospital S.P. Botkin

Moscow, 125284, Russia

Location

Institute of Pediatric Hematology and Transplantology R.M.Gorbacheva

Saint Petersburg, 197022, Russia

Location

National University Hospital

Singapore, 119074, Singapore

Location

Singapore General Hospital

Singapore, 169608, Singapore

Location

Narodny onkologicky ustav

Bratislava, 833 10, Slovakia

Location

Hospital Virgen Del Rocio

Seville, Andalusia, 41013, Spain

Location

Hospital Universitario De Salamanca

Salamanca, Castille and LION, 37007, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Clinic Universitari de Barcelona

Barcelona, 08036, Spain

Location

Institut Catala d'Oncologia-L'Hospitalet

L'Hospitalet de Llobregat (bcn), 08907, Spain

Location

Hospital Universitario de Canarias

La Laguna (Tenerife), 38320, Spain

Location

Hospital de la Princesa

Madrid, 28006, Spain

Location

Universitetssjukhuset

Linköping, 58185, Sweden

Location

Skanes Universitetssjukhus i Lund

Lund, 221 85, Sweden

Location

Chang Gung Medical Foundation - Linkou Branch

Kuei-Shan Hsiang, Taoyuan County, 333, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

National Taiwan University Hospital, Department of Internal Medicine

Taipei, 100, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

Hematology Division Department of Medicine Faculty of Medicine Siriraj Hospital Mahidol University

Bangkoknoi, Bangkok, 10700, Thailand

Location

Chiang Mai University

Chiang Mai, 50200, Thailand

Location

Regional Treatment and Diagnostic Hematology Center Communal Establishment

Cherkasy, 18009, Ukraine

Location

Department of Oncology and Medical Radiology of State Institution

Dnipropetrovsk, 49102, Ukraine

Location

SI"Research Center for Radiation Medicine of NAMS of Ukraine"

Kyiv, 03115, Ukraine

Location

Barts Cancer Centre Dept Haemato-oncology St. Bartholomew's Hospital Barts Health NHS Trust

London, EC1A 7BE, United Kingdom

Location

Chemotherapy Preparative Unit St. Bartholomew's Hospital

London, EC1A 7BE, United Kingdom

Location

Department of Medical Oncology St. Bartholomew's Hospital

London, EC1A 7BE, United Kingdom

Location

The Christie NHS Foundation Trust - Christie Hospital

Manchester, M20 4BX, United Kingdom

Location

Department of Clinical Pathology Newcastle upon Tyne Hospitals NHS Foundation Trust Royal Victoria I

Newcastle upon Tyne, NE1 4LP, United Kingdom

Location

Department of Clinical Biochemistry Newcastle upon Tyne Hospitals

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Northern Centre for Cancer Care

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Nottingham University Hospital

Nottingham, NG5 1PB, United Kingdom

Location

Pathology Department Nottingham University Hospital - City Hospital Campus

Nottingham, NG5 1PB, United Kingdom

Location

Pharmacy Nottingham University Hospital - City Hospital Campus

Nottingham, NG5 1PB, United Kingdom

Location

Local Laboratory Nottingham University Hospital - City Hospital Campus

Nottingham, NG51PB, United Kingdom

Location

New Cross Hospital

Wolverhampton, WV10 0QP, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Lymphoma, Non-HodgkinLymphoma, Large B-Cell, DiffuseLymphoma

Interventions

Inotuzumab OzogamicinRituximabGemcitabine

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLymphoma, B-Cell

Intervention Hierarchy (Ancestors)

CalicheamicinsAminoglycosidesGlycosidesCarbohydratesAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsAntibodies, Monoclonal, Murine-DerivedHeterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Limitations and Caveats

Interpretation of the results is limited by the small number of subjects analyzed and follow-up period was shortened due to the early termination of the study. Adverse Events were calculated using the safety populations.

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 27, 2010

First Posted

November 2, 2010

Study Start

April 4, 2011

Primary Completion

March 28, 2014

Study Completion

March 28, 2014

Last Updated

January 8, 2019

Results First Posted

August 21, 2018

Record last verified: 2018-12

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations