NCT01218516

Brief Summary

The primary objective of this study is to compare the effect of farletuzumab versus placebo in combination with either a platinum agent (carboplatin) with paclitaxel or a platinum agent (carboplatin or cisplatin) with pemetrexed followed by farletuzumab or placebo on investigator-assessed progression free survival (PFS) as determined by Response Evaluation Criteria in Solid Tumors (RECIST) v.1.1 or definitive clinical disease progression (eg, new occurrence of positive fluid cytology) in chemotherapy naive participants with folate receptoralpha (FRA)-expressing Stage IV adenocarcinoma of the lung.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
130

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jun 2011

Geographic Reach
8 countries

93 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 7, 2010

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 11, 2010

Completed
9 months until next milestone

Study Start

First participant enrolled

June 27, 2011

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 15, 2012

Completed
11 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2013

Completed
6.8 years until next milestone

Results Posted

Study results publicly available

August 20, 2020

Completed
Last Updated

August 20, 2020

Status Verified

March 1, 2018

Enrollment Period

1.5 years

First QC Date

October 7, 2010

Results QC Date

March 15, 2018

Last Update Submit

August 10, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression-free Survival (PFS)

    PFS was defined as the time from the date of randomization to the date of the first observation of investigator-assessed (radiology review) progression based on Response Evaluation Criteria In Solid Tumors (RECIST) v.1.1 or other protocol-approved measures of disease progression (e.g., new occurrence of positive fluid cytology, newly diagnosed evidence of disease progression from histologic samples, PET-positive metastases, or new bone or brain metastases), or date of death, whatever the cause. Disease progression as assessed by the investigator per RECIST v1.0 was defined as at least a 20% increase in sum of longest diameters (RECIST definition) compared to baseline (or lowest sum while on study if less than baseline), or any new lesions (measurable or nonmeasurable).

    From date of first administration of study drug up to 6 month follow-up from randomization of the last participant, i.e., cut-off date 15 Dec 2012 for primary analysis and cut-off date of 1 Nov 2013 or up to approximately 28 months for final analysis

Secondary Outcomes (4)

  • Overall Response Rate (ORR)

    From Day 1 until documented radiographic progression, other protocol-approved measures of disease progression, withdrawal by participant, death due to any cause, or cut-off date of 1 Nov 2013, i.e., up to approximately 28 months for final analysis

  • Duration of Response (DR)

    From the first documentation of objective response (CR or PR) to the first documentation of disease progression, death due to any cause, or cut-off date of 1 Nov 2013, i.e., up to approximately 28 months for final analysis

  • Overall Survival (OS)

    From the date of randomization to the date of death due to any cause or up to cut-off date of 1 Nov 2013 (up to approximately 28 months) for final analysis

  • Number of Participants With Treatment-Emergent Adverse Events (TEAEs) and Treatment-Emergent Serious Adverse Events (SAEs)

    For each participant, from the first dose till 30 days after the last dose or cut-off date of 1 Nov 2013, i.e., up to approximately 28 months for final analysis

Study Arms (2)

Farletuzumab plus Chemotherapy

ACTIVE COMPARATOR

During Combination Therapy, farletuzumab will be given with a protocol-approved platinum doublet (either carboplatin/paclitaxel, carboplatin/pemetrexed, or cisplatin/pemetrexed) for at least 4, but not more than 6, cycles. Participants who experience clinical benefit from the Combination Therapy will enter the Monotherapy Phase and receive farletuzumab as monotherapy until disease progression.

Biological: FarletuzumabDrug: CarboplatinDrug: PaclitaxelDrug: PemetrexedDrug: Cisplatin

Placebo plus Chemotherapy

PLACEBO COMPARATOR

During Combination Therapy, placebo will be given with a protocol-approved platinum doublet (either carboplatin/paclitaxel, carboplatin/pemetrexed, or cisplatin/pemetrexed) for at least 4, but not more than 6 cycles. Participants who experience clinical benefit from the Combination Therapy will enter the Monotherapy Phase and receive placebo as monotherapy until disease progression.

Other: PlaceboDrug: CarboplatinDrug: PaclitaxelDrug: PemetrexedDrug: Cisplatin

Interventions

FarletuzumabBIOLOGICAL

Combination Therapy: Farletuzumab 7.5 mg/kg will be administered intravenously on Cycle 1, Week 1 and Cycle 1, Week 2 (loading dose). Beginning on Cycle 2, Week 1, farletuzumab (7.5 mg/kg) will be administered intravenously on Week 1 of all additional cycles. Monotherapy: Farletuzumab 7.5 mg/kg will be administered intravenously on Week 1 of every 3-week cycle until disease progression.

Also known as: MORAb-003
Farletuzumab plus Chemotherapy
PlaceboOTHER

Combination Therapy: Placebo will be administered intravenously on Cycle 1, Week 1 and Cycle 1, Week 2 (loading dose). Beginning on Cycle 2, Week 1, placebo will be administered IV on Week 1 of all additional cycles. Monotherapy: Placebo will be administered intravenously on Week 1 of every 3-week cycle until disease progression.

Placebo plus Chemotherapy

Carboplatin will be administered intravenously to achieve area under the serum concentration-time curve of 5 to 6 mg/mL\^min \[AUC5-6\].

Farletuzumab plus ChemotherapyPlacebo plus Chemotherapy

Paclitaxel 200 mg/m\^2 will be administered intravenously.

Farletuzumab plus ChemotherapyPlacebo plus Chemotherapy

Pemetrexed 500 mg/m\^2 will be administered intravenously.

Farletuzumab plus ChemotherapyPlacebo plus Chemotherapy

Cisplatin 75 mg/m\^2 will be administered intravenously.

Farletuzumab plus ChemotherapyPlacebo plus Chemotherapy

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the lung classified as stage IV
  • Confirmed folate receptor-alpha (FRA) expression by immunohistochemistry (IHC)
  • Measurable disease with at least one unidimensionally measurable lesion according to RECIST criteria version 1.1 by computed tomography (CT) or magnetic resonance imaging (MRI) scans (CT or MRI scans must have been performed within 30 days prior to the first dose of farletuzumab or placebo)
  • Must have received no prior chemotherapy, radiation therapy or surgery with curative intent for adenocarcinoma of the lung

You may not qualify if:

  • Participants who have had previous chemotherapy for adenocarcinoma of the lung
  • Prior surgery with curative intent for adenocarcinoma of the lung
  • Prior radiotherapy for adenocarcinoma of the lung. (Prior treatment with local radiotherapy for symptom control \[i.e., palliative radiation with non-curative intent\] is permitted)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (93)

Ironwood Cancer and Research Center

Chandler, Arizona, 85224, United States

Location

Arizona Center for Hematology Oncology

Glendale, Arizona, 85306-4666, United States

Location

Providence Health System

Beverly Hills, California, 90210-5501, United States

Location

Cancer Care Associates of Fresno Medical Group, Inc.

Fresno, California, 93720, United States

Location

Medical Oncology Hematology

Gilroy, California, 95020, United States

Location

California Cancer Care, Inc.

Greenbrae, California, 94904, United States

Location

Moores University of California San Diego Cancer Center

La Jolla, California, 92093, United States

Location

Wilshire Medical Oncology Group

La Verne, California, 91750, United States

Location

Glendale Adventist Medical Center

Los Angeles, California, 90025, United States

Location

Clinical Trials and Research Associates, Inc.

Montebello, California, 90640, United States

Location

North Country Oncology-Hematology

Oceanside, California, 92056, United States

Location

Pacific Hematology Oncology Associates

San Francisco, California, 94115, United States

Location

Central Coast Medical Oncology

Santa Maria, California, 93454, United States

Location

Rocky Mountain Cancer Centers, LLP

Denver, Colorado, 80218-1237, United States

Location

Hematology Oncology Associates, P.C.

Stamford, Connecticut, 06902-3628, United States

Location

Center for Hematology-Oncology

Boca Raton, Florida, 33486, United States

Location

Medical Specialists of the Palm Beaches

Deerfield Beach, Florida, 33441, United States

Location

Broward General Medical Center

Fort Lauderdale, Florida, 33316, United States

Location

Cancer Care of North Florida

Lake City, Florida, 32024, United States

Location

Florida Cancer Institute-New Hope

New Port Richey, Florida, 34655, United States

Location

Ocala Oncology Center, PL

Ocala, Florida, 34474, United States

Location

MD Anderson Cancer Center-Orlando

Orlando, Florida, 32806, United States

Location

University Hematology Oncology, Inc.

Centralia, Illinois, 62801, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Deaconess Clinic Downtown

Evansville, Indiana, 47713, United States

Location

The Community Hospital

Munster, Indiana, 46321, United States

Location

Kentucky Cancer Center

Hazard, Kentucky, 41701, United States

Location

Baptist Health System, Inc.

Lexington, Kentucky, 40503, United States

Location

Christus Saint Frances, Cabrini Hospital, Cabrini Cancer Center

Alexandria, Louisiana, 71301, United States

Location

Hematology and Oncology Specialists, LLC

Metairie, Louisiana, 70006, United States

Location

National Cancer Institute

Bethesda, Maryland, 20892, United States

Location

Maryland Oncology Hematology, P.A.

Columbia, Maryland, 21044, United States

Location

Berkshire Hematology Oncology, PC

Pittsfield, Massachusetts, 01201, United States

Location

Detroit Clinical Research Center

Farmington Hills, Michigan, 48336, United States

Location

Englewood Hospital and Medical Center

Englewood, New Jersey, 07631, United States

Location

Queens Hospital Center

Jamaica, New York, 11432, United States

Location

Syracuse Veterns Affairs Medical Center

Syracuse, New York, 13210, United States

Location

Willamette Valley Cancer Institute and Research Center

Eugene, Oregon, 97401, United States

Location

St. Luke's Cancer Center Associates

Bethlehem, Pennsylvania, 18015, United States

Location

Gettysburg Cancer Center

Gettysburg, Pennsylvania, 17325, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37203, United States

Location

Texas Oncology - Bedford

Bedford, Texas, 76022, United States

Location

University of Texas Medical Branch

Galveston, Texas, 77555, United States

Location

Houston Cancer Institute

Houston, Texas, 77055, United States

Location

Texas Oncology - Plano East

Plano, Texas, 75075-7787, United States

Location

Northwest Cancer Center

Sugar Land, Texas, 77479, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702-8363, United States

Location

Texas Oncology - Waco

Waco, Texas, 76712, United States

Location

Virginia Cancer Specialists, PC

Fairfax, Virginia, 22031, United States

Location

Delta Hematology Oncology Associates, PC

Portsmouth, Virginia, 23704, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

Rockwood Cancer Treatment Center

Spokane, Washington, 99204, United States

Location

Medical Oncology Associates, PS

Spokane, Washington, 99208, United States

Location

Cancer Team Bellin Health

Green Bay, Wisconsin, 54313, United States

Location

The Tweed Hospital

Tweed Heads, New South Wales, 2485, Australia

Location

Southern Medical Day Oncology Care Centre

Wollongong, New South Wales, 2500, Australia

Location

Royal Brisbane and Women's Hospital, Dept. of Medical Oncology

Brisbane, Queensland, 4029, Australia

Location

Princess Alexandra Hospital

Woolloongabba, Queensland, 4102, Australia

Location

Royal Adelaide Hospital, Cancer Centre

Adelaide, South Australia, 5000, Australia

Location

Flinders Medical Centre, Dept. of Oncology

Bedford Park, South Australia, 5042, Australia

Location

Lyell McEwin Hospital

Elizabeth Vale, South Australia, 5112, Australia

Location

The Queen Elizabeth Hospital

Woodville South, South Australia, 5011, Australia

Location

Box Hill Hospital

Box Hill, Victoria, 3128, Australia

Location

Frankston Hospital, Oncology Day Unit

Frankston, Victoria, 3199, Australia

Location

Epworth Healthcare

Richmond, Victoria, 3002, Australia

Location

Fremantle Hospital

Fremantle, Western Australia, 6160, Australia

Location

Royal Victoria Hospital

Barrie, Ontario, L4M 6M2, Canada

Location

Grand River Regional Cancer Centre

Kitchener, Ontario, N2G 1G3, Canada

Location

Princess Margaret Hospital

Toronto, Ontario, MSG 2L7, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

Universitätsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, 69126, Germany

Location

Klinik Löwenstein gGmbH

Löwenstein, Baden-Wurttemberg, 74245, Germany

Location

Asklepios Fachkliniken München-Gauting

Gauting, Bavaria, 82131, Germany

Location

Krankenhaus Nordwest GmbH

Frankfurt am Main, Hesse, 60488, Germany

Location

Johannes-Wesling-Klinikum Minden

Minden, North Rhine-Westphalia, 32429, Germany

Location

Städtisches Krankenhaus Martha-Maria Halle Dölau gGmbH

Halle, Saxony-Anhalt, 06120, Germany

Location

HELIOS Klinikum Emil von Behring

Berlin, 14165, Germany

Location

Asklepios Klinik Harburg

Hamburg, 21075, Germany

Location

Ospedale Unico Versilia

Lido di Camaiore, Lucca, 55043, Italy

Location

Azienda Ospedaliero-Univesitaria "San Luigi Gonzaga"

Orbassano, Torino, 10043, Italy

Location

Istituto Nazionale per la Ricerca sul Cancro

Genova, 16132, Italy

Location

A.O. Seconda Università degli Studi di Napoli

Napoli, 80131, Italy

Location

Wojewódzki Szpital Zespolony im. L. Rydygiera w Toruniu Szpital Dzieciecy

Torun, Kuyavian-Pomeranian Voivodeship, 87-100, Poland

Location

Centrum Onkologii - Instytut im. M. Sklodowskiej-Curie w Warszawie

Warsaw, Masovian Voivodeship, 02-781, Poland

Location

Specjalistyczny Szpital im. Alfreda Sokolowskiego

Szczecin, West Pomeranian Voivodeship, 70-891, Poland

Location

Republican Clinical Oncologic Dispensary of Ministry of health of Republic Tatarstan

Kazan', Tatarstan Republic, 420029, Russia

Location

Cancer Research Center n.a. N.N. Blokhin

Moscow, 115478, Russia

Location

City Oncology Hospital # 62

Moscow, 143423, Russia

Location

Hospital Regional Carlos Haya

Málaga, Malaga, 29010, Spain

Location

Hospital General Vall d'Hebron, Barcelona

Barcelona, 08035, Spain

Location

Hospital Clinic i Provincial de Barcelona

Barcelona, 08036, Spain

Location

Hospital Germans Trías i Pujol

Barcelona, 08916, Spain

Location

Fundación Jiménez Díaz

Madrid, 28040, Spain

Location

MeSH Terms

Conditions

Adenocarcinoma of Lung

Interventions

farletuzumabCarboplatinPaclitaxelPemetrexedCisplatin

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by Site

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsDiterpenesTerpenesGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, DicarboxylicChlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum Compounds

Results Point of Contact

Title
Morphotek (subsidiary of Eisai)
Organization
Morphotek (subsidiary of Eisai)

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 7, 2010

First Posted

October 11, 2010

Study Start

June 27, 2011

Primary Completion

December 15, 2012

Study Completion

November 1, 2013

Last Updated

August 20, 2020

Results First Posted

August 20, 2020

Record last verified: 2018-03

Locations