NCT01011283

Brief Summary

The purpose of this study is to compare the response of patients with Intermediate or High Risk myelodysplastic syndromes (MDS) following treatment with decitabine or azacitidine.

Trial Health

35
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
26

participants targeted

Target at below P25 for phase_4

Geographic Reach
1 country

19 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2009

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

November 5, 2009

Completed
6 days until next milestone

First Posted

Study publicly available on registry

November 11, 2009

Completed
1.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2011

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

September 18, 2013

Completed
Last Updated

October 29, 2014

Status Verified

October 1, 2014

Enrollment Period

1.2 years

First QC Date

November 5, 2009

Results QC Date

July 14, 2013

Last Update Submit

October 21, 2014

Conditions

Keywords

MDSMyelodysplastic Syndromes

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate (ORR), Defined as Proportion of Patients Having Complete Response (CR) and Marrow Complete Response (mCR) After Completion of 3 Cycles of Study Drug.

    Based on Modified International Working Group Response Criteria for Altering Natural History of Myelodysplastic Syndromes. Complete Response: Bone marrow: ≤ 5% myeloblasts with normal maturation of all cell lines. Persistent dysplasia will be noted. Peripheral blood Hgb ≥ 11 g/dL; Platelets ≥ 100 X 10\^9/L; Neutrophils ≥ 1.0 X 10\^9/Lb; Blasts 0%. Marrow Complete Response: Bone marrow: ≤ 5% myeloblasts and decrease by ≥ 50% over pretreatment. Peripheral blood: if hematological improvement responses, they will be noted in addition to marrow CR.

    13 Weeks

Secondary Outcomes (1)

  • Overall Response Rate (ORR), Defined as Proportion of Patients Having Complete Response (CR) and Marrow Complete Response (mCR) After Completion of 6 Cycles of Study Drug.

    36 Weeks

Study Arms (2)

1

ACTIVE COMPARATOR
Drug: decitabine

2

ACTIVE COMPARATOR
Drug: azacitidine

Interventions

decitabine 20 mg/m\^2 /day intravenous (IV) infusion for 5 days every 28 days

Also known as: Dacogen (decitabine)
1

azacitidine 75 mg/m\^2 /day subcutaneous (SC) injection for 7 days every 28 days

Also known as: Vidaza (azacitidine)
2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects who meet all of the following criteria may be included in the study:
  • Must have a diagnosis of primary myelodysplastic syndromes (MDS) of Intermediate-1 transfusion dependent, Intermediate-2, or High-risk \[defined by International Prognostic Scoring System (IPSS) score of ≥0.5\] and recognized French-American-British (FAB) classifications
  • Male or female, 18 years of age or older with signed informed consent
  • Adequate renal function
  • Demonstrated normal liver function
  • Female subjects of childbearing age must have negative pregnancy test within 1 week of study entry and agree to use adequate contraception for the duration of the trial and for a minimum of six months after last dose of decitabine or azacitidine received.
  • Male subjects must agree to use adequate contraception for the duration of the trial and for a minimum of six months after last dose of decitabine or azacitidine received.

You may not qualify if:

  • Subjects who meet any of the following criteria will be excluded from participation in the study:
  • Current use of radiotherapy for extramedullary disease for 2 weeks prior to entering study (permitted if \> 2 weeks from study entry and if recovered from toxic effects of therapy)
  • Systemic fungal, bacterial, or viral infection which is not controlled (i.e., ongoing signs or symptoms of infection and without improvement despite appropriate treatment)
  • Pregnancy or current lactation
  • Significant concurrent disease, illness, or psychiatric disorder
  • Treatment with an investigational agent 30 days prior to the first dose of decitabine or azacitidine

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (19)

Birmingham Hematology and Oncology Associates

Birmingham, Alabama, 35205, United States

Location

Stanford University Cancer Center

Stanford, California, 94305, United States

Location

Stockton Hematology Oncology

Stockton, California, 95204, United States

Location

Florida Cancer Specialists

Fort Myers, Florida, 33619, United States

Location

Pasco Pinellas Cancer Center

New Port Richey, Florida, 34652, United States

Location

Gulf Coast Oncology

St. Petersburg, Florida, 33705, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Siouxland Haeatology - Oncology Associates

Sioux City, Iowa, 51101, United States

Location

Center for Cancer and Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Sletten Cancer Institute

Great Falls, Montana, 59405, United States

Location

Cornell Medical Center

New York, New York, 10021, United States

Location

Carolinas Medical Center NorthEast NorthEast Oncology Associates

Concord, North Carolina, 28025, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

Oncology and Hematology Care

Cincinnati, Ohio, 45242, United States

Location

University of Pittsburgh School of Medicine

Pittsburgh, Pennsylvania, 15232, United States

Location

Charleston Hematology Oncology Associates

Charleston, South Carolina, 29403, United States

Location

Sarah Cannon Cancer Center

Nashville, Tennessee, 37203, United States

Location

Utah Cancer Specialists

Salt Lake City, Utah, 84106, United States

Location

Gunderson Clinic Ltd.

La Crosse, Wisconsin, 54601, United States

Location

MeSH Terms

Conditions

Myelodysplastic Syndromes

Interventions

DecitabineAzacitidine

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Aza CompoundsOrganic ChemicalsCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleosidesNucleic Acids, Nucleotides, and NucleosidesRibonucleosides

Results Point of Contact

Title
Erhan Berrack, M.D.
Organization
Eisai Inc.

Study Officials

  • Karen Stein

    Eisai Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 5, 2009

First Posted

November 11, 2009

Study Start

November 1, 2009

Primary Completion

January 1, 2011

Last Updated

October 29, 2014

Results First Posted

September 18, 2013

Record last verified: 2014-10

Locations