NCT01002248

Brief Summary

This is a randomized Phase III study to evaluate the efficacy and safety of perifosine when added to the combination of bortezomib and dexamethasone in multiple myeloma patients who have relapsed on a prior bortezomib treatment regimen.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
135

participants targeted

Target at below P25 for phase_3 multiple-myeloma

Timeline
Completed

Started Dec 2009

Shorter than P25 for phase_3 multiple-myeloma

Geographic Reach
9 countries

86 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 23, 2009

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 27, 2009

Completed
1 month until next milestone

Study Start

First participant enrolled

December 1, 2009

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2013

Completed
Last Updated

February 9, 2018

Status Verified

March 1, 2013

Enrollment Period

3.2 years

First QC Date

October 23, 2009

Last Update Submit

February 6, 2018

Conditions

Keywords

Multiple MyelomaRelapsed multiple myelomaRefractory multiple myelomaRelapsed refractory multiple myeloma

Outcome Measures

Primary Outcomes (1)

  • Determine the PFS (progression free survival) in patients with multiple myeloma, treated with perifosine, bortezomib and dexamethasone compared to patients treated with placebo, bortezomib and dexamethasone

    Progression-free survival will be defined as the time between randomization and the date of progression that occurred during the Core Phase.

    6 - 24 months

Secondary Outcomes (3)

  • Overall survival (OS)

    Up to 24 months

  • Overall response rate (ORR)

    6 - 24 months

  • Adverse Events

    Up to 24 months

Study Arms (2)

Perifosine added to combination

EXPERIMENTAL

Perifosine added to the combination of Bortezomib and Dexamethasone. Perifosine is is supplied as a film-coated tablet containing 50 mg of active ingredient. Perifosine will be administered orally on an outpatient basis throughout the study. Daily administration will be one 50 mg tablet. The first dose of perifosine should be taken on the same day that bortezomib and dexamethasone are administered (Cycle 1 Day 1).

Drug: PerifosineDrug: BortezomibDrug: Dexamethasone

Perifosine Placebo added to combination

PLACEBO COMPARATOR

Perifosine placebo added to the combination of Bortezomib and Dexamethasone. The placebo for perifosine is provided in 256 mg white to off-white, round, biconvex film-coated tablets to permit a blinded trial with perifosine 50 mg film coated tablets. Placebo will be administered orally on an outpatient basis throughout the study. Daily administration will be one perifosine placebo tablet. The first dose of placebo should be taken on the same day that bortezomib and dexamethasone are administered (Cycle 1 Day 1).

Drug: Perifosine PlaceboDrug: BortezomibDrug: Dexamethasone

Interventions

Perifosine will be dosed as one 50 mg pill every day of each cycle.

Also known as: D-21266, KRX-0401
Perifosine added to combination

Perifosine placebo will be dosed as one 50 mg pill every day of each cycle.

Perifosine Placebo added to combination

Bortezomib will be dosed at 1.3 mg/m2 on Days 1, 4, 8, and 11 every 21 days.

Perifosine Placebo added to combinationPerifosine added to combination

Dexamethasone will be administered orally at 20 mg on Days 1, 2, 4, 5, 8, 9, 11, and 12 of each 21-day cycle.

Perifosine Placebo added to combinationPerifosine added to combination

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient was previously diagnosed with multiple myeloma based on standard diagnostic criteria.
  • Patients must have relapsed (progressed \> 60 days) after their last dose of bortezomib-based therapy. In addition, patients may be relapsed or refractory to other non-bortezomib-based therapies.
  • Patient has received at least 1 but not more than 4 prior anti-myeloma regimens and has progressive disease after the most recent treatment regimen.
  • Patients must have adequate organ and marrow function.

You may not qualify if:

  • Patients must not be refractory to any bortezomib-containing regimen.
  • History of allergic reactions or intolerance attributed to compounds of similar chemical or biologic composition to perifosine (miltefosine or edelfosine), bortezomib or dexamethasone or any of their components.
  • Prior treatment with perifosine or an investigational proteasome inhibitor.
  • Chemotherapy or other therapy experimental or proven that is or may be active against myeloma within two weeks (14 days) prior to Cycle 1 Day 1.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (86)

Unknown Facility

La Verne, California, 91750, United States

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San Francisco, California, 94143, United States

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San Pablo, California, 94806, United States

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Aurora, Colorado, 80012, United States

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Boulder, Colorado, 80303, United States

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Colorado Springs, Colorado, 80909, United States

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Denver, Colorado, 80218, United States

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Lakewood, Colorado, 80228, United States

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Littleton, Colorado, 80120, United States

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Longmont, Colorado, 80501, United States

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Parker, Colorado, 80138, United States

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Pueblo, Colorado, 81008, United States

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Thornton, Colorado, 80260, United States

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Niles, Illinois, 60714, United States

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Winfield, Illinois, 60190, United States

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Baltimore, Maryland, 21201, United States

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Columbia, Maryland, 21044, United States

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Dana Farber Cancer Institute

Boston, Massachusetts, 02115, United States

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Morristown, New Jersey, 07960, United States

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Great Neck, New York, 11042, United States

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Fargo, North Dakota, 58122, United States

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Portland, Oregon, 97225, United States

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Tualatin, Oregon, 97062, United States

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Kingsport, Tennessee, 37660, United States

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Bedford, Texas, 76022, United States

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Dallas, Texas, 75246, United States

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Fort Worth, Texas, 76104, United States

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Kerrville, Texas, 78028, United States

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San Antonio, Texas, 78217, United States

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San Antonio, Texas, 78229, United States

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Tyler, Texas, 75702, United States

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Ogden, Utah, 84403, United States

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Christiansburg, Virginia, 24073, United States

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Roanoke, Virginia, 24014, United States

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Salem, Virginia, 24153, United States

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Seattle, Washington, 98133, United States

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Spokane, Washington, 99202, United States

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Vancouver, Washington, 98686, United States

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Milwaukee, Wisconsin, 53226, United States

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Winnipeg, Manitoba, R3E 0V9, Canada

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Montreal, Quebec, H1T 2M4, Canada

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Montreal, Quebec, H3A 1A1, Canada

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Québec, Quebec, G1R 2J6, Canada

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Brno, Czech Republic, 62500, Czechia

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Prague, Czech Republic, 12821, Czechia

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Keryx / AOI Pharmaceuticals Investigative Site

Dublin, Ireland

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Dublin, Ireland

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Galway, Ireland

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Limerick, Ireland

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Sligo, Ireland

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Tullamore, Ireland

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Waterford, Ireland

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Afula, 18101, Israel

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Ashkelon, 78278, Israel

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Beersheba, 84101, Israel

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Haifa, 31096, Israel

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Jerusalem, 91031, Israel

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Jerusalem, 91120, Israel

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Nahariya, 22100, Israel

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Petah Tikva, 49100, Israel

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Rehovot, 76100, Israel

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Tel Aviv, 64239, Israel

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Tel Litwinsky, 52621, Israel

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Moscow, 125284, Russia

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Moscow, 129110, Russia

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Saint Petersburg, 191024, Russia

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Saint Petersburg, 197022, Russia

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Samara, 443095, Russia

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Košice, Slovak Republic, 04166, Slovakia

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Seoul, 110-744, South Korea

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Seoul, 120-752, South Korea

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Seoul, 135-710, South Korea

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Seoul, 137-701, South Korea

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Seoul, 138-736, South Korea

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Badalona, 08916, Spain

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Barcelona, 08025, Spain

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Barcelona, 08035, Spain

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Barcelona, 08036, Spain

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Madrid, 28006, Spain

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Madrid, 28034, Spain

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Madrid, 28040, Spain

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Madrid, 28041, Spain

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Pamplona, 31008, Spain

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San Cristóbal de La Laguna, 38320, Spain

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Valencia, 46026, Spain

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Zaragoza, 50009, Spain

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Related Publications (1)

  • Richardson PG, Nagler A, Ben-Yehuda D, Badros A, Hari P, Hajek R, Spicka I, Kaya H, Le Blanc R, Yoon SS, Kim K, Martinez-Lopez J, Mittelman M, Shpilberg O, Tothova E, Laubach JP, Ghobria IM, Leiba M, Gatt ME, Sportelli P, Chen M, Anderson KC. Randomized Placebo-Controlled Phase III Study Of Perifosine Combined With Bortezomib and Dexamethasone In Relapsed, Refractory Multiple Myeloma Patients Previously Treated With Bortezomib. Blood 2013 ASH Meeting Proceedings;122:abstract 3189

    RESULT

MeSH Terms

Conditions

Multiple Myeloma

Interventions

perifosineBortezomibDexamethasone

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Boronic AcidsAcids, NoncarboxylicAcidsInorganic ChemicalsBoron CompoundsOrganic ChemicalsPyrazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, Fluorinated

Study Officials

  • Paul Richardson, MD

    Dana-Farber Cancer Institute

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 23, 2009

First Posted

October 27, 2009

Study Start

December 1, 2009

Primary Completion

March 1, 2013

Study Completion

March 1, 2013

Last Updated

February 9, 2018

Record last verified: 2013-03

Locations