NCT00338377

Brief Summary

Objectives: The primary objective will be to determine whether patients receiving the combination of dendritic cells and high dose IL-2 (Cohort A) have sustained persistence of infused T cells compared to patients treated with T cells and high dose IL-2 alone. Secondary endpoints will include evaluations for tumor response and studies to determine whether dendritic cells enhance the infused T cells in anti-tumor activity and their ability to migrate to the tumor site. In addition, we will evaluate the characteristics of the infused T cells that correspond with effectiveness in vivo. Additionally, secondary objectives will include correlation of clinical parameters with survival (overall survival and progression-free survival) for all cohorts. COHORT C In a separate cohort (Cohort C) the primary endpoint will be the overall response rate of TIL treatment for patients who have not achieved PR or CR or have progressive disease from treatment of the BRAF inhibitor alone. COHORT D The primary objective of Cohort D is to confirm the safety of adoptively transferred, TIL into the CSF. The secondary objective is the evaluation of clinical imaging and CSF response. Correlative objectives will assess if the intrathecally-infused T cells persist in the CSF, assess circulating tumor cells in the CSF, and assess various cytokine and other analyses,as feasible. COHORT E The primary objective of Cohort E is to determine the overall response rate of TIL treatment with cells grown by the TIL 3.0 pre-REP (Turnstile 1) phase of cellular growth.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,230

participants targeted

Target at P75+ for phase_2

Timeline
46mo left

Started Feb 2006

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress84%
Feb 2006Feb 2030

Study Start

First participant enrolled

February 1, 2006

Completed
9 days until next milestone

First Submitted

Initial submission to the registry

February 10, 2006

Completed
4 months until next milestone

First Posted

Study publicly available on registry

June 20, 2006

Completed
23.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 28, 2030

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 28, 2030

Last Updated

March 20, 2026

Status Verified

March 1, 2026

Enrollment Period

24.1 years

First QC Date

February 10, 2006

Last Update Submit

March 17, 2026

Conditions

Keywords

MelanomaRegional nodal diseaseDendritic Cell ImmunizationLymphodepletionAdoptive Cell TransferT CellsVaccineCyclosphosphamideCytoxanNeosarDendritic CellsTumor Infiltrating LymphocytesTIL CellsMART PeptideFludarabineFludarabine PhosphateFludaraProleukinIL-2Interleukin-2Leptomeningeal disease

Outcome Measures

Primary Outcomes (3)

  • Objective Response (OR)

    Objective response (OR) defined as immune-related Best Overall Response (irBOR). irBOR is best confirmed immune-related response criteria (irRC) overall response over the study as a whole, recorded between the date of first dose until the last tumor assessment before subsequent therapy (except for local palliative radiotherapy for painful bone lesions) for the individual subjects in the study.

    Clinical Evaluation during first 70 Days, CT Scan at 6-8 weeks (+/- 7 days) after cell infusion.

  • Longitudinal Immune Response in Cohort D

    Longitudinal immune response defined as: Conversion of positive to negative cytology. Any perceptible improvement of the MRI findings confirmed by radiologist and/or the investigator confirmed by 2 successive MRIs 4 weeks apart. Any clinical improvement in terms of neurological symptoms.

    4 weeks

  • Overall response rate (ORR) of TIL generated with the TIL 3.0 pre-REP methodology in Cohort E

    ORR defined as CR/PR/SD\>6m (i.e., success = CR or PR or SD \> 6m).

    At about 6 weeks and at 12 weeks after the T-cell and/or vaccine infusion

Study Arms (5)

Group A: Chemotherapy + IL-2 plus T-cells

EXPERIMENTAL

Cyclophosphamide 60 mg/kg/d by vein (IV) over 2 hours Days -7 and -6 (with Mesna) and Fludarabine 25 mg/m\^2 IV daily Days -5 to -1 before T cell infusion. On Day 0, up to 1.5 x 10\^11 T cells IV infusion over 30-60 minutes. Interleukin-2 12-16 hours after T cell infusion at standard dose of 720,000 IU/kg as intravenous bolus over 15 minute period every 8-16 hours for up to 15 doses on Days 1-5 and 22-26. Group A has been closed to new patient entry as of January 14, 2016.

Drug: CyclophosphamideDrug: FludarabineBiological: T-CellsBiological: Interleukin-2Drug: Mesna

Group B: Chemotherapy + IL-2 plus T-Cells + Vaccine

EXPERIMENTAL

Chemotherapy and IL-2 plus T-cells and the vaccine of dendritic cells received by vein (IV) about 4 hours after T-cells and again on Day 21 (+/- 7 days). Cyclophosphamide 60 mg/kg/d IV over 2 hours Days -7 and -6 (with Mesna) and Fludarabine 25 mg/m\^2 IV daily Days -5 to -1 before T cell infusion. On Day 0, up to 1.5 x 10\^11 T cells IV infusion over 30-60 minutes. Interleukin-2 12-16 hours after T cell infusion at standard dose of 720,000 IU/kg as intravenous bolus over 15 minute period every 8-16 hours for up to 15 doses on Days 1-5 and 22-26.

Biological: Dendritic Cell ImmunizationDrug: CyclophosphamideDrug: FludarabineBiological: T-CellsBiological: Interleukin-2Drug: Mesna

Group C: Prior Treatment with BRAF Inhibitor

EXPERIMENTAL

Chemotherapy and IL-2 plus T-cells and the vaccine of dendritic cells received by vein (IV) about 4 hours after T-cells and again on Day 21 (+/- 7 days). Cyclophosphamide 60 mg/kg/d IV over 2 hours Days -7 and -6 (with Mesna) and Fludarabine 25 mg/m\^2 IV daily Days -5 to -1 before T cell infusion. On Day 0, up to 1.5 x 10\^11 T cells IV infusion over 30-60 minutes. Interleukin-2 12-16 hours after T cell infusion at standard dose of 720,000 IU/kg as intravenous bolus over 15 minute period every 8-16 hours for up to 15 doses on Days 1-5 and 22-26.

Biological: Dendritic Cell ImmunizationDrug: CyclophosphamideDrug: FludarabineBiological: T-CellsBiological: Interleukin-2Drug: Mesna

Group D: Leptomeningeal Disease

EXPERIMENTAL

T-cells: 5.0x109 TIL administered on Day 1 and 10x109 TIL on Day 15. IL-2: 1.2 MIU of IL- 2 on Days 2, 4, 9, 11, 16 and 18 as tolerated. After this period, patient receives twice weekly IL-2 that will be gradually changed to weekly IL-2. After 4-6 weeks, patients switched to IL-2.

Biological: Intrathecal T-CellsBiological: Intrathecal Interleukin-2

Group E: Chemotherapy + IL-2 plus T-Cells + Vaccine

EXPERIMENTAL

Chemotherapy and IL-2 plus T-cells and the vaccine of dendritic cells received by vein (IV) about 4 hours after T-cells and again on Day 21 (+/- 7 days). Cyclophosphamide 60 mg/kg/d IV over 2 hours Days -7 and -6 (with Mesna) and Fludarabine 25 mg/m\^2 IV daily Days -5 to -1 before T cell infusion. On Day 0, up to 1.5 x 10\^11 T cells IV infusion over 30-60 minutes. Interleukin-2 12-16 hours after T cell infusion at standard dose of 720,000 IU/kg as intravenous bolus over 15 minute period every 8-16 hours for up to 15 doses on Days 1-5 and 22-26.

Biological: Dendritic Cell ImmunizationDrug: CyclophosphamideDrug: FludarabineBiological: T-CellsBiological: Interleukin-2Drug: Mesna

Interventions

1x10\^7 to 2.5x10\^8 MART-1 peptide-pulsed Dendritic Cells given by vein over 20-30 minutes approximately 4 hrs after receiving T cells.

Group B: Chemotherapy + IL-2 plus T-Cells + VaccineGroup C: Prior Treatment with BRAF InhibitorGroup E: Chemotherapy + IL-2 plus T-Cells + Vaccine

60 mg/kg/d by vein over 2 hours on Days -7 and -6 before T cell infusion

Also known as: Cytoxan, Neosar
Group A: Chemotherapy + IL-2 plus T-cellsGroup B: Chemotherapy + IL-2 plus T-Cells + VaccineGroup C: Prior Treatment with BRAF InhibitorGroup E: Chemotherapy + IL-2 plus T-Cells + Vaccine

25 mg/m\^2 by vein daily over 30 minutes on Days -5 to -1 before T cell infusion.

Also known as: Fludarabine Phosphate, Fludara
Group A: Chemotherapy + IL-2 plus T-cellsGroup B: Chemotherapy + IL-2 plus T-Cells + VaccineGroup C: Prior Treatment with BRAF InhibitorGroup E: Chemotherapy + IL-2 plus T-Cells + Vaccine
T-CellsBIOLOGICAL

On Days 0, up to 1.5 x 10\^11 T-cells by vein infusion over 30-60 minutes.

Group A: Chemotherapy + IL-2 plus T-cellsGroup B: Chemotherapy + IL-2 plus T-Cells + VaccineGroup C: Prior Treatment with BRAF InhibitorGroup E: Chemotherapy + IL-2 plus T-Cells + Vaccine
Interleukin-2BIOLOGICAL

12-16 hours after completing the T cell infusion, all will receive high dose IL-2 on an inpatient basis at the standard dose of 720,000 IU/kg as an intravenous bolus over approximately a 15 minute period every 8-16 hours for up to 15 doses on Days 1-5 and 22-26 (+/- 7 days), as tolerated.

Also known as: IL-2, Proleukin
Group A: Chemotherapy + IL-2 plus T-cellsGroup B: Chemotherapy + IL-2 plus T-Cells + VaccineGroup C: Prior Treatment with BRAF InhibitorGroup E: Chemotherapy + IL-2 plus T-Cells + Vaccine
MesnaDRUG

60 mg/kg with D5W or NS at 125 ml/hr infused intravenously over 24 hours on Day -7 and -6.

Also known as: Sodium 2-mercaptoethanesulfonate, Mesnum, Mesnex, NSC-113891
Group A: Chemotherapy + IL-2 plus T-cellsGroup B: Chemotherapy + IL-2 plus T-Cells + VaccineGroup C: Prior Treatment with BRAF InhibitorGroup E: Chemotherapy + IL-2 plus T-Cells + Vaccine

5.0x10\^9 T-cells administered on Day 1, and 10x10\^9 T-cells on Day 15. 1.2 MIU of IL- 2 on Day 2, 4, 9, 11, 16 and 18 as tolerated.

Group D: Leptomeningeal Disease

1.2 MIU of IL- 2 on Day 2, 4, 9, 11, 16 and 18 as tolerated. Then, patient receives twice weekly IL-2 that will be gradually changed to weekly IL-2. After 4-6 weeks patients switched to IL-2 maintenance.

Also known as: IL-2
Group D: Leptomeningeal Disease

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have metastatic melanoma, uveal melanoma or stage III in-transit or regional nodal disease. (Turnstile I)
  • Patients must receive an MRI/CT of the brain or PET/CT within 6 months of consenting. If new lesions are present, PI or his designee should make final determination regarding enrollment. (Turnstile I)
  • Age greater than or equal to 12 years. (Turnstile I)
  • Clinical performance status of ECOG 0-2. (Turnstile I)
  • Patients previously treated with immunotherapy, targeted therapy, or no therapy will be eligible. Patients receiving cytotoxic agents will be evaluated by the PI or his designee as to suitable eligibility. (Turnstile I)
  • Patients must have adequate TIL available. (Turnstile II)
  • Patients must have a documented negative pregnancy test (urine or serum) for women who have menstruation in the past 12 months and without sterilization surgery.
  • Unless surgically sterile by bilateral tubal ligation or vasectomy of partner(s), the patient agrees to continue to use a barrier method of contraception throughout the study such as: condom, diaphragm, hormonal, IUD, or sponge plus spermicide. Abstinence is an acceptable form of birth control. (Turnstile II)
  • Pregnancy testing will be performed within 7 days prior to treatment. (Turnstile II)
  • Hemoglobin greater than or equal to 8.0 g/dl. (Turnstile II - Chemotherapy/Cell Infusion).
  • Patients in Cohort A will be randomized to receive either TIL alone or TIL plus Dendritic cells.
  • Patients must be receiving a B-RAF inhibitor and failed to achieve PR or CR or have progressive disease in response to B-RAF treatment (Cohort C).
  • i. Patients with MRI evidence of LMD, with or without evidence of malignant cells in CSF ("positive cytology"), or ii. Patients with evidence of malignant cells in the CSF (positive cytology), with or without MRI evidence of LMD, or iii. Patients with surgically-proven LMD (leptomeningeal involvement on pathology review) +/- MRI or CSF evidence by MRI or CSF cytology (Cohort D)
  • a. Many patients present with concomitant systemic disease outside of the central nervous system. Extra-CNS disease status should meet the following criteria: i. Patients with concomitant systemic disease under control with current or prior systemic treatment, as per primary treating physician ii. Patients without any evidence of systemic disease, either receiving systemic treatment or on active observation (Cohort D)
  • c. Previous Therapies i. Patients who are currently being treated with IT IL-2 for LMD are eligible. No wash out period is required. ii. Patients who have been previously treated with other IT therapies are eligible, as long as there is at least a 2 week wash out period iii. Patients who have previously received therapy with systemic TIL therapy are eligible.
  • +2 more criteria

You may not qualify if:

  • Has had prior systemic cancer cytotoxic chemotherapy within the past four weeks at the time of the start of the lymphodepletion regimen.
  • Has had prior B-RAF or MEK targeted therapy within 7 days prior to the start of the lymphodepletion regimen (Cohort A and Cohort B).
  • Achieves PR or CR in response to B-RAF treatment (Cohort C).
  • Patients with rapidly advancing systemic disease, especially those without good options of systemic treatment for their disease outside the CNS. (Cohort D)
  • Patients with rapidly advancing parenchymal brain metastases (Cohort D)
  • Pregnant patients (Cohort D)
  • Patients with rapid decline in neurological function as documented on exam and/or as per clinical judgment of treating physician (Cohort D)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Publications (2)

  • Saberian C, Amaria RN, Najjar AM, Radvanyi LG, Haymaker CL, Forget MA, Bassett RL, Faria SC, Glitza IC, Alvarez E, Parshottam S, Prieto V, Lizee G, Wong MK, McQuade JL, Diab A, Yee C, Tawbi HA, Patel S, Shpall EJ, Davies MA, Hwu P, Bernatchez C. Randomized phase II trial of lymphodepletion plus adoptive cell transfer of tumor-infiltrating lymphocytes, with or without dendritic cell vaccination, in patients with metastatic melanoma. J Immunother Cancer. 2021 May;9(5):e002449. doi: 10.1136/jitc-2021-002449.

  • Joseph RW, Peddareddigari VR, Liu P, Miller PW, Overwijk WW, Bekele NB, Ross MI, Lee JE, Gershenwald JE, Lucci A, Prieto VG, McMannis JD, Papadopoulos N, Kim K, Homsi J, Bedikian A, Hwu WJ, Hwu P, Radvanyi LG. Impact of clinical and pathologic features on tumor-infiltrating lymphocyte expansion from surgically excised melanoma metastases for adoptive T-cell therapy. Clin Cancer Res. 2011 Jul 15;17(14):4882-91. doi: 10.1158/1078-0432.CCR-10-2769. Epub 2011 Jun 1.

Related Links

MeSH Terms

Conditions

MelanomaMeningeal Neoplasms

Interventions

Cyclophosphamidefludarabinefludarabine phosphateInterleukin-2aldesleukinMesna

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue DiseasesCentral Nervous System NeoplasmsNervous System NeoplasmsNervous System Diseases

Intervention Hierarchy (Ancestors)

Phosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsInterleukinsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsLymphokinesProteinsBiological FactorsAlkanesulfonatesAlkanesulfonic AcidsAlkanesHydrocarbons, AcyclicSulfhydryl CompoundsSulfur CompoundsSulfonic AcidsSulfur Acids

Study Officials

  • Rodabe N. Amaria, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 10, 2006

First Posted

June 20, 2006

Study Start

February 1, 2006

Primary Completion (Estimated)

February 28, 2030

Study Completion (Estimated)

February 28, 2030

Last Updated

March 20, 2026

Record last verified: 2026-03

Locations