NCT00067808

Brief Summary

The goal of this clinical research study is to learn if decitabine (given at 3 different doses) can help to control Myelodysplastic Syndrome (MDS). The safety of these 3 treatments will also be studied.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
128

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Oct 2003

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 27, 2003

Completed
1 day until next milestone

First Posted

Study publicly available on registry

August 28, 2003

Completed
1 month until next milestone

Study Start

First participant enrolled

October 1, 2003

Completed
5.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2009

Completed
2.1 years until next milestone

Results Posted

Study results publicly available

May 26, 2011

Completed
Last Updated

August 7, 2012

Status Verified

August 1, 2012

Enrollment Period

5.6 years

First QC Date

August 27, 2003

Results QC Date

September 25, 2009

Last Update Submit

August 1, 2012

Conditions

Keywords

Myelodysplastic SyndromeChronic Myelomonocytic LeukemiaMDSDecitabineDacogenMethylation

Outcome Measures

Primary Outcomes (1)

  • Participant Responses

    Objective responses by International Working Group criteria: 'Complete Response' (CR) defined as Normalization of the peripheral blood and bone marrow with \<5% bone marrow blasts, a peripheral blood granulocyte count \> (1.0 x 109/ L, and a platelet count \> 100 x 109/L); 'Other Response' including Partial Remission (PR) defined as above, except for the presence of 6-15% marrow blasts, or 50% reduction if \<15% at start of treatment combined with participants who meet all criteria for CR except for platelet recovery to \>100 x 109/L; and 'No Response'.

    Response to treatment after 8 weeks of therapy

Study Arms (3)

Decitabine 10 mg/m^2 IV

ACTIVE COMPARATOR

10 mg/m\^2 intravenous (IV) over 1 hour daily for 10 days

Drug: Decitabine

Decitabine 20 mg/m2 IV

ACTIVE COMPARATOR

20 mg/m2 IV over 1 hour daily for 5 days

Drug: Decitabine

Decitabine 20 mg/m2 SQ

ACTIVE COMPARATOR

20 mg/m2 subcutaneous (SQ) daily for 5 days

Drug: Decitabine

Interventions

10 mg/m\^2 by vein over 1 hour daily for 10 days

Also known as: Dacogen
Decitabine 10 mg/m^2 IV

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • MDS and 5% or more marrow blasts, or IPSS risk intermediate 1-2 or high risk; or chronic myelomonocytic leukemia
  • Performance status 0-2 (Eastern Cooperative Oncology Group (ECOG) scale); adequate hepatic (bilirubin \< 2 mg/dl) and renal functions (creatinine \<2mg/dl); New York Heart Association (NYHA) cardiac status III-IV excluded.
  • Signed informed consent
  • No prior intensive combination chemotherapy or high-dose ara-C (\>/= 1g/m2 per dose). Prior biologic therapies, targeted therapies and single agent chemotherapy allowed.
  • Patients must have been off chemotherapy for 2 weeks prior to entering this study and recovered from the toxic effects of that therapy, unless there is evidence of rapidly progressive disease. Use of Hydroxyurea for patients with rapidly proliferative disease is allowed for the first two weeks on therapy.

You may not qualify if:

  • Nursing and pregnant females are excluded. Patients of childbearing potential should practice effective methods of contraception. Should a woman become pregnant or suspect she is pregnant while participating in this study, she should inform her treating physician immediately.
  • Patients with active and uncontrolled infections
  • Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, or psychiatric illness/social situations that would limit compliance with study requirements

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of Texas - MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Publications (1)

  • Oki Y, Jelinek J, Shen L, Kantarjian HM, Issa JP. Induction of hypomethylation and molecular response after decitabine therapy in patients with chronic myelomonocytic leukemia. Blood. 2008 Feb 15;111(4):2382-4. doi: 10.1182/blood-2007-07-103960. Epub 2007 Nov 30.

Related Links

MeSH Terms

Conditions

Myelodysplastic SyndromesLeukemia, Myelomonocytic, Chronic

Interventions

Decitabine

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesLeukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsMyelodysplastic-Myeloproliferative DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

AzacitidineAza CompoundsOrganic ChemicalsCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleosidesNucleic Acids, Nucleotides, and NucleosidesRibonucleosides

Results Point of Contact

Title
Hagop Kantarjian, MD / Professor
Organization
The University of Texas M. D. Anderson Cancer Center

Study Officials

  • Hagop M Kantarjian, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 27, 2003

First Posted

August 28, 2003

Study Start

October 1, 2003

Primary Completion

May 1, 2009

Study Completion

May 1, 2009

Last Updated

August 7, 2012

Results First Posted

May 26, 2011

Record last verified: 2012-08

Locations