NCT07544654

Brief Summary

This study is open to adults with advanced extrapulmonary neuroendocrine cancer. The purpose of this study is to find out if a study medicine called obrixtamig plus standard chemotherapy (carboplatin and etoposide) improves survival when compared to standard chemotherapy (carboplatin and etoposide) alone. Obrixtamig is an antibody-like molecule that may help the immune system fight cancer. Another purpose of the study is to test a medical device being developed to measure levels of the tumour marker delta-like ligand 3 (DLL3). Participants are put into 2 groups randomly, which means by chance. One group (treatment arm) receives obrixtamig and standard chemotherapy followed by obrixtamig alone for up to 3 years. The other group (control arm) receives standard chemotherapy without obrixtamig for about 4 months. All treatments are given as infusions into a vein. During the study, participants in both groups visit the study site regularly. Participants in the treatment arm stay overnight at the study site following the first 2 obrixtamig treatments. The doctors regularly check participants' health and take note of any unwanted effects. At some of the visits, doctors check the size of the tumour(s). The results are compared between the 2 groups to see whether the treatment works.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
390

participants targeted

Target at P50-P75 for phase_3

Timeline
43mo left

Started Jun 2026

Typical duration for phase_3

Geographic Reach
28 countries

159 active sites

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 16, 2026

Completed
6 days until next milestone

First Posted

Study publicly available on registry

April 22, 2026

Completed
2 months until next milestone

Study Start

First participant enrolled

June 15, 2026

Expected
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 13, 2029

Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 13, 2029

Last Updated

May 6, 2026

Status Verified

May 1, 2026

Enrollment Period

3.5 years

First QC Date

April 16, 2026

Last Update Submit

May 4, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall survival (OS)

    defined as the time from randomisation until death from any cause

    Up to 38 months

Secondary Outcomes (9)

  • Progression-free survival (PFS)

    Up to 38 months

  • Change from baseline to Week 19 in the physical functioning domain of the EORTC QLQ-C30

    At baseline, up to week 19

  • Objective response (OR)

    Up to 38 months

  • Duration of response (DoR)

    Up to 38 months

  • Disease control (DC)

    Up to 38 months

  • +4 more secondary outcomes

Study Arms (2)

Obrixtamig + carboplatin + etoposide

EXPERIMENTAL

Treatment arm

Drug: ObrixtamigDrug: CarboplatinDrug: EtoposideDevice: Ventana DLL3 RxDx assay

Carboplatin + etoposide

ACTIVE COMPARATOR

Control arm

Drug: CarboplatinDrug: EtoposideDevice: Ventana DLL3 RxDx assay

Interventions

Obrixtamig

Obrixtamig + carboplatin + etoposide

Carboplatin

Carboplatin + etoposideObrixtamig + carboplatin + etoposide

Etoposide

Carboplatin + etoposideObrixtamig + carboplatin + etoposide

Ventana DLL3 RxDx assay

Carboplatin + etoposideObrixtamig + carboplatin + etoposide

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with poorly differentiated unresectable locally advanced or metastatic extrapulmonary neuroendocrine carcinoma (epNEC) with Ki-67 \>20% or mitotic rate mitotic rate with number of mitoses \>20 per 2 mm2, regardless of primary site (including site of unknown origin)
  • Patients with tumours with mixed histologies are eligible only if neuroendocrine carcinoma component is predominant and represents more than 70% of the overall tumour tissue
  • No prior systemic treatment for unresectable locally advanced or metastatic epNEC (except for the completed one cycle of standard platinum + etoposide). Prior peri-operative chemotherapy or -radiation for curative intention is allowed if at least 6 months have elapsed between completion of this therapy and diagnosis of unresectable locally advanced or metastatic disease
  • Patients who have finished one cycle of standard platinum + etoposide regimen as first-line treatment (Cycle 0: etoposide with carboplatin or cisplatin, administered at a minimum dose of cisplatin 75 mg/m2 or carboplatin area under the curve (AUC) 5 and etoposide 80 mg/m2) prior to randomisation
  • Patients must comply with criteria for receiving further chemotherapy treatment as first-line standard of care (SoC) treatment within 28 days after the start of the initial chemotherapy (Cycle 0)
  • Adequate archival Formalin-Fixed Paraffin-Embedded (FFPE) tumour tissue, as specified in the Laboratory Manual, must be available for central laboratory analysis of Delta-like ligand 3 (DLL3) expression status. Tumours must be positive (as defined in the diagnostic study protocol) for DLL3 expression status assessed by investigational VENTANA DLL3 (SP347) RxDx Assay
  • Eastern Cooperative Oncology Group (ECOG) score of 0 or 1

You may not qualify if:

  • Presence of leptomeningeal disease and/or carcinomatous meningitis
  • Patients with diagnosis of Merkel cell carcinoma or medullary thyroid carcinoma
  • Patients with neuroendocrine prostate cancer
  • Patients with well-differentiated neuroendocrine tumours of any grade according to the world health organization (WHO) classification, 5th edition
  • Patients with a history of well differentiated Neuroendocrine tumour (NET) tumour that transformed into poorly differentiated Neuroendocrine carcinoma (NEC)
  • Previous treatment with obrixtamig or other DLL3-targeting therapies (e.g. T-cell engager (TcEs), cell therapies, antibody-drug conjugates, or radiopharmaceuticals)
  • Previous treatment with anti-PD-1 or programmed death ligand 1 (PD-L1) therapies during the one cycle of standard platinum + etoposide first-line chemotherapy (Cycle 0)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (163)

Mayo Clinic

Scottsdale, Arizona, 85259, United States

Location

City of Hope-Duarte-56419

Duarte, California, 91010, United States

Location

Stanford Cancer Center

Palo Alto, California, 94304, United States

Location

University of California San Francisco

San Francisco, California, 94158, United States

Location

University of California Los Angeles

Santa Monica, California, 90404, United States

Location

Mayo Clinic - Florida

Jacksonville, Florida, 32224, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

The Skip Viragh Outpatient Cancer Research Building

Baltimore, Maryland, 21287, United States

Location

Mayo Clinic, Rochester

Rochester, Minnesota, 55905, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10022, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15232, United States

Location

University of Tennessee

Knoxville, Tennessee, 37920, United States

Location

SCRI Oncology Partners

Nashville, Tennessee, 37203, United States

Location

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Centro Medico Reumatologico - OMI

CABA, 1015, Argentina

Location

Hospital Britanico de Buenos Aires

CABA, 1280AEB, Argentina

Location

Clinica Privada Independencia

Munro, B1605, Argentina

Location

Sanatorio Parque S.A.

Rosario, S2000DSV, Argentina

Location

Royal North Shore Hospital

St Leonards, New South Wales, 2065, Australia

Location

Flinders Medical Centre

Bedford Park, South Australia, 5042, Australia

Location

Peter MacCallum Cancer Centre

Melbourne, Victoria, 3000, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

Medical University Graz

Graz, 8036, Austria

Location

AKH - Medical University of Vienna

Vienna, 1090, Austria

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Edegem - UNIV UZ Antwerpen

Edegem, 2650, Belgium

Location

UZ Leuven

Leuven, 3000, Belgium

Location

Centre Hospitalier Universitaire de Liège

Liège, 4000, Belgium

Location

Hospital de Amor

Barretos, 14784-400, Brazil

Location

Instituto D'Or de Pesquisa E Ensino - Pe

Recife, 50070-480, Brazil

Location

Fundacao Faculdade Regional de Medicina de Sao Jose do Rio Preto

São José do Rio Preto, 15090-000, Brazil

Location

ICESP - Instituto do Cancer do Estado de Sao Paulo

São Paulo, 01246-000, Brazil

Location

A.C. Camargo

São Paulo, 01509-010, Brazil

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3M5, Canada

Location

Instituto Oncológico FALP

Providencia, Chile

Location

Bradford Hill- Centro de Investigación Clínica

Recoleta, 8420383, Chile

Location

Clínica Alemana de Santiago S.A.

Santiago, 7650568, Chile

Location

Beijing Cancer Hospital

Beijing, 100142, China

Location

Beijing GoBroad Hospital

Beijing, 102200, China

Location

The First Hospital of Jilin University

Changchun, 130021, China

Location

Xiangya Hospital, Central South University

Changsha, 410008, China

Location

Hunan Province Tumor Hospital

Changsha, 410013, China

Location

Sichuan Cancer Hospital

Chengdu, 610041, China

Location

West China Hospital, Sichuan University

Chengdu, 610041, China

Location

Chongqing University Affiliated Cancer Hospital

Chongqing, 400000, China

Location

Fujian Cancer Hospital

Fuzhou, 350014, China

Location

The First Affiliated Hospital,Sun Yat-sen University

Guangzhou, 510080, China

Location

Sir Run Run Shaw Hospital, Zhejiang University, School of Medicine

Hangzhou, 310016, China

Location

Harbin Medical University Cancer Hospital

Harbin, 150081, China

Location

Qilu Hospital, Shangdong University

Jinan, 250012, China

Location

Shandong Cancer Hospital

Jinan, 250117, China

Location

Linyi Cancer Hospital

Linyi, 276034, China

Location

The First Affiliated Hospital of Henan University of Science and Technology

Luoyang, 471003, China

Location

The Affiliated Cancer Hospital, Guangxi Medical University

Nanning, 530021, China

Location

Shanghai General Hospital

Shanghai, 200080, China

Location

Hubei Cancer Hospital

Wuhan, 430000, China

Location

First Affiliated Hospital of Xi'an JiaoTong University

Xi'an, 710061, China

Location

First Affiliated Hospital of Xiamen University

Xiamen, 361003, China

Location

Henan Cancer Hospital

Zhengzhou, 450003, China

Location

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, 450052, China

Location

Masaryk Memorial Cancer Institute

Brno, 65653, Czechia

Location

University Hospital Hradec Kralove (FNHK)

Hradec Králové, 50005, Czechia

Location

Aarhus University Hospital

Aarhus N, 8200, Denmark

Location

Rigshospitalet

Copenhagen, 2100, Denmark

Location

Odense University Hospital

Odense C, 5000, Denmark

Location

Helsinki University Hospital

Helsinki, 00290, Finland

Location

KYS Sädesairaala

Kuopio, 70029, Finland

Location

Tampere University Hospital

Tampere, 33520, Finland

Location

Turku University Hospital / TYKS

Turku, 20520, Finland

Location

Hôpital Beaujon

Clichy, 92110, France

Location

HOP François Mitterrand

Dijon, 21000, France

Location

Hôpital Edouard Herriot

Lyon, 69437, France

Location

INS Paoli-Calmettes

Marseille, 13009, France

Location

HOP Haut-Lévêque

Pessac, 33604, France

Location

CTR Eugène Marquis

Rennes, 35042, France

Location

Hôpital Rangueil - CHU de Toulouse

Toulouse, 31059, France

Location

Institut Gustave Roussy

Villejuif, 94800, France

Location

DRK Kliniken Berlin Köpenick

Berlin, 12559, Germany

Location

Universitätsklinikum Bonn AöR

Bonn, 53127, Germany

Location

Universitätsklinikum Köln (AöR)

Cologne, 50937, Germany

Location

Technische Universität Dresden

Dresden, 01307, Germany

Location

Universitätsklinikum Erlangen

Erlangen, 91054, Germany

Location

Universitätsklinikum Freiburg

Freiburg im Breisgau, 79106, Germany

Location

Asklepios Klinik St Georg

Hamburg, 20099, Germany

Location

Universitätsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Universitätsmedizin der Johannes Gutenberg-Universität Mainz

Mainz, 55131, Germany

Location

Westfälische Wilhelms-Universität Münster

Münster, 48149, Germany

Location

Universitätsklinikum Tübingen

Tübingen, 72076, Germany

Location

Universitätsklinikum Würzburg AÖR

Würzburg, 97078, Germany

Location

Prince of Wales Hospital-Hong Kong-20715

Hong Kong, 999077, Hong Kong

Location

Queen Mary Hospital

Hong Kong, 999077, Hong Kong

Location

Soroka Univ. Medical Center

Beersheba, 84101, Israel

Location

Rambam Health Care Campus

Haifa, 3109601, Israel

Location

Hadassah Medical Center, Ein-Karem

Jerusalem, 9112001, Israel

Location

Sourasky Medical Center

Tel Aviv, 6093246, Israel

Location

Azienda Universitaria Ospedaliera Consorziale Policlinico Bari

Bari, 70124, Italy

Location

A. O. Universitaria Careggi

Florence, 50134, Italy

Location

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, 20133, Italy

Location

Istituto Europeo di Oncologia

Milan, 20141, Italy

Location

Istituto Nazionale IRCCS Tumori Fondazione Pascale

Naples, 80131, Italy

Location

Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

Palermo, 90129, Italy

Location

Fondazione Policlinico Universitario Campus Bio-medico

Roma, 00128, Italy

Location

Centro Ricerche Cliniche di Verona S.r.l.

Verona, 37134, Italy

Location

Aichi Cancer Center Hospital

Aichi, Nagoya, 464-8681, Japan

Location

National Cancer Center Hospital East

Chiba, Kashiwa, 277-8577, Japan

Location

Shikoku Cancer Center

Ehime, Matsuyama, 791-0280, Japan

Location

Kyushu University Hospital

Fukuoka, Fukuoka, 812-8582, Japan

Location

Hokkaido University Hospital

Hokkaido, Sapporo, 060-8648, Japan

Location

Kanazawa University Hospital

Ishikawa, Kanazawa, 920-8641, Japan

Location

Kanagawa Cancer Center

Kanagawa, Yokohama, 241-8515, Japan

Location

Kyoto University Hospital

Kyoto, Kyoto, 606-8507, Japan

Location

Tohoku University Hospital

Miyagi, Sendai, 980-8574, Japan

Location

Okayama University Hospital

Okayama, Okayama, 700-8558, Japan

Location

Osaka International Cancer Institute

Osaka, Osaka, 541-8567, Japan

Location

Shizuoka Cancer Center

Shizuoka, Sunto-gun, 411-8777, Japan

Location

National Cancer Center Hospital

Tokyo, Chuo-ku, 104-0045, Japan

Location

Health Pharma Professional Research S.A. de C.V.

Mexico City, 03100, Mexico

Location

Nederlands Kanker Instituut - Antoni van Leeuwenhoek Amsterdam (METC AVL)

Amsterdam, 1066CX, Netherlands

Location

Universitair Medisch Centrum Groningen

Groningen, 9713 GZ, Netherlands

Location

Maastricht University Medisch Centrum

Maastricht, 6229 HX, Netherlands

Location

Erasmus Medisch Centrum

Rotterdam, 3015 CP, Netherlands

Location

Auckland City Hospital

Grafton / Auckland, 1023, New Zealand

Location

Haukeland Universitetssykehus

Bergen, 5021, Norway

Location

Oslo Universitetssykehus HF, Radiumhospitalet

Oslo, N-0379, Norway

Location

Helse Stavanger, Stavanger Universitetssykehus

Stavanger, 4011, Norway

Location

St. Olavs Hospital, Universitetssykehuset i Trondheim

Trondheim, 7030, Norway

Location

Medical University Gdansk

Gdansk, 80-214, Poland

Location

Silesian Medical University in Katowice

Katowice, 40514, Poland

Location

IPO Lisboa Francisco Gentil, EPE

Lisbon, 1099-023, Portugal

Location

Hospital Lusíadas Lisboa

Lisbon, 1500-458, Portugal

Location

Unidade Local de Saúde Santa Maria

Lisbon, 1699-035, Portugal

Location

Hospital CUF Porto

Porto, 4100-180, Portugal

Location

IPO Porto Francisco Gentil, EPE

Porto, 4200-072, Portugal

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Severance Hospital

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Institut Català d'Oncologia de Badalona

Badalona, 8916, Spain

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Universitario Ramon Y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario Fundacion Jimenez Diaz

Madrid, 28040, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Regional Universitario de Málaga

Málaga, 29010, Spain

Location

Complejo Hospitalario de Navarra

Pamplona, 31008, Spain

Location

Hospital Universitario Marqués de Valdecilla

Santander, 39008, Spain

Location

Hospital Virgen del Rocío

Seville, 41013, Spain

Location

Hospital Clinico De Valencia (INCLIVA)

Valencia, 46010, Spain

Location

Sahlgrenska Universitetsjukhuset

Gothenburg, 41345, Sweden

Location

Skånes universitetssjukhus

Lund, 22185, Sweden

Location

Uppsala University Hospital

Uppsala, 751 85, Sweden

Location

National Cheng Kung University Hospital

Tainan, 70403, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 112201, Taiwan

Location

Chang Gung Memorial Hospital, Linkou

Taoyuan City, 333, Taiwan

Location

Addenbrooke's Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

Western General Hospital

Edinburgh, EH4 2XU, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, G12 0YN, United Kingdom

Location

Guy's Hospital

London, SE1 9RT, United Kingdom

Location

The Christie Hospital

Manchester, M20 4BX, United Kingdom

Location

Related Links

MeSH Terms

Interventions

CarboplatinEtoposide

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPolycyclic CompoundsGlucosidesGlycosidesCarbohydrates

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 16, 2026

First Posted

April 22, 2026

Study Start (Estimated)

June 15, 2026

Primary Completion (Estimated)

December 13, 2029

Study Completion (Estimated)

December 13, 2029

Last Updated

May 6, 2026

Record last verified: 2026-05

Data Sharing

IPD Sharing
Will share

Once the criteria in section "Time Frame" are fulfilled, researchers can use the following link https://www.clinicalstudies.boehringer-ingelheim.com/msw/datasharing to request access to the clinical study documents regarding this study, and upon a signed "Document Sharing Agreement". Furthermore, researchers can request access to the clinical study data, for this and other listed studies, after the submission of a research proposal and according to the terms outlined in the website.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
One year after the approval has been granted by major Regulatory Authorities and after the primary manuscript has been accepted for publication, or after termination of the development program.
Access Criteria
For study documents - upon signing of a 'Document Sharing Agreement'. For study data - 1. after the submission and approval of the research proposal (checks will be performed by the sponsor and/or the independent review panel, including checking that the planned analysis does not compete with sponsor's publication plan); 2. and upon signing of a legal agreement.
More information

Locations