NCT06541665

Brief Summary

To confirm the tolerability and safety of combined administration of ONO-4059 and R-MPV therapy in untreated PCNSL patients.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at P25-P50 for phase_1

Timeline
28mo left

Started May 2024

Longer than P75 for phase_1

Geographic Reach
1 country

44 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress46%
May 2024Aug 2028

Study Start

First participant enrolled

May 17, 2024

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

August 2, 2024

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 7, 2024

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 28, 2028

Expected
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 31, 2028

Last Updated

June 3, 2025

Status Verified

May 1, 2025

Enrollment Period

4 years

First QC Date

August 2, 2024

Last Update Submit

June 1, 2025

Conditions

Outcome Measures

Primary Outcomes (2)

  • Tolerability evaluation

    The number of subjects who experienced adverse events and side effects will be tallied. In the tolerability evaluation part, the number of subjects who experienced Dose Limiting Toxicity(DLT) will be tallied

    29 Days

  • Incidence and severity of adverse events (AEs) and serious adverse events (SAEs) during induction

    Adverse events at each visit with the NCI CTCAE v5.0 used as a guide for the grading of severity.

    2 years

Secondary Outcomes (5)

  • Summary of plasma tirabrutinib concentration at trough and post 2 hours dosing

    30days

  • Duration of response (DOR)

    2 years

  • Time to response (TTR)

    1 year

  • Best overall response (BOR)

    1 year

  • Complete response rate (CRR)

    4 months

Study Arms (1)

Tirabrutinib + R-MPV in patients with newly diagnosed, treatment naïve PCNSL

EXPERIMENTAL
Drug: ONO-4059Drug: RituximabDrug: MethotrexateDrug: ProcarbazineDrug: Vincristine

Interventions

Specified dose, once daily

Also known as: Tirabrutinib Hydrochloride
Tirabrutinib + R-MPV in patients with newly diagnosed, treatment naïve PCNSL

Specified dose on specified days

Tirabrutinib + R-MPV in patients with newly diagnosed, treatment naïve PCNSL

Specified dose on specified days

Tirabrutinib + R-MPV in patients with newly diagnosed, treatment naïve PCNSL

Specified dose on specified days

Tirabrutinib + R-MPV in patients with newly diagnosed, treatment naïve PCNSL

Specified dose on specified days

Tirabrutinib + R-MPV in patients with newly diagnosed, treatment naïve PCNSL

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients diagnosed with PCNSL
  • Patients who have not received treatment for PCNSL in the past
  • Patients with ECOG Performance Status 0-2
  • Patients expected to survive for 6 months or more

You may not qualify if:

  • Patients with intraocular PCNSL without brain lesions
  • Patients are unable to swallow oral medications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (44)

Aichi Cancer Center

Nagoya, Aichi-ken, Japan

Location

Nagoya City University Hospital

Nagoya, Aichi-ken, Japan

Location

Akita University Hospital

Akita, Akita, Japan

Location

Juntendo University Urayasu Hospital

Urayasu-shi, Chiba, Japan

Location

Fukuoka University Hospital

Fukuoka, Fukuoka, Japan

Location

Kyushu University Hospital

Fukuoka, Fukuoka, Japan

Location

Hospital of the University of Occupational and Environmental Health,Japan

Kitakyushu-shi, Fukuoka, Japan

Location

Kurume University Hospital

Kurume-shi, Fukuoka, Japan

Location

Fukushima Medical University Hospital

Fukushima, Fukushima, Japan

Location

Gifu University Hospital (Tokai National Higher Education and Research System)

Gifu, Gifu, Japan

Location

Gunma University Hospital

Maebashi, Gunma, Japan

Location

Sapporo Medical University Hospital

Sapporo, Hokkaido, Japan

Location

Kobe City Medical Center General Hospital

Kobe, Hyōgo, Japan

Location

Hyogo Medical University Hospital

Nishinomiya-shi, Hyōgo, Japan

Location

University of Tsukuba Hospital

Tsukuba, Ibaraki, Japan

Location

Kanazawa Medical University Hospital

Kahoku-gun, Ishikawa-ken, Japan

Location

Kagawa University Hospital

Kita-gun, Kagawa-ken, Japan

Location

St. Marianna University Hospital

Kawasaki-shi, Kanagawa, Japan

Location

Yokohama City University Hospital

Yokohama, Kanagawa, Japan

Location

Kochi Medical School Hospital

Nankoku-shi, Kochi, Japan

Location

University of Miyazaki Hospital

Miyazaki, Miyazaki, Japan

Location

NAGASAKI University Hospital

Nagasaki, Nagasaki, Japan

Location

Kindai University Nara Hospital

Ikoma-shi, Nara, Japan

Location

Nara Medical University

Kashihara-shi, Nara, Japan

Location

Niigata University Medical & Dental Hospital

Niigata, Niigata, Japan

Location

Oita University Hospital

Yufu-shi, Oita Prefecture, Japan

Location

Kurashiki Central Hospital

Kurashiki-shi, Okayama-ken, Japan

Location

Osaka International Cancer Institute

Osaka, Osaka, Japan

Location

Kindai University Hospital

Osakasayama-shi, Osaka, Japan

Location

Osaka University Hospital

Suita-shi, Osaka, Japan

Location

Saga University Hospital

Saga, Saga-ken, Japan

Location

Saitama Medical Center

Kawagoe-shi, Saitama, Japan

Location

Shizuoka Cancer Center

Sunto-gun, Shizuoka, Japan

Location

Dokkyo Medical University Hospital

Shimotsuga-gun, Tochigi, Japan

Location

Institute of Science Tokyo Hospital

Bunkyo-ku, Tokyo, Japan

Location

The Cancer Institute Hospital of JFCR

Koto-ku, Tokyo, Japan

Location

National Hospital Organization Disaster Medical Center

Midorichō, Tokyo, Japan

Location

The Jikei University Hospital

Minato-ku, Tokyo, Japan

Location

Toranomon Hospital

Minato-ku, Tokyo, Japan

Location

Tokyo Medical University Hospital

Shinjuku-ku, Tokyo, Japan

Location

Tokyo Women's Medical University Hospital

Shinjuku-ku, Tokyo, Japan

Location

Toyama University Hospital

Toyama, Toyama, Japan

Location

Yamaguchi University Hospital

Ube-shi, Yamaguchi, Japan

Location

University of Yamanashi Hospital

Chuo-shi, Yamanashi, Japan

Location

MeSH Terms

Interventions

tirabrutinibRituximabMethotrexateProcarbazineVincristine

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsAminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsBenzamidesAmidesOrganic ChemicalsBenzoatesAcids, CarbocyclicCarboxylic AcidsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsIndolesIndolizidinesIndolizines

Study Officials

  • Project Leader

    Ono Pharmaceutical Co. Ltd

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 2, 2024

First Posted

August 7, 2024

Study Start

May 17, 2024

Primary Completion (Estimated)

April 28, 2028

Study Completion (Estimated)

August 31, 2028

Last Updated

June 3, 2025

Record last verified: 2025-05

Data Sharing

IPD Sharing
Will not share

Locations