NCT06504381

Brief Summary

This is a multicenter, open-label study of DB107-RRV (formerly Toca 511) and DB107-FC (formerly Toca FC) when administered following surgical resection in newly diagnosed High Grade Glioma (HGG) patients. The study is designed to evaluate whether treatment with DB107-RRV in combination with DB107-FC when added to standard of care provides clinical benefit to newly diagnosed HGG when compared to historical performance previously determined in well controlled clinical trials published in the peer reviewed literature. This study is going to be conducted in newly diagnosed HGG patients receiving with maximum surgical resection treatment followed by radiation and temozolomide treatment using the established Stupp Protocol for O6-methylguanine-DNA methyl-transferase (MGMT) methylated patients or radiation therapy for MGMT unmethylated patients.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P75+ for phase_1

Timeline
192mo left

Started Jan 2025

Longer than P75 for phase_1

Geographic Reach
1 country

5 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress8%
Jan 2025Jan 2042

First Submitted

Initial submission to the registry

July 9, 2024

Completed
7 days until next milestone

First Posted

Study publicly available on registry

July 16, 2024

Completed
6 months until next milestone

Study Start

First participant enrolled

January 8, 2025

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 31, 2028

Expected
14 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 31, 2042

Last Updated

March 11, 2026

Status Verified

March 1, 2026

Enrollment Period

3.1 years

First QC Date

July 9, 2024

Last Update Submit

March 9, 2026

Conditions

Keywords

Gene therapyCombination therapy

Outcome Measures

Primary Outcomes (3)

  • Proportion of participants with dose limiting toxicities (Phase I)

    Tolerability is defined as the proportion of participants receiving at least one dose of DB107-RRV and DB107-FC with a reported dose-limiting toxicity for all participants in Phase I.

    Up to 1 year

  • Proportion of participants with treatment-emergent adverse events (Phase I)

    Safety is defined as the proportion of participants with treatment-emergent adverse events as classified by the Medical Dictionary for Regulatory Activities (MEDDRA) preferred terms and graded for severity according to the NCI Common Terminology Criteria for Adverse Events (CTCAE) version 5.0 for participants in Phase 1.

    Up to 3 years

  • Median Progression free survival (PFS) by biomarker status (Phase IIa)

    PFS is defined as time from first receipt of DB107-RRV until progression or death, whichever occurs first for newly diagnosed HGG patients with unmethylated MGMT and methylated MGMT. Participants without an event will be censored at the last disease assessment. PFS (months) = (earlier date of documentation of progression of disease or death/censored - date of first dose of DB107-RRV+1) (365.25/12) using Immunotherapy Response Assessment for Neuro-Oncology (iRANO) criteria to determine disease status. The median and the 95% confidence interval will be estimated using the Kaplan-Meier method.

    Up to 3 years

Secondary Outcomes (6)

  • Recommended Phase 2 Dose (RP2D) (Phase I)

    Up to 1 year

  • Overall Response Rate (ORR) (Phase IIa)

    Up to 5 years

  • Median Progression-free survival (PFS) at 6 months (Phase IIa)

    Up to 6 months

  • Median Progression-free survival (PFS) (Phase IIa)

    6 months

  • Median Overall Survival (OS) at 6 months (Phase IIa)

    6 months

  • +1 more secondary outcomes

Study Arms (2)

No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

EXPERIMENTAL

Participants receive a 4.0 x 10\^8 transduction units per milliliter (TU/mL)) dose of DB107-RRV intracranially (IC) at resection and a 1.4 x 10\^9 TU/mL dose IV prior to leaving surgery room. Participants have up to 6 weeks for surgical recovery. Unmethylated MGMT participants receive 300 mg/kg/day DB107-FC PO during RT over 5 days during weeks 1-2, \& 5-6. 2 gray (Gy)/day standard of care (SOC) RT will be given for 5 consecutive days for 6 weeks. After RT, participants receive 1.4 x 10\^9 TU/mL of DB107-RRV IV on days 7 and 14 and continue during a 4-week rest period between RT and adjuvant therapy. Participants who begin adjuvant therapy receive 300 mg/kg/day DB107-FC PO on days 1-5 of a 28-day cycle up to 6 cycles or until PD. Participants with no PD during adjuvant treatment may receive additional cycles of DB107-FC until PD, withdrawal, death or study closure. Participants will be followed up for safety and survival status for up to 15 years.

Genetic: DB107-RRVDrug: DB107-FCRadiation: Radiation Therapy (RT)Drug: TemozolomideProcedure: Magnetic Resonance Imaging (MRI)Procedure: Surgical resection

Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)

EXPERIMENTAL

Participants receive a 4.0 x 10\^8 TU/mL dose of DB107-RRV IC at resection and a 1.4 x 10\^9 TU/mL dose IV prior to prior to leaving surgery room. Participants have up to 6 weeks for surgical recovery. Low to high MGMT methylation participants receive 75 mg/m\^2 TMZ per SOC and 300mg/kg/day DB107-FC PO concurrent with 2 Gy/day over 5 consecutive days during weeks 1-2, \& 5-6. After RT, participants receive 1.4 x 10\^9 TU/mL DB107-RRV IV on days 7 and 14. IV DB107-RRV occurs during a 4-week rest period between RT and adjuvant portions of the protocol. Participants who begin adjuvant therapy receive 300 mg/kg/day DB107-FC PO on days 1-5 of a 28-day cycle for up to 6 cycles or until PD with 150-200 mg/m\^2 adjuvant TMZ per SOC on days 1-5 of each cycle for up to 6 cycles. Participants with no PD may continue to receive additional cycles of DB107-FC PD, withdrawal, death or study closure. Participants will be followed up for safety and survival status for up to 15 years.

Genetic: DB107-RRVDrug: DB107-FCRadiation: Radiation Therapy (RT)Drug: TemozolomideProcedure: Magnetic Resonance Imaging (MRI)Procedure: Surgical resection

Interventions

DB107-RRVGENETIC

Given intracranially (IC) during resection and intravenously (IV) immediately following

Also known as: Toca 511, Vocimagene amiretrorepvec
Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

Given orally (PO)

Also known as: Toca FC, Extended-release 5-fluorocytosine, 5-fluorocytosine
Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

Undergo standard of care MRI

Also known as: MR, MRI
Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

Undergo RT

Also known as: Radiation Treatment
Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

Given PO

Also known as: Temozolomide (TMZ)
Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

Undergo non-investigational tumor resection

Also known as: Surgical tumor resection, Brain surgery
Low to High MGMT Methylation (DB107-RRV, DB107-FC, Temozolomide (TMZ), Radiation therapy)No MGMT Methylation (DB107-RRV, DB107-FC, Radiation therapy)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participant has provided written informed consent.
  • Participant is between 18 years of age and 75 years of age, inclusive.
  • Participant must have a Karnofsky Performance Scale (KPS) of \>= 70.
  • Participant must have newly diagnosed adult-type diffuse gliomas (World Health Organization Classification 2021) that has not been previously treated with surgery, radiation or chemotherapy (specifically astrocytoma, Isocitrate dehydrogenase (IDH)-mutant or glioblastoma, IDH-wildtype).
  • Based on the pre-operative evaluation by neurosurgeon, participant is a candidate for \>= 80% resection of the enhancing region.
  • The primary tumor must be made available for central testing for IDH1 mutation, O6-methylguanine-DNA methyl-transferase (MGMT) methylation status.
  • Willing to provide a blood sample to determine Denovo Genomic Marker 7 (DGM7) status.
  • Laboratory values adequate for patient to undergo surgery, including:
  • Platelet count \>= 60,000/mm\^3
  • Hemoglobin \>= 10 g/dL
  • Absolute neutrophil count (ANC) \>= 1,500/mm\^3
  • Absolute lymphocyte count \>= 500/mm\^3
  • Total bilirubin \<=1.5 x upper limit of normal (ULN) (unless patient had Gilbert's syndrome)
  • alanine aminotransferase (ALT) \<= 2.5 x ULN
  • Estimated glomerular filtration rate of at least 50 mL/min by Cockcroft Gault Formula
  • +6 more criteria

You may not qualify if:

  • Prior treatment for High Grade Glioma (HGG).
  • Histological confirmed oligodendroglioma (IDH-mutant and 1p.19q-codeleted) or mixed glioma.
  • A contrast-enhancing brain tumor that is any of the following:
  • Multi-focal (defined as 2 separate areas of presumed tumor whether contrast enhancing or not, measuring at least 1cm in 2 planes that are not contiguous
  • Associated with either diffuse subependymal or leptomeningeal dissemination or
  • \> 5cm in any dimension.
  • Participant has or had an active infection requiring antibiotic, antifungal or antiviral therapy in the 4 weeks preceding study Cycle 1: Day 1.
  • Participant has any bleeding diathesis, or must take anticoagulants, or antiplatelet agents, including nonsteroidal anti-inflammatory drugs (NSAIDs), at the time of the scheduled resection that cannot be interrupted for surgery.
  • Participant is HIV positive.
  • Participant has Hepatitis B (positive test for hepatitis B surface antigen (HBsAg) or hepatitis B core antibody (HBcAb) and positive test for hepatitis B Virus (HBV) DNA) or Hepatitis C (positive tests for hepatitis C Virus (HCV) Antibody and HCV-RNA) or Hepatitis B and C co-infection (positive test for HBsAg or HBcAb and positive test for HCV Antibody).
  • Participant has a history of allergy or intolerance to flucytosine (DB107-FC).
  • Participant has a gastrointestinal disease that would, in the opinion of the Investigator, prevent him or her from being able to swallow or absorb flucytosine.
  • Participant intends to undergo treatment with the Gliadel® wafer at the time of resection surgery or has received Gliadel® wafer \< 30 days from Cycle 1: Day 1.
  • Severe pulmonary, cardiac or other systemic disease, which as per Investigator assessment would prevent surgical resection.
  • Participant who have any other disease or condition, which as per Investigator assessment may affect the participant's compliance or place the participant at higher risk of potential treatment complications.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

University of Southern California

Los Angeles, California, 90089, United States

RECRUITING

University of California, San Diego

San Diego, California, 92093, United States

RECRUITING

University of California

San Francisco, California, 94143, United States

RECRUITING

University of Miami

Miami, Florida, 33136, United States

RECRUITING

Northwell Health

Lake Success, New York, 11042, United States

RECRUITING

MeSH Terms

Conditions

Glioma

Interventions

vocimagene amiretrorepvecFlucytosineRadiotherapyTemozolomideMagnetic Resonance Spectroscopy

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Intervention Hierarchy (Ancestors)

CytosinePyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsTherapeuticsDacarbazineTriazenesOrganic ChemicalsImidazolesAzolesSpectrum AnalysisChemistry Techniques, AnalyticalInvestigative Techniques

Study Officials

  • Nicholas Butowski, MD

    University of California, San Francisco

    PRINCIPAL INVESTIGATOR
  • Noriyuki Kasahara, MD, PhD

    University of California, San Francisco

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Stephanie Lewis, RN

CONTACT

Neuro-Oncology New Patient Coordinator

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor in Residence

Study Record Dates

First Submitted

July 9, 2024

First Posted

July 16, 2024

Study Start

January 8, 2025

Primary Completion (Estimated)

January 31, 2028

Study Completion (Estimated)

January 31, 2042

Last Updated

March 11, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

De-identified data may be shared with study collaborators and research partners

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Through study closeout

Locations