NCT05614739

Brief Summary

The main purpose of this study is to learn more about the safety, side effects, and effectiveness of LOXO-435 by itself or when it is combined with other standard medicines that treat cancer. LOXO-435 may be used to treat cancer of the cells that line the urinary system and other solid tumor cancers that have a change in a particular gene (known as the FGFR3 gene). Participation could last up to 30 months (2.5 years) and possibly longer if the disease does not get worse.

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
535

participants targeted

Target at P75+ for phase_1

Timeline
11mo left

Started Jan 2023

Longer than P75 for phase_1

Geographic Reach
14 countries

82 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
Jan 2023Jun 2027

First Submitted

Initial submission to the registry

November 7, 2022

Completed
7 days until next milestone

First Posted

Study publicly available on registry

November 14, 2022

Completed
2 months until next milestone

Study Start

First participant enrolled

January 12, 2023

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2027

Last Updated

May 19, 2026

Status Verified

May 1, 2026

Enrollment Period

4.4 years

First QC Date

November 7, 2022

Last Update Submit

May 18, 2026

Conditions

Keywords

Bladder CancerBladder Urothelial CarcinomaUrinary Bladder CancerUrinary Tract CancerRenal Pelvis CancerUreter Cancer

Outcome Measures

Primary Outcomes (3)

  • Phase 1a: To determine the recommended dose of LOXO-435: Safety, number of participants with dose-limiting toxicities (DLTs)

    Number of participants with DLTs

    Minimum of the first 21-day cycle of LOXO-435 treatment

  • Phase 1b: To evaluate the preliminary antitumor activity of LOXO-435: Overall response rate (ORR)

    ORR per investigator assessed RECIST v1.1

    Up to approximately 30 months or 2.5 years

  • Number of Participants with One or More Treatment Emergent Adverse Events (TEAEs) and Serious Adverse Event(s) (SAEs) Considered by the Investigator to be Related to Study Drug Administration

    A summary of TEAEs and SAEs regardless of causality, will be reported in the Reported Adverse Events module

    Up to approximately 30 months or 2.5 years

Secondary Outcomes (10)

  • To assess the pharmacokinetics (PK) of LOXO-435: Area under the concentration versus time curve (AUC)

    Up to 2 months

  • To assess the PK of LOXO-435: Minimum plasma concentration (Cmin)

    Up to 2 months

  • To evaluate the preliminary antitumor activity of LOXO-435: Objective response rate (ORR)

    Up to approximately 30 months or 2.5 years]

  • To evaluate the preliminary antitumor activity of LOXO-435: Duration of response (DoR)

    Up to approximately 30 months or 2.5 years

  • To evaluate the preliminary antitumor activity of LOXO-435: Time to response (TTR)

    Up to approximately 30 months or 2.5 years

  • +5 more secondary outcomes

Study Arms (5)

Phase 1a: Cohort A1 LOXO-435 Monotherapy Dose Escalation

EXPERIMENTAL

LOXO-435 administered orally

Drug: LOXO-435

Phase 1a: Cohort A2 LOXO-435 Monotherapy Dose Optimization

EXPERIMENTAL

LOXO-435 administered orally

Drug: LOXO-435

Phase 1b: Cohort B1, B2, B4, and C1 LOXO-435 Monotherapy Dose Expansion

EXPERIMENTAL

LOXO-435 administered orally

Drug: LOXO-435

Phase 1b: Cohort B3 LOXO-435 Plus Pembrolizumab

EXPERIMENTAL

LOXO-435 administered orally in combination with pembrolizumab administered intravenously (IV)

Drug: LOXO-435Drug: Pembrolizumab

Phase 1b: Cohort B5 LOXO-435 Plus Pembrolizumab Plus Enfortumab Vedotin

EXPERIMENTAL

LOXO-435 administered orally in combination with pembrolizumab administered IV and enfortumab vedotin administered IV

Drug: LOXO-435Drug: PembrolizumabDrug: enfortumab vedotin

Interventions

Oral

Also known as: LY3866288
Phase 1a: Cohort A1 LOXO-435 Monotherapy Dose EscalationPhase 1a: Cohort A2 LOXO-435 Monotherapy Dose OptimizationPhase 1b: Cohort B1, B2, B4, and C1 LOXO-435 Monotherapy Dose ExpansionPhase 1b: Cohort B3 LOXO-435 Plus PembrolizumabPhase 1b: Cohort B5 LOXO-435 Plus Pembrolizumab Plus Enfortumab Vedotin

IV

Phase 1b: Cohort B3 LOXO-435 Plus PembrolizumabPhase 1b: Cohort B5 LOXO-435 Plus Pembrolizumab Plus Enfortumab Vedotin

IV

Phase 1b: Cohort B5 LOXO-435 Plus Pembrolizumab Plus Enfortumab Vedotin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have solid tumor cancer with an FGFR3 pathway alteration on molecular testing in tumor or blood sample that is deemed as actionable
  • Cohort A1: Presence of an alteration in FGFR3 or its ligands
  • Cohort A2, B2, B3, and B5: Histological diagnosis of urothelial cancer (UC) that is locally advanced or metastatic with a qualifying FGFR3 genetic alteration
  • Cohorts B1 and B4: Histological diagnosis of urothelial cancer that is locally advanced or metastatic
  • Cohort C1: Must have histological diagnosis of a non-urothelial solid tumor malignancy that is locally advanced or metastatic with a qualifying FGFR3 genetic alteration
  • Measurability of disease:
  • Cohort A1 and B3: Measurable or non-measurable disease as defined by Response Evaluation Criteria in Solid Tumors v 1.1 (RECIST v1.1)
  • Cohorts A2, B1, B2, B4, B5, and C1: Measurable disease required as defined by RECIST v1.1
  • Have adequate tumor tissue sample available. Participants with inadequate tissue sample availability may still be considered for enrollment upon review
  • Have an Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 for Cohorts A1, A2, B3, and B5
  • Less than or equal to 2 for Cohorts B1, B2, B4, and C1
  • Prior Systemic Therapy Criteria:
  • Cohort A1/C1: Participant has received all standard therapies for which the participant was deemed to be an appropriate candidate by the treating Investigator; OR the participant is refusing the remaining most appropriate standard of care treatment; OR there is no standard therapy available for the disease. There is no restriction on number of prior therapies.
  • Cohort A2, B2, B3 participants must have received at least one prior regimen, and cohorts B1 and B4 participants at least 2 prior regimens, in the locally advanced or metastatic setting
  • There is no restriction on number of prior therapies
  • +5 more criteria

You may not qualify if:

  • Participants with primary central nervous system (CNS) malignancy
  • Untreated or uncontrolled CNS metastases
  • Current evidence of corneal keratopathy or retinal disorder. Individuals with asymptomatic ophthalmic conditions may be eligible
  • Any serious unresolved toxicities from prior therapy
  • Significant cardiovascular disease
  • Prolongation of the QT interval corrected for heart rate using Fridericia's formula (QTcF)
  • Active uncontrolled systemic infection or other clinically significant medical conditions
  • Participants who are pregnant, lactating, or plan to breastfeed during the study or within 6 months of the last dose of study treatment. Participants who have stopped breastfeeding may be enrolled

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (82)

University of Arizona - Cancer Center

Tucson, Arizona, 85719, United States

RECRUITING

City of Hope

Duarte, California, 91010, United States

RECRUITING

University of California, Los Angeles (UCLA) - Division of Hematology-Oncology

Los Angeles, California, 90095, United States

RECRUITING

University of California - Irvine

Orange, California, 92868, United States

RECRUITING

University of California (UC) Davis Comprehensive Cancer Center

Sacramento, California, 95817, United States

RECRUITING

Stanford Medicine Cancer Center

Stanford, California, 94305, United States

RECRUITING

Advent Health

Orlando, Florida, 32804, United States

RECRUITING

Emory University Hospital

Atlanta, Georgia, 30322, United States

RECRUITING

The University of Chicago Medical Center (UCMC)

Chicago, Illinois, 60637, United States

RECRUITING

Indiana University (IU) Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202, United States

RECRUITING

Mary Bird Perkins Cancer Center

Baton Rouge, Louisiana, 70809, United States

RECRUITING

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

RECRUITING

Johns Hopkins Kimmel Cancer Center

Baltimore, Maryland, 21231-2410, United States

RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

RECRUITING

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

RECRUITING

Washington University in St. Louis

St Louis, Missouri, 63108, United States

RECRUITING

New York University (NYU)

New York, New York, 10016, United States

RECRUITING

Weill Cornell Medicine

New York, New York, 10021, United States

NOT YET RECRUITING

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

RECRUITING

Columbia University

New York, New York, 10032, United States

RECRUITING

David H. Koch Center for Cancer Care at Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

RECRUITING

University of Rochester - Wilmot Cancer Institute

Rochester, New York, 14642, United States

RECRUITING

Montefiore Medical Center

The Bronx, New York, 10467, United States

RECRUITING

University of North Carolina (UNC) - Chapel Hill

Chapel Hill, North Carolina, 27599, United States

RECRUITING

University of Cincinnati Medical Center (UCMC)

Cincinnati, Ohio, 45267, United States

RECRUITING

The Ohio State University (OSU)

Columbus, Ohio, 43210, United States

RECRUITING

University of Oklahoma - Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

RECRUITING

Penn Medicine Lancaster General Hospital - Ann B. Barshinger Cancer Institute

Lancaster, Pennsylvania, 17601, United States

RECRUITING

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

RECRUITING

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

RECRUITING

Allegheny General Hospital

Pittsburgh, Pennsylvania, 15212, United States

RECRUITING

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

RECRUITING

Carolina Urologic Research Center

Myrtle Beach, South Carolina, 29572, United States

RECRUITING

Sarah Cannon and HCA Research Institute

Nashville, Tennessee, 37203, United States

RECRUITING

Tennessee Oncology

Nashville, Tennessee, 37203, United States

RECRUITING

Vanderbilt University Medical Center

Nashville, Tennessee, 37212, United States

RECRUITING

University of Texas Southwestern

Dallas, Texas, 75244, United States

RECRUITING

Texas Oncology, P.A

Dallas, Texas, 75251, United States

RECRUITING

MD Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

University of Utah

Salt Lake City, Utah, 84132, United States

RECRUITING

University of Vermont Medical Center

Burlington, Vermont, 05401, United States

RECRUITING

St Vincent's Hospital

Darlinghurst, NSW 2010, Australia

RECRUITING

Calvary Mater Newcastle

Hunter Region, NSW, 2310, Australia

RECRUITING

GenesisCare North Shore

St Leonards, 2065, Australia

RECRUITING

Macquarie University

Sydney, 2109, Australia

RECRUITING

Princess Margaret Hospital

Toronto, M5G 2M9, Canada

RECRUITING

British Columbia Cancer Agency

Vancouver, V5Z 1J3, Canada

RECRUITING

Beijing Cancer hospital

Beijing, 100142, China

RECRUITING

Beijing Hospital

Beijing, 100730, China

RECRUITING

Sun Yat-Sen University- Cancer Center

Guangdong, 510060, China

RECRUITING

Sir Run Run Shaw Hospital, School of Medicine, Zhejiang University

Hangzhou, 310002, China

RECRUITING

Renji Hospital, Shanghai Jiaotong University School of Medicine

Shanghai, 200000, China

RECRUITING

Tianjin Medical University Cancer Institute & Hospital

Tianjin, 300060, China

RECRUITING

The First Affiliated Hospital of Xi'an Jiaotong University

Xi'an, 710061, China

RECRUITING

Zhejiang Provincial People's Hospital

Zhejiang, 310003, China

RECRUITING

Institut Bergonie

Bordeaux, 33076, France

RECRUITING

Centre Leon Berard

Lyon, 69373, France

RECRUITING

Institut Gustave Roussy

Villejuif, 94805, France

RECRUITING

Klinikum der Technischen Universitaet Muenchen (TUM Klinikum)

München, 81675, Germany

RECRUITING

Universitaetsklinikum Tuebingen

Tübingen, 72016, Germany

RECRUITING

Rabin Medical Center, Beilinson Hospital

Petah Tikva, 49100, Israel

RECRUITING

Sheba Medical Center

Tel Litwinsky, 5265601, Israel

RECRUITING

IRCCS Ospedale San Raffaele

Milan, 20132, Italy

RECRUITING

UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore

Roma, 00168, Italy

RECRUITING

National Cancer Center Hospital East

Chiba, 277-8577, Japan

RECRUITING

Aichi Cancer Center Hospital

Nagoya, 464-8681, Japan

RECRUITING

National Cancer Center Hospital

Tokyo, 104-0045, Japan

RECRUITING

Cancer Institute Hospital of JFCR

Tokyo, 135-8550, Japan

RECRUITING

Erasmus MC

GE Rotterdam, 3015, Netherlands

RECRUITING

Haukeland University Hospital

Bergen, 5021, Norway

RECRUITING

Oslo University Hospital

Oslo, 0450, Norway

RECRUITING

Seoul National University Hospital

Seoul, 03080, South Korea

RECRUITING

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

RECRUITING

Asan Medical Center

Seoul, 05505, South Korea

RECRUITING

Samsung Medical Center

Seoul, 06351, South Korea

RECRUITING

Institut Catala d'Oncologia - L'Hospitalet

Barcelona, 08908, Spain

RECRUITING

Fundacion MD Anderson International Espana

Madrid, 28033, Spain

RECRUITING

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

RECRUITING

South Texas Accelerated Research Therapeutics (START) Madrid - CIOCC

Madrid, 28050, Spain

RECRUITING

Hospital Universitario Marques De Valdecilla

Santander, 39008, Spain

RECRUITING

The Christie NHS Foundation Trust

Manchester, M20 4BX, United Kingdom

RECRUITING

Sheffield Teaching Hospitals NHS Foundation Trust

Sheffield, S10 2SB, United Kingdom

RECRUITING

Related Links

MeSH Terms

Conditions

Urinary Bladder NeoplasmsNeoplasm MetastasisUreteral NeoplasmsUrologic Neoplasms

Interventions

pembrolizumabenfortumab vedotin

Condition Hierarchy (Ancestors)

Urogenital NeoplasmsNeoplasms by SiteNeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesUrinary Bladder DiseasesUrologic DiseasesMale Urogenital DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsUreteral Diseases

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 8 AM - 8 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Central Study Contacts

Trial questions or participation questions: 1-877-CTLILLY (1-877-285-4559) or

CONTACT

Physicians interested in becoming principal investigators please contact

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Masking Details
Cohort A2 is randomized
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 7, 2022

First Posted

November 14, 2022

Study Start

January 12, 2023

Primary Completion (Estimated)

June 1, 2027

Study Completion (Estimated)

June 1, 2027

Last Updated

May 19, 2026

Record last verified: 2026-05

Data Sharing

IPD Sharing
Will not share

Locations